NCT05306340

Brief Summary

This Phase III, randomized, open-label, multicenter study will evaluate the efficacy and safety of giredestrant plus everolimus compared with the physician's choice of endocrine therapy plus everolimus in participants with estrogen receptor (ER)-positive, human epidermal growth factor receptor 2 (HER2)-negative locally advanced or metastatic breast cancer who have had previous treatment with cyclin-dependent kinase 4/6 inhibitors (CDK4/6is) and endocrine therapy, either in the locally advanced/metastatic or the adjuvant setting.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Strong global presence with extensive site network
Enrollment
373

participants targeted

Target at P50-P75 for phase_3

Timeline
5mo left

Started Aug 2022

Typical duration for phase_3

Geographic Reach
13 countries

135 active sites

Status
active not recruiting

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Progress90%
Aug 2022Oct 2026

First Submitted

Initial submission to the registry

March 23, 2022

Completed
9 days until next milestone

First Posted

Study publicly available on registry

April 1, 2022

Completed
4 months until next milestone

Study Start

First participant enrolled

August 3, 2022

Completed
3 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

July 16, 2025

Completed
1.2 years until next milestone

Study Completion

Last participant's last visit for all outcomes

October 15, 2026

Expected
Last Updated

April 30, 2026

Status Verified

April 1, 2026

Enrollment Period

3 years

First QC Date

March 23, 2022

Last Update Submit

April 24, 2026

Conditions

Outcome Measures

Primary Outcomes (1)

  • Progression-Free Survival, as Determined by the Investigator According to RECIST v1.1, in the ESR1m Subpopulation and ITT Population

    The Intent-to-Treat (ITT) population consists of all randomized participants, and the ESR1m subpopulation is defined as participants in the ITT population whose tumors harbor a detectable Estrogen Receptor 1 (ESR1) mutation at baseline as measured in circulating tumor DNA (ctDNA).

    From randomization until the first occurrence of disease progression or death from any cause, whichever occurs first (up to 42 months)

Secondary Outcomes (14)

  • Overall Survival, in the ESR1m Subpopulation and ITT Population

    From randomization until death from any cause (up to 42 months)

  • Objective Response Rate (ORR), as Determined by the Investigator According to RECIST v1.1, in the ESR1m Subpopulation and ITT Population

    From randomization until progressive disease or death (up to 42 months)

  • Duration of Response (DOR), as Determined by the Investigator According to RECIST v1.1, in the ESR1m Subpopulation and ITT Population

    From the first occurrence of a documented objective response to disease progression or death from any cause, whichever occurs first (up to 42 months)

  • Clinical Benefit Rate (CBR), as Determined by the Investigator According to RECIST v1.1, in the ESR1m Subpopulation and ITT Population

    From Baseline until progressive disease or death (up to 42 months)

  • Time to Confirmed Deterioration in Pain Severity, as Determined Using the Brief Pain Inventory Short-Form (BPI-SF) Worst Pain Item Score, in the ESR1m Subpopulation and ITT Population

    From randomization until 90 days after treatment discontinuation (up to 42 months)

  • +9 more secondary outcomes

Study Arms (2)

Giredestrant plus Everolimus

EXPERIMENTAL
Drug: GiredestrantDrug: EverolimusDrug: LHRH AgonistDrug: Dexamethasone Mouth Rinse

Physician's Choice of Endocrine Therapy plus Everolimus

ACTIVE COMPARATOR

The physician's choice of endocrine therapy is defined as either exemestane, fulvestrant, or tamoxifen.

Drug: ExemestaneDrug: FulvestrantDrug: TamoxifenDrug: EverolimusDrug: LHRH AgonistDrug: Dexamethasone Mouth Rinse

Interventions

Participants will receive treatment with giredestrant 30 milligrams (mg) orally once a day (QD) on Days 1-28 of each 28-day cycle until unacceptable toxicity or disease progression as determined by the investigator according to Response Evaluation Criteria in Solid Tumors, version 1.1 (RECIST v1.1).

Also known as: GDC-9545, RO7197597, RG6171
Giredestrant plus Everolimus

If exemestane is chosen as the physician's choice of endocrine therapy, the participant will receive exemestane at a dose of 25 mg orally once a day (QD) on Days 1-28 of each 28-day cycle or as per local label, until unacceptable toxicity or disease progression as determined by investigator according to RECIST v1.1.

Physician's Choice of Endocrine Therapy plus Everolimus

If fulvestrant is chosen as the physician's choice of endocrine therapy, the participant will receive fulvestrant in the clinic at a dose of 500 mg intramuscularly on Day 1 and Day 15 of Cycle 1, then Day 1 of each cycle thereafter (1 cycle is 28 days) or as per local prescribing information, until unacceptable toxicity or disease progression as determined by investigator according to RECIST v1.1.

Physician's Choice of Endocrine Therapy plus Everolimus

If tamoxifen is chosen as the physician's choice of endocrine therapy, the participant will receive tamoxifen at a dose of 20 mg orally QD on Days 1-28 of each 28-day cycle or as per local prescribing information, until unacceptable toxicity or disease progression as determined by investigator according to RECIST v1.1.

Physician's Choice of Endocrine Therapy plus Everolimus

Participants will receive treatment with everolimus 10 mg orally QD during each 28-day cycle until unacceptable toxicity or disease progression as determined by the investigator according to RECIST v1.1.

Giredestrant plus EverolimusPhysician's Choice of Endocrine Therapy plus Everolimus

Only premenopausal/perimenopausal female participants and male participants will receive a luteinizing hormone-releasing hormone (LHRH) agonist on Day 1 of each 28-day treatment cycle. The investigator will determine and supply the appropriate LHRH agonist locally approved for use in breast cancer.

Giredestrant plus EverolimusPhysician's Choice of Endocrine Therapy plus Everolimus

A compounded alcohol-free mouthwash of dexamethasone (0.5 mg in 5 mL) will be supplied, where feasible. It is strongly recommended for prophylaxis or treatment of stomatitis/mucositis. Participants should use the alcohol-free mouthwash of dexamethasone four times QD for 8 weeks started concurrently with study treatment, and use it reactively thereafter with the first appearance of symptoms.

Giredestrant plus EverolimusPhysician's Choice of Endocrine Therapy plus Everolimus

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Locally advanced unresectable or metastatic adenocarcinoma of the breast, not amenable to treatment with curative intent
  • Documented estrogen receptor-positive (ER+) tumor and HER2-negative tumor, assessed locally
  • Ability to provide a blood sample for circulating-tumor deoxyribonucleic acid (ctDNA) Estrogen Receptor 1 (ESR1) mutation status determination by central testing
  • Prior endocrine therapy (ET) in combination with cyclin-dependent kinase 4/6 inhibitors in either setting as follows:
  • Metastatic setting: Disease progression after ≥6 months on ET plus CDK4/6 inhibitor in the locally advanced or metastatic setting. If ET plus CDK4/6 inhibitor is not the most recent therapy, then patient must also have had disease progression after ≥4 months on most recent ET
  • Adjuvant Setting: Relapse either while taking or within 12 months of exposure to combination adjuvant ET and CDK4/6 inhibitor. Patients must have taken at least 12 months of adjuvant ET, 6 months of which was in combination with a CDK4/6 inhibitor.
  • Measurable disease as defined per RECIST v.1.1 or evaluable bone metastases. Patients with evaluable bone disease in the absence of measurable disease outside of the bone must have at least one predominantly lytic bone lesion confirmed by computed tomography (CT) or magnetic resonance imaging (MRI) which can be followed
  • Eastern Cooperative Oncology Group Performance Status 0-1
  • For women who are premenopausal or perimenopausal and for men: treatment with approved luteinizing hormone-releasing hormone (LHRH) agonist therapy for the duration of study treatment

You may not qualify if:

  • Prior treatment with another oral selective estrogen receptor degrader (SERD), proteolysis targeting chimera (PROTAC), complete estrogen receptor antagonist (CERAN), novel oral selective estrogen receptor modulator (SERM), or everolimus in any setting. Prior fulvestrant is allowed if treatment was terminated at least 28 days prior to randomization. Prior treatment with tamoxifen is allowed.
  • Progression on more than 2 prior lines of systemic endocrine therapy in the locally advanced unresectable or metastatic breast cancer setting
  • Prior chemotherapy for locally advanced unresectable or metastatic disease
  • Treatment with strong Cytochrome P450 3A4 (CYP3A4) inhibitors or inducers within 14 days or 5 drug elimination half-lives (whichever is longer) prior to randomization
  • Treatment with any investigational therapy within 28 days prior to initiation of study treatment
  • Major surgery, chemotherapy, radiotherapy, or other anti-cancer therapy within 14 days prior to randomization
  • History of any other malignancy other than breast cancer within 5 years prior to screening, except for appropriately treated carcinoma in situ of the cervix, nonmelanoma skin carcinoma, papillary thyroid cancer treated with surgery, Stage I endometrial cancer, or other non-breast cancers at very low risk of recurrence
  • Advanced, symptomatic, visceral spread that is at risk of life-threatening complications in the short term
  • Known active uncontrolled or symptomatic central nervous system (CNS) metastases, carcinomatous meningitis, or leptomeningeal disease
  • Active cardiac disease or history of cardiac dysfunction
  • Known clinically significant history of liver disease consistent with Child-Pugh Class B or C including active viral or other hepatitis virus, current alcohol abuse, or cirrhosis
  • Active inflammatory bowel disease, chronic diarrhea, short bowel syndrome, or major upper gastrointestinal (GI) surgery including gastric resection
  • Interstitial lung disease or severe dyspnea at rest or requiring oxygen therapy
  • Serious infection requiring oral or intravenous (IV) antibiotics, or other clinically significant infection, within 14 days prior to randomization
  • Any serious medical condition or abnormality in clinical laboratory tests that, in the investigator's judgment, precludes the patient's safe participation in and completion of the study
  • +3 more criteria

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (135)

Arizona Oncology Associates, PC-CASA

Tucson, Arizona, 85711, United States

Location

University of Arkansas for Medical Sciences

Little Rock, Arkansas, 72205-7199, United States

Location

Alta Bates Summit Medical Center

Berkeley, California, 94704, United States

Location

Beverly Hills Cancer Center

Beverly Hills, California, 90211, United States

Location

TOI Clinical Research

Cerritos, California, 90703, United States

Location

Women's Cancer Care

Fresno, California, 93710, United States

Location

Scripps Health

La Jolla, California, 92037, United States

Location

Los Angeles Hematology Oncology Medical Group

Los Angeles, California, 90017, United States

Location

University of California, Irvine Medical Center

Orange, California, 92868, United States

Location

Yale Cancer Center

New Haven, Connecticut, 06520, United States

Location

Mount Sinai Medical Center

Miami Beach, Florida, 33140, United States

Location

Orlando Health Cancer Institute

Orlando, Florida, 32806, United States

Location

Northwest Georgia Oncology Centers PC - Marietta

Marietta, Georgia, 30060, United States

Location

Summit Cancer Care PC

Savannah, Georgia, 31405, United States

Location

Northwestern University

Chicago, Illinois, 60611, United States

Location

Springfield Clinic

Springfield, Illinois, 62702, United States

Location

Indiana University Melvin and Bren Simon Cancer Center

Indianapolis, Indiana, 46202, United States

Location

University of Kansas Cancer Center

Westwood, Kansas, 66205, United States

Location

Eastern Maine Medical Center

Brewer, Maine, 04412, United States

Location

New England Cancer Specialists

Scarborough, Maine, 04074, United States

Location

Anne Arundel Medical Center

Annapolis, Maryland, 21401, United States

Location

University of Maryland Greenebaum Cancer Center

Baltimore, Maryland, 21201, United States

Location

Mercy Medical Center

Baltimore, Maryland, 21202, United States

Location

Dana Farber Cancer Institute

Boston, Massachusetts, 02215, United States

Location

Metro-Minnesota Community Oncology Research Consortium

Saint Louis Park, Minnesota, 55416, United States

Location

Oncology Hematology West, PC dba Nebraska Cancer Specialists

Omaha, Nebraska, 68103, United States

Location

Renown Regional Medical Center

Reno, Nevada, 89502, United States

Location

Memorial Sloan Kettering - Basking Ridge

Basking Ridge, New Jersey, 07920, United States

Location

Memorial Sloan Kettering - Monmouth

Middletown, New Jersey, 07748, United States

Location

San Juan Oncology Associates

Farmington, New Mexico, 87401, United States

Location

The Blavatnik Family ? Chelsea Medical Center at Mount Sinai

New York, New York, 10011, United States

Location

Icahn School of Medicine at Mount Sinai

New York, New York, 10029, United States

Location

Memorial Sloan-Kettering Cancer Center

New York, New York, 10065, United States

Location

Stony Brook University Medical Center

Stony Brook, New York, 11794, United States

Location

SCRI Mark H. Zangmeister Center

Columbus, Ohio, 43219, United States

Location

Oklahoma Cancer Specialists and Research Institute

Tulsa, Oklahoma, 74146, United States

Location

St Charles Medical Center Bend

Bend, Oregon, 97701, United States

Location

Abramson Cancer Center

Philadelphia, Pennsylvania, 19104, United States

Location

UPMC Hillman Cancer Center - Magee-Women?s Hospital

Pittsburgh, Pennsylvania, 15213, United States

Location

Abramson Cancer Center Chester County Hospital

West Chester, Pennsylvania, 19380, United States

Location

McGlinn Cancer Institute at Reading Hospital

West Reading, Pennsylvania, 19611, United States

Location

Avera Cancer Institute

Sioux Falls, South Dakota, 57105, United States

Location

West Cancer Center

Germantown, Tennessee, 38138, United States

Location

Texas Oncology - Baylor Charles A. Sammons Cancer Center

Bedford, Texas, 76022, United States

Location

Texas Oncology - Baylor Charles A. Sammons Cancer Center

Dallas, Texas, 75246, United States

Location

Texas Oncology-Denton South

Denton, Texas, 76201, United States

Location

Texas Oncology, P.A. - El Paso

El Paso, Texas, 79902, United States

Location

Houston Methodist Cancer Center

Houston, Texas, 77030, United States

Location

Millennium Research & Clinical Development

Houston, Texas, 77090, United States

Location

Texas Oncology P.A.

San Antonio, Texas, 78229, United States

Location

Inova Fairfax Hospital

Fairfax, Virginia, 22031, United States

Location

Virginia Cancer Specialists

Fairfax, Virginia, 22031, United States

Location

Virginia Oncology Associates

Norfolk, Virginia, 23502, United States

Location

Northwest Medical Specialties, PLLC

Tacoma, Washington, 98405, United States

Location

Instituto de Oncología Ángel H. Roffo

Agronomía, Ciudad Autónoma de BuenosAires, C1417DTB, Argentina

Location

Centro de Investigaciones Médicas y Desarrollo LC S.R.L

Buenos Aires, Ciudad Autónoma de BuenosAires, C1113AAE, Argentina

Location

Consultorios Médicos Dr. Doreski

Ciudad Autonoma Buenos Aires, C1426ABP, Argentina

Location

Centro Medico Privado CEMAIC

Córdoba, X5008AAC, Argentina

Location

Fundacion Centro Oncologico de Integracion Regional (COIR)

Mendoza, M5500AYB, Argentina

Location

Instituto Medico de la Fundacion Estudios Clinicos

Rosario, S2000DEJ, Argentina

Location

Hospital Provincial del Centenario

Rosario, S2002KDS, Argentina

Location

Instituto de Oncologia de Rosario

Rosario, S2013KZE, Argentina

Location

Centro Polivalente de Asistencia e Investigacion Clinica - CER San Juan

San Juan, J5402DIL, Argentina

Location

Organizacion Medica de Investigacion

San Nicolás, C1015ABO, Argentina

Location

Centro de Investigación Clínica ? Clínica Viedma

Viedma, R8500ACE, Argentina

Location

Knappschaft Kliniken Marienhospital Bottrop

Bottrop, 46236, Germany

Location

Universitatsklinikum Erlangen

Erlangen, 91054, Germany

Location

Kliniken Essen-Mitte

Essen, 45136, Germany

Location

Universitätsklinikum Heidelberg

Heidelberg, 69120, Germany

Location

Universitaetsmedizin der Johannes Gutenberg-Universitaet Mainz

Mainz, 55101, Germany

Location

University of Athens, Hematological Clinic,

Athens, 115 27, Greece

Location

Attikon University General Hospital

Athens, 12464, Greece

Location

Metropolitan General Hospital

Cholargós, 155 62, Greece

Location

University General Hospital of Heraklion

Heraklio, 711 10, Greece

Location

University General Hospital of Larissa

Larissa, 412 21, Greece

Location

IASO Obstetrics Gynecology Clinic

Marousi, 151 23, Greece

Location

Agios Loucas Clinic SA

Panórama, 552 36, Greece

Location

Olympion Clinic

Pátrai, 264 43, Greece

Location

Metaxa Cancer Hospital of Piraeus

Piraeus, 185 37, Greece

Location

Interbalkan Medical Center of Thessaloniki

Thessaloniki, 546 39, Greece

Location

Azienda Ospedaliero - Universitaria di Modena Policlinico

Modena, Emilia-Romagna, 41110, Italy

Location

Istituto Nazionale Tumori Regina Elena IRCCS

Rome, Lazio, 00144, Italy

Location

IRCCS AOM Azienda Ospedaliera Metropolitana

Genoa, Liguria, 16132, Italy

Location

Asst Grande Ospedale Metropolitano Niguarda

Milan, Lombardy, 20162, Italy

Location

Azienda Ospedaliero Universitaria Ospedali Riuniti

Torrette Di Ancona, The Marches, 60126, Italy

Location

"Azienda Ospedaliera Universitaria Integrata Verona Ospedale Borgo Trento"

Verona, Veneto, 37124, Italy

Location

Aichi Cancer Center

Aichi, 464-8681, Japan

Location

Nagoya University Hospital

Aichi, 466-8560, Japan

Location

Chiba Cancer Center

Chiba, 260-8717, Japan

Location

National Cancer Center Hospital East

Chiba, 277-8577, Japan

Location

Shikoku Cancer Center

Ehime, 791-0280, Japan

Location

Hiroshima City Hiroshima Citizens Hospital

Hiroshima, 730-8518, Japan

Location

Hiroshima University Hospital

Hiroshima, 734-8551, Japan

Location

Hokkaido University Hospital

Hokkaido, 060-8648, Japan

Location

Hyogo Cancer Center

Hyōgo, 673-0021, Japan

Location

University of Tsukuba Hospital

Ibaraki, 305-8576, Japan

Location

Kanagawa Cancer Center

Kanagawa, 241-8515, Japan

Location

Tokai University Hospital

Kanagawa, 259-1193, Japan

Location

Kumamoto University Hospital

Kumamoto, 860-8556, Japan

Location

Niigata Cancer Center Hospital

Niigata, 951-8566, Japan

Location

National Hospital Organization Osaka National Hospital

Osaka, 540-0006, Japan

Location

Juntendo University Hospital

Tokyo, 113-8431, Japan

Location

The Cancer Institute Hospital of JFCR

Tokyo, 135-8550, Japan

Location

National University Hospital

Singapore, 117599, Singapore

Location

Oncocare Cancer Centre

Singapore, 258500, Singapore

Location

Medical Oncology Centre of Rosebank

Johannesburg, 2196, South Africa

Location

Chungbuk National University Hospital

Cheongju-si, 28644, South Korea

Location

Soon Chun Hyang University Cheonan Hospital

Dongnam-gu, Cheonan-si, 31151, South Korea

Location

National Cancer Center

Goyang-si, 10408, South Korea

Location

Seoul National University Bundang Hospital

Seongnam-si, 13620, South Korea

Location

Seoul National University Hospital

Seoul, 03080, South Korea

Location

Severance Hospital Yonsei University Health System - PPDS

Seoul, 03722, South Korea

Location

Korea University Guro Hospital

Seoul, 08308, South Korea

Location

Complejo Hospitalario Universitario A Coruña (CHUAC, Materno Infantil), Oncología

A Coruña, LA Coruna, 15006, Spain

Location

Hospital Dexeus

Barcelona, 08028, Spain

Location

Hospital Clinic de Barcelona

Barcelona, 08036, Spain

Location

C.H. Regional Reina Sofia - PPDS

Córdoba, 14004, Spain

Location

Hospital General Universitario Gregorio Marañon

Madrid, 28007, Spain

Location

Hospital Universitario Ramón y Cajal

Madrid, 28034, Spain

Location

Hospital Clinico San Carlos

Madrid, 28040, Spain

Location

Hospital Universitario 12 de Octubre

Madrid, 28041, Spain

Location

Hospital General Universitario J.M Morales Meseguer

Murcia, 30008, Spain

Location

Hospital Clinico Universitario de Valencia

Valencia, 46010, Spain

Location

Changhua Christian Hospital

Chang-hua, 500, Taiwan

Location

Chang Gung Memorial Hospital

Kaohsiung Country, 833, Taiwan

Location

National Cheng Kung University Hospital

Tainan, 70457, Taiwan

Location

National Taiwan University Hospital

Taipei, 100229, Taiwan

Location

Koo Foundation Sun Yat-Sen Cancer Center

Taipei, 112, Taiwan

Location

Chang Gung Memorial Hospital - Linkou Branch

Taipei, Taiwan

Location

Memorial Ankara Hastanesi

Ankara, 06520, Turkey (Türkiye)

Location

SAKARYA University Medical Faculty

Sakarya, 811, Turkey (Türkiye)

Location

Dorset County Hospital

Dorchester, DT1 2JY, United Kingdom

Location

North Middlesex Uni Hospital

London, N18 1QX, United Kingdom

Location

The Christie NHS Foundation Trust - SSC Parent

Manchester, M20 4BX, United Kingdom

Location

Nottingham City Hospital

Nottingham, NG5 1PB, United Kingdom

Location

MeSH Terms

Conditions

Breast Neoplasms

Interventions

giredestrantexemestaneFulvestrantTamoxifenEverolimusGonadotropin-Releasing Hormone

Condition Hierarchy (Ancestors)

Neoplasms by SiteNeoplasmsBreast DiseasesSkin DiseasesSkin and Connective Tissue Diseases

Intervention Hierarchy (Ancestors)

EstradiolEstrenesEstranesSteroidsFused-Ring CompoundsPolycyclic CompoundsEstradiol CongenersGonadal Steroid HormonesGonadal HormonesHormonesHormones, Hormone Substitutes, and Hormone AntagonistsStilbenesBenzylidene CompoundsBenzene DerivativesHydrocarbons, AromaticHydrocarbons, CyclicHydrocarbonsOrganic ChemicalsSirolimusMacrolidesLactonesPituitary Hormone-Releasing HormonesHypothalamic HormonesPeptide HormonesNeuropeptidesPeptidesAmino Acids, Peptides, and ProteinsOligopeptidesNerve Tissue ProteinsProteins

Study Officials

  • Clinical Trials

    Genentech, Inc.

    STUDY DIRECTOR

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

March 23, 2022

First Posted

April 1, 2022

Study Start

August 3, 2022

Primary Completion

July 16, 2025

Study Completion (Estimated)

October 15, 2026

Last Updated

April 30, 2026

Record last verified: 2026-04

Data Sharing

IPD Sharing
Will share

For eligible studies, qualified researchers may request access to individual patient level clinical data. See Roche's commitment to transparency of clinical study information here: https://go.roche.com/data\_sharing

Locations