NCT01106625

Brief Summary

The purpose of this study is to evaluate the efficacy and safety of 2 different doses of canagliflozin compared with placebo in patients with type 2 diabetes mellitus who are receiving treatment with metformin and sulphonylurea and have inadequate glycemic (blood sugar) control.

Trial Health

98
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
469

participants targeted

Target at P50-P75 for phase_3 diabetes-mellitus-type-2

Timeline
Completed

Started May 2010

Typical duration for phase_3 diabetes-mellitus-type-2

Geographic Reach
12 countries

76 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

April 1, 2010

Completed
19 days until next milestone

First Posted

Study publicly available on registry

April 20, 2010

Completed
11 days until next milestone

Study Start

First participant enrolled

May 1, 2010

Completed
1.3 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

September 1, 2011

Completed
7 months until next milestone

Study Completion

Last participant's last visit for all outcomes

April 1, 2012

Completed
1.2 years until next milestone

Results Posted

Study results publicly available

May 29, 2013

Completed
Last Updated

June 20, 2013

Status Verified

June 1, 2013

Enrollment Period

1.3 years

First QC Date

April 1, 2010

Results QC Date

April 10, 2013

Last Update Submit

June 12, 2013

Conditions

Keywords

CanagliflozinPlaceboMetforminSulphonylureaHemoglobin A1cType 2 diabetes mellitus

Outcome Measures

Primary Outcomes (1)

  • Change in HbA1c From Baseline to Week 26

    The table below shows the least-squares (LS) mean change in HbA1c from Baseline to Week 26 for each treatment group. The statistical analyses show the treatment differences (ie, each canagliflozin group minus placebo) in the LS mean change.

    Day 1 (Baseline) and Week 26

Secondary Outcomes (6)

  • Percentage of Patients With HbA1c <7% at Week 26

    Week 26

  • Change in Fasting Plasma Glucose (FPG) From Baseline to Week 26

    Day 1 (Baseline) and Week 26

  • Percent Change in Body Weight From Baseline to Week 26

    Day 1 (Baseline) and Week 26

  • Change in Systolic Blood Pressure (SBP) From Baseline to Week 26

    Day 1 (Baseline) and Week 26

  • Percent Change in Triglycerides From Baseline to Week 26

    Day 1 (Baseline) and Week 26

  • +1 more secondary outcomes

Study Arms (3)

Canagliflozin 100 mg

EXPERIMENTAL

Each patient will receive 100 mg of canagliflozin once daily for 52 weeks with protocol-specified doses of metformin and sulphonylurea.

Drug: CanagliflozinDrug: MetforminDrug: Sulphonylruea

Canagliflozin 300 mg

EXPERIMENTAL

Each patient will receive 300 mg of canagliflozin once daily for 52 weeks with protocol-specified doses of metformin and sulphonylurea.

Drug: CanagliflozinDrug: MetforminDrug: Sulphonylruea

Placebo

PLACEBO COMPARATOR

Each patient will receive matching placebo once daily for 52 weeks with protocol-specified doses of metformin and sulphonylurea.

Drug: PlaceboDrug: MetforminDrug: Sulphonylruea

Interventions

One 100 mg or 300 mg over-encapsulated tablet orally (by mouth) once daily for 52 weeks with protocol-specified doses of metformin and sulphonylurea.

Canagliflozin 100 mgCanagliflozin 300 mg

One matching placebo capsule orally once daily for 52 weeks with protocol-specified doses of metformin and sulphonylurea.

Placebo

The patient's stable dose of background metformin therapy should be continued throughout the study.

Canagliflozin 100 mgCanagliflozin 300 mgPlacebo

The patient's stable dose of background sulphonylurea therapy should be continued throughout the study.

Canagliflozin 100 mgCanagliflozin 300 mgPlacebo

Eligibility Criteria

Age18 Years - 80 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • All patients must have a diagnosis of T2DM and be currently treated with metformin and sulphonylurea
  • Patients in the study must have a HbA1c between \>=7 and \<=10.5%
  • Patients must have a fasting plasma glucose (FPG) \<270 mg/dL (15 mmol/L)

You may not qualify if:

  • History of diabetic ketoacidosis, type 1 diabetes mellitus (T1DM), pancreas or beta cell transplantation, or diabetes secondary to pancreatitis or pancreatectomy, or a severe hypoglycemic episode within 6 months before screening

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (76)

Unknown Facility

Huntsville, Alabama, United States

Location

Unknown Facility

Little Rock, Alaska, United States

Location

Unknown Facility

Phoenix, Arizona, United States

Location

Unknown Facility

Chino, California, United States

Location

Unknown Facility

Fair Oaks, California, United States

Location

Unknown Facility

Roseville, California, United States

Location

Unknown Facility

Wes Hills, California, United States

Location

Unknown Facility

Waterbury, Connecticut, United States

Location

Unknown Facility

Jacksonville, Florida, United States

Location

Unknown Facility

New Port Richey, Florida, United States

Location

Unknown Facility

Ocala, Florida, United States

Location

Unknown Facility

St. Petersburg, Florida, United States

Location

Unknown Facility

West Palm Beach, Florida, United States

Location

Unknown Facility

Augusta, Georgia, United States

Location

Unknown Facility

Roswell, Georgia, United States

Location

Unknown Facility

Chicago, Illinois, United States

Location

Unknown Facility

Lexington, Kentucky, United States

Location

Unknown Facility

New Orleans, Louisiana, United States

Location

Unknown Facility

Reisterstown, Maryland, United States

Location

Unknown Facility

Olive Branch, Mississippi, United States

Location

Unknown Facility

St Louis, Missouri, United States

Location

Unknown Facility

Westfield, New York, United States

Location

Unknown Facility

Greenville, North Carolina, United States

Location

Unknown Facility

Cincinnati, Ohio, United States

Location

Unknown Facility

Tulsa, Oklahoma, United States

Location

Unknown Facility

Medford, Oregon, United States

Location

Unknown Facility

Altoona, Pennsylvania, United States

Location

Unknown Facility

Harleysville, Pennsylvania, United States

Location

Unknown Facility

Levittown, Pennsylvania, United States

Location

Unknown Facility

Sellersville, Pennsylvania, United States

Location

Unknown Facility

Greer, South Carolina, United States

Location

Unknown Facility

Bryan, Texas, United States

Location

Unknown Facility

Dallas, Texas, United States

Location

Unknown Facility

DeSoto, Texas, United States

Location

Unknown Facility

Salt Lake City, Utah, United States

Location

Unknown Facility

South Burlington, Vermont, United States

Location

Unknown Facility

Wenatchee, Washington, United States

Location

Unknown Facility

Freemantle, Australia

Location

Unknown Facility

Heidelberg Heights, Australia

Location

Unknown Facility

Meadowbrook, Australia

Location

Unknown Facility

Nedlands, Australia

Location

Unknown Facility

Wollongong, Australia

Location

Unknown Facility

Aalst, Belgium

Location

Unknown Facility

Bonheiden, Belgium

Location

Unknown Facility

Edegem, Belgium

Location

Unknown Facility

Leuven, Belgium

Location

Unknown Facility

Corbeil-Essonnes, France

Location

Unknown Facility

La Rochelle, France

Location

Unknown Facility

Le Creusot, France

Location

Unknown Facility

Poitiers, France

Location

Unknown Facility

Vénissieux, France

Location

Unknown Facility

Guatemala City, Guatemala

Location

Unknown Facility

Balatonfüred, Hungary

Location

Unknown Facility

Budapest, Hungary

Location

Unknown Facility

Győr, Hungary

Location

Unknown Facility

Zalaegerszeg, Hungary

Location

Unknown Facility

Haifa, Israel

Location

Unknown Facility

Holon, Israel

Location

Unknown Facility

Jerusalem, Israel

Location

Unknown Facility

Tel Aviv, Israel

Location

Unknown Facility

Guadalajara, Mexico

Location

Unknown Facility

Monterrey, Mexico

Location

Unknown Facility

Carolina, Puerto Rico

Location

Unknown Facility

Trujillo Alto, Puerto Rico

Location

Unknown Facility

Arkhangelsk, Russia

Location

Unknown Facility

Saint Petersburg, Russia

Location

Unknown Facility

Samara, Russia

Location

Unknown Facility

Alicante, Spain

Location

Unknown Facility

Almería, Spain

Location

Unknown Facility

Málaga, Spain

Location

Unknown Facility

Seville, Spain

Location

Unknown Facility

Valencia, Spain

Location

Unknown Facility

Belfast, United Kingdom

Location

Unknown Facility

Bolton, United Kingdom

Location

Unknown Facility

Liverpool, United Kingdom

Location

Unknown Facility

Manchester, United Kingdom

Location

Related Publications (17)

  • Cai J, Delahanty LM, Akapame S, Slee A, Traina S. Impact of Canagliflozin Treatment on Health-Related Quality of Life among People with Type 2 Diabetes Mellitus: A Pooled Analysis of Patient-Reported Outcomes from Randomized Controlled Trials. Patient. 2018 Jun;11(3):341-352. doi: 10.1007/s40271-017-0290-4.

  • Davies MJ, Merton K, Vijapurkar U, Yee J, Qiu R. Efficacy and safety of canagliflozin in patients with type 2 diabetes based on history of cardiovascular disease or cardiovascular risk factors: a post hoc analysis of pooled data. Cardiovasc Diabetol. 2017 Mar 21;16(1):40. doi: 10.1186/s12933-017-0517-7.

  • Pfeifer M, Townsend RR, Davies MJ, Vijapurkar U, Ren J. Effects of canagliflozin, a sodium glucose co-transporter 2 inhibitor, on blood pressure and markers of arterial stiffness in patients with type 2 diabetes mellitus: a post hoc analysis. Cardiovasc Diabetol. 2017 Feb 27;16(1):29. doi: 10.1186/s12933-017-0511-0.

  • Gilbert RE, Mende C, Vijapurkar U, Sha S, Davies MJ, Desai M. Effects of Canagliflozin on Serum Magnesium in Patients With Type 2 Diabetes Mellitus: A Post Hoc Analysis of Randomized Controlled Trials. Diabetes Ther. 2017 Apr;8(2):451-458. doi: 10.1007/s13300-017-0232-0. Epub 2017 Feb 14.

  • Qiu R, Balis D, Xie J, Davies MJ, Desai M, Meininger G. Longer-term safety and tolerability of canagliflozin in patients with type 2 diabetes: a pooled analysis. Curr Med Res Opin. 2017 Mar;33(3):553-562. doi: 10.1080/03007995.2016.1271780. Epub 2017 Jan 4.

  • John M, Cerdas S, Violante R, Deerochanawong C, Hassanein M, Slee A, Canovatchel W, Hamilton G. Efficacy and safety of canagliflozin in patients with type 2 diabetes mellitus living in hot climates. Int J Clin Pract. 2016 Sep;70(9):775-85. doi: 10.1111/ijcp.12868.

  • Watts NB, Bilezikian JP, Usiskin K, Edwards R, Desai M, Law G, Meininger G. Effects of Canagliflozin on Fracture Risk in Patients With Type 2 Diabetes Mellitus. J Clin Endocrinol Metab. 2016 Jan;101(1):157-66. doi: 10.1210/jc.2015-3167. Epub 2015 Nov 18.

  • Lavalle-Gonzalez FJ, Eliaschewitz FG, Cerdas S, Chacon Mdel P, Tong C, Alba M. Efficacy and safety of canagliflozin in patients with type 2 diabetes mellitus from Latin America. Curr Med Res Opin. 2016;32(3):427-39. doi: 10.1185/03007995.2015.1121865. Epub 2016 Jan 14.

  • Blonde L, Woo V, Mathieu C, Yee J, Vijapurkar U, Canovatchel W, Meininger G. Achievement of treatment goals with canagliflozin in patients with type 2 diabetes mellitus: a pooled analysis of randomized controlled trials. Curr Med Res Opin. 2015 Nov;31(11):1993-2000. doi: 10.1185/03007995.2015.1082991. Epub 2015 Sep 28.

  • Gavin JR 3rd, Davies MJ, Davies M, Vijapurkar U, Alba M, Meininger G. The efficacy and safety of canagliflozin across racial groups in patients with type 2 diabetes mellitus. Curr Med Res Opin. 2015;31(9):1693-702. doi: 10.1185/03007995.2015.1067192. Epub 2015 Sep 4.

  • Cefalu WT, Stenlof K, Leiter LA, Wilding JP, Blonde L, Polidori D, Xie J, Sullivan D, Usiskin K, Canovatchel W, Meininger G. Effects of canagliflozin on body weight and relationship to HbA1c and blood pressure changes in patients with type 2 diabetes. Diabetologia. 2015 Jun;58(6):1183-7. doi: 10.1007/s00125-015-3547-2. Epub 2015 Mar 27.

  • Weir MR, Januszewicz A, Gilbert RE, Vijapurkar U, Kline I, Fung A, Meininger G. Effect of canagliflozin on blood pressure and adverse events related to osmotic diuresis and reduced intravascular volume in patients with type 2 diabetes mellitus. J Clin Hypertens (Greenwich). 2014 Dec;16(12):875-82. doi: 10.1111/jch.12425. Epub 2014 Oct 20.

  • Usiskin K, Kline I, Fung A, Mayer C, Meininger G. Safety and tolerability of canagliflozin in patients with type 2 diabetes mellitus: pooled analysis of phase 3 study results. Postgrad Med. 2014 May;126(3):16-34. doi: 10.3810/pgm.2014.05.2753.

  • Weir MR, Kline I, Xie J, Edwards R, Usiskin K. Effect of canagliflozin on serum electrolytes in patients with type 2 diabetes in relation to estimated glomerular filtration rate (eGFR). Curr Med Res Opin. 2014 Sep;30(9):1759-68. doi: 10.1185/03007995.2014.919907. Epub 2014 May 22.

  • Sinclair A, Bode B, Harris S, Vijapurkar U, Mayer C, Fung A, Shaw W, Usiskin K, Desai M, Meininger G. Efficacy and safety of canagliflozin compared with placebo in older patients with type 2 diabetes mellitus: a pooled analysis of clinical studies. BMC Endocr Disord. 2014 Apr 18;14:37. doi: 10.1186/1472-6823-14-37.

  • Polidori D, Mari A, Ferrannini E. Canagliflozin, a sodium glucose co-transporter 2 inhibitor, improves model-based indices of beta cell function in patients with type 2 diabetes. Diabetologia. 2014 May;57(5):891-901. doi: 10.1007/s00125-014-3196-x. Epub 2014 Mar 1.

  • Nyirjesy P, Sobel JD, Fung A, Mayer C, Capuano G, Ways K, Usiskin K. Genital mycotic infections with canagliflozin, a sodium glucose co-transporter 2 inhibitor, in patients with type 2 diabetes mellitus: a pooled analysis of clinical studies. Curr Med Res Opin. 2014 Jun;30(6):1109-19. doi: 10.1185/03007995.2014.890925. Epub 2014 Feb 21.

MeSH Terms

Conditions

Diabetes Mellitus, Type 2

Interventions

CanagliflozinMetformin

Condition Hierarchy (Ancestors)

Diabetes MellitusGlucose Metabolism DisordersMetabolic DiseasesNutritional and Metabolic DiseasesEndocrine System Diseases

Intervention Hierarchy (Ancestors)

ThiophenesSulfur CompoundsOrganic ChemicalsHeterocyclic Compounds, 1-RingHeterocyclic CompoundsGlucosidesGlycosidesCarbohydratesBiguanidesGuanidinesAmidines

Results Point of Contact

Title
Vice President, Franchise Medical Leader, Cardiovascular & Metabolism Franchise
Organization
Janssen Research & Development, LLC

Study Officials

  • Janssen Research & Development, LLC C. Clinical Trial

    Janssen Research & Development, LLC

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
TRIPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

April 1, 2010

First Posted

April 20, 2010

Study Start

May 1, 2010

Primary Completion

September 1, 2011

Study Completion

April 1, 2012

Last Updated

June 20, 2013

Results First Posted

May 29, 2013

Record last verified: 2013-06

Locations