NCT03112603

Brief Summary

The purpose of this study is to assess the efficacy of ruxolitinib against best available therapy in participants with steroid-refractory chronic graft-versus-host disease (SR cGvHD).

Trial Health

98
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Strong global presence with extensive site network
Enrollment
330

participants targeted

Target at P50-P75 for phase_3

Timeline
Completed

Started Jun 2017

Longer than P75 for phase_3

Geographic Reach
30 countries

187 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

April 4, 2017

Completed
9 days until next milestone

First Posted

Study publicly available on registry

April 13, 2017

Completed
3 months until next milestone

Study Start

First participant enrolled

June 29, 2017

Completed
2.9 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

May 8, 2020

Completed
1.9 years until next milestone

Results Posted

Study results publicly available

April 15, 2022

Completed
8 months until next milestone

Study Completion

Last participant's last visit for all outcomes

December 15, 2022

Completed
Last Updated

August 12, 2025

Status Verified

August 1, 2025

Enrollment Period

2.9 years

First QC Date

April 4, 2017

Results QC Date

December 10, 2021

Last Update Submit

August 8, 2025

Conditions

Keywords

Graft-versus-host disease (GvHD)Chronic GvHD (cGvHD)steroid-refractoryruxolitinibJanus kinase inhibitor

Outcome Measures

Primary Outcomes (1)

  • Efficacy of Ruxolitinib Versus Investigator's Choice Best Available Therapy (BAT) in Participants With Moderate or Severe Steroid Refractory Chronic Graft Versus Host Disease (SR-cGvHD) Assessed by Overall Response Rate (ORR) at the Cycle 7 Day 1 Visit

    ORR was defined as the percentage of participants in each arm demonstrating a complete response (CR) or partial response (PR) based on chronic GvHD (cGvHD) disease assessments (National Institutes of Health Consensus Criteria) without the requirement of additional systemic therapies for an earlier progression, mixed response, or non-response. Scoring of response was relative to the organ score at the time of randomization. CR: complete resolution of all signs and symptoms of cGVHD in all evaluable organs without the initiation or addition of new systemic therapy. PR: improvement in at least one organ (e.g., improvement of 1 or more points on a 4- to 7-point scale, or an improvement of 2 or more points on a 10- to 12-point scale) without progression in other organs or sites, initiation, or addition of new systemic therapies.

    Cycle 7 Day 1 (each cycle was comprised of 4 weeks)

Secondary Outcomes (23)

  • Rate of Participants With Clinically Relevant Improvement of the Modified Lee cGvHD Symptom Scale Score

    Baseline; Cycle 7 Day 1 (each cycle was comprised of 4 weeks)

  • Rate of Failure-free Survival (FFS)

    Baseline to when the last participant reached Cycle 7 Day 1 (each cycle was comprised of 4 weeks)

  • Rate of FFS at Study Completion

    From Baseline to Last Participant Last Visit (LPLV) (approximately 5 years)

  • Best Overall Response (BOR) at Cycle 7 Day 1

    up to Cycle 7 Day 1 (each cycle was comprised of 4 weeks)

  • BOR During Cross-over Treatment With Ruxolitinib

    from Crossover Cycle 1 Day 1 to any time point up to and including Crossover Cycle 7 Day 1 (each cycle was comprised of 4 weeks)

  • +18 more secondary outcomes

Study Arms (2)

Ruxolitinib

EXPERIMENTAL

Ruxolitinib for the treatment period and extension period.

Drug: Ruxolitinib

Best Available Therapy

ACTIVE COMPARATOR

Best available therapy for the treatment period and extension period, with optional crossover to ruxolitinib after Cycle 6.

Drug: Extracorporeal photopheresis (ECP)Drug: Low-dose methotrexate (MTX)Drug: Mycophenolate mofetil (MMF)Drug: mechanistic Target of Rapamycin (mTOR) inhibitors (everolimus or sirolimus)Drug: InfliximabDrug: RituximabDrug: PentostatinDrug: ImatinibDrug: Ibrutinib

Interventions

Ruxolitinib twice daily at the protocol-defined starting dose.

Also known as: Jakafi, INCB018424
Ruxolitinib

Best available therapy (BAT) will be selected by the investigator for each participant. BAT may not include experimental agents (ie, those not approved for the treatment of any indication) as well as a limited number of other selected drugs in accordance with the protocol-defined requirements. The BAT in this study will be among the following treatments currently used in this setting (no other types or combinations of BATs are permitted in this study).

Best Available Therapy

Patients will receive BAT based on the Investigator's opinion, taking into account the manufacturer's instructions, labeling, subject's medical condition, and institutional guidelines for any dose adjustment.

Best Available Therapy

Patients will receive BAT based on the Investigator's opinion, taking into account the manufacturer's instructions, labeling, subject's medical condition, and institutional guidelines for any dose adjustment.

Best Available Therapy

Patients will receive BAT based on the Investigator's opinion, taking into account the manufacturer's instructions, labeling, subject's medical condition, and institutional guidelines for any dose adjustment.

Best Available Therapy

Patients will receive BAT based on the Investigator's opinion, taking into account the manufacturer's instructions, labeling, subject's medical condition, and institutional guidelines for any dose adjustment.

Best Available Therapy

Patients will receive BAT based on the Investigator's opinion, taking into account the manufacturer's instructions, labeling, subject's medical condition, and institutional guidelines for any dose adjustment.

Best Available Therapy

Patients will receive BAT based on the Investigator's opinion, taking into account the manufacturer's instructions, labeling, subject's medical condition, and institutional guidelines for any dose adjustment.

Best Available Therapy

Patients will receive BAT based on the Investigator's opinion, taking into account the manufacturer's instructions, labeling, subject's medical condition, and institutional guidelines for any dose adjustment.

Best Available Therapy

Patients will receive BAT based on the Investigator's opinion, taking into account the manufacturer's instructions, labeling, subject's medical condition, and institutional guidelines for any dose adjustment.

Best Available Therapy

Eligibility Criteria

Age12 Years+
Sexall
Healthy VolunteersNo
Age GroupsChild (0-17), Adult (18-64), Older Adult (65+)

You may qualify if:

  • Have undergone allogeneic stem cell transplantation (alloSCT) from any donor source (matched unrelated donor, sibling, haplo-identical) using bone marrow, peripheral blood stem cells, or cord blood. Recipients of non-myeloablative, myeloablative, and reduced intensity conditioning are eligible
  • Evident myeloid and platelet engraftment: Absolute neutrophil count (ANC) \> 1000/mm\^3 and platelet count \> 25,000/ mm\^3
  • Participants with clinically diagnosed moderate to severe cGvHD according to NIH Consensus Criteria prior to randomization:
  • Moderate cGvHD: At least one organ (not lung) with a score of 2, 3 or more organs involved with a score of 1 in each organ, or lung score of 1
  • Severe cGvHD: at least 1 organ with a score of 3, or lung score of 2 or 3
  • Participants currently receiving systemic or topical corticosteroids for the treatment of cGvHD for a duration of \< 12 months prior to Cycle 1 Day 1 (if applicable), and have a confirmed diagnosis of steroid-refractory cGvHD defined per 2014 NIH consensus criteria irrespective of the concomitant use of a calcineurin inhibitor (CNI), as follows:
  • A lack of response or disease progression after administration of minimum prednisone 1 mg/kg/day for at least 1 week, OR
  • Disease persistence without improvement despite continued treatment with prednisone at \> 0.5 mg/kg/day or 1 mg/kg/every other day for at least 4 weeks, OR
  • Increase to prednisolone dose to \> 0.25 mg/kg/day after 2 unsuccessful attempts to taper the dose
  • Participant must accept to be treated with only one of the following BAT options on Cycle 1 Day 1 (additions and changes are allowed during the course of the study, but only with BAT from the following BAT options): extracorporeal photopheresis (ECP), low-dose methotrexate (MTX), mycophenolate mofetil (MMF), mTOR inhibitors (everolimus or sirolimus), infliximab, rituximab, pentostatin, imatinib, ibrutinib

You may not qualify if:

  • Participants who have received 2 or more systemic treatment for cGvHD in addition to corticosteroids ± CNI for cGvHD
  • Patients that transition from active aGvHD to cGvHD without tapering off corticosteroids ± CNI and any systemic treatment
  • \* Patients receiving up to 30 mg by mouth once a day of hydrocortisone (i.e., physiologic replacement dose) of corticosteroids are allowed.
  • Participants who were treated with prior JAK inhibitors for aGvHD; except when the participant achieved complete or partial response and has been off JAK inhibitor treatment for at least 8 weeks prior to Cycle 1 Day 1
  • Failed prior alloSCT within the past 6 months from Cycle 1 Day 1
  • Participants with relapsed primary malignancy, or who have been treated for relapse after the alloSCT was performed
  • Steroid refractory cGvHD occurring after a non-scheduled donor lymphocyte infusion (DLI) administered for preemptive treatment of malignancy recurrence. Participants who have received a scheduled DLI as part of their transplant procedure and not for management of malignancy relapse are eligible
  • Any corticosteroid therapy for indications other than cGvHD at doses \> 1 mg/kg/day methylprednisolone or equivalent within 7 days of Cycle 1 Day 1

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (191)

Incyte Investigative Site

Tucson, Arizona, 85724, United States

Location

Incyte Investigative Site

Duarte, California, 31010, United States

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Incyte Investigative Site

La Jolla, California, 92093-0987, United States

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Incyte Investigative Site

Los Angeles, California, 90033, United States

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Incyte Investigative Site

New Haven, Connecticut, 06510, United States

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Incyte Investigative Site

Wilmington, Delaware, 19803, United States

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Incyte Investigative Site

Gainesville, Florida, 32610, United States

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Incyte Investigative Site

Tampa, Florida, 33612, United States

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Incyte Investigative Site

Chicago, Illinois, 60611, United States

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Incyte Investigative Site

Chicago, Illinois, 60612, United States

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Incyte Investigative Site

Chicago, Illinois, 60637, United States

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Incyte Investigative Site

Maywood, Illinois, 60153, United States

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Incyte Investigative Site

Indianapolis, Indiana, 46237, United States

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Incyte Investigative Site

Westwood, Kansas, 66205, United States

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Incyte Investigative Site

Lexington, Kentucky, 40536, United States

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Incyte Investigative Site

Boston, Massachusetts, 02114, United States

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Incyte Investigative Site

Boston, Massachusetts, 02215, United States

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Incyte Investigative Site

Omaha, Nebraska, 68198-7680, United States

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Incyte Investigative Site

Hackensack, New Jersey, 07601, United States

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Incyte Investigative Site

New York, New York, 10021, United States

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Incyte Investigative Site

New York, New York, 10032, United States

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Incyte Investigative Site

New York, New York, 11040, United States

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Incyte Investigative Site

Chapel Hill, North Carolina, 27599, United States

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Incyte Investigative Site

Durham, North Carolina, 27710, United States

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Incyte Investigative Site

Winston-Salem, North Carolina, 27157, United States

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Incyte Investigative Site

Cincinnati, Ohio, 45242, United States

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Incyte Investigative Site

Cleveland, Ohio, 44106-5048, United States

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Incyte Investigative Site

Cleveland, Ohio, 44195, United States

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Incyte Investigative Site

Columbus, Ohio, 43210, United States

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Incyte Investigative Site

Oklahoma City, Oklahoma, 73104, United States

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Incyte Investigative Site

Philadelphia, Pennsylvania, 19104, United States

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Incyte Investigative Site

Pittsburgh, Pennsylvania, 15224, United States

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Incyte Investigative Site

Pittsburgh, Pennsylvania, 15232, United States

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Incyte Investigative Site

Nashville, Tennessee, 37232, United States

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Incyte Investigative Site

Dallas, Texas, 75390, United States

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Incyte Investigative Site

Houston, Texas, 77030, United States

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Incyte Investigative Site

Seattle, Washington, 98109, United States

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Incyte Investigative Site

Milwaukee, Wisconsin, 53226, United States

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Novartis Investigative Site

Darlinghurst, New South Wales, 2010, Australia

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Novartis Investigative Site

Parkville, Victoria, 3002, Australia

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Novartis Investigative Site

Innsbruck, Tyrol, 6020, Austria

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Novartis Investigative Site

Graz, 8036, Austria

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Novartis Investigative Site

Linz, A-4010, Austria

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Novartis Investigative Site

Vienna, A-1090, Austria

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Novartis Investigative Site

Antwerp, 2060, Belgium

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Novartis Investigative Site

Bruges, 8000, Belgium

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Novartis Investigative Site

Brussels, 1200, Belgium

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Novartis Investigative Site

Ghent, 9000, Belgium

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Novartis Investigative Site

Leuven, 3000, Belgium

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Novartis Investigative Site

Liège, 4000, Belgium

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Novartis Investigative Site

Sofia, 1527, Bulgaria

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Novartis Investigative Site

Sofia, 1756, Bulgaria

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Novartis Investigative Site

Vancouver, British Columbia, V5Z 1M9, Canada

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Novartis Investigative Site

Hamilton, Ontario, L8V 5C2, Canada

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Novartis Investigative Site

Ottawa, Ontario, K1H 8L6, Canada

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Novartis Investigative Site

Toronto, Ontario, M5G 2M9, Canada

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Novartis Investigative Site

Prague, Czech Republic, 128 20, Czechia

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Novartis Investigative Site

Hradec Králové, CZE, 500 05, Czechia

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Novartis Investigative Site

Prague, 150 06, Czechia

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Novartis Investigative Site

Copenhagen, DK-2100, Denmark

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Novartis Investigative Site

Odense, DK 5000, Denmark

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Novartis Investigative Site

Bordeaux, Aquitaine, 33076, France

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Novartis Investigative Site

Amiens Cedex1, 80054, France

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Novartis Investigative Site

Caen, 14033, France

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Novartis Investigative Site

Lille, 59037, France

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Novartis Investigative Site

Limoges, 87042, France

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Novartis Investigative Site

Lyon, 69373, France

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Novartis Investigative Site

Montpellier, 34295, France

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Novartis Investigative Site

Paris, 75475, France

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Novartis Investigative Site

Paris, 75571, France

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Novartis Investigative Site

Paris, 75935, France

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Novartis Investigative Site

Pierre-Benite Cédex, 69495, France

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Novartis Investigative Site

Rennes, 35033, France

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Novartis Investigative Site

Rouen, 76038, France

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Novartis Investigative Site

Saint-Priest-en-Jarez, 42271, France

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Novartis Investigative Site

Strasbourg, 67098, France

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Novartis Investigative Site

Toulouse, 31059, France

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Novartis Investigative Site

Vandœuvre-lès-Nancy, 54511, France

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Novartis Investigative Site

Mannheim, Baden-Wurttemberg, 68167, Germany

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Novartis Investigative Site

Augsburg, 86156, Germany

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Novartis Investigative Site

Berlin, 13125, Germany

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Novartis Investigative Site

Cologne, 50937, Germany

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Novartis Investigative Site

Dresden, 01307, Germany

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Novartis Investigative Site

Düsseldorf, 40225, Germany

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Novartis Investigative Site

Erlangen, 91054, Germany

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Novartis Investigative Site

Essen, 45147, Germany

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Novartis Investigative Site

Frankfurt, 60590, Germany

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Novartis Investigative Site

Freiburg im Breisgau, 79106, Germany

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Novartis Investigative Site

Hamburg, 20099, Germany

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Novartis Investigative Site

Hamburg, 20246, Germany

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Novartis Investigative Site

Jena, 07747, Germany

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Novartis Investigative Site

Kiel, 24105, Germany

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Novartis Investigative Site

Leipzig, 04103, Germany

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Novartis Investigative Site

Mainz, 55131, Germany

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Novartis Investigative Site

Mannheim, 68167, Germany

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Novartis Investigative Site

Münster, 48149, Germany

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Novartis Investigative Site

Ulm, Germany

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Novartis Investigative Site

Würzburg, 97080, Germany

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Novartis Investigative Site

Athens, GR, Greece

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Novartis Investigative Site

Pátrai, GR, 265 00, Greece

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Novartis Investigative Site

Thessaloniki, GR, Greece

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Novartis Investigative Site

Athens, Greece

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Novartis Investigative Site

Budapest, 1097, Hungary

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Novartis Investigative Site

Navi Mumbai, Maharashtra, 410210, India

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Novartis Investigative Site

Pune, Maharashtra, 411004, India

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Novartis Investigative Site

Delhi, 110 085, India

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Novartis Investigative Site

Vellore, 632004, India

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Novartis Investigative Site

Haifa, 31096, Israel

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Novartis Investigative Site

Jerusalem, 91120, Israel

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Novartis Investigative Site

Petah Tikva, 49100, Israel

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Novartis Investigative Site

Tel Aviv, 64239, Israel

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Novartis Investigative Site

Ancona, AN, 60126, Italy

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Novartis Investigative Site

Bergamo, BG, 24127, Italy

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Novartis Investigative Site

Bologna, BO, 40138, Italy

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Novartis Investigative Site

Brescia, BS, 25123, Italy

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Novartis Investigative Site

Genova, GE, 16132, Italy

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Novartis Investigative Site

Genova, GE, 16147, Italy

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Novartis Investigative Site

Milan, MI, 20132, Italy

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Novartis Investigative Site

Milan, MI, 20133, Italy

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Novartis Investigative Site

Rozzano, MI, 20089, Italy

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Novartis Investigative Site

Palermo, PA, 90146, Italy

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Novartis Investigative Site

Pescara, PE, 65124, Italy

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Novartis Investigative Site

Parma, PR, 43100, Italy

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Novartis Investigative Site

Pavia, PV, 27100, Italy

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Novartis Investigative Site

Roma, RM, 00133, Italy

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Novartis Investigative Site

Roma, RM, 00165, Italy

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Novartis Investigative Site

Roma, RM, 00168, Italy

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Novartis Investigative Site

Torino, TO, 10126, Italy

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Novartis Investigative Site

Udine, UD, 33100, Italy

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Novartis Investigative Site

Perugia, 06132, Italy

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Novartis Investigative Site

Nagoya, Aichi-ken, 453-8511, Japan

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Novartis Investigative Site

Fukuoka, Fukuoka, 812-8582, Japan

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Novartis Investigative Site

Sapporo, Hokkaido, 060-8648, Japan

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Novartis Investigative Site

Kobe, Hyōgo, 650-0047, Japan

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Novartis Investigative Site

Nishinomiya, Hyōgo, 663 8501, Japan

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Novartis Investigative Site

Isehara, Kanagawa, 259-1193, Japan

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Novartis Investigative Site

Sendai, Miyagi, 980-8574, Japan

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Novartis Investigative Site

Osaka, Osaka, 545-8586, Japan

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Novartis Investigative Site

Suita, Osaka, 565-0871, Japan

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Novartis Investigative Site

Shimotsuke, Tochigi, 329-0498, Japan

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Novartis Investigative Site

Bunkyō-ku, Tokyo, 113-8677, Japan

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Novartis Investigative Site

Minato-ku, Tokyo, 105-8470, Japan

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Novartis Investigative Site

Shinjuku-ku, Tokyo, 160-8582, Japan

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Novartis Investigative Site

Kyoto, 606-8507, Japan

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Novartis Investigative Site

Okayama, 700-8558, Japan

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Novartis Investigative Site

Amman, 11941, Jordan

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Novartis Investigative Site

Utrecht, The Netherlands, 3508 GA, Netherlands

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Novartis Investigative Site

Leiden, 2333 ZA, Netherlands

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Novartis Investigative Site

Nijmegen, 6525 GA, Netherlands

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Novartis Investigative Site

Rotterdam, 3015 CE, Netherlands

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Novartis Investigative Site

Oslo, 0424, Norway

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Novartis Investigative Site

Wroclaw, Lower Silesian Voivodeship, Poland

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Novartis Investigative Site

Gliwice, Silesian Voivodeship, Poland

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Novartis Investigative Site

Katowice, Poland

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Novartis Investigative Site

Krakow, Poland

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Novartis Investigative Site

Warsaw, Poland

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Novartis Investigational Site

Lisbon, Portugal

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Novartis Investigative Site

Porto, Portugal

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Incyte Investigative Site

Ponce, 11040, Puerto Rico

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Novartis Investigational Site

Bucharest, 022328, Romania

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Novartis Investigational Site

Bucharest, Romania

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Novartis Investigative Site

Moscow, 125167, Russia

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Novartis Investigative Site

Saint Petersburg, 197022, Russia

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Novartis Investigative Site

Riyadh, 11211, Saudi Arabia

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Novartis Investigative Site

Seoul, 03080, South Korea

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Novartis Investigative Site

Seoul, 06351, South Korea

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Novartis Investigative Site

Córdoba, Andalusia, 14004, Spain

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Novartis Investigative Site

Seville, Andalusia, 41013, Spain

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Novartis Investigative Site

Donostia / San Sebastian, Basque Country, 20080, Spain

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Novartis Investigative Site

Salamanca, Castille and León, 37007, Spain

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Novartis Investigative Site

Barcelona, Catalonia, 08026, Spain

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Novartis Investigative Site

Barcelona, Catalonia, 08035, Spain

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Novartis Investigative Site

L'Hospitalet de Llobregat, Catalonia, 08907, Spain

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Novartis Investigative Site

Santiago de Compostela, Galicia, 15706, Spain

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Novartis Investigative Site

El Palmar, Murica, Spain

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Novartis Investigative Site

Valencia, Valencia, 46010, Spain

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Novartis Investigative Site

Barcelona, 08026, Spain

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Novartis Investigative Site

Las Palmas de Gran Canaria, 35012, Spain

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Novartis Investigative Site

Madrid, 28006, Spain

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Novartis Investigative Site

Madrid, 28041, Spain

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Novartis Investigative Site

Gothenburg, SE-413 45, Sweden

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Novartis Investigative Site

Uppsala, SE-751 85, Sweden

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Novartis Investigative Site

Basel, 4031, Switzerland

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Novartis Investigative Site

Zurich, 8091, Switzerland

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Novartis Investigative Site

Ankara, 06100, Turkey (Türkiye)

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Novartis Investigative Site

Ankara, 06460, Turkey (Türkiye)

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Novartis Investigative Site

Antalya, 07100, Turkey (Türkiye)

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Novartis Investigative Site

Glasgow, G51 4TF, United Kingdom

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Novartis Investigative Site

London, NW1 2PQ, United Kingdom

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Novartis Investigative Site

London, SE5 9RS, United Kingdom

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Novartis Investigative Site

Manchester, M13 9WL, United Kingdom

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Related Publications (5)

  • Zeiser R, Russo D, Ram R, Hashmi SK, Chakraverty R, Middeke JM, Musso M, Giebel S, Uzay A, Langmuir P, Hamad N, Burock K, Gowda M, Stefanelli T, Lee SJ, Teshima T, Locatelli F. Ruxolitinib in Patients With Corticosteroid-Refractory or Corticosteroid-Dependent Chronic Graft-Versus-Host Disease: 3-Year Final Analysis of the Phase III REACH3 Study. J Clin Oncol. 2025 Aug 10;43(23):2566-2571. doi: 10.1200/JCO-24-02477. Epub 2025 Jun 25.

  • Mahmoudjafari Z, Kintsch E, Xue Z, Bhatt V, Galvin J, Locatelli F, Zeiser R. Impact of concomitant azoles on ruxolitinib treatment in patients with GVHD: post hoc analyses of REACH2 and REACH3. Blood Adv. 2025 Aug 26;9(16):4206-4216. doi: 10.1182/bloodadvances.2025016212.

  • Le RQ, Wang X, Zhang H, Li H, Przepiorka D, Vallejo J, Leong R, Ma L, Goldberg KB, Pazdur R, Theoret MR, De Claro A. FDA Approval Summary: Ruxolitinib for Treatment of Chronic Graft-Versus-Host Disease after Failure of One or Two Lines of Systemic Therapy. Oncologist. 2022 Jun 8;27(6):493-500. doi: 10.1093/oncolo/oyac042.

  • Zeiser R, Polverelli N, Ram R, Hashmi SK, Chakraverty R, Middeke JM, Musso M, Giebel S, Uzay A, Langmuir P, Hollaender N, Gowda M, Stefanelli T, Lee SJ, Teshima T, Locatelli F; REACH3 Investigators. Ruxolitinib for Glucocorticoid-Refractory Chronic Graft-versus-Host Disease. N Engl J Med. 2021 Jul 15;385(3):228-238. doi: 10.1056/NEJMoa2033122.

  • Jagasia M, Zeiser R, Arbushites M, Delaite P, Gadbaw B, Bubnoff NV. Ruxolitinib for the treatment of patients with steroid-refractory GVHD: an introduction to the REACH trials. Immunotherapy. 2018 Apr;10(5):391-402. doi: 10.2217/imt-2017-0156. Epub 2018 Jan 10.

MeSH Terms

Conditions

Graft vs Host DiseaseBronchiolitis Obliterans Syndrome

Interventions

ruxolitinibPhotopheresisMethotrexateMycophenolic AcidProto-Oncogene Proteins c-rafEverolimusSirolimusInfliximabRituximabPentostatinImatinib Mesylateibrutinib

Condition Hierarchy (Ancestors)

Immune System DiseasesOrganizing PneumoniaBronchiolitis ObliteransBronchiolitisBronchitisBronchial DiseasesRespiratory Tract DiseasesLung Diseases, ObstructiveLung Diseases

Intervention Hierarchy (Ancestors)

PUVA TherapyUltraviolet TherapyPhototherapyTherapeuticsExtracorporeal CirculationSurgical Procedures, OperativeAminopterinPterinsPteridinesHeterocyclic Compounds, 2-RingHeterocyclic Compounds, Fused-RingHeterocyclic CompoundsCaproatesAcids, AcyclicCarboxylic AcidsOrganic ChemicalsFatty AcidsLipidsraf KinasesMAP Kinase Kinase KinasesProtein Serine-Threonine KinasesProtein KinasesPhosphotransferases (Alcohol Group Acceptor)PhosphotransferasesTransferasesEnzymesEnzymes and CoenzymesIntracellular Signaling Peptides and ProteinsProteinsAmino Acids, Peptides, and ProteinsProto-Oncogene ProteinsOncogene ProteinsNeoplasm ProteinsMacrolidesLactonesAntibodies, MonoclonalAntibodiesImmunoglobulinsImmunoproteinsBlood ProteinsSerum GlobulinsGlobulinsAntibodies, Monoclonal, Murine-DerivedCoformycinFormycinsPyrimidine NucleosidesPyrimidinesHeterocyclic Compounds, 1-RingDeoxyribonucleosidesNucleosidesNucleic Acids, Nucleotides, and NucleosidesBenzamidesAmidesBenzoatesAcids, CarbocyclicBenzene DerivativesHydrocarbons, AromaticHydrocarbons, CyclicHydrocarbonsPiperazines

Results Point of Contact

Title
Incyte Corporation
Organization
Call Center

Study Officials

  • Rodica Morariu-Zamfir

    Incyte Corporation

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR
Expanded Access
Yes

Study Record Dates

First Submitted

April 4, 2017

First Posted

April 13, 2017

Study Start

June 29, 2017

Primary Completion

May 8, 2020

Study Completion

December 15, 2022

Last Updated

August 12, 2025

Results First Posted

April 15, 2022

Record last verified: 2025-08

Data Sharing

IPD Sharing
Will not share

Locations