NCT00703820

Brief Summary

The purpose of this study is to assess the feasibility and efficacy of a novel form of therapy-haploidentical NK cell transplantation-in patients with standard-risk AML. In addition, we will investigate the efficacy of clofarabine + cytarabine (Clo/AraC) in newly diagnosed patients with AML and attempt to optimize outcome through the use of MRD-adapted therapy and further improvements in supportive care.

Trial Health

90
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
324

participants targeted

Target at P50-P75 for phase_3

Timeline
Completed

Started Aug 2008

Longer than P75 for phase_3

Geographic Reach
2 countries

8 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

June 20, 2008

Completed
4 days until next milestone

First Posted

Study publicly available on registry

June 24, 2008

Completed
1 month until next milestone

Study Start

First participant enrolled

August 4, 2008

Completed
8.7 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

March 30, 2017

Completed
1 year until next milestone

Results Posted

Study results publicly available

April 2, 2018

Completed
2.4 years until next milestone

Study Completion

Last participant's last visit for all outcomes

August 14, 2020

Completed
Last Updated

August 10, 2021

Status Verified

July 1, 2021

Enrollment Period

8.7 years

First QC Date

June 20, 2008

Results QC Date

March 2, 2018

Last Update Submit

August 6, 2021

Conditions

Outcome Measures

Primary Outcomes (1)

  • Day 22 Minimal Residual Disease (MRD) Measured by Flow Cytometry

    MRD-negative is defined as \<0.1% blasts with leukemia-associated phenotype detected by flow cytometry. MRD-positive is defined as \>=0.1% blasts with leukemia-associated phenotype detected by flow cytometry.

    Day 22 MRD measurement after one course of therapy

Secondary Outcomes (2)

  • Event-free Survival of Standard Risk Patients Who Receive Chemotherapy Alone.

    3 years after completion of therapy

  • Event-free Survival of Standard Risk Patients Who Receive Chemotherapy Followed by Natural Killer Cell Transplantation.

    3 years after completion of therapy

Study Arms (2)

ADE

ACTIVE COMPARATOR

Cytarabine + Daunorubicin + Etoposide NK cells for infusion are prepared using the CliniMACS System.

Drug: CytarabineDrug: DaunorubicinDrug: EtoposideDevice: CliniMACS

Clo/AraC

ACTIVE COMPARATOR

Clofarabine + Cytarabine NK cells for infusion are prepared using the CliniMACS System.

Drug: CytarabineDrug: ClofarabineDevice: CliniMACS

Interventions

See Detailed Description

Also known as: Ara-C, Cytosar-U®
ADEClo/AraC

See Detailed Description

Also known as: Daunomycin, Cerubidine®
ADE

See Detailed Description

Also known as: VP-16, Vepesid®
ADE

See Detailed Description

Also known as: Clolar^TM, Clofarex
Clo/AraC
CliniMACSDEVICE

The mechanism of action of the CliniMACS Cell Selection System is based on magnetic-activated cell sorting (MACS). The CliniMACS device is a powerful tool for the isolation of many cell types from heterogeneous cell mixtures, (e.g. apheresis products). These can then be separated in a magnetic field using an immunomagnetic label specific for the cell type of interest, such as CD3+ human T cells.

Also known as: Cell Selection System
ADEClo/AraC

Eligibility Criteria

AgeUp to 21 Years
Sexall
Healthy VolunteersNo
Age GroupsChild (0-17), Adult (18-64)

You may qualify if:

  • Age less than or equal to 21 years at time of study entry.
  • No prior therapy for this malignancy except for one dose of intrathecal therapy and the use of hydroxyurea or low-dose cytarabine (100-200 mg/m2 per day for one week or less ) for hyperleukocytosis.
  • Written informed consent according to institutional guidelines
  • Female patients of childbearing potential must have a negative serum pregnancy test within 2 weeks prior to enrollment
  • Male and female participants must use an effective contraceptive method during the study and for a minimum of 6 months after study treatment.

You may not qualify if:

  • Down syndrome
  • Acute Promyelocytic Leukemia (APL)
  • Juvenile Myelomonocytic Leukemia (JMML)
  • Fanconi anemia (FA)
  • Kostmann syndrome
  • Shwachman syndrome
  • Other bone marrow failure syndromes
  • Use of concomitant chemotherapy, radiation therapy, or immunotherapy other than as specified in the protocol.
  • Use of investigational agents within 30 days or any anticancer therapy within 2 weeks before study entry with the exception of IT therapy, hydroxyurea, or low-dose cytarabine as stated above. The patient must have recovered from all acute toxicities from any previous therapy.
  • Systemic fungal, bacterial, viral, or other infection not controlled (defined as exhibiting ongoing signs/symptoms related to the infection and without improvement, despite appropriate antibiotics or other treatment).
  • Pregnant or lactating patients.
  • Any significant concurrent disease, illness, or psychiatric disorder that would compromise patient safety or compliance, interfere with consent, study participation, follow up, or interpretation of study results.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (8)

Stanford University Medical Center

Palo Alto, California, 94304, United States

Location

Rady Children's Hospital

San Diego, California, 92123, United States

Location

University of Chicago

Chicago, Illinois, 60637, United States

Location

Dana Farber Cancer Institute and Children's Hospital

Boston, Massachusetts, 02215-5450, United States

Location

Children's Hospital of Michigan

Detroit, Michigan, 48201, United States

Location

St. Jude Children's Research Hospital

Memphis, Tennessee, 38105, United States

Location

Cook's Children's Medical Center

Fort Worth, Texas, 76104, United States

Location

National University Health System

Singapore, 119228, Singapore

Location

Related Publications (2)

  • Rubnitz JE, Lacayo NJ, Inaba H, Heym K, Ribeiro RC, Taub J, McNeer J, Degar B, Schiff D, Yeoh AE, Coustan-Smith E, Wang L, Triplett B, Raimondi SC, Klco J, Choi J, Pounds S, Pui CH. Clofarabine Can Replace Anthracyclines and Etoposide in Remission Induction Therapy for Childhood Acute Myeloid Leukemia: The AML08 Multicenter, Randomized Phase III Trial. J Clin Oncol. 2019 Aug 10;37(23):2072-2081. doi: 10.1200/JCO.19.00327. Epub 2019 Jun 27.

  • Nguyen R, Wu H, Pounds S, Inaba H, Ribeiro RC, Cullins D, Rooney B, Bell T, Lacayo NJ, Heym K, Degar B, Schiff D, Janssen WE, Triplett B, Pui CH, Leung W, Rubnitz JE. A phase II clinical trial of adoptive transfer of haploidentical natural killer cells for consolidation therapy of pediatric acute myeloid leukemia. J Immunother Cancer. 2019 Mar 20;7(1):81. doi: 10.1186/s40425-019-0564-6.

Related Links

MeSH Terms

Conditions

Leukemia, Myeloid, Acute

Interventions

CytarabineDaunorubicinEtoposideClofarabine

Condition Hierarchy (Ancestors)

Leukemia, MyeloidLeukemiaNeoplasms by Histologic TypeNeoplasmsHematologic DiseasesHemic and Lymphatic Diseases

Intervention Hierarchy (Ancestors)

CytidinePyrimidine NucleosidesPyrimidinesHeterocyclic Compounds, 1-RingHeterocyclic CompoundsArabinonucleosidesNucleosidesNucleic Acids, Nucleotides, and NucleosidesAnthracyclinesNaphthacenesPolycyclic Aromatic HydrocarbonsHydrocarbons, AromaticHydrocarbons, CyclicHydrocarbonsOrganic ChemicalsPolycyclic CompoundsAminoglycosidesGlycosidesCarbohydratesPodophyllotoxinTetrahydronaphthalenesNaphthalenesGlucosidesAdenine NucleotidesPurine NucleotidesPurinesHeterocyclic Compounds, 2-RingHeterocyclic Compounds, Fused-RingNucleotidesRibonucleotides

Results Point of Contact

Title
Jeffrey E. Rubnitz, MD, PhD
Organization
St. Jude Children's Research Hospital

Study Officials

  • Jeffrey Rubnitz, MD

    St. Jude Children's Research Hospital

    PRINCIPAL INVESTIGATOR

Publication Agreements

PI is Sponsor Employee
Yes

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
OTHER
Responsible Party
SPONSOR

Study Record Dates

First Submitted

June 20, 2008

First Posted

June 24, 2008

Study Start

August 4, 2008

Primary Completion

March 30, 2017

Study Completion

August 14, 2020

Last Updated

August 10, 2021

Results First Posted

April 2, 2018

Record last verified: 2021-07

Locations