NCT06528496

Brief Summary

The purpose of this study is to find out whether N10 chemotherapy is a safe and effective treatment for children with high-risk neuroblastoma.

Trial Health

77
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
45

participants targeted

Target at P25-P50 for phase_2

Timeline
38mo left

Started Jul 2024

Longer than P75 for phase_2

Geographic Reach
1 country

1 active site

Status
recruiting

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Progress38%
Jul 2024Jul 2029

First Submitted

Initial submission to the registry

July 22, 2024

Completed
Same day until next milestone

Study Start

First participant enrolled

July 22, 2024

Completed
8 days until next milestone

First Posted

Study publicly available on registry

July 30, 2024

Completed
5 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

July 22, 2029

Expected
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

July 22, 2029

Last Updated

February 10, 2026

Status Verified

February 1, 2026

Enrollment Period

5 years

First QC Date

July 22, 2024

Last Update Submit

February 9, 2026

Conditions

Keywords

High-risk neuroblastomaneuroblastomachildhood neuroblastomaN10Memorial Sloan Kettering Cancer Center24-144

Outcome Measures

Primary Outcomes (1)

  • Evaluate participant response

    To assess the early Complete Response/CR rate in newly-diagnosed HR-NB patients.

    After 2 cycles of mAb-based therapy (each cycle is 21 days)

Study Arms (1)

Participants with Neuroblastoma

EXPERIMENTAL

Participants will receive 4 cycles of induction chemotherapy followed by a response-based intervention.

Biological: DANYELZABiological: SargramostimDrug: CytoxanDrug: TopotecanDrug: VincristineDrug: DoxorubicinDrug: IfosfamideDrug: EtoposideDrug: CarboplatinDrug: IrinotecanDrug: Temozolomide

Interventions

Topotecan is a topoisomerase I-inhibitor that is a semisynthetic derivative of camptothecin.

Participants with Neuroblastoma

Vincristine is an alkaloid isolated from Vinca rosea Linn (periwinkle).

Also known as: Oncovin
Participants with Neuroblastoma

Doxorubicin is an anthracycline antibiotic

Also known as: Adriamycin
Participants with Neuroblastoma

Ifosfamide is a structural analogue of cyclophosphamide

Also known as: Isophosphamide
Participants with Neuroblastoma

Etoposide for Injection is available as a 20 mg/mL solution in sterile multiple dose vials (5 mL, 25 mL, or 50 mL each).

Also known as: VePesid, Etopophos, VP-16
Participants with Neuroblastoma

Carboplatin is available in 50 mg, 150 mg, 450 mg, and 600 mg vials.

Also known as: Paraplatin
Participants with Neuroblastoma

Irinotecan hydrochloride trihydrate (CPT-11) is a topoisomerase I inhibitor

Also known as: Camptosar
Participants with Neuroblastoma

Temozolomide is administered intravenously

Also known as: Temodar
Participants with Neuroblastoma

Cyclophosphamide is an alkylating agent related to nitrogen mustard

Also known as: Cyclophosphamide
Participants with Neuroblastoma
DANYELZABIOLOGICAL

DANYELZA is a humanized monoclonal antibody of the IgG1 subclass

Also known as: Naxitamab
Participants with Neuroblastoma
SargramostimBIOLOGICAL

Yeast derived recombinant human Sargramostim (GM-CSF)

Also known as: granulocyte-macrophage colony-stimulating factor, GM-CSF
Participants with Neuroblastoma

Eligibility Criteria

Age18 Months - 19 Years
Sexall
Healthy VolunteersNo
Age GroupsChild (0-17), Adult (18-64)

You may qualify if:

  • Diagnosis of NB as defined by histopathology, BM metastases plus high urine catecholamine levels, or positivity in MIBG scan.
  • HR-NB, defined as MYCN-amplified stage L2/M/MS at any age and stage M in patients \>18 months old.
  • No more than one prior cycle of HR-NB chemotherapy
  • Age \<19 years.
  • Signed informed consent indicating awareness of the investigational nature of this treatment.

You may not qualify if:

  • Severe dysfunction of major organs, i.e., renal, cardiac, hepatic, neurologic, pulmonary, hematologic, or gastrointestinal toxicity \>/= to grade 3
  • Inability to comply with protocol requirements
  • Pregnancy

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (1)

Memorial Sloan Kettering Cancer Center

New York, New York, 10065, United States

RECRUITING

Related Links

MeSH Terms

Conditions

Neuroblastoma

Interventions

naxitamabsargramostimGranulocyte-Macrophage Colony-Stimulating FactorCyclophosphamideTopotecanVincristineDoxorubicinIfosfamideEtoposideetoposide phosphateCarboplatinIrinotecanTemozolomide

Condition Hierarchy (Ancestors)

Neuroectodermal Tumors, Primitive, PeripheralNeuroectodermal Tumors, PrimitiveNeoplasms, NeuroepithelialNeuroectodermal TumorsNeoplasms, Germ Cell and EmbryonalNeoplasms by Histologic TypeNeoplasmsNeoplasms, Glandular and EpithelialNeoplasms, Nerve Tissue

Intervention Hierarchy (Ancestors)

Colony-Stimulating FactorsGlycoproteinsGlycoconjugatesCarbohydratesHematopoietic Cell Growth FactorsCytokinesIntercellular Signaling Peptides and ProteinsPeptidesAmino Acids, Peptides, and ProteinsProteinsBiological FactorsPhosphoramide MustardsNitrogen Mustard CompoundsMustard CompoundsHydrocarbons, HalogenatedHydrocarbonsOrganic ChemicalsPhosphoramidesOrganophosphorus CompoundsCamptothecinAlkaloidsHeterocyclic CompoundsVinca AlkaloidsSecologanin Tryptamine AlkaloidsIndole AlkaloidsIndolesHeterocyclic Compounds, 2-RingHeterocyclic Compounds, Fused-RingIndolizidinesIndolizinesDaunorubicinAnthracyclinesNaphthacenesPolycyclic Aromatic HydrocarbonsHydrocarbons, AromaticHydrocarbons, CyclicPolycyclic CompoundsAminoglycosidesGlycosidesOxazinesHeterocyclic Compounds, 1-RingPodophyllotoxinTetrahydronaphthalenesNaphthalenesGlucosidesCoordination ComplexesDacarbazineTriazenesImidazolesAzoles

Study Officials

  • Brian Kushner, MD

    Memorial Sloan Kettering Cancer Center

    PRINCIPAL INVESTIGATOR

Central Study Contacts

Brian Kushner, MD

CONTACT

Fiorella Iglasias Cardenas, MD, MS

CONTACT

Study Design

Study Type
interventional
Phase
phase 2
Allocation
NA
Masking
NONE
Purpose
TREATMENT
Intervention Model
SEQUENTIAL
Sponsor Type
OTHER
Responsible Party
SPONSOR

Study Record Dates

First Submitted

July 22, 2024

First Posted

July 30, 2024

Study Start

July 22, 2024

Primary Completion (Estimated)

July 22, 2029

Study Completion (Estimated)

July 22, 2029

Last Updated

February 10, 2026

Record last verified: 2026-02

Data Sharing

IPD Sharing
Will share

Memorial Sloan Kettering Cancer Center supports the international committee of medical journal editors (ICMJE) and the ethical obligation of responsible sharing of data from clinical trials. The protocol summary, a statistical summary, and informed consent form will be made available on clinicaltrials.gov when required as a condition of Federal awards, other agreements supporting the research and/or as otherwise required. Requests for deidentified individual participant data can be made beginning 12 months after publication and for up to 36 months post publication. Deidentified individual participant data reported in the manuscript will be shared under the terms of a Data Use Agreement and may only be used for approved proposals. Requests may be made to: crdatashare@mskcc.org.

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