Genzyme, a Sanofi Company
524
10
19
377
Key Highlights
Risk & Performance
Pipeline Risk Assessment
Pipeline Risk Assessment
Based on historical performance
High Risk
Score: 65/100
18.7%
98 terminated/withdrawn out of 524 trials
79.4%
-7.2% vs industry average
25%
131 trials in Phase 3/4
49%
183 of 377 completed trials have results
Key Signals
Enrollment Performance
Analytics
Activity Timeline
Global Presence
Clinical Trials (524)
Long-term Safety and Efficacy Study of Fitusiran in Patients With Hemophilia A or B, With or Without Inhibitory Antibodies to Factor VIII or IX
Role: lead
Fitusiran Prophylaxis in Male Pediatric Subjects Aged 1 to Less Than 12 Years With Hemophilia A or B
Role: lead
Isatuximab, Carfilzomib, Pomalidomide, and Dexamethasone for the Treatment of Relapsed or Refractory Multiple Myeloma
Role: collaborator
Avalglucosidase Alfa French Post-trial Access for Participants With Pompe Disease (PTA Avalglucosidase)
Role: lead
Developing a Management Approach for Patients With "Late-Onset" Pompe Disease
Role: collaborator
A Study to Evaluate Efficacy, Safety, and Tolerability of Alemtuzumab in Pediatric Patients With RRMS With Disease Activity on Prior DMT
Role: lead
ScreenPlus: A Comprehensive, Flexible, Multi-disorder Newborn Screening Program
Role: collaborator
Isatuximab in Patients With Monoclonal Gammopathy of Renal Significance
Role: collaborator
Isatuximab During Stem Cell Collection and Transplant in Patients With Multiple Myeloma and Lymphoma
Role: collaborator
Venglustat in Combination With Cerezyme in Adult Patients With Gaucher Disease Type 3 With Venglustat Monotherapy Extension
Role: lead
Pompe Disease Registry Protocol
Role: lead
Fabry Disease Registry & Pregnancy Sub-registry
Role: lead
Isa-Pom-Dex in Elderly/Frail Subjects With RRMM
Role: collaborator
A Prospective Assessment of Bone Health in Patients With Severe Hemophilia A on Factor VIII vs Factor Mimetic Prophylaxis (Efa Emi Bone Health Study)
Role: collaborator
Isa-Rd for Frail and/or Much Older Patients With Newly Diagnosed Multiple Myeloma
Role: collaborator
LEMTRADA Pregnancy Registry in Multiple Sclerosis
Role: lead
Cognition and MRI Markers in MS Patients With Aubagio® Treatment
Role: collaborator
Rabbit Antithymocyte Globulin (Thymoglobuline) With Ciclosporin for Patients With Acquired Aplastic Anaemia
Role: collaborator
Pompe Pregnancy Sub-Registry
Role: lead
International Collaborative Gaucher Group (ICGG) Gaucher Disease Registry & Pregnancy Sub-registry
Role: lead