NCT00054665

Brief Summary

This study will examine the safety and effectiveness of an experimental drug called Bortezomib (PS-341), given alone and in combination with a chemotherapy regimen called Etoposide, Prednisone, Vincristine, Cyclophosphamide, Doxorubicin and Filgrastim (EPOCH), in treating non-Hodgkin's B-cell lymphoma. In the laboratory, PS-341 kills lymphoma cells and makes them more sensitive to chemotherapy. The EPOCH treatment regimen includes the drugs doxorubicin, etoposide, vincristine, cyclophosphamide, prednisone, and filgrastim. Patients 18 years of age and older with an aggressive non-Hodgkin's lymphoma that has relapsed after treatment or is not responding to chemotherapy may be eligible for this study. Candidates will be screened with a medical history and physical examination. Other tests that may be required include blood and urine tests; lung function studies; imaging tests such as magnetic resonance imaging, computed tomography and x-rays; and biopsy (surgical removal of a small tissue sample) of tumor, bone marrow, or other tissue. Upon entering the study, all participants will receive PS-341. The drug is given as a 3- to 5-second intravenous (through a vein) injection twice a week for 2 weeks. This is followed by a 1-week rest. Each 3-week period comprises one treatment cycle. The number of cycles a patient receives depends on how well he or she responds to the drug. Patients who do not have a complete remission or whose tumor grows on this therapy will be offered PS-341 in combination with up to six cycles of EPOCH chemotherapy. The treatment for patients taking PS-341 plus EPOCH is as follows:

  • PS-341, given by 3- to 5-second intravenous (IV) injection on days 1 and 4 of each cycle.
  • Doxorubicin, etoposide, and vincristine, given by continuous IV infusion over 4 days, beginning on day 1 and ending on day 5 of each cycle. The drugs are delivered through a lightweight portable infusion pump to an indwelling IV catheter (plastic tube) in a vein.
  • Cyclophosphamide, given by IV infusion over 15 minutes on day 5 of each cycle.
  • Prednisone, given by mouth (pills) twice a day on days 1 through 5 of each cycle.
  • Filgrastim, given by injection under the skin starting on day 6 of each cycle and continuing until the white blood cell count increases or until day 19 of the cycle. Patients also take a combination of antibiotics 3 days a week during EPOCH to prevent infection while resistance is lowered because of the chemotherapy. Etoposide, doxorubicin, and cyclophosphamide doses are adjusted as needed, based on white blood cell counts of the previous cycle. The first patients in the study will receive a low dose of PS-341. The dose will be increased in subsequent small groups of patients as long as the preceding dose is well tolerated. Drug therapy for patients who are candidates for bone marrow transplant will be tailored to permit transplantation. Patients who are not eligible for or who choose not to have a bone marrow transplant will be followed at the National Institutes of Health (NIH) every 3 months the first year, every 4 months the second year, every 6 months the third year, and then once a year until their disease progresses or the study ends. Patients may have tumor and bone marrow biopsies, blood draws, and computed tomography (CT) scans periodically to evaluate disease status and drug side effects.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
50

participants targeted

Target at P25-P50 for phase_2

Timeline
Completed

Started Feb 2003

Longer than P75 for phase_2

Geographic Reach
1 country

2 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

February 1, 2003

Completed
4 days until next milestone

First Submitted

Initial submission to the registry

February 5, 2003

Completed
1 day until next milestone

First Posted

Study publicly available on registry

February 6, 2003

Completed
5.6 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

September 1, 2008

Completed
10 months until next milestone

Study Completion

Last participant's last visit for all outcomes

July 1, 2009

Completed
3.2 years until next milestone

Results Posted

Study results publicly available

September 11, 2012

Completed
Last Updated

September 11, 2012

Status Verified

August 1, 2012

Enrollment Period

5.6 years

First QC Date

February 5, 2003

Results QC Date

June 25, 2012

Last Update Submit

August 10, 2012

Conditions

Keywords

BCL-2NFK-BDrug ResistanceTranslationalLymphomaLarge B-Cell Lymphoma

Outcome Measures

Primary Outcomes (2)

  • Clinical Response Rate

    Clinical Response Rate is the number of participants with a partial and complete response assessed by the criteria for lymphoma. A complete response is complete disappearance of all detectable clinical and radiographic evidence of disease and disappearance of all disease-related symptoms if present before therapy and normalization of those biochemical abnormalities. Partial response is a greater than or equal to 50% decrease in the sum of the products of the greatest diameters of 6 largest dominant nodes or nodal masses. No increase in size of nodes, liver or spleen and no new sites of disease

    18 weeks

  • Number of Participants With Adverse Events

    Here is the number of participants with adverse events. For the detailed list of adverse events see the adverse event module.

    43 months

Study Arms (2)

Part A: PS-341 Alone

EXPERIMENTAL

1.3 mg/m\^2 intravenous injection days 1, 4, 8, 11 every 3 weeks

Drug: PS-341

Part B: PS-341 & EPOCH

EXPERIMENTAL

PS-341: level 1: 0.5 mg/m\^2 intravenous (IV) days 1, 4; level 2: 1.0 mg/m\^2 IV days 1, 4; level 3: 1.5 mg/m\^2 IV days 1, 4; level 4: 1.7 mg/m\^2 IV days 1, 4. EPOCH: Etoposide: 50 mg/m\^2 day continuous intravenous infusion (CIV) days 1-4, 96 hour infusion; Doxorubicin: 10 mg/m\^2 day CIV days 1-4, 96 hour infusion; Vincristine: 0.4 mg/m\^2 day CIV days 1-4, 96 hour infusion; Cyclophosphamide: 750 mg/m\^2 day IV day 5 bolus; Prednisone: 60 mg/m\^2 by mouth twice a day days 1-5; Filgrastim: 300 micrograms subcutaneously days 6 to absolute neutrophil count recovery greater than or equal to 5000/mm\^3. Repeat cycles every 21 days.

Drug: PS-341Drug: EtoposideDrug: DoxorubicinDrug: VincristineDrug: CyclophosphamideDrug: PrednisoneDrug: Filgrastim

Interventions

PS-341DRUG

1.3 mg/m\^2 intravenous injection days 1, 4, 8, 11 every 3 weeks

Also known as: Velcade, Bortezomib, LDB-341, MLN-341
Part A: PS-341 AlonePart B: PS-341 & EPOCH

50 mg/m\^2 day continuous intravenous infusion (CIV) days 1-4, 96 hour infusion. Repeat cycle every 21 days.

Also known as: Vepesid, VP-16
Part B: PS-341 & EPOCH

10 mg/m\^2 day CIV days 1-4, 96 hour infusion. Repeat cycle every 21 days.

Also known as: Adriamycin
Part B: PS-341 & EPOCH

0.4 mg/m\^2 day CIV days 1-4, 96 hour infusion. Repeat cycle every 21 days.

Also known as: Oncovin
Part B: PS-341 & EPOCH

750 mg/m\^2 day IV day 5 bolus. Repeat cycle every 21 days.

Also known as: Cytoxan
Part B: PS-341 & EPOCH

60 mg/m\^2 by mouth twice a day days 1-5. Repeat cycle every 21 days.

Also known as: Deltasone
Part B: PS-341 & EPOCH

300 micrograms subcutaneously days 6 to absolute neutrophil count recovery greater than or equal to 5000/mm\^3. Repeat cycle every 21 days.

Also known as: Neupogen
Part B: PS-341 & EPOCH

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)
* ELIGIBILITY CRITERIA: Large B-cell lymphoma (subtypes: DLBCL (diffuse large B-cell lymphoma); mediastinal (thymic) large B-cell lymphoma; transformed large B-cell lymphoma; follicular grade IIIB large B-cell lymphoma; intravascular large B-cell lymphoma). Confirmed pathological diagnosis at the treating institution. Prior anthracycline-based treatment. Age greater than or equal to 18 years. Available tumor tissue for biopsy. Eastern Cooperative Oncology Group (ECOG) performance 2 or better. Major organ function: Absolute neutrophil count (ANC) greater than or equal to 1,000/microliters, Platelet greater than or equal to 50,000/microliters, creatinine less than or equal to 1.5 mg/dl or creatinine clearance greater than 60 cc/min; serum glutamic pyruvic transaminase (SGPT) less than 5 x upper limit of normal; bilirubin less than 2 mg/dl (total) except less than 5 mg/dl in patients with Gilbert's syndrome as defined by greater than 80 percent unconjugated; unless impairment due to organ involvement by lymphoma. Informed consent and willingness to use contraception by both men and women. Not pregnant or nursing because of an unknown potential for teratogenic or abortifacient effects. Both male and female patients must be willing to use adequate contraception. Human immunodeficiency virus (HIV) serology negative. HIV positive patients receiving combination anti-retroviral therapy are excluded from the study because of positive pharmacokinetic interactions with PS-341 or the combination of PS-341 and EPOCH. Additionally, the biology of HIV associated DLBCL's is often quite different from HIV negative disease due to involvement of Epstein Barr Virus (EBV). Hepatitis B surface antigen negative. No symptomatic cardiac disease or cardiac ejection fraction less than 40 percent (in patients receiving EPOCH). No active central nervous system (CNS) lymphoma. No systemic cytotoxic or experimental treatments within 4 weeks of treatment.

Contact the study team to discuss eligibility requirements. They can help determine if this study is right for you.

Sponsors & Collaborators

Study Sites (2)

National Cancer Institute (NCI)

Bethesda, Maryland, 20892, United States

Location

Roswell Parck Cancer Institute

Buffalo, New York, 14263, United States

Location

Related Publications (2)

  • Baldwin AS Jr. The NF-kappa B and I kappa B proteins: new discoveries and insights. Annu Rev Immunol. 1996;14:649-83. doi: 10.1146/annurev.immunol.14.1.649.

    PMID: 8717528BACKGROUND
  • Dunleavy K, Pittaluga S, Czuczman MS, Dave SS, Wright G, Grant N, Shovlin M, Jaffe ES, Janik JE, Staudt LM, Wilson WH. Differential efficacy of bortezomib plus chemotherapy within molecular subtypes of diffuse large B-cell lymphoma. Blood. 2009 Jun 11;113(24):6069-76. doi: 10.1182/blood-2009-01-199679. Epub 2009 Apr 20.

    PMID: 19380866BACKGROUND

Related Links

MeSH Terms

Conditions

Lymphoma, B-CellLymphoma

Interventions

BortezomibEtoposideDoxorubicinVincristineCyclophosphamidePrednisoneFilgrastim

Condition Hierarchy (Ancestors)

Lymphoma, Non-HodgkinNeoplasms by Histologic TypeNeoplasmsLymphoproliferative DisordersLymphatic DiseasesHemic and Lymphatic DiseasesImmunoproliferative DisordersImmune System Diseases

Intervention Hierarchy (Ancestors)

Boronic AcidsAcids, NoncarboxylicAcidsInorganic ChemicalsBoron CompoundsOrganic ChemicalsPyrazinesHeterocyclic Compounds, 1-RingHeterocyclic CompoundsPodophyllotoxinTetrahydronaphthalenesNaphthalenesPolycyclic Aromatic HydrocarbonsHydrocarbons, AromaticHydrocarbons, CyclicHydrocarbonsPolycyclic CompoundsGlucosidesGlycosidesCarbohydratesDaunorubicinAnthracyclinesNaphthacenesAminoglycosidesVinca AlkaloidsSecologanin Tryptamine AlkaloidsIndole AlkaloidsAlkaloidsIndolesHeterocyclic Compounds, 2-RingHeterocyclic Compounds, Fused-RingIndolizidinesIndolizinesPhosphoramide MustardsNitrogen Mustard CompoundsMustard CompoundsHydrocarbons, HalogenatedPhosphoramidesOrganophosphorus CompoundsPregnadienediolsPregnadienesPregnanesSteroidsFused-Ring CompoundsGranulocyte Colony-Stimulating FactorColony-Stimulating FactorsGlycoproteinsGlycoconjugatesHematopoietic Cell Growth FactorsCytokinesIntercellular Signaling Peptides and ProteinsPeptidesAmino Acids, Peptides, and ProteinsProteinsBiological Factors

Results Point of Contact

Title
Wyndham Wilson, M.D.
Organization
National Cancer Institute, National Institues of Health

Study Officials

  • Wyndham Wilson, M.D.

    National Cancer Institute, National Institutes of Health

    PRINCIPAL INVESTIGATOR

Publication Agreements

PI is Sponsor Employee
No
Restrictive Agreement
No

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
SINGLE GROUP
Sponsor Type
NIH
Responsible Party
PRINCIPAL INVESTIGATOR
PI Title
Dr. Wyndham Wilson

Study Record Dates

First Submitted

February 5, 2003

First Posted

February 6, 2003

Study Start

February 1, 2003

Primary Completion

September 1, 2008

Study Completion

July 1, 2009

Last Updated

September 11, 2012

Results First Posted

September 11, 2012

Record last verified: 2012-08

Locations