NCT03085914

Brief Summary

This was an open-label, nonrandomized, Phase 1/2 study designed to determine the safety, tolerability, and efficacy of epacadostat when given in combination with pembrolizumab and 7 different chemotherapy regimens described as Treatment Groups A through G below (see Study Drug and Background Therapies, Dose, and Mode of Administration). Phase 1 consisted of a 3 + 3 + 3 design intended to determine the MTD or PAD of epacadostat when given in combination with pembrolizumab and chemotherapy; efficacy was also explored. Phase 2 was designed to enroll efficacy expansion cohorts to further evaluate the safety, tolerability, and efficacy of epacadostat at the MTD or PAD (as selected in Phase 1) when given in combination with pembrolizumab and chemotherapy. Each efficacy expansion cohort was to enroll participants with 1 specific type of advanced or metastatic solid tumor. Additional cohorts (ie, the mandatory biopsy cohorts) were designed to evaluate changes in the tumor microenvironment in participants with any advanced or metastatic solid tumor who had progressed on previous therapy with a PD-1 or a PD-L1 inhibitor. No participants were enrolled in any Phase 2 efficacy expansion cohort, or in any Phase 2 mandatory biopsy cohort receiving Treatment A, B, F, or G. Phase 2 mandatory biopsy cohort participants received Treatments C, D, or E (ie, were included in Treatment Groups C, D, or E). Participants were assigned to a treatment group based on the chemotherapy regimen most appropriate for their tumor type.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
70

participants targeted

Target at P75+ for phase_1

Timeline
Completed

Started May 2017

Typical duration for phase_1

Geographic Reach
1 country

16 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

February 28, 2017

Completed
21 days until next milestone

First Posted

Study publicly available on registry

March 21, 2017

Completed
1 month until next milestone

Study Start

First participant enrolled

May 2, 2017

Completed
1.7 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

January 25, 2019

Completed
1.3 years until next milestone

Results Posted

Study results publicly available

May 7, 2020

Completed
2 months until next milestone

Study Completion

Last participant's last visit for all outcomes

July 13, 2020

Completed
Last Updated

September 23, 2022

Status Verified

September 1, 2022

Enrollment Period

1.7 years

First QC Date

February 28, 2017

Results QC Date

January 21, 2020

Last Update Submit

September 12, 2022

Conditions

Keywords

solid tumorscolorectal cancerpancreatic ductal adenocarcinomanon-small cell lung cancerPD-1PD-L1epacadostatIDO inhibitor

Outcome Measures

Primary Outcomes (3)

  • Phases 1 & 2: Number of Participants With Treatment-emergent Adverse Events (TEAEs) and Serious TEAEs

    A TEAE is any AE either reported for the first time or worsening of a pre-existing event after first dose of epacadostat, pembrolizumab, or chemotherapy. Serious adverse event is defined as an event that meets 1 of the following criteria: is fatal or life threatening, requires inpatient hospitalization or prolongation of existing hospitalization, results in persistent or significant disability, incapacity, or a substantial disruption of a person's ability to conduct normal life functions, constitutes a congenital anomaly or birth defect,is a medically important event that may jeopardize the participant or may require medical or surgical intervention to prevent 1 of the outcomes listed above.

    Up to 21 months

  • Phases 1 and 2: Number of Participants With Dose Limiting Toxicities (DLTs)

    A DLT was defined as the occurrence of any of the protocol-specified toxicities occurring up to and including Day 28 for the cohorts where mFOLFOX6 and nab-paclitaxel/gemcitabine are administered and Day 21 for all other chemotherapy regimens in Phase 1, except those with a clear alternative explanation (eg, disease progression) or transient (≤ 72 hours) abnormal laboratory values without associated clinically significant signs or symptoms based on investigator determination.

    28 days

  • Phases 1 and 2: Objective Response Rate (ORR)

    ORR was defined as the percentage of participants having a complete response (CR) or partial response (PR) as determined by investigator assessment of radiographic disease per Response Evaluation Criteria in Solid Tumors (RECIST) v1.1.

    Up to Week 18

Study Arms (7)

Treatment Group A

EXPERIMENTAL

Epacadostat + pembrolizumab + mFOLFOX6 (oxaliplatin, leucovorin, 5-fluorouracil)

Drug: EpacadostatDrug: PembrolizumabDrug: OxaliplatinDrug: LeucovorinDrug: 5-Fluorouracil

Treatment Group B

EXPERIMENTAL

Epacadostat + pembrolizumab + gemcitabine and nab-paclitaxel

Drug: EpacadostatDrug: PembrolizumabDrug: GemcitabineDrug: nab-Paclitaxel

Treatment Group C

EXPERIMENTAL

Epacadostat + pembrolizumab + carboplatin and paclitaxel

Drug: EpacadostatDrug: PembrolizumabDrug: CarboplatinDrug: Paclitaxel

Treatment Group D

EXPERIMENTAL

Epacadostat + pembrolizumab + pemetrexed and investigators choice of platinum agent

Drug: EpacadostatDrug: PembrolizumabDrug: PemetrexedDrug: CarboplatinDrug: CisplatinDrug: Investigator's choice of platinum agent

Treatment Group E

EXPERIMENTAL

Epacadostat + pembrolizumab + cyclophosphamide

Drug: EpacadostatDrug: PembrolizumabDrug: Cyclophosphamide

Treatment Group F

EXPERIMENTAL

Epacadostat + pembrolizumab + gemcitabine and investigators choice of platinum agent

Drug: EpacadostatDrug: PembrolizumabDrug: Gemcitabine

Treatment Group G

EXPERIMENTAL

Epacadostat + pembrolizumab + investigators choice of platinum agent and 5-fluorouracil

Drug: EpacadostatDrug: PembrolizumabDrug: CarboplatinDrug: CisplatinDrug: 5-FluorouracilDrug: Investigator's choice of platinum agent

Interventions

Epacadostat oral twice-daily continuous daily dosing at the protocol-defined dose.

Also known as: INCB024360
Treatment Group ATreatment Group BTreatment Group CTreatment Group DTreatment Group ETreatment Group FTreatment Group G

Pembrolizumab

Treatment Group ATreatment Group BTreatment Group CTreatment Group DTreatment Group ETreatment Group FTreatment Group G

Oxaliplatin

Treatment Group A

Leucovorin

Treatment Group A

5-Fluorouracil

Treatment Group A

Gemcitabine

Treatment Group BTreatment Group F

nab-Paclitaxel

Treatment Group B

Carboplatin

Treatment Group C

Paclitaxel

Treatment Group C

Pemetrexed

Treatment Group D

Cyclophosphamide

Treatment Group E

Cisplatin

Treatment Group DTreatment Group G

Investigator's choice of platinum agent: carboplatin or cisplatin

Treatment Group DTreatment Group G

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Histologically or cytologically confirmed diagnosis of selected advanced or metastatic solid tumors.
  • Presence of measurable disease per RECIST v1.1.
  • Eastern Cooperative Oncology Group (ECOG) performance status of 0 or 1.

You may not qualify if:

  • Laboratory and medical history parameters not within the Protocol-defined range.
  • Receipt of anticancer medications or investigational drugs within the Protocol-defined intervals before the first administration of study drug.
  • Previous radiotherapy within 2 weeks of starting study therapy.
  • Known active central nervous system (CNS) metastases and/or carcinomatous meningitis.
  • Has not recovered to ≤ Grade 1 from toxic effects of previous therapy and/or complications from previous surgical intervention before starting study therapy.
  • Receipt of a live vaccine within 30 days of planned start of study therapy.
  • Active infection requiring systemic therapy.
  • Subjects who have any active or inactive autoimmune disease or syndrome.
  • Women who are pregnant or breastfeeding.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (16)

Mayo Clinic Arizona

Phoenix, Arizona, 85054, United States

Location

University of California San Diego Medical Center, Moores Cancer Center

La Jolla, California, 92093, United States

Location

The Angeles Clinic and Research Institute

Los Angeles, California, 90025, United States

Location

Mayo Clinic

Jacksonville, Florida, 32224, United States

Location

University of Chicago

Chicago, Illinois, 60637, United States

Location

Mayo Clinic

Rochester, Minnesota, 55905, United States

Location

Washington University School of Medicine

St Louis, Missouri, 63110, United States

Location

Memorial Sloan Kettering Cancer Center

New York, New York, 10065, United States

Location

Carolina Bio-Oncology Institute, PLLC

Huntersville, North Carolina, 28078, United States

Location

Oregon Health and Science University

Portland, Oregon, 97239, United States

Location

University of Pennsylvania Health System

Philadelphia, Pennsylvania, 19104, United States

Location

University of Pittsburgh Cancer Institute

Pittsburgh, Pennsylvania, 15237, United States

Location

Tennessee Oncology - Nashville; The Sarah Cannon Research Institute

Nashville, Tennessee, 37203, United States

Location

Vanderbilt University; Henry Joyce Cancer Clinic

Nashville, Tennessee, 37232, United States

Location

MD Anderson Cancer Center

Houston, Texas, 77030, United States

Location

Huntsman Cancer Institute at University of Utah

Salt Lake City, Utah, 84112, United States

Location

Related Publications (1)

  • Powderly JD, Klempner SJ, Naing A, Bendell J, Garrido-Laguna I, Catenacci DVT, Taylor MH, Lee JJ, Zheng F, Zhou F, Gong X, Gowda H, Beatty GL. Epacadostat Plus Pembrolizumab and Chemotherapy for Advanced Solid Tumors: Results from the Phase I/II ECHO-207/KEYNOTE-723 Study. Oncologist. 2022 Nov 3;27(11):905-e848. doi: 10.1093/oncolo/oyac174.

MeSH Terms

Conditions

Colorectal NeoplasmsCarcinoma, Non-Small-Cell Lung

Interventions

epacadostatpembrolizumabOxaliplatinLeucovorinFluorouracilGemcitabine130-nm albumin-bound paclitaxelCarboplatinPaclitaxelPemetrexedCyclophosphamideCisplatin

Condition Hierarchy (Ancestors)

Intestinal NeoplasmsGastrointestinal NeoplasmsDigestive System NeoplasmsNeoplasms by SiteNeoplasmsDigestive System DiseasesGastrointestinal DiseasesColonic DiseasesIntestinal DiseasesRectal DiseasesCarcinoma, BronchogenicBronchial NeoplasmsLung NeoplasmsRespiratory Tract NeoplasmsThoracic NeoplasmsLung DiseasesRespiratory Tract Diseases

Intervention Hierarchy (Ancestors)

Coordination ComplexesOrganic ChemicalsFormyltetrahydrofolatesTetrahydrofolatesFolic AcidPterinsPteridinesHeterocyclic Compounds, 2-RingHeterocyclic Compounds, Fused-RingHeterocyclic CompoundsCoenzymesEnzymes and CoenzymesUracilPyrimidinonesPyrimidinesHeterocyclic Compounds, 1-RingDeoxycytidineCytidinePyrimidine NucleosidesTaxoidsCyclodecanesCycloparaffinsHydrocarbons, AlicyclicHydrocarbons, CyclicHydrocarbonsDiterpenesTerpenesGuanineHypoxanthinesPurinonesPurinesGlutamatesAmino Acids, AcidicAmino AcidsAmino Acids, Peptides, and ProteinsAmino Acids, DicarboxylicPhosphoramide MustardsNitrogen Mustard CompoundsMustard CompoundsHydrocarbons, HalogenatedPhosphoramidesOrganophosphorus CompoundsChlorine CompoundsInorganic ChemicalsNitrogen CompoundsPlatinum Compounds

Limitations and Caveats

Enrollment in this study was permanently discontinued on 25 Oct 2018 due to a strategic decision and not based on safety concerns.

Results Point of Contact

Title
Study Director
Organization
Incyte Corporation

Study Officials

  • Fred Zheng, MD

    Incyte Corporation

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 1
Allocation
NON RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

February 28, 2017

First Posted

March 21, 2017

Study Start

May 2, 2017

Primary Completion

January 25, 2019

Study Completion

July 13, 2020

Last Updated

September 23, 2022

Results First Posted

May 7, 2020

Record last verified: 2022-09

Data Sharing

IPD Sharing
Will share

Incyte shares data with qualified external researchers after a research proposal is submitted. These requests are reviewed and approved by a review panel on the basis of scientific merit. All data provided is anonymized to respect the privacy of patients who have participated in the trial in line with applicable laws and regulations. The trial data availability is according to the criteria and process described on https://www.incyte.com/our-company/compliance-and-transparency

Shared Documents
STUDY PROTOCOL, SAP
Time Frame
Data will be shared after the primary publication or 2 years after the study has ended for market authorized products and indications.
Access Criteria
Data from eligible studies will be shared with qualified researchers according to the criteria and process described in the Data Sharing section of the www.incyteclinicaltrials.com website. For approved requests, the researchers will be granted access to anonymized data under the terms of a data sharing agreement
More information

Locations