NCT03631199

Brief Summary

This was a Phase III study of pembrolizumab plus platinum-based doublet chemotherapy with or without canakinumab in previously untreated locally advanced or metastatic non-squamous and squamous NSCLC participants.

Trial Health

68
Monitor

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Strong global presence with extensive site network
Enrollment
673

participants targeted

Target at P75+ for phase_3 nonsmall-cell-lung-cancer

Timeline
Completed

Started Dec 2018

Longer than P75 for phase_3 nonsmall-cell-lung-cancer

Geographic Reach
40 countries

150 active sites

Status
terminated

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

August 6, 2018

Completed
9 days until next milestone

First Posted

Study publicly available on registry

August 15, 2018

Completed
4 months until next milestone

Study Start

First participant enrolled

December 21, 2018

Completed
2.6 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

August 9, 2021

Completed
3.2 years until next milestone

Results Posted

Study results publicly available

October 8, 2024

Completed
1.3 years until next milestone

Study Completion

Last participant's last visit for all outcomes

January 26, 2026

Completed
Last Updated

February 25, 2026

Status Verified

February 1, 2026

Enrollment Period

2.6 years

First QC Date

August 6, 2018

Results QC Date

July 5, 2024

Last Update Submit

February 5, 2026

Conditions

Keywords

ACZ885canakinumabpembrolizumabcarboplatincisplatinpaclitaxelnab-paclitaxelpemetrexedNSCLCnon-small cell lung cancernon small cell lung cancersquamousnon-squamoushsCRPIL-1βPD-L1CANOPYCANOPY-1platinum-based doublet chemotherapyfirst line therapylocally advancedmetastatic

Outcome Measures

Primary Outcomes (3)

  • Part 1 (Safety Run-in): Number of Participants With Dose-limiting Toxicities (DLTs)

    A DLT was defined as an adverse event or abnormal laboratory value assessed as unrelated to disease progression, inter-current illness, or concomitant medications that met certain criteria as defined in the protocol.

    During the first 42 days of dosing

  • Part 2 (Double-blind, Randomized, Placebo-controlled): Progression-free Survival (PFS) Per Investigator Assessment Using RECIST v1.1

    Progression free survival was defined as the time from randomization to the date of the first documented radiological progression using RECIST 1.1 (Response evaluation criteria in solid tumor) or death due to any cause.

    18 months

  • Part 2 (Double-blind, Randomized, Placebo-controlled): Overall Survival (OS) Per Investigator Assessment Using RECIST v1.1

    Overall survival is defined as the time from date of randomization to date of death due to any cause.

    Up to approximately 32 months

Secondary Outcomes (28)

  • Part 1 (Safety Run-in): Overall Response Rate (ORR) Per Investigator Assessment Using RECIST v1.1

    Up to approximately 14 months

  • Part 2 (Double-blind, Randomized, Placebo-controlled): Overall Response Rate (ORR) Per Investigator Assessment Using RECIST v1.1

    Up to approximately 26 months

  • Part 1 (Safety run-in): Disease Control Rate (DCR) Per Investigator Assessment Using RECIST v1.1

    Up to approximately 14 months

  • Part 2 (Double-blind, Randomized, Placebo-controlled): Disease Control Rate (DCR) Per Investigator Assessment Using RECIST v1.1

    Up to approximately 26 months

  • Part 1 (Safety run-in): Duration of Response (DOR) Per Investigator Assessment Using RECIST v1.1

    Up to approximately 25 months

  • +23 more secondary outcomes

Study Arms (5)

Part 1: Cohort A

EXPERIMENTAL

Safety run-in, canakinumab in combination with pembrolizumab, carboplatin, and pemetrexed.

Drug: canakinumabDrug: pembrolizumabDrug: carboplatinDrug: pemetrexed

Part 1: Cohort B

EXPERIMENTAL

Safety run-in, canakinumab in combination with pembrolizumab, cisplatin, and pemetrexed.

Drug: canakinumabDrug: pembrolizumabDrug: cisplatinDrug: pemetrexed

Part 1: Cohort C

EXPERIMENTAL

Safety run-in, canakinumab in combination with pembrolizumab, carboplatin, and paclitaxel.

Drug: canakinumabDrug: pembrolizumabDrug: carboplatinDrug: paclitaxel

Part 2: Canakinumab+pembro+CTx

EXPERIMENTAL

Double-blind, randomized, placebo-controlled, canakinumab in combination with pembrolizumab and platinum-based doublet chemotherapy.

Drug: canakinumabDrug: pembrolizumabDrug: carboplatinDrug: cisplatinDrug: paclitaxelDrug: nab-paclitaxelDrug: pemetrexed

Part 2: Placebo+pembro+CTx

OTHER

Double-blind, randomized, placebo-controlled, canakinumab-matching placebo in combination with pembrolizumab and platinum-based doublet chemotherapy.

Drug: canakinumab-matching placeboDrug: pembrolizumabDrug: carboplatinDrug: cisplatinDrug: paclitaxelDrug: nab-paclitaxelDrug: pemetrexed

Interventions

canakinumab placebo every 3 weeks (squamous and non-squamous)

Part 2: Placebo+pembro+CTx

Area Under the Curve (AUC) 5 mg/mL\*min every 3 weeks (non-squamous) or AUC 6 mg/mL\*min (squamous)

Part 1: Cohort APart 1: Cohort CPart 2: Canakinumab+pembro+CTxPart 2: Placebo+pembro+CTx

75 mg/m\^2 every 3 weeks (non-squamous)

Part 1: Cohort BPart 2: Canakinumab+pembro+CTxPart 2: Placebo+pembro+CTx

200 mg/m\^2 every 3 weeks (squamous)

Part 1: Cohort CPart 2: Canakinumab+pembro+CTxPart 2: Placebo+pembro+CTx

100 mg/m\^2 on Days 1, 8, and 15 of every cycle (squamous)

Part 2: Canakinumab+pembro+CTxPart 2: Placebo+pembro+CTx

500 mg/m\^2 every 3 weeks (non-squamous)

Part 1: Cohort APart 1: Cohort BPart 2: Canakinumab+pembro+CTxPart 2: Placebo+pembro+CTx

canakinumab 200 mg subcutaneous (s.c.) injection every 3 weeks (squamous and non-squamous)

Also known as: ACZ885
Part 1: Cohort APart 1: Cohort BPart 1: Cohort CPart 2: Canakinumab+pembro+CTx

200 mg every 3 weeks (squamous and non-squamous)

Part 1: Cohort APart 1: Cohort BPart 1: Cohort CPart 2: Canakinumab+pembro+CTxPart 2: Placebo+pembro+CTx

Eligibility Criteria

Age18 Years - 100 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Histologically confirmed locally advanced stage IIIB or stage IV NSCLC for treatment in the first-line setting
  • Known PD-L1 status determined by a Novartis designated central laboratory. A newly obtained tissue biopsy or an archival biopsy (block or slides) is required for PD-L1 determination (PD-L1 IHC 22C3 pharmDx assay), prior to study randomization. Note: For the safety run-in part, known PD-L1 status is not required.
  • Eastern Cooperative oncology group (ECOG) performance status of 0 or 1.
  • At least 1 measurable lesion by RECIST 1.1

You may not qualify if:

  • Previous immunotherapy (e.g. anti-PD-1, anti-PD-L1, anti-PD-L2, anti-CTLA-4 antibody, or any other antibody or drug specifically targeting T-cell co-stimulation or immune checkpoint pathways).
  • Prior treatment with canakinumab or drugs of a similar mechanism of action (IL-1β inhibitor).
  • Subjects with epidermal growth factor receptor (EGFR) sensitizing mutations (identified in exons 19, 20, or 21), and/or ALK rearrangement by locally approved laboratory testing.
  • Previously untreated or symptomatic central nervous system (CNS) metastases or lepto-meningeal disease.
  • Subject with suspected or proven immune-compromised state or infections.
  • Subject has prior to starting study drug: received live vaccination ≤3 months, had major surgery ≤4 weeks prior to starting study drug, has thoracic radiotherapy: lung fields ≤ 4 weeks, other anatomic sites ≤ 2 weeks, palliative radiotherapy for bone lesions ≤ 2 weeks.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (152)

Pacific Shores Medical Group

Long Beach, California, 90813, United States

Location

USC Kenneth Norris Comprehensive Cancer Center

Los Angeles, California, 90033, United States

Location

AdventHealth

Orlando, Florida, 32804, United States

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Dana Farber Cancer Institute

Boston, Massachusetts, 02215, United States

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Novartis Investigative Site

Caba, Buenos Aires, C1426ANZ, Argentina

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Novartis Investigative Site

Caba, C1431FWO, Argentina

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Novartis Investigative Site

Westmead, New South Wales, 2145, Australia

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Wooloongabba, Queensland, 4102, Australia

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Melbourne, Victoria, 3000, Australia

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Murdoch, Western Australia, 6150, Australia

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Linz, Upper Austria, 4020, Austria

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Salzburg, 5020, Austria

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Barretos, São Paulo, 14784 400, Brazil

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São Paulo, São Paulo, 01246 000, Brazil

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Novartis Investigative Site

São Paulo, São Paulo, 04014-002, Brazil

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Edmonton, Alberta, T6G 1Z2, Canada

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Brampton, Ontario, L6R 3J7, Canada

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Toronto, Ontario, M5G 2M9, Canada

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Temuco, Región de la Araucanía, 4810469, Chile

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Santiago, 8420383, Chile

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Harbin, Heilongjiang, 150081, China

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Wuhan, Hubei, 430022, China

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Wuhan, Hubei, 430030, China

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Changsha, Hunan, 410013, China

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Changchun, Jilin, 130012, China

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Xi’an, Shanxi, 710038, China

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Hangzhou, Zhejiang, 310022, China

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Beijing, 100036, China

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Valledupar, Cesar Department, 200001, Colombia

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Ostrava, Vitkovice, 703 84, Czechia

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Brno, 625 00, Czechia

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Brno, 656 53, Czechia

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Prague, 128 08, Czechia

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Herning, 7400, Denmark

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Oulu, FIN-90220, Finland

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Marseille, Bouches Du Rhone, 13915, France

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Lyon, 69373, France

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Montpellier, 34070, France

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Nantes, 44093, France

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Paris, 75231, France

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Munich, Bavaria, 81377, Germany

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Göttingen, Lower Saxony, 37075, Germany

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Cologne, North Rhine-Westphalia, 50937, Germany

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Cologne, North Rhine-Westphalia, 51109, Germany

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Dresden, Saxony, 01307, Germany

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Leipzig, Saxony, 04347, Germany

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Halle, Saxony-Anhalt, 06120, Germany

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Berlin, 13125, Germany

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Essen, 45147, Germany

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Georgsmarienhütte, 49124, Germany

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Gerlingen, 70839, Germany

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Heidelberg, 69120, Germany

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Athens, GR, 115 27, Greece

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Athens, 185 47, Greece

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Kowloon, 999999, Hong Kong

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Veszprém, 8200, Hungary

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Reykjavik, 101, Iceland

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Hyderabad, Andhra Pradesh, 500034, India

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Gurgaon, Haryana, 122 001, India

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Pune, Maharashtra, 411013, India

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Jaipur, Rajasthan, 302017, India

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Hyderabad, Telangana, 500082, India

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Kolkata, West Bengal, 700160, India

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Avellino, AV, 83100, Italy

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Genova, GE, 16132, Italy

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Milan, MI, 20132, Italy

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Milan, MI, 20133, Italy

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Milan, MI, 20141, Italy

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Rozzano, MI, 20089, Italy

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Modena, MO, 41124, Italy

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Padua, PD, 35128, Italy

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Perugia, PG, 06129, Italy

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Parma, PR, 43126, Italy

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Orbassano, TO, 10043, Italy

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Nagoya, Aichi-ken, 464 8681, Japan

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Sapporo, Hokkaido, 0608648, Japan

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Himeji, Hyōgo, 670-8520, Japan

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Yokohama, Kanagawa, 241-8515, Japan

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Sakai, Osaka, 591-8555, Japan

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Sunto Gun, Shizuoka, 411 8777, Japan

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Chuo Ku, Tokyo, 1040045, Japan

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Ube, Yamaguchi, 755-0241, Japan

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Osaka, 5458586, Japan

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Beirut, 166830, Lebanon

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Saida, 652, Lebanon

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Kuala Lumpur, Kuala Lumpur, 50586, Malaysia

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Kuantan, Pahang, 25100, Malaysia

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Kuching, Sarawak, 93586, Malaysia

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Kuala Lumpur, 59100, Malaysia

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Groningen, 9713 GZ, Netherlands

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Groningen, 9728 NZ, Netherlands

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Drammen, 3004, Norway

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City of Taguig, National Capital Region, 1634, Philippines

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Makati City, 1229, Philippines

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Quezon, 1102, Philippines

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San Juan City, 1502, Philippines

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Gliwice, 44 101, Poland

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Poznan, 60 569, Poland

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Tomaszw Mazowiecki, 97-200, Poland

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Lisbon, 1769 001, Portugal

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Porto, 4200-072, Portugal

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Cluj-Napoca, Cluj, 400015, Romania

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Craiova, Dolj, 200347, Romania

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Arkhangelsk, 163045, Russia

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Omsk, 644013, Russia

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Saint Petersburg, 192148, Russia

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Saint Petersburg, 196603, Russia

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Saint Petersburg, 197022, Russia

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Singapore, 119228, Singapore

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Singapore, 168583, Singapore

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Singapore, S308433, Singapore

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Bratislava, 83310, Slovakia

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Kosice-Saca, 958 01, Slovakia

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Gyeonggi-do, Korea, 10408, South Korea

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Seoul, Korea, 03080, South Korea

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Seoul, 03722, South Korea

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Seoul, 05505, South Korea

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Seoul, 06591, South Korea

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Granada, Andalusia, 18014, Spain

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Badalona, Barcelona, 08916, Spain

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Donostia / San Sebastian, Gipuzkoa, 20014, Spain

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Las Palmas de Gran C, Las Palmas, 35016, Spain

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Barcelona, 08035, Spain

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Barcelona, 08036, Spain

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Madrid, 28009, Spain

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Madrid, 28040, Spain

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Madrid, 28041, Spain

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Madrid, 28046, Spain

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Málaga, 29010, Spain

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Valencia, 46026, Spain

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Zaragoza, 50009, Spain

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Stockholm, 171 76, Sweden

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Basel, 4031, Switzerland

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Kaohsiung City, 83301, Taiwan

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Tainan, 704, Taiwan

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Taipei, 10002, Taiwan

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Taipei, 11217, Taiwan

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Taoyuan District, 333, Taiwan

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Songkhla, Hat Yai, 90110, Thailand

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Khon Kaen, THA, 40002, Thailand

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Bangkok, 10330, Thailand

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Bangkok, 10400, Thailand

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Bangkok, 10700, Thailand

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Istanbul, Bagcilar, 34214, Turkey (Türkiye)

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Ankara, Bilkent Cankaya, 06800, Turkey (Türkiye)

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Edirne, Merkez, 22030, Turkey (Türkiye)

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Ankara, Sihhiye-Altindag, 06230, Turkey (Türkiye)

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High Heaton, Newcastle Upon Tyne, NE7 7DN, United Kingdom

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London, NW3 2QG, United Kingdom

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Manchester, M20 2BX, United Kingdom

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Plymouth, PL6 8DH, United Kingdom

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Hanoi, 100000, Vietnam

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Related Publications (1)

  • Tan DSW, Felip E, de Castro G, Solomon BJ, Greystoke A, Cho BC, Cobo M, Kim TM, Ganguly S, Carcereny E, Paz-Ares L, Bennouna J, Garassino MC, Schenker M, Kim SW, Brase JC, Bury-Maynard D, Passos VQ, Deudon S, Dharan B, Song Y, Caparica R, Johnson BE. Canakinumab Versus Placebo in Combination With First-Line Pembrolizumab Plus Chemotherapy for Advanced Non-Small-Cell Lung Cancer: Results From the CANOPY-1 Trial. J Clin Oncol. 2024 Jan 10;42(2):192-204. doi: 10.1200/JCO.23.00980. Epub 2023 Dec 1.

MeSH Terms

Conditions

Carcinoma, Non-Small-Cell LungNeoplasm Metastasis

Interventions

canakinumabpembrolizumabCarboplatinCisplatinPaclitaxel130-nm albumin-bound paclitaxelPemetrexed

Condition Hierarchy (Ancestors)

Carcinoma, BronchogenicBronchial NeoplasmsLung NeoplasmsRespiratory Tract NeoplasmsThoracic NeoplasmsNeoplasms by SiteNeoplasmsLung DiseasesRespiratory Tract DiseasesNeoplastic ProcessesPathologic ProcessesPathological Conditions, Signs and Symptoms

Intervention Hierarchy (Ancestors)

Coordination ComplexesOrganic ChemicalsChlorine CompoundsInorganic ChemicalsNitrogen CompoundsPlatinum CompoundsTaxoidsCyclodecanesCycloparaffinsHydrocarbons, AlicyclicHydrocarbons, CyclicHydrocarbonsDiterpenesTerpenesGuanineHypoxanthinesPurinonesPurinesHeterocyclic Compounds, 2-RingHeterocyclic Compounds, Fused-RingHeterocyclic CompoundsGlutamatesAmino Acids, AcidicAmino AcidsAmino Acids, Peptides, and ProteinsAmino Acids, Dicarboxylic

Results Point of Contact

Title
Study Director
Organization
Novartis Pharmaceuticals

Study Officials

  • Novartis Pharmaceuticals

    Novartis Pharmaceuticals

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

August 6, 2018

First Posted

August 15, 2018

Study Start

December 21, 2018

Primary Completion

August 9, 2021

Study Completion

January 26, 2026

Last Updated

February 25, 2026

Results First Posted

October 8, 2024

Record last verified: 2026-02

Data Sharing

IPD Sharing
Will share

Novartis is committed to sharing with qualified external researchers, access to patient-level data and supporting clinical documents from eligible studies. These requests are reviewed and approved by an independent expert panel on the basis of scientific merit. All data provided is anonymized to respect the privacy of patients who have participated in the trial in line with applicable laws and regulations. This trial data is currently available according to the process described on www.clinicalstudydatarequest.com.

Locations