NCT01552434

Brief Summary

This phase I trial studies the side effects and best dose of bevacizumab and temsirolimus alone or in combination with valproic acid or cetuximab in treating patients with a malignancy that has spread to other places in the body or other disease that is not cancerous. Immunotherapy with bevacizumab and cetuximab, may induce changes in body's immune system and may interfere with the ability of tumor cells to grow and spread. Temsirolimus may stop the growth of tumor cells by blocking some of the enzymes needed for cell growth. Drugs used in chemotherapy, such as valproic acid, work in different ways to stop the growth of tumor cells, either by killing the cells, by stopping them from dividing, or by stopping them from spreading. It is not yet known whether bevacizumab and temsirolimus work better when given alone or with valproic acid or cetuximab in treating patients with a malignancy or other disease that is not cancerous.

Trial Health

75
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
155

participants targeted

Target at P75+ for phase_1

Timeline
6mo left

Started Oct 2012

Longer than P75 for phase_1

Geographic Reach
1 country

1 active site

Status
active not recruiting

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Progress97%
Oct 2012Oct 2026

First Submitted

Initial submission to the registry

March 7, 2012

Completed
6 days until next milestone

First Posted

Study publicly available on registry

March 13, 2012

Completed
7 months until next milestone

Study Start

First participant enrolled

October 16, 2012

Completed
14 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

October 31, 2026

Expected
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

October 31, 2026

Last Updated

April 24, 2026

Status Verified

October 1, 2025

Enrollment Period

14 years

First QC Date

March 7, 2012

Last Update Submit

April 21, 2026

Conditions

Keywords

TemsirolimusCCI-779ToriselBevacizumabAvastinrhuMAb-VEGFAnti-VEGF Monoclonal AntibodyAdvanced CancersAdvanced MalignancyMetastaticcancerCetuximabC225ErbituxIMC-C225Valproic Acid

Outcome Measures

Primary Outcomes (2)

  • Maximum tolerated dose (MTD) of bevacizumab, defined as the dose level below the dose at which 2 of 6 patients experience drug-related dose limiting toxicity (DLT)

    Graded by the National Cancer Institute (NCI) Common Terminology Criteria for Adverse Events (CTCAE) version 3.0.

    4 weeks

  • MTD of temsirolimus, defined as the dose level below the dose at which 2 of 6 patients experience DLT

    Graded by the NCI CTCAE version 3.0.

    4 weeks

Secondary Outcomes (2)

  • Anti-tumor efficacy of each combination (objective response)

    Up to 6 years

  • Levels of surrogate anti-angiogenesis markers

    Up to week 4 of course 1

Other Outcomes (1)

  • The properties of the tissue microvasculature.

    Up to week 4 of course 1

Study Arms (3)

Group I (temsirolimus, bevacizumab, cetuximab)

EXPERIMENTAL

Patients receive temsirolimus IV over 30-60 minutes on days 1, 8, 15, and 22; bevacizumab IV over 30-90 minutes on days 1 and 15; and cetuximab IV over 60-120 minutes on days 1, 8, 15, and 22. Courses repeat every 28 days in the absence of disease progression or unacceptable toxicity.

Biological: BevacizumabBiological: CetuximabOther: Laboratory Biomarker AnalysisOther: Pharmacological StudyDrug: Temsirolimus

Group II (temsirolimus, bevacizumab, valproic acid)

EXPERIMENTAL

Patients receive temsirolimus and bevacizumab as in Group I and valproic acid PO on days 1-7 and 15-21. Courses repeat every 28 days in the absence of disease progression or unacceptable toxicity.

Biological: BevacizumabOther: Laboratory Biomarker AnalysisOther: Pharmacological StudyDrug: TemsirolimusDrug: Valproic Acid

Group III (temsirolimus, bevacizumab)

EXPERIMENTAL

Patients receive temsirolimus and bevacizumab as in Group I. Courses repeat every 28 days in the absence of disease progression or unacceptable toxicity.

Biological: BevacizumabOther: Laboratory Biomarker AnalysisOther: Pharmacological StudyDrug: Temsirolimus

Interventions

BevacizumabBIOLOGICAL

Given IV

Also known as: Anti-VEGF, Anti-VEGF Humanized Monoclonal Antibody, Anti-VEGF rhuMAb, Avastin, Bevacizumab Biosimilar BEVZ92, Bevacizumab Biosimilar BI 695502, Bevacizumab Biosimilar CBT 124, Bevacizumab Biosimilar FKB238, Bevacizumab Biosimilar MIL60, Bevacizumab Biosimilar QL 1101, BEVACIZUMAB, LICENSE HOLDER UNSPECIFIED, Immunoglobulin G1 (Human-Mouse Monoclonal rhuMab-VEGF Gamma-Chain Anti-Human Vascular Endothelial Growth Factor), Disulfide With Human-Mouse Monoclonal rhuMab-VEGF Light Chain, Dimer, Recombinant Humanized Anti-VEGF Monoclonal Antibody, rhuMab-VEGF
Group I (temsirolimus, bevacizumab, cetuximab)Group II (temsirolimus, bevacizumab, valproic acid)Group III (temsirolimus, bevacizumab)
CetuximabBIOLOGICAL

Given IV

Also known as: Cetuximab Biosimilar CMAB009, Chimeric Anti-EGFR Monoclonal Antibody, Chimeric MoAb C225, Chimeric Monoclonal Antibody C225, Erbitux, IMC-C225
Group I (temsirolimus, bevacizumab, cetuximab)

Optional correlative studies

Group I (temsirolimus, bevacizumab, cetuximab)Group II (temsirolimus, bevacizumab, valproic acid)Group III (temsirolimus, bevacizumab)

Optional correlative studies

Group I (temsirolimus, bevacizumab, cetuximab)Group II (temsirolimus, bevacizumab, valproic acid)Group III (temsirolimus, bevacizumab)

Given IV

Also known as: CCI-779, CCI-779 Rapamycin Analog, Cell Cycle Inhibitor 779, Rapamycin Analog, Rapamycin Analog CCI-779, Torisel
Group I (temsirolimus, bevacizumab, cetuximab)Group II (temsirolimus, bevacizumab, valproic acid)Group III (temsirolimus, bevacizumab)

Given PO

Also known as: Depakene, Stavzor, Valproate
Group II (temsirolimus, bevacizumab, valproic acid)

Eligibility Criteria

Sexall
Healthy VolunteersNo
Age GroupsChild (0-17), Adult (18-64), Older Adult (65+)

You may qualify if:

  • Patients with advanced or metastatic cancer that is refractory to standard therapy, relapsed after standard therapy, or have no standard therapy that induces a complete response of at least 10% or improves survival by at least three months; in addition, patients with disease that are "benign" by pathology, but relentlessly progressive, leading to disability, pain, and premature death in the majority of cases (including, but not limited to lymphangioleiomyomatosis \[LAM\], type 2 neurofibromatosis \[NF\], Erdheim Chester disease, and Castleman's disease) may also be considered for enrollment
  • Patients should be at least four weeks from the last day of therapeutic radiation or cytotoxic chemotherapy or from antibody therapy, or at least five half-lives from non-cytotoxic targeted or biologic therapy; patients may have received palliative radiation immediately before (or during) treatment provided radiation is not to the only target lesion available
  • Eastern Cooperative Oncology Group (ECOG) performance status =\< 2
  • Karnofsky \>= 60%
  • Lansky performance status of \>= 60% for participants 16 years old or younger
  • Absolute neutrophil count \>= 1,000/mL
  • Platelets \>= 50,000/mL
  • Creatinine =\< 3 X upper limit of normal (ULN)
  • Total bilirubin =\< 3.0
  • Aspartate aminotransferase (AST) (serum glutamic oxaloacetic transaminase \[SGOT\])/alanine aminotransferase (ALT) (serum glutamate pyruvate transaminase \[SGPT\]) =\< 5 X ULN
  • Fasting level of total cholesterol of no more than 350 mg/dL
  • Triglyceride level of no more than 400 mg/dL
  • Women of child-bearing potential and men must agree to use adequate contraception (hormonal or barrier method of birth control; abstinence) prior to study entry, for the duration of study participation, and for 90 days after the last dose
  • Ability to understand and the willingness to sign a written informed consent document
  • Patients may not be receiving any other investigational agents and/or any other concurrent anticancer agents or therapies

You may not qualify if:

  • Patients with clinically significant unexplained bleeding within 28 days prior to entering the study
  • Uncontrolled systemic vascular hypertension (systolic blood pressure \> 140 mmHg, diastolic blood pressure \> 90 mmHg on medication)
  • Patients with clinically significant cardiovascular disease: History of CVA (cerebrovascular accident) within 6 months, myocardial infarction or unstable angina within 6 months, unstable angina pectoris
  • Pregnant or breast-feeding women
  • History of hypersensitivity to bevacizumab, murine products, or any component of the formulation
  • History of hypersensitivity to temsirolimus or its metabolites (including sirolimus), polysorbate 80, or to any component of the formulation
  • History of hypersensitivity to cetuximab, murine products, or any component of the formulation
  • Patients that are taking cytochrome P450 family 3, subfamily A, polypeptide 4 (CYP3A4) inducers and/or inhibitors; if a patient has a history of taking CYP3A4 inducers and/or inhibitors prior to enrollment on the protocol, it is strongly recommended that the patient stops the drug and waits at least 5 half-lives of said drug before initiating therapy on protocol
  • Colorectal cancer patients with known v-Ki-ras2 Kirsten rat sarcoma viral oncogene homolog (KRAS) mutation (for the arm combining bevacizumab, temsirolimus and cetuximab)
  • Patients who have had major surgery within 6 weeks of enrollment in the study

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (1)

M D Anderson Cancer Center

Houston, Texas, 77030, United States

Location

Related Publications (2)

  • Piha-Paul SA, Tseng C, Thompson E, Stafford RJ, Le H, Kang L, Fu S, Tsimberidou A, Blumenschein G, Ahnert JR, Slopis JM, Hong D, Naing A, Meric-Bernstam F, Ng CS, Westin S, Sood AK. Phase I study of bevacizumab and temsirolimus combination therapy in advanced malignancies: safety, efficacy, and ovarian cancer expansion. Oncologist. 2026 Feb 5;31(3):oyaf413. doi: 10.1093/oncolo/oyaf413.

  • Nelson BE, Tsimberidou AM, Fu X, Fu S, Subbiah V, Sood AK, Rodon J, Karp DD, Blumenschein G, Kopetz S, Pant S, Piha-Paul SA. A Phase I Trial of Bevacizumab and Temsirolimus in Combination With Valproic Acid in Advanced Solid Tumors. Oncologist. 2023 Dec 11;28(12):1100-e1292. doi: 10.1093/oncolo/oyad158.

Related Links

MeSH Terms

Conditions

Castleman DiseaseErdheim-Chester DiseaseMouth NeoplasmsLymphangioleiomyomatosisEndocrine Gland NeoplasmsNeoplasmsUrologic NeoplasmsNeoplasms, MesothelialNeoplasm MetastasisCarcinoma, Transitional CellNeurofibromatosis 2SarcomaBreast NeoplasmsRecurrencePharyngeal NeoplasmsThyroid NeoplasmsSoft Tissue Neoplasms

Interventions

BevacizumabImmunoglobulin GDisulfidesCetuximabtemsirolimusSirolimusValproic Acid

Condition Hierarchy (Ancestors)

Lymphoproliferative DisordersLymphatic DiseasesHemic and Lymphatic DiseasesImmunoproliferative DisordersImmune System DiseasesHistiocytosis, Non-Langerhans-CellHistiocytosisHead and Neck NeoplasmsNeoplasms by SiteMouth DiseasesStomatognathic DiseasesLymphangiomyomaNeoplasm, Lymphatic TissueNeoplasms by Histologic TypePerivascular Epithelioid Cell NeoplasmsNeoplasms, Connective and Soft TissueEndocrine System DiseasesUrogenital NeoplasmsFemale Urogenital DiseasesFemale Urogenital Diseases and Pregnancy ComplicationsUrogenital DiseasesMale Urogenital DiseasesUrologic DiseasesNeoplasms, Glandular and EpithelialNeoplastic ProcessesPathologic ProcessesPathological Conditions, Signs and SymptomsCarcinomaNeuroma, AcousticNeurilemmomaNeuroendocrine TumorsNeuroectodermal TumorsNeoplasms, Germ Cell and EmbryonalNeurofibromatosesNeurofibromaNerve Sheath NeoplasmsNeoplasms, Nerve TissueNeuromaNeoplastic Syndromes, HereditaryVestibulocochlear Nerve DiseasesRetrocochlear DiseasesEar DiseasesOtorhinolaryngologic DiseasesOtorhinolaryngologic NeoplasmsCranial Nerve NeoplasmsCranial Nerve DiseasesNervous System DiseasesNeurocutaneous SyndromesHeredodegenerative Disorders, Nervous SystemNeurodegenerative DiseasesGenetic Diseases, InbornCongenital, Hereditary, and Neonatal Diseases and AbnormalitiesBreast DiseasesSkin DiseasesSkin and Connective Tissue DiseasesDisease AttributesPharyngeal DiseasesThyroid Diseases

Intervention Hierarchy (Ancestors)

Antibodies, Monoclonal, HumanizedAntibodies, MonoclonalAntibodiesImmunoglobulinsImmunoproteinsBlood ProteinsProteinsAmino Acids, Peptides, and ProteinsSerum GlobulinsGlobulinsImmunoglobulin IsotypesSulfidesAnionsIonsElectrolytesInorganic ChemicalsHydrogen SulfideSulfur CompoundsOrganic ChemicalsMacrolidesLactonesPentanoic AcidsValeratesAcids, AcyclicCarboxylic AcidsFatty Acids, VolatileFatty AcidsLipids

Study Officials

  • Sarina A Piha-Paul

    M.D. Anderson Cancer Center

    PRINCIPAL INVESTIGATOR

Study Design

Study Type
interventional
Phase
phase 1
Allocation
NON RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
OTHER
Responsible Party
SPONSOR

Study Record Dates

First Submitted

March 7, 2012

First Posted

March 13, 2012

Study Start

October 16, 2012

Primary Completion (Estimated)

October 31, 2026

Study Completion (Estimated)

October 31, 2026

Last Updated

April 24, 2026

Record last verified: 2025-10

Locations