NCT00001337

Brief Summary

5-Drug Combination Chemotherapy with Hematologic Toxicity Attenuation. Etoposide phosphate, prednisone, vincristine sulfate (Oncovin), cyclophosphamide, and doxorubicin hydrochloride (hydroxydaunorubicin)(EPOCH): Etoposide, VP-16, NSC-141540; Prednisone, PRED, NSC-10023; Vincristine, VCR, NSC-67574; Cyclophosphamide, CTX, NSC-26271; Doxorubicin, DOX, NSC-123127; with Granulocyte Colony-Stimulating Factor (Amgen), Granulocyte colony-stimulating factor (G-CSF), NSC-614629.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
348

participants targeted

Target at P75+ for phase_2

Timeline
Completed

Started May 1993

Longer than P75 for phase_2

Geographic Reach
1 country

5 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

May 8, 1993

Completed
6.5 years until next milestone

First Submitted

Initial submission to the registry

November 3, 1999

Completed
1 day until next milestone

First Posted

Study publicly available on registry

November 4, 1999

Completed
24.6 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

May 24, 2024

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

May 24, 2024

Completed
1.1 years until next milestone

Results Posted

Study results publicly available

June 12, 2025

Completed
Last Updated

June 22, 2025

Status Verified

June 1, 2025

Enrollment Period

31.1 years

First QC Date

November 3, 1999

Results QC Date

April 15, 2025

Last Update Submit

June 12, 2025

Conditions

Keywords

Primary Mediastinal B-Cell LymphomaCD20 +Diffuse Large B-Cell LymphomaAnaplastic Large Cell LymphomaDe Novo

Outcome Measures

Primary Outcomes (2)

  • Overall Response (Complete Response + Partial Response)

    Overall response defined as a Complete Response + Partial Response was measured by the Response Criteria. Complete Response is disappearance of all signs and symptoms of lymphoma for a period of at least one month. Partial Response is 50% or greater decrease in the sum of the products of the longest perpendicular diameters of all measured lesions lasting for a period of at least one month.

    Time frame was from beginning of therapy until the end of therapy, an average of 6 months

  • Progression Free Survival (PFS)

    The Dixon-Simon method will be used to determine whether large B-cell lymphomas expressing BCL-2 (+) participants may experience an improved progression free survival with Etoposide, VP-16, and Doxorubicin with Prednisone, Cyclophosphamide, and Rituximab (EPOCH-R) compared to EPOCH alone, and to obtain a concurrent, precisely determined measure of progression free survival. PFS is the time from start of treatment to documented evidence of disease progression. Progression is an increase of 25% or more in the sum of the products of the longest perpendicular diameters of all measured lesions, or the appearance of any new lesions measured by the Response Criteria.

    Progression free survival was calculated from study entry until progression or death from any cause. Median follow up of evaluable participants was 5 years (range 2-7 years)

Secondary Outcomes (1)

  • Proportion of Participants With Serious and/or Non-serious Adverse Events Leading to Discontinuation of Therapy

    Initiation of study drug until 30 days after treatment, an average of 6 months

Other Outcomes (1)

  • Number of Participants With Serious and/or Non-serious Adverse Events Assessed by the Common Terminology Criteria for Adverse Events (CTCAE v4.0)

    Time frame is from study entry until 30 days after completing study therapy, approximately 5 years.

Study Arms (2)

With EPOCH-R (Etoposide, Doxorubicin, Prednisone, Cyclophosphamide and Rituximab)

EXPERIMENTAL

Subgroup 1 (SG1) - All participants who received combination Rituximab (EPOCH-R). Rituximab 375 mg/m\^2 intravenous (IV) on day 1, every 21 days, prednisone 100mg by mouth (PO) twice a day (bid) on days 1 through 5 every 21 days, and cyclophosphamide 750mg/m\^2 on day 5 every 21 days. Doxorubicin 10mg/m\^2/day, vincristine 0.4mg/m\^2/day, and etoposide 50mg/m\^2/day were delivered as continuous intravenous (CIV) infusions over 96 hours starting on day 1 every 21 days. Dose levels were adjusted on doxorubicin, etoposide, and cyclophosphamide each cycle based on neutrophil nadir.

Drug: EtoposideBiological: RituximabDrug: PrednisoneDrug: CyclophosphamideDrug: VincristineDrug: DoxorubicinDiagnostic Test: MRIDiagnostic Test: CTProcedure: BiopsyDiagnostic Test: PET scanProcedure: LaparotomyOther: OndansetronOther: ProchlorperazineOther: OmeprazoleOther: Docusate Sodium + SennosidesOther: Lactulose

EPOCH Alone (Etoposide, Doxorubicin, Prednisone, and Cyclophosphamide)

EXPERIMENTAL

Subgroup 2 (SG2) - EPOCH alone: All participants who received Prednisone 100mg by mouth (PO) twice a day (bid) on days 1 through 5 every 21 days, and cyclophosphamide 750mg/m\^2 on day 5 every 21 days. Doxorubicin 10mg/m\^2/day, vincristine 0.4mg/m\^2/day, and etoposide 50mg/m\^2/day were delivered as continuous intravenous (CIV) infusions over 96 hours starting on day 1 every 21 days. Dose levels were adjusted on doxorubicin, etoposide, and cyclophosphamide each cycle based on neutrophil nadir.

Drug: EtoposideDrug: PrednisoneDrug: CyclophosphamideDrug: VincristineDrug: DoxorubicinDiagnostic Test: MRIDiagnostic Test: CTProcedure: BiopsyDiagnostic Test: PET scanProcedure: LaparotomyOther: OndansetronOther: ProchlorperazineOther: OmeprazoleOther: Docusate Sodium + SennosidesOther: Lactulose

Interventions

Etoposide 50mg/m\^2/day were delivered as continuous intravenous (CIV) infusions over 96 hours starting on day 1 every 21 days. Combination chemotherapy given with Rituximab, Etoposide, VP-16; Prednisone, Cyclophosphamide, Vincristine, and Doxorubicin (EPOCH-R) intravenous (IV) every 3 weeks for 6 cycles.

Also known as: VP-16
EPOCH Alone (Etoposide, Doxorubicin, Prednisone, and Cyclophosphamide)With EPOCH-R (Etoposide, Doxorubicin, Prednisone, Cyclophosphamide and Rituximab)
RituximabBIOLOGICAL

Rituximab given on Day 1 of combination chemotherapy (EPOCH-R) every 3 weeks for 6 cycles. Combination chemotherapy given with Rituximab, Etoposide, VP-16; Prednisone, Cyclophosphamide, Vincristine, and Doxorubicin (EPOCH-R) intravenous (IV) every 3 weeks for 6 cycles.

Also known as: Rituxan
With EPOCH-R (Etoposide, Doxorubicin, Prednisone, Cyclophosphamide and Rituximab)

Prednisone 100mg by mouth (PO) twice a day (bid) on days 1 through 5 every 21 days. Combination chemotherapy given with Rituximab, Etoposide, VP-16; Prednisone, Cyclophosphamide, Vincristine, and Doxorubicin (EPOCH-R) intravenous (IV) every 3 weeks for 6 cycles.

Also known as: Rayos, Deltasone, Prednisone Intensol
EPOCH Alone (Etoposide, Doxorubicin, Prednisone, and Cyclophosphamide)With EPOCH-R (Etoposide, Doxorubicin, Prednisone, Cyclophosphamide and Rituximab)

Cyclophosphamide 750mg/m\^2 on day 5 every 21 days. Combination chemotherapy given with Rituximab, Etoposide, VP-16; Prednisone, Cyclophosphamide, Vincristine, and Doxorubicin (EPOCH-R) intravenous (IV) every 3 weeks for 6 cycles.

Also known as: Cytoxan
EPOCH Alone (Etoposide, Doxorubicin, Prednisone, and Cyclophosphamide)With EPOCH-R (Etoposide, Doxorubicin, Prednisone, Cyclophosphamide and Rituximab)

Vincristine 0.4mg/m\^2/day. Combination chemotherapy given with Rituximab, Etoposide, VP-16; Prednisone, Cyclophosphamide, Vincristine, and Doxorubicin (EPOCH-R) intravenous (IV) every 3 weeks for 6 cycles.

Also known as: Marqibo, Vincasar PFS
EPOCH Alone (Etoposide, Doxorubicin, Prednisone, and Cyclophosphamide)With EPOCH-R (Etoposide, Doxorubicin, Prednisone, Cyclophosphamide and Rituximab)

Doxorubicin 10mg/m\^2/day. Combination chemotherapy given with Rituximab, Etoposide, VP-16; Prednisone, Cyclophosphamide, Vincristine, and Doxorubicin (EPOCH-R) intravenous (IV) every 3 weeks for 6 cycles.

Also known as: Lipodox, Lipodox 50, Doxil
EPOCH Alone (Etoposide, Doxorubicin, Prednisone, and Cyclophosphamide)With EPOCH-R (Etoposide, Doxorubicin, Prednisone, Cyclophosphamide and Rituximab)
MRIDIAGNOSTIC_TEST

Baseline and/or on completion of therapy.

Also known as: Magnetic resonance imaging
EPOCH Alone (Etoposide, Doxorubicin, Prednisone, and Cyclophosphamide)With EPOCH-R (Etoposide, Doxorubicin, Prednisone, Cyclophosphamide and Rituximab)
CTDIAGNOSTIC_TEST

Baseline and/or on completion of therapy.

Also known as: Computed tomography
EPOCH Alone (Etoposide, Doxorubicin, Prednisone, and Cyclophosphamide)With EPOCH-R (Etoposide, Doxorubicin, Prednisone, Cyclophosphamide and Rituximab)
BiopsyPROCEDURE

Baseline and/or on completion of therapy.

EPOCH Alone (Etoposide, Doxorubicin, Prednisone, and Cyclophosphamide)With EPOCH-R (Etoposide, Doxorubicin, Prednisone, Cyclophosphamide and Rituximab)
PET scanDIAGNOSTIC_TEST

As clinically indicated.

Also known as: positron emission tomography scan
EPOCH Alone (Etoposide, Doxorubicin, Prednisone, and Cyclophosphamide)With EPOCH-R (Etoposide, Doxorubicin, Prednisone, Cyclophosphamide and Rituximab)
LaparotomyPROCEDURE

As clinically indicated.

EPOCH Alone (Etoposide, Doxorubicin, Prednisone, and Cyclophosphamide)With EPOCH-R (Etoposide, Doxorubicin, Prednisone, Cyclophosphamide and Rituximab)

Nausea and/or vomiting.

Also known as: Zofran ODT, Zuplenz, Zofran
EPOCH Alone (Etoposide, Doxorubicin, Prednisone, and Cyclophosphamide)With EPOCH-R (Etoposide, Doxorubicin, Prednisone, Cyclophosphamide and Rituximab)

Nausea and/or vomiting.

Also known as: Compro
EPOCH Alone (Etoposide, Doxorubicin, Prednisone, and Cyclophosphamide)With EPOCH-R (Etoposide, Doxorubicin, Prednisone, Cyclophosphamide and Rituximab)

Gastroesophageal reflux disease (GERD).

Also known as: Prilosec OTC, Zegerid, OmePPi
EPOCH Alone (Etoposide, Doxorubicin, Prednisone, and Cyclophosphamide)With EPOCH-R (Etoposide, Doxorubicin, Prednisone, Cyclophosphamide and Rituximab)

Constipation.

Also known as: Senna-Plus, Colace 2-in-1, Dok Plus
EPOCH Alone (Etoposide, Doxorubicin, Prednisone, and Cyclophosphamide)With EPOCH-R (Etoposide, Doxorubicin, Prednisone, Cyclophosphamide and Rituximab)

Constipation

Also known as: Kristalose, Enulose, Generlac
EPOCH Alone (Etoposide, Doxorubicin, Prednisone, and Cyclophosphamide)With EPOCH-R (Etoposide, Doxorubicin, Prednisone, Cyclophosphamide and Rituximab)

Eligibility Criteria

Age12 Years+
Sexall
Healthy VolunteersNo
Age GroupsChild (0-17), Adult (18-64), Older Adult (65+)

You may qualify if:

  • Non-Hodgkin's lymphomas in the following categories: mediastinal gray zone lymphoma and primary mediastinal B cell lymphoma.
  • Diagnosis confirmed by staff of the Hematopathology Section, Laboratory of Pathology, National Cancer Institute (NCI). Tissue blocks from patients treated in extramural sites must be forwarded to the NCI for analysis of B-cell leukemia/lymphoma 2 (bcl-2) by immunohistochemistry (IHC) and other markers within 1 month of study entry.
  • Patients greater than or equal to 12 years old.
  • Stage and Prognosis of Patients: Any stage for mediastinal gray zone lymphoma (MGZL) and primary mediastinal B-cell lymphoma (PMBL).
  • No prior systemic chemotherapy. Patients may be entered if they have had prior limited-field radiotherapy, a short course of glucocorticoids and/or cyclophosphamide for an urgent problem at diagnosis (e.g. epidural cord compression, superior vena cava syndrome).
  • Human immunodeficiency virus (HIV) negative.
  • Not pregnant or nursing.
  • Adequate major organ function \[in adults: serum creatinine less than or equal to 1.5 mg/dl or creatinine clearance greater than 60 ml/min; and in children serum creatinine (CR) less than or equal to age-adjusted normal (age 12 to 15 maximum serum creatinine 1.2 mg/dl and age greater than 15 maximum serum creatinine 1.5 mg/dl); bilirubin less than 1.5 mg/dl; absolute neutrophil count (ANC) greater than 1,000 and platelets greater than 100,000) unless impairment is due to organ involvement by lymphoma or immune-mediated mechanism caused by lymphoma.
  • No active symptomatic ischemic heart disease, myocardial infarction or congestive heart failure within the past year. If multi-gated acquisition (MUGA) is obtained, the left ventricular ejection fraction (LVEF) should exceed 40%.
  • No other serious concomitant medical illnesses or uncontrolled active infection that would jeopardize the patient's ability to receive the regimen with reasonable safety.
  • No history of unrelated (non-lymphomatous) neoplasms within past 5 years other than non-melanoma skin cancer or in-situ cancer.
  • Ability to give informed consent.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (5)

Holy Cross Hospital, Fort Lauderdale

Fort Lauderdale, Florida, 33308, United States

Location

University of Maryland, Baltimore

Baltimore, Maryland, 21201-1595, United States

Location

National Institutes of Health Clinical Center

Bethesda, Maryland, 20892, United States

Location

Brigham and Women's Hospital

Boston, Massachusetts, 02115, United States

Location

St. Luke's Roosevelt Hospital

New York, New York, 10025, United States

Location

Related Publications (10)

  • Klimo P, Connors JM. MACOP-B chemotherapy for the treatment of diffuse large-cell lymphoma. Ann Intern Med. 1985 May;102(5):596-602. doi: 10.7326/0003-4819-102-5-596.

    PMID: 2580468BACKGROUND
  • Lai GM, Chen YN, Mickley LA, Fojo AT, Bates SE. P-glycoprotein expression and schedule dependence of adriamycin cytotoxicity in human colon carcinoma cell lines. Int J Cancer. 1991 Nov 11;49(5):696-703. doi: 10.1002/ijc.2910490512.

    PMID: 1682280BACKGROUND
  • DeVita VT Jr, Canellos GP, Chabner B, Schein P, Hubbard SP, Young RC. Advanced diffuse histiocytic lymphoma, a potentially curable disease. Lancet. 1975 Feb 1;1(7901):248-50. doi: 10.1016/s0140-6736(75)91142-3.

    PMID: 46388BACKGROUND
  • Lai C, Cole DE, Steinberg SM, Lucas N, Dombi E, Melani C, Roschewski M, Balis F, Widemann BC, Wilson WH. Doxorubicin pharmacokinetics and toxicity in patients with aggressive lymphoma and hepatic impairment. Blood Adv. 2023 Feb 28;7(4):529-532. doi: 10.1182/bloodadvances.2022007431.

  • Miljkovic MD, Melani C, Pittaluga S, Lakhotia R, Lucas N, Jacob A, Yusko E, Jaffe ES, Wilson WH, Roschewski M. Next-generation sequencing-based monitoring of circulating tumor DNA reveals clonotypic heterogeneity in untreated PTCL. Blood Adv. 2021 Oct 26;5(20):4198-4210. doi: 10.1182/bloodadvances.2020003679.

  • Kurtz DM, Scherer F, Jin MC, Soo J, Craig AFM, Esfahani MS, Chabon JJ, Stehr H, Liu CL, Tibshirani R, Maeda LS, Gupta NK, Khodadoust MS, Advani RH, Levy R, Newman AM, Duhrsen U, Huttmann A, Meignan M, Casasnovas RO, Westin JR, Roschewski M, Wilson WH, Gaidano G, Rossi D, Diehn M, Alizadeh AA. Circulating Tumor DNA Measurements As Early Outcome Predictors in Diffuse Large B-Cell Lymphoma. J Clin Oncol. 2018 Oct 1;36(28):2845-2853. doi: 10.1200/JCO.2018.78.5246. Epub 2018 Aug 20.

  • Melani C, Advani R, Roschewski M, Walters KM, Chen CC, Baratto L, Ahlman MA, Miljkovic MD, Steinberg SM, Lam J, Shovlin M, Dunleavy K, Pittaluga S, Jaffe ES, Wilson WH. End-of-treatment and serial PET imaging in primary mediastinal B-cell lymphoma following dose-adjusted EPOCH-R: a paradigm shift in clinical decision making. Haematologica. 2018 Aug;103(8):1337-1344. doi: 10.3324/haematol.2018.192492. Epub 2018 May 10.

  • Wilson WH, Pittaluga S, Nicolae A, Camphausen K, Shovlin M, Steinberg SM, Roschewski M, Staudt LM, Jaffe ES, Dunleavy K. A prospective study of mediastinal gray-zone lymphoma. Blood. 2014 Sep 4;124(10):1563-9. doi: 10.1182/blood-2014-03-564906. Epub 2014 Jul 14.

  • Dunleavy K, Pittaluga S, Shovlin M, Steinberg SM, Cole D, Grant C, Widemann B, Staudt LM, Jaffe ES, Little RF, Wilson WH. Low-intensity therapy in adults with Burkitt's lymphoma. N Engl J Med. 2013 Nov 14;369(20):1915-25. doi: 10.1056/NEJMoa1308392.

  • Dunleavy K, Pittaluga S, Maeda LS, Advani R, Chen CC, Hessler J, Steinberg SM, Grant C, Wright G, Varma G, Staudt LM, Jaffe ES, Wilson WH. Dose-adjusted EPOCH-rituximab therapy in primary mediastinal B-cell lymphoma. N Engl J Med. 2013 Apr 11;368(15):1408-16. doi: 10.1056/NEJMoa1214561.

Related Links

MeSH Terms

Conditions

Lymphoma, Large B-Cell, DiffuseBurkitt LymphomaLymphoma, Large-Cell, Anaplastic

Interventions

EtoposideRituximabPrednisoneCyclophosphamideVincristineDoxorubicinliposomal doxorubicinMagnetic Resonance ImagingTomography, X-Ray ComputedBiopsyPositron-Emission TomographyLaparotomyOndansetronProchlorperazineOmeprazoleomeprazole, sodium bicarbonate drug combinationDioctyl Sulfosuccinic AcidSennosidesdoxidanLactulose

Condition Hierarchy (Ancestors)

Lymphoma, B-CellLymphoma, Non-HodgkinLymphomaNeoplasms by Histologic TypeNeoplasmsLymphoproliferative DisordersLymphatic DiseasesHemic and Lymphatic DiseasesImmunoproliferative DisordersImmune System DiseasesEpstein-Barr Virus InfectionsHerpesviridae InfectionsDNA Virus InfectionsVirus DiseasesInfectionsTumor Virus InfectionsLymphoma, T-Cell

Intervention Hierarchy (Ancestors)

PodophyllotoxinTetrahydronaphthalenesNaphthalenesPolycyclic Aromatic HydrocarbonsHydrocarbons, AromaticHydrocarbons, CyclicHydrocarbonsOrganic ChemicalsPolycyclic CompoundsGlucosidesGlycosidesCarbohydratesAntibodies, Monoclonal, Murine-DerivedAntibodies, MonoclonalAntibodiesImmunoglobulinsImmunoproteinsBlood ProteinsProteinsAmino Acids, Peptides, and ProteinsSerum GlobulinsGlobulinsPregnadienediolsPregnadienesPregnanesSteroidsFused-Ring CompoundsPhosphoramide MustardsNitrogen Mustard CompoundsMustard CompoundsHydrocarbons, HalogenatedPhosphoramidesOrganophosphorus CompoundsVinca AlkaloidsSecologanin Tryptamine AlkaloidsIndole AlkaloidsAlkaloidsHeterocyclic CompoundsIndolesHeterocyclic Compounds, 2-RingHeterocyclic Compounds, Fused-RingIndolizidinesIndolizinesDaunorubicinAnthracyclinesNaphthacenesAminoglycosidesTomographyDiagnostic ImagingDiagnostic Techniques and ProceduresDiagnosisImage Interpretation, Computer-AssistedRadiographic Image EnhancementImage EnhancementPhotographyRadiographyTomography, X-RayCytodiagnosisCytological TechniquesClinical Laboratory TechniquesSpecimen HandlingDiagnostic Techniques, SurgicalSurgical Procedures, OperativeInvestigative TechniquesTomography, Emission-ComputedRadionuclide ImagingDiagnostic Techniques, RadioisotopeImidazolesAzolesHeterocyclic Compounds, 1-RingCarbazolesHeterocyclic Compounds, 3-RingPhenothiazinesSulfur Compounds2-PyridinylmethylsulfinylbenzimidazolesSulfoxidesPyridinesBenzimidazolesSuccinatesDicarboxylic AcidsAcids, AcyclicCarboxylic AcidsSenna ExtractAnthraquinonesAnthronesAnthracenesQuinonesPlant ExtractsPlant PreparationsBiological ProductsComplex MixturesDisaccharidesOligosaccharidesPolysaccharidesSugars

Results Point of Contact

Title
Dr. Mark J. Roschewski
Organization
National Cancer Institute

Study Officials

  • Mark J Roschewski, M.D.

    National Cancer Institute (NCI)

    PRINCIPAL INVESTIGATOR

Publication Agreements

PI is Sponsor Employee
No
Restrictive Agreement
No

Study Design

Study Type
interventional
Phase
phase 2
Allocation
NON RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
SINGLE GROUP
Sponsor Type
NIH
Responsible Party
PRINCIPAL INVESTIGATOR
PI Title
Investigator

Study Record Dates

First Submitted

November 3, 1999

First Posted

November 4, 1999

Study Start

May 8, 1993

Primary Completion

May 24, 2024

Study Completion

May 24, 2024

Last Updated

June 22, 2025

Results First Posted

June 12, 2025

Record last verified: 2025-06

Data Sharing

IPD Sharing
Will share

All individual participant data (IPD) recorded in the medical record will be shared with intramural investigators upon request.

Shared Documents
STUDY PROTOCOL, SAP, ICF
Time Frame
Clinical data available during the study and indefinitely.
Access Criteria
Clinical data will be made available via subscription to Biomedical Translational Research Information System (BTRIS) and with the permission of the study principal investigator (PI).

Locations