NCT00972101

Brief Summary

The goal of this clinical research study is to learn if treating umbilical cord blood with growth factors before a transplant can help to improve the body's ability to accept the cord blood transplants.

Trial Health

15
At Risk

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Trial has exceeded expected completion date
Timeline
Completed

Started Sep 2009

Typical duration for phase_1

Status
withdrawn

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

September 1, 2009

Completed
2 days until next milestone

First Submitted

Initial submission to the registry

September 3, 2009

Completed
1 day until next milestone

First Posted

Study publicly available on registry

September 4, 2009

Completed
2 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

September 1, 2011

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

September 1, 2011

Completed
Last Updated

October 11, 2012

Status Verified

October 1, 2012

Enrollment Period

2 years

First QC Date

September 3, 2009

Last Update Submit

October 10, 2012

Conditions

Keywords

Blood And Marrow TransplantationLeukemiaLymphomaPediatricsEtoposideExpanded Cord Blood T CellsFilgrastimFludarabineMelphalanMycophenolate MofetilRituximabTacrolimusThiotepaThymoglobulinTotal Body Irradiation

Outcome Measures

Primary Outcomes (1)

  • Maximum Tolerated Dose (MTD)

    Days 14 to 100

Study Arms (2)

Regimen 1: No TBI

EXPERIMENTAL

High Dose Chemotherapy without Total Body Irradiation (TBI)

Drug: MelphalanDrug: ThiotepaDrug: FludarabineDrug: RituximabDrug: Anti-thymocyte globulin (ATG)Drug: Mycophenolate Mofetil (MMF)Drug: TacrolimusProcedure: Cord Blood InfusionDrug: G-CSFProcedure: Ex vivo expanded T cell Infusion

Regimen 2: TBI

EXPERIMENTAL

High Dose Chemotherapy with Total Body Irradiation (TBI)

Radiation: Total Body Irradiation (TBI)Drug: RituximabDrug: EtoposideDrug: Anti-thymocyte globulin (ATG)Drug: Mycophenolate Mofetil (MMF)Drug: TacrolimusProcedure: Cord Blood InfusionDrug: G-CSFProcedure: Ex vivo expanded T cell Infusion

Interventions

3 Gy of radiation on Days -7,-6, -5 and -4.

Regimen 2: TBI

140 mg/m\^2 by vein over 30 minutes as a single dose on Day -8

Also known as: Alkeran
Regimen 1: No TBI

10 mg/kg by vein over 4 hours as a single dose on Day -7

Regimen 1: No TBI

40 mg/m\^2 by vein over about 30 minutes 1 time each day on Days -6 through -3.

Also known as: Fludara, Fludarabine Phosphate
Regimen 1: No TBI

Regimen 1: 375 mg/m\^2 may be given by vein over 4 - 6 hours on Day -9 if needed Regimen 2: 375 mg/m\^2 may be given by vein over 4 - 6 hours on Day -8 if needed

Also known as: Rituxan
Regimen 1: No TBIRegimen 2: TBI

60 mg/m\^2 by vein over 1-2 hours as a single dose on Day -3.

Also known as: VePesid
Regimen 2: TBI

Regimen 1: 1.25 and 1.75 mg/kg by vein over 4-6 hours on the Days -4 and -3. Regimen 2: 0.5, 1.0 and 1.5 mg/kg by vein over 4-6 hours on respective Days -3, -2, and -1.

Also known as: Thymoglublin
Regimen 1: No TBIRegimen 2: TBI

15 mg/kg pills twice a day starting on day -3, and continued until Day 100+ after transplant (1 gram may be given by vein if necessary).

Also known as: CellCept
Regimen 1: No TBIRegimen 2: TBI

0.03 mg/kg by vein Day -2 as 24 hour continuous infusion for several weeks. After stem cell transplant, tacrolimus given by mouth 2 times a day for up to 6 months.

Also known as: FK506, Prograf
Regimen 1: No TBIRegimen 2: TBI

Cord blood infusion of larger portion through vein using Central Venous Catheter (CVC) on Day 0.

Also known as: Cord Blood T Cells Infusion
Regimen 1: No TBIRegimen 2: TBI
G-CSFDRUG

5 mcg/kg day subcutaneously (may round up to the next vial) beginning on day +1 and continuing till absolute neutrophil count is \> 2.5 x 10e\^9/L.

Also known as: Filgrastim, Neupogen
Regimen 1: No TBIRegimen 2: TBI

Infusion by vein of treated cord blood beginning dose of 1 x 10e\^5 T cells/kg on Day 14+.

Regimen 1: No TBIRegimen 2: TBI

Eligibility Criteria

AgeUp to 55 Years
Sexall
Healthy VolunteersNo
Age GroupsChild (0-17), Adult (18-64)

You may qualify if:

  • Patient must have one of the following hematologic malignancies:
  • AML
  • ALL
  • CML
  • NHL
  • HD, or
  • CLL (Select from Criteria #2 through #7)
  • Acute Myelogenous Leukemia (AML), Myelodysplastic Syndrome (MDS; Myelodysplastic syndromes with International Prognostic Scoring System score \>2 or myelodysplasia that has not responded to chemotherapy): induction failure, high-risk for relapse 1st remission (with high-risk cytogenetics or FLT3 mutation), 2nd or 3rd complete remission, or 2nd relapse with less than 10% blasts in the bone marrow and/or peripheral blood.
  • Acute Lymphoblastic Leukemia (ALL): induction failure, 1st complete remission with Philadelphia chromosome or translocation, 2nd or 3rd complete remission, or 2nd relapse with less than 10% blasts in the bone marrow and/or peripheral blood.
  • Chronic Myelogenous Leukemia (CML) second chronic phase, accelerated phase or blast crisis with less than 10% blasts in the bone marrow and/or peripheral blood and failure of at least one tyrosine kinase inhibitor.
  • Non-Hodgkin's Lymphoma (NHL): Induction failures, second or third complete remission, or relapse (including relapse post autologous hematopoietic stem cell transplant).
  • Hodgkin's Disease (HD): Induction failures, second or third complete remission, or relapse (including relapse post autologous hematopoietic stem cell transplant).
  • Chronic Lymphocytic Leukemia (CLL): Failure of one multi-agent regimen including fludarabine or other nucleoside analog
  • Patient's Age Criteria: Age \>/= 6 months and \</= 55 years
  • Performance score of \< 3 (Zubrod score).
  • +9 more criteria

You may not qualify if:

  • HIV positive (due to the extreme immunosuppressive nature of allogeneic stem cell transplant)
  • Patient with active (untreated) CNS disease
  • Availability of an appropriate, willing, HLA-matched related marrow donor
  • Active invasive infections.
  • Pregnant or breast-feeding

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Related Links

MeSH Terms

Conditions

LeukemiaLymphoma

Interventions

Whole-Body IrradiationMelphalanThiotepafludarabinefludarabine phosphateRituximabEtoposideAntilymphocyte SerumMycophenolic AcidTacrolimusGranulocyte Colony-Stimulating FactorFilgrastim

Condition Hierarchy (Ancestors)

Neoplasms by Histologic TypeNeoplasmsHematologic DiseasesHemic and Lymphatic DiseasesLymphoproliferative DisordersLymphatic DiseasesImmunoproliferative DisordersImmune System Diseases

Intervention Hierarchy (Ancestors)

RadiotherapyTherapeuticsInvestigative TechniquesNitrogen Mustard CompoundsMustard CompoundsHydrocarbons, HalogenatedHydrocarbonsOrganic ChemicalsPhenylalanineAmino Acids, AromaticAmino Acids, CyclicAmino AcidsAmino Acids, Peptides, and ProteinsPhosphoramidesOrganophosphorus CompoundsTriethylenephosphoramideAziridinesAzirinesHeterocyclic Compounds, 1-RingHeterocyclic CompoundsAntibodies, Monoclonal, Murine-DerivedAntibodies, MonoclonalAntibodiesImmunoglobulinsImmunoproteinsBlood ProteinsProteinsSerum GlobulinsGlobulinsPodophyllotoxinTetrahydronaphthalenesNaphthalenesPolycyclic Aromatic HydrocarbonsHydrocarbons, AromaticHydrocarbons, CyclicPolycyclic CompoundsGlucosidesGlycosidesCarbohydratesImmune SeraBiological ProductsComplex MixturesCaproatesAcids, AcyclicCarboxylic AcidsFatty AcidsLipidsMacrolidesLactonesColony-Stimulating FactorsGlycoproteinsGlycoconjugatesHematopoietic Cell Growth FactorsCytokinesIntercellular Signaling Peptides and ProteinsPeptidesBiological Factors

Study Officials

  • Laura L. Worth, MD, PHD

    UT MD Anderson Cancer Center

    STUDY CHAIR
0

Study Design

Study Type
interventional
Phase
phase 1
Allocation
NON RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
SINGLE GROUP
Sponsor Type
OTHER
Responsible Party
SPONSOR

Study Record Dates

First Submitted

September 3, 2009

First Posted

September 4, 2009

Study Start

September 1, 2009

Primary Completion

September 1, 2011

Study Completion

September 1, 2011

Last Updated

October 11, 2012

Record last verified: 2012-10