NCT03663205

Brief Summary

This study evaluated the efficacy and safety of tislelizumab in combination with platinum (cisplatin or carboplatin) and pemetrexed compared with platinum and pemetrexed alone as first-line treatment in participants with Stage IIIB or IV non-squamous non-small cell lung cancer (NSCLC).

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
334

participants targeted

Target at P25-P50 for phase_3 nonsmall-cell-lung-cancer

Timeline
Completed

Started Jul 2018

Geographic Reach
1 country

47 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

July 23, 2018

Completed
24 days until next milestone

First Submitted

Initial submission to the registry

August 16, 2018

Completed
25 days until next milestone

First Posted

Study publicly available on registry

September 10, 2018

Completed
1.4 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

January 23, 2020

Completed
3.3 years until next milestone

Study Completion

Last participant's last visit for all outcomes

April 26, 2023

Completed
1.6 years until next milestone

Results Posted

Study results publicly available

November 25, 2024

Completed
Last Updated

February 4, 2025

Status Verified

September 1, 2024

Enrollment Period

1.5 years

First QC Date

August 16, 2018

Results QC Date

April 11, 2024

Last Update Submit

February 2, 2025

Conditions

Outcome Measures

Primary Outcomes (1)

  • Progression Free Survival (PFS) Assessed by Independent Review Committee (IRC) Assessment

    PFS is defined as the time from randomization until first documentation of progression or death from any cause, whichever occurs first, as assessed by the IRC per Response Evaluation Criteria in Solid Tumors (RECIST) v1.1

    Through primary analysis data cut-off date of 23JAN2020 (up to approximately 1 year and 6 months)

Secondary Outcomes (10)

  • Objective Response Rate (ORR) by IRC Assessment

    Through study completion data cut-off date of 26APR2023 (up to approximately 4 years and 9 months)

  • Duration of Response (DOR) by IRC Assessment

    Through study completion data cut-off date of 26APR2023 (up to approximately 4 years and 9 months)

  • Overall Survival (OS)

    Through study completion data cut-off date of 26APR2023 (up to approximately 4 years and 9 months)

  • PFS by Investigator Assessment

    Through study completion data cut-off date of 26APR2023 (up to approximately 4 years and 9 months)

  • ORR by Investigator Assessment

    Through study completion data cut-off date of 26APR2023 (up to approximately 4 years and 9 months)

  • +5 more secondary outcomes

Study Arms (2)

Tislelizumab + Platinum + Pemetrexed

EXPERIMENTAL

Tislelizumab 200 milligrams (mg) administered intravenously (IV) once every 3 weeks plus cisplatin 75 mg/m\^2 or carboplatin area under the plasma or serum concentration-time curve (AUC) 5 once every 3 weeks for 4 to 6 cycles and pemetrexed 500 mg/m\^2 once every 3 weeks until unacceptable toxicity or disease progression (each cycle is 21 days)

Drug: TislelizumabDrug: CisplatinDrug: CarboplatinDrug: Pemetrexed

Platinum + Pemetrexed

ACTIVE COMPARATOR

Cisplatin 75 mg/m\^2 or carboplatin AUC 5 once every 3 weeks for 4 to 6 cycles and pemetrexed 500 mg/m\^2 administered IV once every 3 weeks until unacceptable toxicity or disease progression (each cycle is 21 days)

Drug: CisplatinDrug: CarboplatinDrug: Pemetrexed

Interventions

Administered intravenously

Also known as: Tevimbra, BGB-A317
Tislelizumab + Platinum + Pemetrexed

Administered intravenously

Platinum + PemetrexedTislelizumab + Platinum + Pemetrexed

Administered intravenously

Platinum + PemetrexedTislelizumab + Platinum + Pemetrexed

Administered intravenously

Platinum + PemetrexedTislelizumab + Platinum + Pemetrexed

Eligibility Criteria

Age18 Years - 75 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Age 18-75 years old, male or female, signed informed consent form
  • Advanced NSCLC diagnosed by pathological or clinical physicians
  • Eastern Cooperative Oncology Group (ECOG) performance score ≤ 1
  • Participants must have ≥ 1 measurable lesion as defined per RECIST v1.1
  • Participants must have no prior systemic chemotherapy for advanced or metastatic NSCLC
  • Life expectancy ≥ 12 weeks
  • Participants must have adequate organ function
  • Male/female is willing to use a highly effective method of birth control

You may not qualify if:

  • Diagnosed with NSCLC but with epidermal growth factor receptor (EGFR)-sensitizing mutation or anaplastic lymphoma kinase (ALK) gene translocation
  • Received any approved systemic anticancer therapy within 28 days prior to the initiation of study treatment
  • Received prior treatment with EGFR inhibitors or ALK inhibitors
  • Received prior therapies targeting programmed cell death protein-1 (PD-1) or programmed cell death protein ligand-1 (PD-L1)
  • With history of interstitial lung disease, non-infectious pneumonitis or uncontrolled systemic diseases
  • Clinically significant pericardial effusion
  • Severe infections, active leptomeningeal disease or uncontrolled, untreated brain metastasis
  • Any major surgical procedure ≤ 28 days before randomization
  • Human immunodeficiency virus (HIV) infection
  • Participants with untreated hepatitis B or C virus (HBV/HCV)
  • Active autoimmune diseases or history of autoimmune diseases
  • History of allergic reactions to chemotherapy

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (47)

Anhui Provincial Hospital

Hefei, Anhui, 230000, China

Location

Cancer Hospital Chinese Academy of Medical Sciences

Beijing, Beijing Municipality, 100021, China

Location

Beijing Cancer Hospital

Beijing, Beijing Municipality, 100142, China

Location

Beijing Hospital

Beijing, Beijing Municipality, 100730, China

Location

Peking Union Medical College Hospital

Beijing, Beijing Municipality, 100730, China

Location

Chinese Pla General Hospital

Beijing, Beijing Municipality, 100853, China

Location

The Second Affiliated Hospital of Chongqing Medical University

Chongqing, Chongqing Municipality, 400010, China

Location

Daping Hospital, Third Military Medical University

Chongqing, Chongqing Municipality, 400042, China

Location

Chongqing Three Gorges Central Hospital

Chongqing, Chongqing Municipality, 404000, China

Location

Fujian Cancer Hospital

Fuzhou, Fujian, 350014, China

Location

The First Affiliated Hospital of Xiamen University

Xiamen, Fujian, 361003, China

Location

Cancer Center of Guangzhou Medical University

Guangzhou, Guangdong, 510030, China

Location

Nanfang Hospital of Southern Medical University

Guangzhou, Guangdong, 510515, China

Location

Cancer Hospital of Shantou University Medical College

Shantou, Guangdong, 515031, China

Location

Affiliated Hospital of Guilin Medical University

Guilin, Guangxi, 541001, China

Location

The Peoples Hospital of Guangxi Zhuang Autonomous Region

Nanning, Guangxi, 530021, China

Location

Guizhou Cancer Hospital

Guiyang, Guizhou, 550000, China

Location

The Affiliated Hospital of Zunyi Medical College

Zunyi, Guizhou, 563000, China

Location

Hainan General Hospital

Haikou, Hainan, 570206, China

Location

Harbin Medical University Cancer Hospital

Harbin, Heilongjiang, 150000, China

Location

Henan Cancer Hospital

Zhengzhou, Henan, 450000, China

Location

The First Affiliated Hospital of Zhengzhou University

Zhengzhou, Henan, 450052, China

Location

Hubei Cancer Hospital

Wuhan, Hubei, 430079, China

Location

Changsha Central Hospital

Changsha, Hunan, 410004, China

Location

Hunan Cancer Hospital

Changsha, Hunan, 410013, China

Location

The First Affiliated Hospital of Soochow University Branch Shizi

Suzhou, Jiangsu, 215006, China

Location

Xuzhou Central Hospital

Xuzhou, Jiangsu, 221000, China

Location

The First Hospital of Jilin University

Changchun, Jilin, 130021, China

Location

The First Hospital of China Medical University

Shenyang, Liaoning, 110001, China

Location

Liaoning Cancer Hospital and Institute

Shenyang, Liaoning, 110042, China

Location

The First Affiliated Hospital of Xian Jiaotong University

Xi'an, Shaanxi, 710061, China

Location

Qilu Hospital of Shandong University

Jinan, Shandong, 250000, China

Location

Jinan Central Hospital

Jinan, Shandong, 250013, China

Location

Jinan Military General Hospital

Jinan, Shandong, 250031, China

Location

Shandong Cancer Hospital

Jinan, Shandong, 250117, China

Location

Weifang Peoples Hospital

Weifang, Shandong, 261000, China

Location

Fudan University Shanghai Cancer Center

Shanghai, Shanghai Municipality, 200000, China

Location

Shanghai Chest Hospital

Shanghai, Shanghai Municipality, 200030, China

Location

West China Hospital, Sichuan University

Chengdu, Sichuan, 610041, China

Location

Tianjin Medical University General Hospital

Tianjin, Tianjin Municipality, 300052, China

Location

Tianjin Medical University Cancer Institute and Hospital

Tianjin, Tianjin Municipality, 300060, China

Location

Yunnan Cancer Hospital

Kunming, Yunnan, 650100, China

Location

The First Affiliated Hospital, Zhejiang University School of Medicine

Hangzhou, Zhejiang, 310003, China

Location

Hangzhou First Peoples Hospital

Hangzhou, Zhejiang, 310006, China

Location

Zhejiang University College of Medicine Second Affiliated Hospital

Hangzhou, Zhejiang, 310009, China

Location

Sir Run Run Shaw Hospital, Zhejiang University School of Medicine

Hangzhou, Zhejiang, 310016, China

Location

Zhejiang Cancer Hospital

Hangzhou, Zhejiang, 310022, China

Location

Related Publications (3)

  • Lu S, Wang J, Yu Y, Yu X, Hu Y, Ai X, Ma Z, Li X, Zhuang W, Liu Y, Li W, Cui J, Wang D, Liao W, Zhou J, Wang Z, Sun Y, Qiu X, Gao J, Bao Y, Liang L, Wang M. Tislelizumab Plus Chemotherapy as First-Line Treatment for Locally Advanced or Metastatic Nonsquamous NSCLC (RATIONALE 304): A Randomized Phase 3 Trial. J Thorac Oncol. 2021 Sep;16(9):1512-1522. doi: 10.1016/j.jtho.2021.05.005. Epub 2021 May 23.

  • Lu S, Wang J, Yu Y, Yu X, Hu Y, Wangjun L, Li X, Liu Y, Li W, Qu X, Bao Y, Wang M. First-Line Tislelizumab Plus Chemotherapy in Advanced Non-Squamous Non-Small Cell Lung Cancer: PD-L1 >/= 50% Subgroup Analysis from the RATIONALE-304 Trial. Oncol Ther. 2025 Dec;13(4):1087-1104. doi: 10.1007/s40487-025-00378-8. Epub 2025 Sep 14.

  • Lu S, Yu Y, Barnes G, Qiu X, Bao Y, Tang B. Examining the Impact of Tislelizumab Added to Chemotherapy on Health-Related Quality-of-Life Outcomes in Previously Untreated Patients With Nonsquamous Non-Small Cell Lung Cancer. Cancer J. 2022 Mar-Apr 01;28(2):96-104. doi: 10.1097/PPO.0000000000000583.

MeSH Terms

Conditions

Carcinoma, Non-Small-Cell Lung

Interventions

tislelizumabCisplatinCarboplatinPemetrexed

Condition Hierarchy (Ancestors)

Carcinoma, BronchogenicBronchial NeoplasmsLung NeoplasmsRespiratory Tract NeoplasmsThoracic NeoplasmsNeoplasms by SiteNeoplasmsLung DiseasesRespiratory Tract Diseases

Intervention Hierarchy (Ancestors)

Chlorine CompoundsInorganic ChemicalsNitrogen CompoundsPlatinum CompoundsCoordination ComplexesOrganic ChemicalsGuanineHypoxanthinesPurinonesPurinesHeterocyclic Compounds, 2-RingHeterocyclic Compounds, Fused-RingHeterocyclic CompoundsGlutamatesAmino Acids, AcidicAmino AcidsAmino Acids, Peptides, and ProteinsAmino Acids, Dicarboxylic

Results Point of Contact

Title
Study Director
Organization
BeiGene

Study Officials

  • Study Director

    BeiGene

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

August 16, 2018

First Posted

September 10, 2018

Study Start

July 23, 2018

Primary Completion

January 23, 2020

Study Completion

April 26, 2023

Last Updated

February 4, 2025

Results First Posted

November 25, 2024

Record last verified: 2024-09

Data Sharing

IPD Sharing
Will share

Locations