NCT03128619

Brief Summary

This phase I/II trial studies side effects and best dose of copanlisib when given together with letrozole and palbociclib and to see how well they work in treating hormone receptor positive HER2 negative stage I-IV breast cancer. Copanlisib and palbociclib may stop the growth of tumor cells by blocking some of the enzymes needed for cell growth. Drugs, such as letrozole, may lessen the amount of estrogen made by the body. Giving copanlisib, letrozole, and palbociclib may work better in treating patients with breast cancer.

Trial Health

57
Monitor

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
10

participants targeted

Target at below P25 for phase_1

Timeline
Completed

Started Aug 2017

Longer than P75 for phase_1

Geographic Reach
1 country

1 active site

Status
terminated

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

April 4, 2017

Completed
21 days until next milestone

First Posted

Study publicly available on registry

April 25, 2017

Completed
3 months until next milestone

Study Start

First participant enrolled

August 2, 2017

Completed
4.7 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

March 31, 2022

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

March 31, 2022

Completed
Last Updated

September 26, 2022

Status Verified

April 1, 2021

Enrollment Period

4.7 years

First QC Date

April 4, 2017

Last Update Submit

September 22, 2022

Conditions

Outcome Measures

Primary Outcomes (2)

  • Change in Ki-67 expression defined as the percent of cells staining positive by validated central assay (Phase II)

    Will be evaluated on the log Ki-67 ratio scale. Primary analysis of this variable will utilize a linear model with treatment, PR status as fixed effects. The comparison of treatment arms will be based on the least squares mean (LSM) estimates and standard errors derived from this model. For descriptive purposes, LSM estimates and associated confidence intervals (CIs) will be back transformed to the geometric mean percent change scale. A second post-baseline evaluation of Ki67 expression will be performed following the completion of 4 months of treatment. Analysis of change from baseline to com

    Baseline to 2 weeks

  • Incidence of dose-limiting toxicities (DLT) evaluated according to National Cancer Institute (NCI) CTCAE version 4.0 to determine MTD (Phase Ib)

    If \>= 2 of 6 participants treated at a dose level experience DLTs, then the MTD will have been exceeded. Up to 3 additional patients may be entered at the lower dose level to obtain additional safety information (if only 3 participants were treated previously at that dose) to demonstrate that =\< 1 of 6 patients experience DLT.

    Up to 112 days

Secondary Outcomes (10)

  • Clinical objective response rate (ORR) evaluated by RECIST 1.1 using caliper measurements

    Up to 1 month after surgery

  • Gene expression and/or biomarker changes

    Up to 1 month after surgery

  • Incidence of adverse events (AEs) evaluated according to NCI CTCAE version 4.0

    Up to 1 month after surgery

  • pCR rate defined as the percentage of randomized patients with a pCR

    Up to 1 month after surgery

  • The pharmacokinetic (PK) parameter - area under the plasma concentration-time curve (AUC) will be determined for copanlisib in arms A, B, and escalation dose levels.

    At pre-infusion, 10 minutes, 1, 2, 3, and 5 hours after start of infusion on days 1 and 8, course 1 (Ib); at pre-infusion and 1 hour after start of infusion on day 1, course 1 and pre-infusion, 5-15 minutes, 1, and 1-1.5 hours on day 8, course 2 (II)

  • +5 more secondary outcomes

Study Arms (4)

Arm A (copanlisib, letrozole)

EXPERIMENTAL

PHASE II: Patients receive copanlisib (MTD) IV over 1 hour on days 1, 8, and 15 and letrozole PO continuously on days 1-28. Treatment repeats every 28 days for up to 4 courses in the absence of disease progression, or unacceptable toxicity.

Drug: CopanlisibOther: Laboratory Biomarker AnalysisDrug: LetrozoleOther: Pharmacological Study

Arm B (copanlisib, palbociclib, letrozole)

EXPERIMENTAL

PHASE II: Patients receive copanlisib (MTD) IV over 1 hour on days 1, 8, and 15, palbociclib PO QD on days 1-21, and letrozole PO continuously on days 1-28. Treatment repeats every 28 days for up to 4 courses in the absence of disease progression or unacceptable toxicity.

Procedure: Biopsy of BreastDrug: CopanlisibOther: Laboratory Biomarker AnalysisDrug: LetrozoleDrug: PalbociclibOther: Pharmacological Study

Arm C (copanlisib, palbociclib, letrozole)

EXPERIMENTAL

PHASE II: Patients receive palbociclib PO QD for days 1-14 of course 1 and letrozole PO continuously on days 1-14. Patients then undergo biopsy. Patients then receive copanlisib IV over 1 hour on days 1, 8, and 15 and letrozole PO continuously on days 1-28. Treatment with copanlisib (MTD) and letrozole repeats every 28 days for up to 3.5 courses in the absence of disease progression or unacceptable toxicity.

Procedure: Biopsy of BreastDrug: CopanlisibOther: Laboratory Biomarker AnalysisDrug: LetrozoleDrug: PalbociclibOther: Pharmacological Study

Phase Ib (copanlisib, palbociclib, letrozole)

EXPERIMENTAL

PHASE Ib: Patients with metastatic breast cancer receive copanlisib IV over 1 hour on days 1, 8, and 15, palbociclib PO QD on days 1-21, and letrozole PO continuously on days 1-28. Treatment repeats every 28 days for up to 4 courses in the absence of disease progression or unacceptable toxicity.

Drug: CopanlisibOther: Laboratory Biomarker AnalysisDrug: LetrozoleDrug: PalbociclibOther: Pharmacological Study

Interventions

Undergo biopsy

Also known as: Breast Biopsy
Arm B (copanlisib, palbociclib, letrozole)Arm C (copanlisib, palbociclib, letrozole)

Given IV

Also known as: BAY 80-6946, PI3K Inhibitor BAY 80-6946
Arm A (copanlisib, letrozole)Arm B (copanlisib, palbociclib, letrozole)Arm C (copanlisib, palbociclib, letrozole)Phase Ib (copanlisib, palbociclib, letrozole)

Correlative studies

Arm A (copanlisib, letrozole)Arm B (copanlisib, palbociclib, letrozole)Arm C (copanlisib, palbociclib, letrozole)Phase Ib (copanlisib, palbociclib, letrozole)

Given PO

Also known as: CGS 20267, Femara
Arm A (copanlisib, letrozole)Arm B (copanlisib, palbociclib, letrozole)Arm C (copanlisib, palbociclib, letrozole)Phase Ib (copanlisib, palbociclib, letrozole)

Given PO

Also known as: Ibrance, PD-0332991, PD-332991
Arm B (copanlisib, palbociclib, letrozole)Arm C (copanlisib, palbociclib, letrozole)Phase Ib (copanlisib, palbociclib, letrozole)

Correlative studies

Arm A (copanlisib, letrozole)Arm B (copanlisib, palbociclib, letrozole)Arm C (copanlisib, palbociclib, letrozole)Phase Ib (copanlisib, palbociclib, letrozole)

Eligibility Criteria

Age19 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Post-menopausal (if female) defined as: 1) prior bilateral oophorectomy, 2) age 60 or over, or 3) \< 60 years and amenorrheic for at least 12 months with follicle-stimulating hormone (FSH) and estradiol in the postmenopausal range per institutional parameters); use of luteinizing hormone-releasing hormone (LHRH) agonists to induce chemical ovarian ablation will not be allowed for this study
  • Tumor is hormone receptor (HR)+ (estrogen receptor and/or progesterone receptor positive with at least 10% expression of either receptor by local immunohistochemical staining) and HER2 negative based on local assessment
  • FOR PHASE Ib PORTION OF THE STUDY:
  • Locally advanced/non-operable or metastatic breast cancer that has not been previously treated in the metastatic setting with systemic therapy (i.e. first line treatment)
  • Measurable disease per RECIST 1.1
  • FOR PHASE II PORTION OF THE STUDY:
  • Breast cancer suitable for mandatory baseline core biopsy
  • No prior systemic therapy or radiotherapy for currently-diagnosed invasive or noninvasive breast cancer
  • FOR ALL PHASES (Ib AND II):
  • Absolute neutrophil count (ANC) \>= 1.5 x 10\^9/L
  • Platelets \> 100 x 10\^9/L
  • Hemoglobin \>= 8 g/dL (phase Ib) or \>= 10 g/dL (for phase II portion)
  • For phase Ib portion only: patients may receive erythrocyte transfusions to achieve this hemoglobin level at the discretion of the investigator; however, initial study drug treatment must not begin earlier than the day of the erythrocyte transfusion
  • Bilirubin =\< 1.5 times the upper limit of normal (ULN)
  • Alanine aminotransferase (ALT) and aspartate aminotransferase (AST) =\< 3.0 times ULN
  • +6 more criteria

You may not qualify if:

  • FOR PHASE Ib ONLY:
  • Early stage (curable) breast cancer
  • FOR PHASE II ONLY:
  • Metastatic breast cancer (local spread to axillary or internal mammary lymph nodes is permitted)
  • Prior systemic therapy for invasive or non-invasive (DCIS) breast cancer
  • Prior radiotherapy to the ipsilateral chest wall or breast for any malignancy
  • Bilateral invasive breast cancer
  • FOR ALL PHASES (Ib AND II): Inflammatory breast cancer
  • FOR ALL PHASES (Ib AND II): Concurrent therapy with any other non-protocol anti-cancer therapy
  • FOR ALL PHASES (Ib AND II): History of any other malignancy within the past 5 years, with the exception of non-melanoma skin cancer or carcinoma-in-situ of the cervix
  • FOR ALL PHASES (Ib AND II): Concurrent diagnosis of pheochromocytoma
  • FOR ALL PHASES (Ib AND II): Current therapy with raloxifene, tamoxifen, aromatase inhibitor, or other selective estrogen receptor modulator (SERM), either for osteoporosis or prevention of breast cancer; subjects must have discontinued therapies for at least 28 days prior to first baseline biopsy
  • FOR ALL PHASES (Ib AND II): Concurrent treatment with postmenopausal hormone replacement therapy; prior treatment must be stopped for at least 28 days prior to first baseline biopsy
  • FOR ALL PHASES (Ib AND II): Type I diabetes or patients on insulin therapy are not allowed; uncontrolled type II diabetes not allowed (glycosylated hemoglobin \[HbA1c\] \> 7.5)
  • FOR ALL PHASES (Ib AND II): Proteinuria of \>= Common Terminology Criteria for Adverse Events (CTCAE) grade 3 as estimated by urine protein : creatinine ratio \> 3.5 on a random urine sample
  • +21 more criteria

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (1)

UCLA / Jonsson Comprehensive Cancer Center

Los Angeles, California, 90095, United States

Location

MeSH Terms

Conditions

Breast Neoplasms

Interventions

copanlisibLetrozolepalbociclib

Condition Hierarchy (Ancestors)

Neoplasms by SiteNeoplasmsBreast DiseasesSkin DiseasesSkin and Connective Tissue Diseases

Intervention Hierarchy (Ancestors)

NitrilesOrganic ChemicalsTriazolesAzolesHeterocyclic Compounds, 1-RingHeterocyclic Compounds

Study Officials

  • Sara Hurvitz

    UCLA / Jonsson Comprehensive Cancer Center

    PRINCIPAL INVESTIGATOR

Study Design

Study Type
interventional
Phase
phase 1
Allocation
RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
OTHER
Responsible Party
SPONSOR

Study Record Dates

First Submitted

April 4, 2017

First Posted

April 25, 2017

Study Start

August 2, 2017

Primary Completion

March 31, 2022

Study Completion

March 31, 2022

Last Updated

September 26, 2022

Record last verified: 2021-04

Locations