NCT03139604

Brief Summary

The purpose of this study is to evaluate itacitinib or placebo in combination with corticosteroids as first-line treatment of participants with Grade II to IV acute graft-versus-host disease (aGVHD).

Trial Health

98
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Strong global presence with extensive site network
Enrollment
439

participants targeted

Target at P50-P75 for phase_3

Timeline
Completed

Started Jul 2017

Typical duration for phase_3

Geographic Reach
18 countries

128 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

May 2, 2017

Completed
2 days until next milestone

First Posted

Study publicly available on registry

May 4, 2017

Completed
3 months until next milestone

Study Start

First participant enrolled

July 19, 2017

Completed
1.8 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

May 2, 2019

Completed
1 year until next milestone

Results Posted

Study results publicly available

May 15, 2020

Completed
2 months until next milestone

Study Completion

Last participant's last visit for all outcomes

July 13, 2020

Completed
Last Updated

September 2, 2025

Status Verified

August 1, 2025

Enrollment Period

1.8 years

First QC Date

May 2, 2017

Results QC Date

May 1, 2020

Last Update Submit

August 28, 2025

Conditions

Keywords

Acute graft-versus-host diseaseJanus kinase (JAK) inhibitoritacitinibcorticosteroidsallogeneic hematopoietic stem cell transplant (allo-HSCT)

Outcome Measures

Primary Outcomes (1)

  • Overall Response Rate Based on Center for International Blood and Marrow Transplant Research (CIBMTR) Response Index

    Defined as the percentage of participants demonstrating a complete response (CR), very good partial response (VGPR), or partial response (PR).

    Day 28

Secondary Outcomes (19)

  • Nonrelapse Mortality

    Month 6,9,12 and 24

  • Duration of Response

    Baseline through 30-35 days after end of treatment, total particpation expected to average 24 months

  • Cmax of Itacitinib When Administered in Combination With Corticosteroids

    Protocol-defined timepoints up to Day 28

  • Cmin of Itacitinib When Administered in Combination With Corticosteroids

    Protocol-defined timepoints up to Day 28

  • Tmax of Itacitinib When Administered in Combination With Corticosteroids

    Protocol-defined timepoints up to Day 28

  • +14 more secondary outcomes

Study Arms (2)

Itacitinib

EXPERIMENTAL

Itacitinib plus corticosteroids

Drug: ItacitinibDrug: PrednisoneDrug: Methylprednisolone

Placebo

PLACEBO COMPARATOR

Matching placebo plus corticosteroids

Drug: PlaceboDrug: PrednisoneDrug: Methylprednisolone

Interventions

Itacitinib at the protocol-defined dose administered orally once daily (QD) plus corticosteroids.

Also known as: INCB039110
Itacitinib

Matching placebo tablets administered orally once daily (QD) plus corticosteroids.

Placebo

Oral prednisone may be used to begin standard corticosteroid background treatment at the investigator's discretion, at a dose equivalent to methylprednisolone 2 mg/kg per day.

Also known as: Deltasone, Prednicot, predniSONE Intensol, Rayos, Sterapred, Sterapred DS
ItacitinibPlacebo

Methylprednisolone 2 mg/kg IV daily (or prednisone equivalent) or at a dose appropriate for the severity of disease as background treatment.

Also known as: Medrol, Medrol Dosepak, Solu-Medrol
ItacitinibPlacebo

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Has undergone 1 allo-HSCT from any donor (related or unrelated with any degree of HLA matching) and any donor source (bone marrow, peripheral blood stem cells, or cord blood) for a hematologic malignancy or disorder. Recipients of myeloablative and reduced-intensity conditioning regimens are eligible.
  • Clinically suspected Grade II to IV aGVHD as per MAGIC criteria, occurring after allo-HSCT and any GVHD prophylaxis regimen.
  • Evidence of myeloid engraftment. Use of growth factor supplementation is allowed.
  • Serum creatinine ≤ 2.0 mg/dL or creatinine clearance ≥ 40 mL/min measured or calculated by Cockroft Gault equation.
  • Willing to avoid pregnancy or fathering children.
  • Able to give written informed consent and comply with all study visits and procedures.
  • Able to swallow and retain oral medication.

You may not qualify if:

  • Has received more than 1 allo-HSCT.
  • Has received more than 2 days of systemic corticosteroids for aGVHD.
  • Presence of GVHD overlap syndrome.
  • Presence of an active uncontrolled infection.
  • Known human immunodeficiency virus infection.
  • Active hepatitis B virus (HBV) or hepatitis C virus infection that requires treatment or at risk for HBV reactivation.
  • Participants with evidence of relapsed primary disease, or participants who have been treated for relapse after the allo-HSCT was performed.
  • Any corticosteroid therapy for indications other than GVHD at doses \> 1 mg/kg per day methylprednisolone (or prednisone equivalent) within 7 days of randomization.
  • Severe organ dysfunction unrelated to underlying GVHD, including:
  • Cholestatic disorders or unresolved veno-occlusive disease of the liver.
  • Clinically significant or uncontrolled cardiac disease.
  • Clinically significant respiratory disease that requires mechanical ventilation support or 50% oxygen.
  • Currently breast feeding.
  • Received JAK inhibitor therapy after allo-HSCT for any indication. Treatment with a JAK inhibitor before allo-HSCT is permitted.
  • Treatment with any other investigational agent, device, or procedure within 21 days (or 5 half-lives, whichever is greater) of enrollment.
  • +2 more criteria

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (129)

University of California, San Diego (UCSD) - Moores Cancer Center

La Jolla, California, 92093-0698, United States

Location

University of Southern California

Los Angeles, California, 90033, United States

Location

University of California, Los Angeles (UCLA) - Medical Center

Los Angeles, California, 90095-1678, United States

Location

Stanford Cancer Center

Stanford, California, 94305, United States

Location

University of Colorado - Aurora Cancer Center

Aurora, Colorado, 80045, United States

Location

University of Florida (UF) - Division of Hematology & Oncology

Gainesville, Florida, 32610, United States

Location

University of Miami - Sylvester Cancer Center

Miami, Florida, 33136, United States

Location

Florida Hospital Cancer Institute

Orlando, Florida, 32804, United States

Location

University of Illinois at Chicago

Chicago, Illinois, 60612, United States

Location

University of Chicago

Chicago, Illinois, 60637, United States

Location

Advocate Lutheran General Hospital - Oncology Specialists SC

Park Ridge, Illinois, 60028, United States

Location

Indiana University (IU) Melvin and Bren Simon Cancer Center

Indianapolis, Indiana, 46202, United States

Location

Indiana Blood and Marrow Transplant

Indianapolis, Indiana, 46237, United States

Location

University of Iowa

Iowa City, Iowa, 52242, United States

Location

University of Kansas Cancer Center

Westwood, Kansas, 66205, United States

Location

Tulane University Medical Center

New Orleans, Louisiana, 70112, United States

Location

University of Maryland Medical Center

Baltimore, Maryland, 21201, United States

Location

Tufts Medical Center

Boston, Massachusetts, 02111, United States

Location

Massachusetts General Hospital

Boston, Massachusetts, 02114, United States

Location

Beth Israel Deaconess Medical Center

Boston, Massachusetts, 02215, United States

Location

Dana Farber Cancer Institute

Boston, Massachusetts, 02215, United States

Location

University of Michigan

Ann Arbor, Michigan, 48109, United States

Location

Henry Ford Hospital

Detroit, Michigan, 48202, United States

Location

Spectrum Health

Grand Rapids, Michigan, 49503, United States

Location

University of Mississippi Medical Center

Jackson, Mississippi, 39216, United States

Location

Washington University School of Medicine

St Louis, Missouri, 63110, United States

Location

University of Nebraska Medical Center

Omaha, Nebraska, 68198-7680, United States

Location

Dartmouth Hitchcock Medical Center

Lebanon, New Hampshire, 03756, United States

Location

John Theurer Cancer Center At Hackensack UMC

Hackensack, New Jersey, 07601, United States

Location

Rutgers Cancer Institute of New Jersey

New Brunswick, New Jersey, 08903-2681, United States

Location

Northwell Health

Lake Success, New York, 11042, United States

Location

Columbia University

New York, New York, 10032, United States

Location

Memorial Sloan Kettering Cancer Center

New York, New York, 10065, United States

Location

Stony Brook University Medical Center

Stony Brook, New York, 11794, United States

Location

Levine Cancer Institute

Charlotte, North Carolina, 28204, United States

Location

Wake Forest Baptist Medical Center - Wake Forest University School of Medicine

Winston-Salem, North Carolina, 27157, United States

Location

Oncology Hematology in Cincinnati

Cincinnati, Ohio, 45236, United States

Location

University Hospitals Cleveland Medical Center

Cleveland, Ohio, 44106, United States

Location

The Ohio State University (OSU)

Columbus, Ohio, 43210, United States

Location

University of Oklahoma - Health Sciences Center

Oklahoma City, Oklahoma, 73104, United States

Location

Oregon Health & Science University (OHSU)

Portland, Oregon, 97239-3098, United States

Location

Thomas Jefferson University

Philadelphia, Pennsylvania, 19107, United States

Location

University of Pittsburgh Medical Center (UPMC) - Hillman Cancer Center

Pittsburgh, Pennsylvania, 15232, United States

Location

Greenville Health System

Greenville, South Carolina, 29615, United States

Location

Methodist Healthcare Foundation

Memphis, Tennessee, 38104, United States

Location

Sarah Cannon Research Institute, LLC (SCRI)

Nashville, Tennessee, 37203, United States

Location

Vanderbilt University Medical Center

Nashville, Tennessee, 37232, United States

Location

Texas Transplant Institute

San Antonio, Texas, 78229, United States

Location

University of Virginia Medical Center

Charlottesville, Virginia, 22908, United States

Location

St Vincents Hospital Sydney Limited

Darlinghurst, NSW 2010, Australia

Location

Ordensklinikum Linz GmbH Elisabethinen

Linz, 4020, Austria

Location

ZNA Stuivenberg

Antwerp, 2060, Belgium

Location

General Hospital Sint-Jan Brugge-Oostend

Bruges, 8000, Belgium

Location

Institut Jules Bordet

Brussels, 1000, Belgium

Location

Cliniques Universitaires Saint-Luc

Brussels, 1200, Belgium

Location

Universitair Ziekenhuis Gent (UZG)

Ghent, 9000, Belgium

Location

Jessa Ziekenhuis

Hasselt, 3500, Belgium

Location

Hopital universitaire du Sart Tilman de Liege

Liège, 4000, Belgium

Location

AZ Delta

Roeselare, 8800, Belgium

Location

UHKT Prague - Institute of Hematology and Blood Transfusion

Prague, 128 20, Czechia

Location

Helsinki University Central Hospital

Helsinki, 00290, Finland

Location

CHU Amiens Picardie - Hopital Sud

Amiens, 80054, France

Location

CHRU de Lille-Hopital Claude Huriez

Lille, 59037, France

Location

Hotel Dieu Hospital - Hematologie

Nantes, 44000, France

Location

Hopital Saint Louis

Paris, 75010, France

Location

Hopital Haut Leveque - CHU Bordeaux - Maladies du sang

Pessac, 33604, France

Location

Hopital de Hautepierre

Strasbourg, 67098, France

Location

Institut Claudius Regaud-Universitaire du Cancer Toulouse Oncopol

Toulouse, 31059, France

Location

CHU de Nancy

Vandœuvre-lès-Nancy, 54500, France

Location

Universitaet zu Koln - Universitaetsklinikum Koeln (Uniklinik Koeln)

Cologne, 50924, Germany

Location

University Clinic Carl Gustav Carus, Technical University Dresden

Dresden, 1307, Germany

Location

Universitatsklinikum Freiburg - Klinik fur Innere Medizin I

Freiburg im Breisgau, 79106, Germany

Location

Universitatsklinikum Hamburg - Eppendorf

Hamburg, 20246, Germany

Location

Universitaetsklinikum Leipzig

Leipzig, 4103, Germany

Location

Universitaetsmedizin der Johannes Gutenberg

Mainz, 55131, Germany

Location

UKGM Marburg Innere Medizin: Haematologie Onkolog

Marburg, 35043, Germany

Location

General Hospital of Thessaloniki G. Papanikolaou - Hematology Department

Chortiatis, 57010, Greece

Location

Rambam Health Care Campus

Haifa, 3109601, Israel

Location

Hadassah Hebrew University Medical Center Ein Karem

Jerusalem, 9112001, Israel

Location

Chaim Sheba Medical Center

Ramat Gan, 5262160, Israel

Location

Tel Aviv Sourasky Medical Center

Tel Aviv, 6423906, Israel

Location

Azienda Socio Sanitaria Territoriale Papa Giovanni XXIII

Bergamo, 24127, Italy

Location

C.T.M.O. Ospedale Roberto Binaghi ATS Cagliari

Cagliari, 09126, Italy

Location

Azienda Ospedaliero Universitaria (AOU) Policlinico - Vittorio Emanuele - Presidio Ospedaliero Ferrarotto Alessi

Catania, 95124, Italy

Location

Azienda Ospedaliero Universitaria Careggi

Florence, 50134, Italy

Location

Fondazione IRCCS Ca Granda Ospedale Maggiore Policlinico di Milano

Milan, 20122, Italy

Location

IRCCS Ospedale San Raffaele

Milan, 20132, Italy

Location

ASST Grande Ospedale Metropolitano Niguarda

Milan, 20162, Italy

Location

Clinica Ematologica CTA, Ospedale "San Gerardo" di Monza

Monza, 20900, Italy

Location

Casa di Cura La Maddalena

Palermo, 90146, Italy

Location

Fondazione IRCCS Policlinco San Matteo

Pavia, 27100, Italy

Location

Presidio Ospedaliero Pescara

Pescara, 65124, Italy

Location

Azienda Ospedaliera Bianchi-Melacrino-Morelli Ospedali Riuniti

Reggio Calabria, 89124, Italy

Location

Azienda Unità Sanitaria Locale di Reggio Emilia

Reggio Emilia, 42123, Italy

Location

University of Rome La Sapienza

Roma, 00161, Italy

Location

Istituto Clinico Humanitas

Rozzano, 20089, Italy

Location

A.O.U. Città della Salute e della Scienza di Torino

Torino, 10126, Italy

Location

SOC Clinica Ematologica, Azienda Ospediero-Universitaria di Udine

Udine, 33100, Italy

Location

Auckland District Health Board

Auckland, 1023, New Zealand

Location

Centrum Onkologii- Instytut w Gliwicach

Gliwice, 44-101, Poland

Location

Klinika Transplantacji Komorek Krwiotworczych - Instytut Hematologii i Transfuzjologii

Warsaw, 02-776, Poland

Location

Instituto Portugues de Oncologia de Lisboa Francisco Gentil EPE (IPO-Lisboa)

Lisbon, 1099-023, Portugal

Location

Centro Hospitalar Lisboa Norte - Hospital de Santa Maria

Lisbon, 1649-035, Portugal

Location

Instituto Portugues de Oncologia do Porto Francisco Gentil, EPE

Porto, 4200-072, Portugal

Location

Seoul National University Hospital

Seoul, 3080, South Korea

Location

Hospital de la Santa Creu i Sant Pau - Servei de Hematologia Clinica

Barcelona, 08025, Spain

Location

Hospital Universitario Vall d'Hebron

Barcelona, 08035, Spain

Location

Hospital Clinic i Provincial de Barcelona

Barcelona, 08036, Spain

Location

Instituto Catalan de Oncologia - Hospital Duran i Reynals

Barcelona, 08907, Spain

Location

Complejo Hospitalario Universitario de Granada - Hospital Universitario Virgen de las Nieves

Granada, 18014, Spain

Location

Hospital General Universitario Gregorio Maranon

Madrid, 28007, Spain

Location

Hospital Universitario Ramon y Cajal

Madrid, 28034, Spain

Location

Hospital Universitario La Paz

Madrid, 28046, Spain

Location

Hospital Universitario Puerta de Hierro Majadahonda

Madrid, 28222, Spain

Location

Hospital Universitario de Salamanca

Salamanca, 37007, Spain

Location

Hospital Universitario de Donostia

San Sebastián, 20014, Spain

Location

Hospital Universitario Marques de Valdecilla

Santander, 39008, Spain

Location

Hospital Clinico de Santiago de Compostela

Santiago de Compostela, 15706, Spain

Location

Hospital Universitario Virgen del Rocio

Seville, 41013, Spain

Location

Hospital Clinico Universitario de Valencia

Valencia, 46010, Spain

Location

Hospital Universitari i Politecnic La Fe

Valencia, 46026, Spain

Location

Universtity Hospital Basel - Haematology

Basel, 4031, Switzerland

Location

Hopitaux Universitaires de Geneve

Geneva, 1211, Switzerland

Location

Universitaetsspital Zuerich - Klinik fuer Haematology

Zurich, CH-8091, Switzerland

Location

China Medical University Hospital

Taichung, 40447 ROC, Taiwan

Location

Addenbrooke's Hospital

Cambridge, CB2 0QQ, United Kingdom

Location

University Hospital of Wales

Cardiff, CF14 4XW, United Kingdom

Location

Hammersmith Hospital

London, W12 0HS, United Kingdom

Location

Nottingham University Hospitals

Nottingham, NG5 1PB, United Kingdom

Location

Related Publications (2)

  • Pratta M, Paczesny S, Socie G, Barkey N, Liu H, Owens S, Arbushites MC, Schroeder MA, Howell MD. A biomarker signature to predict complete response to itacitinib and corticosteroids in acute graft-versus-host disease. Br J Haematol. 2022 Aug;198(4):729-739. doi: 10.1111/bjh.18300. Epub 2022 Jun 11.

  • Zeiser R, Socie G, Schroeder MA, Abhyankar S, Vaz CP, Kwon M, Clausen J, Volodin L, Giebel S, Chacon MJ, Meyers G, Ghosh M, Deeren D, Sanz J, Morariu-Zamfir R, Arbushites M, Lakshminarayanan M, Barbour AM, Chen YB. Efficacy and safety of itacitinib versus placebo in combination with corticosteroids for initial treatment of acute graft-versus-host disease (GRAVITAS-301): a randomised, multicentre, double-blind, phase 3 trial. Lancet Haematol. 2022 Jan;9(1):e14-e25. doi: 10.1016/S2352-3026(21)00367-7.

MeSH Terms

Conditions

Graft vs Host Disease

Interventions

itacitinibINCB039110PrednisoneMethylprednisoloneMethylprednisolone Hemisuccinate

Condition Hierarchy (Ancestors)

Immune System Diseases

Intervention Hierarchy (Ancestors)

PregnadienediolsPregnadienesPregnanesSteroidsFused-Ring CompoundsPolycyclic CompoundsPrednisolonePregnadienetriols

Results Point of Contact

Title
Study Director
Organization
Incyte Corporation

Study Officials

  • Rodica Morariu-Zamfir, MD

    Incyte Corporation

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
DOUBLE
Who Masked
PARTICIPANT, INVESTIGATOR
Masking Details
Double Blind
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

May 2, 2017

First Posted

May 4, 2017

Study Start

July 19, 2017

Primary Completion

May 2, 2019

Study Completion

July 13, 2020

Last Updated

September 2, 2025

Results First Posted

May 15, 2020

Record last verified: 2025-08

Data Sharing

IPD Sharing
Will not share

Locations