NCT02589145

Brief Summary

The goal of this clinical research study is to find the highest tolerable dose of lenalidomide that can be given in combination with vorinostat, gemcitabine, busulfan, and melphalan, with a stem cell transplant, and with or without rituximab. Researchers also want to learn about the safety and effectiveness of this combination.

Trial Health

57
Monitor

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
8

participants targeted

Target at below P25 for phase_1 lymphoma

Timeline
Completed

Started Jun 2016

Geographic Reach
1 country

1 active site

Status
terminated

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

October 26, 2015

Completed
2 days until next milestone

First Posted

Study publicly available on registry

October 28, 2015

Completed
8 months until next milestone

Study Start

First participant enrolled

June 22, 2016

Completed
2.8 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

April 8, 2019

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

April 8, 2019

Completed
8 months until next milestone

Results Posted

Study results publicly available

December 13, 2019

Completed
Last Updated

December 13, 2019

Status Verified

November 1, 2019

Enrollment Period

2.8 years

First QC Date

October 26, 2015

Results QC Date

November 6, 2019

Last Update Submit

November 26, 2019

Conditions

Keywords

Blood And Marrow TransplantationDiffuse large B-cell lymphomaDLBCLBusulfanBusulfexMyleranLenalidomideCC-5013RevlimidVorinostatSAHASuberoylanilide Hydroxamic AcidMSK-390ZolinzaGemcitabineGemcitabine HydrochlorideGemzarMelphalanAlkeranRituximabRituxanDexamethasoneDecadronGlutamineEnterexGlutapack-10NutreStoreResourceGlutaSolveSympt-X G.I.Symptx-XPyridoxineEnoxaparinLovenox InjectionPaliferminKepivance

Outcome Measures

Primary Outcomes (2)

  • Maximum Tolerated Dose (MTD)

    Established the maximum tolerated dose (MTD) of lenalidomide combined with vorinostat/gemcitabine/busulfan/melphalan with autologous stem-cell transplant ASCT). Maximum tolerated dose (MTD) of lenalidomide based on DLT was defined as any Grade 4 or 5 nonhematologic, noninfectious toxicity or any grade 3 mucositis or skin toxicity lasting \> 5 days at their peak severity. Lenalidomide doses were chosen adaptively for successive cohorts with a minimum size of 2 patients. Toxicity scoring followed the National Cancer Institute Common Toxicity Criteria, version 4.

    Enrollment up to day 30 post transplant for each dosing cohort

  • Event-free Survival (EFS)

    Determined the 2-year event-free survival (EFS)

    Up to 2 years post transplant

Secondary Outcomes (5)

  • Overall Survival (OS)

    Up to 2 years post transplant

  • Complete Remission (CR) Rate

    Up to 2 years post transplant

  • Overall Remission Rate (ORR)

    Up to 2 years post transplant

  • Toxicity Profile

    Up to 2 years post transplant

  • Pharmacodynamic Studies

    Up to 2 years post transplant

Study Arms (1)

Lenalidomide + Vorinostat/Gem/Bu/Mel + AutoSCT

EXPERIMENTAL

Vorinostat and lenalidomide administered orally at the same time within 1 hour before the daily dose of chemotherapy. Gemcitabine administered as a loading dose of 75 mg/m2 followed by infusion on days -8 and -3. Busulfan test dose administered as outpatient before admission, or as inpatient on day -10. The "test dose" of 32 mg/m2 based on actual body weight. Doses of days -6 and -5 subsequently adjusted to target an AUC of 4,000 microMol.min-1. Melphalan administered at 60 mg/m2 on days -3 and -2. Patients with CD20+ tumors receive rituximab 375 mg/m2 on day -9 in the AM as an inpatient. Dexamethasone 8 mg by vein twice a day from day -8 to day -2. Caphosol oral rinses 30 mL four times a day used from day -8. Oral glutamine, 15 g four times a day, swished, gargled and swallowed started on day -8. Pyridoxine 100 mg by vein or mouth three times a day from day -1. Enoxaparin 40 mg subcutaneously daily from admission until platelet count drops below 50,000/mm3.

Drug: LenalidomideDrug: VorinostatDrug: GemcitabineDrug: BusulfanDrug: MelphalanDrug: RituximabDrug: DexamethasoneDrug: CaphosolDrug: GlutamineDrug: PyridoxineDrug: EnoxaparinProcedure: Stem Cell TransplantDrug: Palifermin

Interventions

Dose Escalation Phase Starting dose of Lenalidomide: 50 mg by mouth on Days -9 to -2. Dose Expansion Phase Starting Dose: Maximum tolerated dose from Phase I.

Also known as: CC-5013, Revlimid
Lenalidomide + Vorinostat/Gem/Bu/Mel + AutoSCT

1000 mg by mouth on Days -9 to -2.

Also known as: SAHA, Suberoylanilide Hydroxamic Acid, MSK-390, Zolinza
Lenalidomide + Vorinostat/Gem/Bu/Mel + AutoSCT

Gemcitabine administered as a loading dose of 75 mg/m2 by vein on Day -8 and 2775 mg by vein on Day -3.

Also known as: Gemcitabine Hydrochloride, Gemzar
Lenalidomide + Vorinostat/Gem/Bu/Mel + AutoSCT

Busulfan test dose administered by vein either as outpatient before admission, or as inpatient on day -10. The "test dose" of 32 mg/m2 based on actual body weight. Doses of days -6 and -5 subsequently adjusted to target an AUC of 4,000 microMol.min-1.

Also known as: Busulfex, Myleran
Lenalidomide + Vorinostat/Gem/Bu/Mel + AutoSCT

60 mg/m2 by vein on days -3 and -2.

Also known as: Alkeran
Lenalidomide + Vorinostat/Gem/Bu/Mel + AutoSCT

Patients with CD20+ tumors receive Rituximab 375 mg/m2 by vein on day -9 in the AM as an inpatient.

Also known as: Rituxan
Lenalidomide + Vorinostat/Gem/Bu/Mel + AutoSCT

8 mg by vein twice a day from Day -8 AM to Day -2 PM.

Also known as: Decadron
Lenalidomide + Vorinostat/Gem/Bu/Mel + AutoSCT

Caphosol oral rinses 30 mL four times a day used from Day -8.

Lenalidomide + Vorinostat/Gem/Bu/Mel + AutoSCT

Oral glutamine, 15 g four times a day, swished, gargled and swallowed started on Day -8.

Also known as: Enterex, Glutapak-10, NutreStore, Resource, GlutaSolve, Sympt-X G.I., Symptx-X
Lenalidomide + Vorinostat/Gem/Bu/Mel + AutoSCT

100 mg by vein or mouth three times a day from Day -1

Lenalidomide + Vorinostat/Gem/Bu/Mel + AutoSCT

40 mg subcutaneously daily from admission until platelet count drops below 50,000/mm3.

Also known as: Lovenox Injection
Lenalidomide + Vorinostat/Gem/Bu/Mel + AutoSCT

Stem cell transplant performed on Day 0.

Also known as: SCT
Lenalidomide + Vorinostat/Gem/Bu/Mel + AutoSCT

Palifermin per departmental standard of care with 3 doses to be administered prior to starting chemotherapy and 3 doses starting on day 0.

Also known as: Kepivance
Lenalidomide + Vorinostat/Gem/Bu/Mel + AutoSCT

Eligibility Criteria

Age15 Years - 65 Years
Sexall
Healthy VolunteersNo
Age GroupsChild (0-17), Adult (18-64), Older Adult (65+)

You may qualify if:

  • Age 15-65
  • Patients with ABC (determined by immunohistochemistry using the Hans algorithmI) DLBCL with primary refractory disease, relapse \<12 months after initial therapy, secondary International Prognostic Index (IPI) \>1, less than partial response to salvage treatment or exposure to \>3 salvage regimens
  • Adequate renal function, as defined by an estimated serum creatinine clearance \>/= 50 ml/min (MDRD method) and/or serum creatinine \</= 1.8 mg/dL
  • Adequate hepatic function (SGOT and/or SGPT \</= 3 x ULN; bilirubin and ALP \</= 2 x ULN
  • Adequate pulmonary function with FEV1, FVC and DLCO (corrected for Hgb) \>/= 50%
  • Adequate cardiac function with left ventricular ejection fraction \>/= 40%. No uncontrolled arrhythmias or symptomatic cardiac disease
  • ECOG performance status \<2
  • Negative Beta HCG in woman with child-bearing potential
  • All study participants must be registered into the mandatory Revlimid REMS program, and be willing and able to comply with the requirements of the REMS program.
  • Females of reproductive potential must adhere to the scheduled pregnancy testing as required in the Revlimid REMS program.

You may not qualify if:

  • Grade \>/= 3 non-hematologic toxicity from previous therapy that has not resolved to \</= G1
  • Prior whole brain irradiation
  • Active hepatitis B, either active carrier (HBsAg +) or viremic (HBV DNA \>/= 10,000 copies/mL, or \>/= 2,000 IU/mL)
  • Evidence of either cirrhosis or stage 3-4 liver fibrosis in patients with chronic hepatitis C or positive hepatitis C serology
  • Active infection requiring parenteral antibiotics
  • HIV infection, unless receiving effective antiretroviral therapy with undetectable viral load and normal CD4 counts
  • Radiation therapy in the month prior to enrollment
  • History of arterial thromboembolic events in the past 3 months and of venous thromboembolic events in the past month
  • History of hypersensitivity of lenalidomide or thalidomide

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (1)

University of Texas MD Anderson Cancer Center

Houston, Texas, 77030, United States

Location

Related Links

MeSH Terms

Conditions

LymphomaLymphoma, Large B-Cell, Diffuse

Interventions

LenalidomideVorinostatGemcitabineBusulfanMelphalanRituximabDexamethasoneCalcium DobesilateGlutamineHealth ResourcesPyridoxineEnoxaparinStem Cell TransplantationFibroblast Growth Factor 7

Condition Hierarchy (Ancestors)

Neoplasms by Histologic TypeNeoplasmsLymphoproliferative DisordersLymphatic DiseasesHemic and Lymphatic DiseasesImmunoproliferative DisordersImmune System DiseasesLymphoma, B-CellLymphoma, Non-Hodgkin

Intervention Hierarchy (Ancestors)

PhthalimidesPhthalic AcidsAcids, CarbocyclicCarboxylic AcidsOrganic ChemicalsPiperidonesPiperidinesHeterocyclic Compounds, 1-RingHeterocyclic CompoundsIsoindolesHeterocyclic Compounds, 2-RingHeterocyclic Compounds, Fused-RingAnilidesAmidesAniline CompoundsAminesHydroxamic AcidsHydroxylaminesHydroxy AcidsDeoxycytidineCytidinePyrimidine NucleosidesPyrimidinesButylene GlycolsGlycolsAlcoholsMesylatesAlkanesulfonatesAlkanesulfonic AcidsAlkanesHydrocarbons, AcyclicHydrocarbonsSulfonic AcidsSulfur AcidsSulfur CompoundsNitrogen Mustard CompoundsMustard CompoundsHydrocarbons, HalogenatedPhenylalanineAmino Acids, AromaticAmino Acids, CyclicAmino AcidsAmino Acids, Peptides, and ProteinsAntibodies, Monoclonal, Murine-DerivedAntibodies, MonoclonalAntibodiesImmunoglobulinsImmunoproteinsBlood ProteinsProteinsSerum GlobulinsGlobulinsPregnadienetriolsPregnadienesPregnanesSteroidsFused-Ring CompoundsPolycyclic CompoundsSteroids, FluorinatedBenzenesulfonatesBenzene DerivativesHydrocarbons, AromaticHydrocarbons, CyclicArylsulfonatesArylsulfonic AcidsAmino Acids, BasicAmino Acids, DiaminoAmino Acids, NeutralHealth PlanningHealth Care Economics and OrganizationsDelivery of Health CareHealth Care Quality, Access, and EvaluationVitamin B 6PicolinesPyridinesHeparin, Low-Molecular-WeightHeparinGlycosaminoglycansPolysaccharidesCarbohydratesCell TransplantationCell- and Tissue-Based TherapyBiological TherapyTherapeuticsTransplantationSurgical Procedures, OperativeFibroblast Growth FactorsIntercellular Signaling Peptides and ProteinsPeptidesBiological Factors

Results Point of Contact

Title
Dr. Yago Nieto/Professor, Stem Cell Transplantation
Organization
UT MD Anderson Cancer Center

Study Officials

  • Yago Nieto, MD, PHD

    M.D. Anderson Cancer Center

    PRINCIPAL INVESTIGATOR

Publication Agreements

PI is Sponsor Employee
Yes

Study Design

Study Type
interventional
Phase
phase 1
Allocation
NA
Masking
NONE
Purpose
TREATMENT
Intervention Model
SINGLE GROUP
Sponsor Type
OTHER
Responsible Party
SPONSOR

Study Record Dates

First Submitted

October 26, 2015

First Posted

October 28, 2015

Study Start

June 22, 2016

Primary Completion

April 8, 2019

Study Completion

April 8, 2019

Last Updated

December 13, 2019

Results First Posted

December 13, 2019

Record last verified: 2019-11

Locations