NCT04083599

Brief Summary

The goal of this trial is to learn about the antibody GEN1042 when it is used alone and when it is used together with another antibody cancer drug, pembrolizumab (with or without chemotherapy), for treatment of participants with certain types of cancer.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
350

participants targeted

Target at P75+ for phase_1

Timeline
6mo left

Started Sep 2019

Longer than P75 for phase_1

Geographic Reach
12 countries

76 active sites

Status
active not recruiting

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Progress93%
Sep 2019Nov 2026

First Submitted

Initial submission to the registry

September 6, 2019

Completed
4 days until next milestone

First Posted

Study publicly available on registry

September 10, 2019

Completed
7 days until next milestone

Study Start

First participant enrolled

September 17, 2019

Completed
6.3 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

December 30, 2025

Completed
10 months until next milestone

Study Completion

Last participant's last visit for all outcomes

November 1, 2026

Expected
Last Updated

May 6, 2026

Status Verified

May 1, 2026

Enrollment Period

6.3 years

First QC Date

September 6, 2019

Last Update Submit

May 5, 2026

Conditions

Outcome Measures

Primary Outcomes (2)

  • Dose Escalation and Safety Run-in Parts: Number of Participants With Dose-Limiting Toxicities (DLTs)

    Toxicities will be graded for severity according to the National Cancer Institute Common Terminology Criteria for Adverse Events (NCI-CTCAE) criteria version 5.0

    First Cycle (21 days)

  • Dose Expansion: Objective Response Rate (ORR)

    ORR is defined as the percentage of participants with best overall response (BOR) \[complete or partial response (PR or CR)\] based on Response Evaluation Criteria in Solid Tumors (RECIST) version 1.1 as assessed by the investigator.

    Up to approximately 2 years and 4 months

Secondary Outcomes (10)

  • All Parts: Number of Participants with Adverse Events (AEs) and Serious Adverse Events (SAEs)

    From first dose until the end of the study (approximately 2 years and 4 months)

  • Dose Escalation: ORR

    Up to approximately 2 years and 4 months

  • All Parts: Duration of Objective Response (DOR)

    Up to approximately 2 years and 4 months

  • All Parts: Disease Control Rate (DCR)

    Up to approximately 2 years and 4 months

  • All Parts: Progression-Free Survival (PFS)

    Up to approximately 2 years and 4 months

  • +5 more secondary outcomes

Study Arms (2)

Monotherapy - Dose Escalation and Dose Expansion Parts

EXPERIMENTAL
Biological: GEN1042

Combination Therapy - Safety Run-in and Expansion Parts

EXPERIMENTAL
Biological: GEN1042Drug: PembrolizumabDrug: CisplatinDrug: CarboplatinDrug: 5-FUDrug: GemcitabineDrug: Nab paclitaxelDrug: PemetrexedDrug: Paclitaxel

Interventions

Intravenous

Combination Therapy - Safety Run-in and Expansion Parts

Intravenous

Combination Therapy - Safety Run-in and Expansion Parts

Intravenous

Combination Therapy - Safety Run-in and Expansion Parts
GEN1042BIOLOGICAL

Intravenous

Combination Therapy - Safety Run-in and Expansion PartsMonotherapy - Dose Escalation and Dose Expansion Parts
5-FUDRUG

Intravenous

Combination Therapy - Safety Run-in and Expansion Parts

Intravenous

Combination Therapy - Safety Run-in and Expansion Parts

Intravenous

Combination Therapy - Safety Run-in and Expansion Parts

Intravenous

Combination Therapy - Safety Run-in and Expansion Parts

Intravenous

Combination Therapy - Safety Run-in and Expansion Parts

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Monotherapy - Dose Escalation and Dose Expansion Parts
  • Participants with non-CNS solid tumors that is metastatic or unresectable and for whom there is no available standard therapy.
  • Participants with a confirmed diagnosis of relapsed or refractory, advanced and/or metastatic melanoma, NSCLC, or CRC and for whom there is no available standard therapy
  • Combination Therapy - Dose Expansion Part
  • Participants with unresectable Stage III or Stage IV melanoma with no prior systemic anticancer therapy for unresectable or metastatic disease. Primary ocular or mucosal melanoma is excluded.
  • Participants with Stage IV metastatic or recurrent NSCLC with no prior systemic anticancer therapy, no actionable mutation.
  • Participants with recurrent or metastatic HNSCC with no prior systemic therapy administered in the recurrent or metastatic setting.
  • Participants with confirmed metastatic PDAC with no previous radiotherapy, surgery, chemotherapy, or investigational therapy for the treatment of metastatic disease.
  • General (all phases):
  • Must be age ≥ 18 years of age on the day of signing informed consent, or the legal age of consent in the jurisdiction in which the trial is taking place.
  • Measurable disease according to RECIST 1.1
  • Eastern Cooperative Oncology Group (ECOG) 0-1
  • Normal or adequate liver, renal, cardiac and bone marrow function

You may not qualify if:

  • Monotherapy - Dose Escalation and Dose Expansion Parts
  • Treatment with an anti-cancer agent (within 21 days or after at least 5 half-lives of the drug, whichever is shorter), prior to GEN1042 administration
  • Radiotherapy within 14 days prior to first GEN1042 administration
  • Toxicities from previous anti-cancer therapies that have not resolved
  • Combination Therapy - Dose Expansion Part
  • Has received prior systemic cytotoxic chemotherapy, biological therapy, OR major surgery within 3 weeks or at least 5 half-lives of the drug (whichever is shorter) of the first dose of trial treatment.
  • Radiotherapy within 14 days of start of trial treatment or received lung radiation therapy of \> 30 Gy within 6 months of the first dose of trial treatment.
  • General (all phases)
  • Participants has an active, known, or suspected autoimmune disease.
  • History of non-infectious pneumonitis that required steroids or currently has pneumonitis.
  • History of ≥ grade 3 allergic reactions to monoclonal antibody (mAb) therapy
  • Participants with a condition requiring systemic treatment with either corticosteroids (\>10 mg daily prednisone equivalent) or other immunosuppressive medications within 14 days of first treatment.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (76)

Alaska Oncology and Hematology LLC

Anchorage, Alaska, 99508, United States

Location

Cancer & Blood Specialty Clinic

Los Alamitos, California, 90720, United States

Location

Moores Cancer Center at the UC San Diego Health

San Diego, California, 92037, United States

Location

Yale University Cancer Center

New Haven, Connecticut, 06520, United States

Location

ChristianaCare

Newark, Delaware, 19713, United States

Location

Mount Sinai Comprehensive Cancer Center

Miami Beach, Florida, 33140, United States

Location

Florida Cancer Affiliates

Ocala, Florida, 34474, United States

Location

Hope and Healing Cancer Services

Hinsdale, Illinois, 60521, United States

Location

University of Kentucky

Lexington, Kentucky, 40536, United States

Location

Norton Cancer Institute

Louisville, Kentucky, 40202, United States

Location

Maryland Oncology Hematology PA

Columbia, Maryland, 21044, United States

Location

Washington University School of Medicine

St Louis, Missouri, 63110, United States

Location

Levine Cancer Center

Charlotte, North Carolina, 28204, United States

Location

Novant Health Cancer Institute - Forsyth (Medical Oncology)

Winston-Salem, North Carolina, 27103, United States

Location

Kaiser Permanente (KP) Oncology/Hematology

Portland, Oregon, 97227, United States

Location

University of Pennsylvania

Philadelphia, Pennsylvania, 19104, United States

Location

Fox Chase Cancer Center

Philadelphia, Pennsylvania, 19111, United States

Location

Sarah Cannon Research Institute

Nashville, Tennessee, 37203, United States

Location

Lumi Research

Kingwood, Texas, 77339, United States

Location

Utah Cancer Specialists

Salt Lake City, Utah, 84124, United States

Location

Virgina Cancer Specialists

Fairfax, Virginia, 22031, United States

Location

Adventist Health System/Sunbelt,Inc

Seattle, Washington, 98109, United States

Location

Medical Oncology Associates, PS

Spokane, Washington, 99204, United States

Location

Rigshospitalet (Copenhagen University Hospital)

Copenhagen, Denmark

Location

Herlev University Hospital

Herlev, Denmark

Location

University Hospital of Southern Denmark, Vejle Hospital

Vejle, Denmark

Location

Centre hospitalier Universitaire de Bordeaux

Bordeaux, France

Location

Centre Antoine Lacassagne

Nice, France

Location

Gustave Roussy

Villejuif, France

Location

ARENSIA Research Clinic at the Research Institute of Clinical Medicine

Tbilisi, Georgia

Location

Nationales Centrum fr Tumorerkrankungen NCT

Heidelberg, Germany

Location

Klinikum der Stadt Ludwigshafen am Rhein gGmbH

Ludwigshafen, Germany

Location

Department of Dermatology, University of Mainz

Mainz, Germany

Location

Universitätsmedizin Mannheim Dermatologie

Mannheim, Germany

Location

Universitaetsklinikum Wuerzburg

Würzburg, Germany

Location

Rabin Medical Center

Petah Tikva, Israel

Location

Tel Aviv Sourasky Medical Center

Tel Aviv, Israel

Location

Azienda Ospedaliera Spedali Civili di Brescia

Brescia, Italy

Location

Azienda Ospedaliera S.Croce e Carle Cuneo

Cuneo, Italy

Location

Istituto Nazionale dei Tumori

Milan, Italy

Location

Istituto Clinico Humanitas

Rozzano, Italy

Location

ARENSIA Research Clinic at the Oncology Institute

Chisinau, Moldova

Location

Chungbuk National University Hospital

Cheongju-si, South Korea

Location

Jeonbuk National University Hospital

Jeonju, South Korea

Location

Gachon University Gil Medical Center

Namdong, South Korea

Location

Korea University Guro Hospital

Seoul, South Korea

Location

Samsung Medical Center

Seoul, South Korea

Location

Severance Hospital, Yonsei University Health System

Seoul, South Korea

Location

Pusan National University Yangsan Hospital

Yangsan, South Korea

Location

H. Vall d'Hebron

Barcelona, Spain

Location

START Barcelona HM Nou Delfos

Barcelona, Spain

Location

Hospital Duran i Reynals - ICO L Hospitalet

L'Hospitalet de Llobregat, Spain

Location

Hospital Universitario Insular de Gran Canaria

Las Palmas de Gran Canaria, 35016, Spain

Location

Hospital Universitario Lucus Augusti

Lugo, Spain

Location

Clinica Universidad de Navarra

Madrid, Spain

Location

HM CIOCC Hospital Universitario HM Sanchinarro

Madrid, Spain

Location

Hospital Clinico San Carlos

Madrid, Spain

Location

Hospital General Universitario Gregorio Maran

Madrid, Spain

Location

Hospital Universitario 12 de Octubre

Madrid, Spain

Location

Hospital Universitario La Paz

Madrid, Spain

Location

Hospital Universitario Ramon y Cajal

Madrid, Spain

Location

MD Anderson Cancer Center Madrid

Madrid, Spain

Location

START Madrid - Hospital Universitario Fundacion Jimenez Diaz

Madrid, Spain

Location

Hospital Universitario Virgen de la Victoria

Málaga, Spain

Location

Clinica Universidad de Navarra

Pamplona, Spain

Location

Complejo Hospitalario Universitario de Santiago (CHUS)

Santiago de Compostela, Spain

Location

Hospital Virgen del Rocio

Seville, Spain

Location

Hospital Clinico Universitario de Valencia

Valencia, Spain

Location

Chang Gung Memorial Hospital (CGMH) - Kaohsiung Branch

Kaohsiung City, Taiwan

Location

Kaohsiung Medical University Memorial Hospital

Kaohsiung City, Taiwan

Location

China Medical University Hospital

Taichung, Taiwan

Location

National Cheng Kung University Hospital

Tainan, Taiwan

Location

Taipei Medical University Hospital

Taipei, Taiwan

Location

Taipei Veterans General Hospital, VGHTPE

Taipei, Taiwan

Location

Chang Gung Memorial Hospital Linkou Branch

Taoyuan, Taiwan

Location

Royal Marsden NHS Foundation Trust

Sutton, United Kingdom

Location

Related Publications (1)

  • Muik A, Adams 3rd HC, Gieseke F, Altintas I, Schoedel KB, Blum JM, Sanger B, Burm SM, Stanganello E, Verzijl D, Spires VM, Vascotto F, Toker A, Quinkhardt J, Fereshteh M, Diken M, Satijn DPE, Kreiter S, Ahmadi T, Breij ECW, Tureci O, Sasser K, Sahin U, Jure-Kunkel M. DuoBody-CD40x4-1BB induces dendritic-cell maturation and enhances T-cell activation through conditional CD40 and 4-1BB agonist activity. J Immunother Cancer. 2022 Jun;10(6):e004322. doi: 10.1136/jitc-2021-004322.

MeSH Terms

Conditions

Carcinoma, Non-Small-Cell LungColorectal NeoplasmsMelanomaSquamous Cell Carcinoma of Head and Neck

Interventions

pembrolizumabCisplatinCarboplatinFluorouracilGemcitabineTaxesPemetrexedPaclitaxel

Condition Hierarchy (Ancestors)

Carcinoma, BronchogenicBronchial NeoplasmsLung NeoplasmsRespiratory Tract NeoplasmsThoracic NeoplasmsNeoplasms by SiteNeoplasmsLung DiseasesRespiratory Tract DiseasesIntestinal NeoplasmsGastrointestinal NeoplasmsDigestive System NeoplasmsDigestive System DiseasesGastrointestinal DiseasesColonic DiseasesIntestinal DiseasesRectal DiseasesNeuroendocrine TumorsNeuroectodermal TumorsNeoplasms, Germ Cell and EmbryonalNeoplasms by Histologic TypeNeoplasms, Nerve TissueNevi and MelanomasSkin NeoplasmsSkin DiseasesSkin and Connective Tissue DiseasesCarcinoma, Squamous CellCarcinomaNeoplasms, Glandular and EpithelialHead and Neck Neoplasms

Intervention Hierarchy (Ancestors)

Chlorine CompoundsInorganic ChemicalsNitrogen CompoundsPlatinum CompoundsCoordination ComplexesOrganic ChemicalsUracilPyrimidinonesPyrimidinesHeterocyclic Compounds, 1-RingHeterocyclic CompoundsDeoxycytidineCytidinePyrimidine NucleosidesEconomicsHealth Care Economics and OrganizationsGuanineHypoxanthinesPurinonesPurinesHeterocyclic Compounds, 2-RingHeterocyclic Compounds, Fused-RingGlutamatesAmino Acids, AcidicAmino AcidsAmino Acids, Peptides, and ProteinsAmino Acids, DicarboxylicTaxoidsCyclodecanesCycloparaffinsHydrocarbons, AlicyclicHydrocarbons, CyclicHydrocarbonsDiterpenesTerpenes

Study Officials

  • Study Official

    Genmab

    STUDY DIRECTOR

Study Design

Study Type
interventional
Phase
phase 1
Allocation
NON RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
SEQUENTIAL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

September 6, 2019

First Posted

September 10, 2019

Study Start

September 17, 2019

Primary Completion

December 30, 2025

Study Completion (Estimated)

November 1, 2026

Last Updated

May 6, 2026

Record last verified: 2026-05

Data Sharing

IPD Sharing
Will not share

Locations