NCT02605915

Brief Summary

This is a Phase Ib, open-label, two-stage study with two active regimens in each stage designed to evaluate the safety and tolerability of combination treatment with atezolizumab, trastuzumab, and pertuzumab (with and without docetaxel) or atezolizumab and trastuzumab emtansine in participants with human epidermal growth factor receptor 2 (HER2) positive metastatic breast cancer (MBC) and locally advanced early breast cancer (EBC), and atezolizumab with doxorubicin and cyclophosphamide in HER2-negative breast cancer.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
98

participants targeted

Target at P75+ for phase_1

Timeline
Completed

Started Dec 2015

Longer than P75 for phase_1

Geographic Reach
1 country

20 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

November 12, 2015

Completed
4 days until next milestone

First Posted

Study publicly available on registry

November 16, 2015

Completed
2 months until next milestone

Study Start

First participant enrolled

December 31, 2015

Completed
3.9 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

November 13, 2019

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

November 13, 2019

Completed
Last Updated

February 5, 2020

Status Verified

January 1, 2020

Enrollment Period

3.9 years

First QC Date

November 12, 2015

Last Update Submit

January 31, 2020

Conditions

Outcome Measures

Primary Outcomes (3)

  • Percentage of Participants With Dose Limiting Toxicities (DLT) - Cohort 1A, 1B, 1C, 1D, 1F

    Baseline up to Day 21

  • Percentage of Participants With DLT - Cohort 1E

    Baseline up to Day 28

  • Percentage of Participants With Adverse Events (AEs) According to National Cancer Institute Common Terminology Criteria for AEs, Version 4.0 (NCI CTCAE V4.0)

    Baseline up to approximately 3 years

Secondary Outcomes (17)

  • Maximum Serum Concentration (Cmax) of Atezolizumab

    Cohorts 1A, 1B, 1C, 1D, E1, 1F, 2A, 2B, 2C, 2D: pre-infusion (Hour 0), 30 minutes after end of atezolimumab infusion on Day 1 Cycle 1 (cycle length=21 days) up to approximately 3 years (detailed timeframe provided in measure description)

  • Minimum Serum Concentration (Cmin) of Atezolizumab

    pre-infusion (Hour 0) on Day 1 of Cycle 1, 2, 3 (except cohort 1E), 4, 8 (cycle length=21 days), on Day 1 of every 8 cycles until study treatment/early discontinuation, 120 days after treatment completion/discontinuation (up to approximately 3 years)

  • Cmin of Trastuzumab

    Cohorts 1A, 1F, 2A, 2D: pre-infusion (Hour 0) on Day 1 of Cycle 1, 3 (cycle length=21 days), at study treatment/early discontinuation, 120 days after treatment completion or discontinuation (up to approximately 3 years)

  • Cmin of Trastuzumab Emtansine

    Cohorts 1B, 1C, 1D, 2B, 2C: pre-infusion (Hour 0) on Day 1 of Cycle 1, 3 (cycle length=21 days), at study treatment/early discontinuation, 120 days after treatment completion or discontinuation (up to approximately 3 years)

  • Cmin of Pertuzumab

    Cohorts 1A, 1F, 2A, 2D: pre-infusion (Hour 0) on Day 1 of Cycle 1, 3 (cycle length=21 days), at study treatment/early discontinuation, 120 days after treatment completion or discontinuation (up to approximately 3 years)

  • +12 more secondary outcomes

Study Arms (10)

Cohort 1A: Atezolizumab/Trastuzumab/Pertuzumab

EXPERIMENTAL

Participants will receive atezolizumab in combination with trastuzumab and pertuzumab every 3 weeks.

Drug: AtezolizumabDrug: PertuzumabDrug: Trastuzumab

Cohort 1B: Atezolizumab/Trastuzumab emtansine 3.6 mg

EXPERIMENTAL

Participants will receive atezolizumab in combination with trastuzumab emtansine (3.6 mg/kg) every 3 weeks.

Drug: AtezolizumabDrug: Trastuzumab emtansine

Cohort 1C: Atezolizumab/Trastuzumab emtansine 3.0 mg

EXPERIMENTAL

Participants will receive atezolimumab in combination with trastzumab emtansine (3.0 mg/kg) every 3 weeks.

Drug: AtezolizumabDrug: Trastuzumab emtansine

Cohort 1D: Atezolizumab/Trastuzumab emtansine 2.4 mg

EXPERIMENTAL

Participants will receive atezolimumab in combination with trastzumab emtansine (2.4 mg/kg) every 3 weeks.

Drug: AtezolizumabDrug: Trastuzumab emtansine

Cohort 1E: Atezolizumab/ doxorubicin/ cyclophosphamide

EXPERIMENTAL

Participants with HER2-negative breast cancer will receive atezolizumab (every 2 weeks) in combination with doxorubicin (every 2 weeks) and cyclophosphamide for four cycles. After the completion of four cycles of combination atezolizumab /doxorubicin / cyclophosphamide, atezolizumab will be continued as a single-agent at a dose of 1200 mg every 3 weeks.

Drug: AtezolizumabDrug: DoxorubicinDrug: Cyclophosphamide

Cohort 1F: Atezolizumab/Trastuzumab/Pertuzumab/ Docetaxel

EXPERIMENTAL

Participants will receive atezolizumab in combination with trastuzumab, pertuzumab, and docetaxel every 3 weeks.

Drug: AtezolizumabDrug: DocetaxelDrug: PertuzumabDrug: Trastuzumab

Cohort 2A: Atezolizumab/Trastuzumab/Pertuzumab

EXPERIMENTAL

Participants will receive atezolizumab in combination with trastuzumab and pertuzumab every 3 weeks for 2 cycles, followed by docetaxel, carboplatin, trastuzumab and pertuzumab every 3 weeks for 6 cycles. Breast surgery will be performed no later than 6 weeks after neoadjuvant therapy. Upon the completion of surgery, participants will receive 12 cycles of single-agent trastuzumab every 3 weeks.

Drug: AtezolizumabDrug: CarboplatinDrug: DocetaxelDrug: PertuzumabDrug: Trastuzumab

Cohort 2B: Atezolizumab/Trastuzumab emtansine

EXPERIMENTAL

Participants will receive atezolizumab in combination with trastuzumab emtansine every 3 weeks for 2 cycles, followed by docetaxel, carboplatin, trastuzumab and pertuzumab every 3 weeks for 6 cycles. Breast surgery will be performed no later than 6 weeks after neoadjuvant therapy. Upon the completion of surgery, participants will receive 12 cycles of single-agent trastuzumab every 3 weeks.

Drug: AtezolizumabDrug: CarboplatinDrug: DocetaxelDrug: PertuzumabDrug: TrastuzumabDrug: Trastuzumab emtansine

Cohort 2C: Safety Expansion

EXPERIMENTAL

Participants with HER2-positive metastatic breast cancer/unresectable locally advanced breast cancer who received prior treatment with trastuzumab and a taxane chemotherapy will receive atezolizumab in combination with trastuzumab emtansine at the dose determined from stage 1, every 3 weeks until disease progression, lack of clinical benefit, or unacceptable toxicity.

Drug: AtezolizumabDrug: Trastuzumab emtansine

Cohort 2D: Safety Expansion

EXPERIMENTAL

Participants with HER2-positive metastatic breast cancer recently progressed on an HP containing regimen will receive atezolimumab in combination with trastuzumab and pertuzumab every 3 weeks until disease progression, lack of clinical benefit, or unacceptable toxicity.

Drug: AtezolizumabDrug: PertuzumabDrug: Trastuzumab

Interventions

Atezolizumab 1200 milligrams (mg) or 840 mg (Cohort 1E only) flat dose administered via intravenous (IV) infusion on Day 1 of every 21-day cycle.

Also known as: Tecentriq, RO5541267
Cohort 1A: Atezolizumab/Trastuzumab/PertuzumabCohort 1B: Atezolizumab/Trastuzumab emtansine 3.6 mgCohort 1C: Atezolizumab/Trastuzumab emtansine 3.0 mgCohort 1D: Atezolizumab/Trastuzumab emtansine 2.4 mgCohort 1E: Atezolizumab/ doxorubicin/ cyclophosphamideCohort 1F: Atezolizumab/Trastuzumab/Pertuzumab/ DocetaxelCohort 2A: Atezolizumab/Trastuzumab/PertuzumabCohort 2B: Atezolizumab/Trastuzumab emtansineCohort 2C: Safety ExpansionCohort 2D: Safety Expansion

Carboplatin will be administered at an initial target of area under the curve (AUC) of 6 milligrams per milliliter\*min (mg/mL\*min) via an IV infusion on Day 1 of every 21-days for 6 cycles.

Cohort 2A: Atezolizumab/Trastuzumab/PertuzumabCohort 2B: Atezolizumab/Trastuzumab emtansine

Docetaxel 75 mg/m\^2 administered via IV infusion on Day 1 every 21-days for 6 cycles.

Cohort 1F: Atezolizumab/Trastuzumab/Pertuzumab/ DocetaxelCohort 2A: Atezolizumab/Trastuzumab/PertuzumabCohort 2B: Atezolizumab/Trastuzumab emtansine

Pertuzumab 840 mg loading dose then 420 mg administered via IV infusion on Day 1 of every 21-day cycle.

Also known as: RO4368451
Cohort 1A: Atezolizumab/Trastuzumab/PertuzumabCohort 1F: Atezolizumab/Trastuzumab/Pertuzumab/ DocetaxelCohort 2A: Atezolizumab/Trastuzumab/PertuzumabCohort 2B: Atezolizumab/Trastuzumab emtansineCohort 2D: Safety Expansion

Trastuzumab 8 milligram per kilogram (mg/kg) loading dose, then 6 mg/kg administered via IV infusion on Day 1 of every 21-day cycle.

Also known as: RO0452317
Cohort 1A: Atezolizumab/Trastuzumab/PertuzumabCohort 1F: Atezolizumab/Trastuzumab/Pertuzumab/ DocetaxelCohort 2A: Atezolizumab/Trastuzumab/PertuzumabCohort 2B: Atezolizumab/Trastuzumab emtansineCohort 2D: Safety Expansion

Trastuzumab emtansine 3.6 mg/kg administered via IV infusion on Day 1 of every 21-day cycle. Dose de-escalation may occur for trastuzumab emtansine, from the full trastuzumab emtansine dose at 3.6 mg/kg on Day 1 of every 21-day cycle, potentially to 3.0 mg/kg (Cohort 1C) or 2.4 mg/kg q3w (Cohort 1D).

Also known as: RO5304020
Cohort 1B: Atezolizumab/Trastuzumab emtansine 3.6 mgCohort 1C: Atezolizumab/Trastuzumab emtansine 3.0 mgCohort 1D: Atezolizumab/Trastuzumab emtansine 2.4 mgCohort 2B: Atezolizumab/Trastuzumab emtansineCohort 2C: Safety Expansion

Doxorubicin will be administered at 60 mg/m\^2 every 2 weeks as an IV bolus over 3 to 5 minutes or as an infusion over 15 to 30 minutes.

Cohort 1E: Atezolizumab/ doxorubicin/ cyclophosphamide

Cyclophosphamide will be administered at 600 mg/m\^2 on Day 1 of each 21 day cycle as an IV bolus over 3 to 5 minutes or as an infusion, in accordance with local policy.

Cohort 1E: Atezolizumab/ doxorubicin/ cyclophosphamide

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Histologically documented HER2-positive and HER2-negative (cohort E only) breast cancer
  • Metastatic breast cancer that is measurable (Stage 1) or early breast cancer with a primary tumor size greater than (\>) 2 centimeter (cm) (Stage 2)
  • Eastern cooperative oncology group (ECOG) performed status of 0, 1 or 2; 0 or 1 (cohort E only)
  • Life expectancy of 12 or more weeks
  • Adequate hematologic and end-organ function
  • Left ventricular ejection fraction greater than or equal to (\>=) 50 percentage (%); \>=55% (cohort E only)

You may not qualify if:

  • Known central nervous system (CNS) disease, except for treated asymptomatic CNS metastases
  • Leptomeningeal disease
  • Pregnancy or lactation
  • History of autoimmune disease
  • Prior allogeneic stem cell or solid organ transplantation
  • Positive test for human immunodeficiency virus (HIV)
  • Active hepatitis B or hepatitis C

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (20)

University of Alabama at Birmingham

Birmingham, Alabama, 35294-3300, United States

Location

University of Arkansas for Medical Sciences; Winthrop Rockefeller Cancer Institute

Little Rock, Arkansas, 72205, United States

Location

Joliet oncology hematology associates

Joliet, Illinois, 60435, United States

Location

Horizon Oncology Research, Inc.

Lafayette, Indiana, 47905, United States

Location

Sidney Kimmel Comprehensive Cancer Center at Johns Hopkins

Baltimore, Maryland, 21287, United States

Location

Karmanos Cancer Center; Department of Oncology

Detroit, Michigan, 48201, United States

Location

HCA Midwest Division

Kansas City, Missouri, 64132, United States

Location

Montefiore Medical Center, Advanced Women's Health Center, Clinical Trials and Research Unit; Depart

The Bronx, New York, 10461, United States

Location

Levine Cancer Institute

Charlotte, North Carolina, 28204, United States

Location

Duke Cancer Center

Durham, North Carolina, 27710, United States

Location

Oncology Hematology Care Inc

Cincinnati, Ohio, 45242, United States

Location

St. Luke's University Health Network

Bethlehem, Pennsylvania, 18015, United States

Location

Kimmel Cancer Center Thomas Jefferson University

Philadelphia, Pennsylvania, 19107, United States

Location

Magee Womens Hospital

Pittsburgh, Pennsylvania, 15213, United States

Location

Tennessee Oncology - Chattanooga; Tennessee Oncology - East Third Street

Chattanooga, Tennessee, 37404, United States

Location

West Clinic

Germantown, Tennessee, 38138, United States

Location

Tennessee Oncology

Nashville, Tennessee, 37203, United States

Location

MD Anderson Cancer Center

Houston, Texas, 77030, United States

Location

Cancer Therapy and Research Center CTRC at UTHSCSA

San Antonio, Texas, 78229, United States

Location

Medical College of Wisconsin

Milwaukee, Wisconsin, 53226, United States

Location

MeSH Terms

Conditions

Breast Neoplasms

Interventions

atezolizumabCarboplatinDocetaxelpertuzumabTrastuzumabAdo-Trastuzumab EmtansineDoxorubicinCyclophosphamide

Condition Hierarchy (Ancestors)

Neoplasms by SiteNeoplasmsBreast DiseasesSkin DiseasesSkin and Connective Tissue Diseases

Intervention Hierarchy (Ancestors)

Coordination ComplexesOrganic ChemicalsTaxoidsCyclodecanesCycloparaffinsHydrocarbons, AlicyclicHydrocarbons, CyclicHydrocarbonsDiterpenesTerpenesAntibodies, Monoclonal, HumanizedAntibodies, MonoclonalAntibodiesImmunoglobulinsImmunoproteinsBlood ProteinsProteinsAmino Acids, Peptides, and ProteinsSerum GlobulinsGlobulinsMaytansineMacrolidesLactonesLactams, MacrocyclicMacrocyclic CompoundsPolycyclic CompoundsDaunorubicinAnthracyclinesNaphthacenesPolycyclic Aromatic HydrocarbonsHydrocarbons, AromaticAminoglycosidesGlycosidesCarbohydratesPhosphoramide MustardsNitrogen Mustard CompoundsMustard CompoundsHydrocarbons, HalogenatedPhosphoramidesOrganophosphorus Compounds

Study Officials

  • Clinical Trials

    Hoffmann-La Roche

    STUDY DIRECTOR

Study Design

Study Type
interventional
Phase
phase 1
Allocation
NON RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

November 12, 2015

First Posted

November 16, 2015

Study Start

December 31, 2015

Primary Completion

November 13, 2019

Study Completion

November 13, 2019

Last Updated

February 5, 2020

Record last verified: 2020-01

Locations