NCT06908993

Brief Summary

The hypothesize is that tepotinib is more effective than the investigator's choice of treatment in patients with MET-mutated NSCLC who have progressed after at least one first-line treatment. The main benefit concerns patient access to tepotinib. There is currently no access to a new-generation MET TKI in France for METex14 patients, due to lack of comparative data. There are no phase III RCTs underway anywhere in the world. This study is the only opportunity, perhaps the last, to generate comparative data which, if positive, will enable the drug to be reimbursed. With this in mind, the methodology of this study was discussed with the HAS on several occasions beforehand, to ensure that it met their expectations. With a response rate of around 50% and a median progression-free survival of 11 months in previously-treated subjects based on clinical trials data, tepotinib is a key drug for METex14 NSCLC patients, who are generally elderly and frail, and for whom therapeutic options are limited. The investigators expect to observe a benefit for patients treated with tepotinib compared to the control arm in terms of PFS, quality of life, objective response rate and duration of response. The overall survival benefit may be compromised by allowing patients in the control arm to cross over to tepotinib once they have progressed. However, the investigators have decided to maintain this crossover and consequently use PFS as the primary endpoint, as there is no clinical equipoise regarding the efficacy of tepotinib in METex14 NSCLC patients. The EMA has already approved tepotinib based on efficacy and safety data from clinical trials, and patients and investigators already consider this treatment as an important therapeutic option. Indeed, both ESMO and ASCO guidelines recommend the use of MET TKIs in these patients. In France, although neither tepotinib nor capmatinib are available, crizotinib, a multi-target TKI also active on MET, can be used off-label. If cross-over to tepotinib was not allowed in this trial, most patients would still benefit from cross-over to a MET TKI by receiving off-label crizotinib, which would in any case lead to a misinterpretation of the OS data. Therefore, the investigators believe it is preferable to control for cross-over and expose progressive patients in the control arm to tepotinib and use PFS as the primary endpoint. Toxicity of MET TKIs is considered as manageable. In the VISION trial, of 313 patients treated with tepotinib (median age: 72 years), 109 (34.8%) experienced grade ≥3 treatment-related adverse events, leading to discontinuation in 46 patients (14.7%). Rates of adverse events (AE) were broadly consistent irrespective of prior therapies. Edema, the most common adverse event of clinical interest (AECI), was reported in 67.1% (grade ≥ 3, 11.2%). Median time to first edema onset was 7.9 weeks (range: 0.1-58.3). Edema was manageable with supportive measures, dose reduction (18.8%), and/or treatment interruption (23.1%), and rarely prompted discontinuation (4.3%). Other AECIs were also manageable and predominantly mild/moderate: hypoalbuminemia, 23.6% (grade ≥ 3, 3.5%); creatinine increase, 22.0% (grade ≥ 3, 1.0%); nausea, 23.3% (grade ≥ 3, 0.6%), diarrhea, 22.4% (grade ≥ 3, 0.3%), decreased appetite (grade ≥ 3, 0.3%), and ALT increase, 14.1% (grade ≥ 3, 2.2%). GI AEs typically occurred early and resolved in the first weeks10,13. Given the efficacy of tepotinib, the manageable safety profile, and the oral administration of tepotinib, the investigators anticipate that treatment with tepotinib will be associated with improved quality of life. Treatments offered in the control group correspond to standard treatments for advanced NSCLC in second line or beyond. In terms of prior lines of treatment, the eligibility criteria of the trial are aligned with the EMA label of tepotinib: "indicated for the treatment of adult patients with advanced non-small cell lung cancer (NSCLC) harboring alterations leading to MET gene exon 14 (METex14) skipping, who require systemic therapy following prior treatment with immunotherapy and/or platinum-based chemotherapy". The investigators have not included platinum-based chemotherapy as a treatment option in the control arm, considering that patients who are eligible to platinum-based chemotherapy should have received this regimen in first-line, as per ESMO guidelines14. Given the low efficacy of immunotherapy in patients with oncogene addiction, it is unlikely that some patients would receive immunotherapy alone as first-line treatment. Thus, the absence of platinum-based chemotherapy as a treatment choice in the control arm seems reasonable and will reduce the heterogeneity of this arm.

Trial Health

77
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
133

participants targeted

Target at P25-P50 for phase_3

Timeline
27mo left

Started Dec 2025

Typical duration for phase_3

Geographic Reach
1 country

29 active sites

Status
recruiting

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Progress16%
Dec 2025Jul 2028

First Submitted

Initial submission to the registry

March 27, 2025

Completed
7 days until next milestone

First Posted

Study publicly available on registry

April 3, 2025

Completed
8 months until next milestone

Study Start

First participant enrolled

December 9, 2025

Completed
2.3 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

March 15, 2028

Expected
4 months until next milestone

Study Completion

Last participant's last visit for all outcomes

July 15, 2028

Last Updated

December 17, 2025

Status Verified

December 1, 2025

Enrollment Period

2.3 years

First QC Date

March 27, 2025

Last Update Submit

December 9, 2025

Conditions

Keywords

TepotinibMET Exon 14 MutationNon Small Cell Lung Cancer

Outcome Measures

Primary Outcomes (1)

  • Progression-Free Survival (PFS)

    Progression-free survival is calculated from the date of randomization until progression as defined by independent review comity according to RECIST 1.1 or death (whichever occurs first).

    About 36 months

Secondary Outcomes (9)

  • Global Health Status Quality of life

    6 weeks after randomization

  • Overall Survival

    About 36 months

  • Second Progression-Free Survival (PFS2)

    About 36 months

  • Time to next treatment or death (TNT-D)

    About 36 months

  • Objective Response Rate (ORR)

    About 36 months

  • +4 more secondary outcomes

Study Arms (2)

Investigator choice treatment

ACTIVE COMPARATOR

Investigator's choice treatment among: * Monochemotherapy (including pemetrexed, docetaxel, paclitaxel with or without bevacizumab, gemcitabine, vinorelbine), * Anti-PD(L)1 agent (including pembrolizumab, nivolumab or atezolizumab), * Best supportive care - available only for patients with i) ECOG PS 3 or ii) contraindication to propose a systemic treatment based on an oncogeriatric assessment or confirmed by the local multidisciplinary tumor board. The treatment chosen cannot be a treatment already received.

Drug: Pemetrexed (Alimta)Drug: VinorelbineDrug: Gemcitabine aloneDrug: DocetaxelDrug: PaclitaxelDrug: PembrolizumabDrug: NivolumabDrug: Atezolizumab

Tepotinib

EXPERIMENTAL
Drug: Tepotinib

Interventions

Tepotinib will be given orally once daily at the dose of 500mg of tepotinib hydrochloride hydrate.

Tepotinib

500 mg/m² every 3 weeks

Investigator choice treatment

25-30 mg/m² D1, D8, every 3 weeks

Investigator choice treatment

1250 mg/m² D1, D8, every 3 weeks

Investigator choice treatment

75 mg/m² every 3 weeks

Investigator choice treatment

90 mg/m² D1, D8, D15 every 4 weeks If bevacizumab added: 10 mg/kg D1, D15 every 4 weeks

Investigator choice treatment

200 mg every 3 weeks

Investigator choice treatment

240 mg every 2 weeks

Investigator choice treatment

1200 mg every 3 weeks

Investigator choice treatment

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Informed, written and signed consent:
  • Patients must have signed and dated the written informed consent form approved by the ethics committee in accordance with the legal and institutional framework.
  • It must have been signed before protocol-related procedures that are not part of normal patient management are performed. Patients should be willing and able to adhere to the schedule of visits, treatment and laboratory tests.
  • Histologically proven advanced NSCLC.
  • Presence of a METex14 mutation (based on local testing). Detection of METex14 mutation should be performed on a tissue sample if available. In case no tissue sample is available, detection of METex14 on a liquid biopsy is authorized. The sponsor should be consulted if there is any doubt about the nature of the mutation.
  • Evidence of disease progression after at least one prior line of treatment including either a platinum-based chemotherapy or an anti-PD(L)1 agent or both.
  • Has received no more than 2 prior lines of treatment.
  • ECOG Performance Status 0-3.
  • Stage IIIB or IIIC non irradiable or stage IV (8th classification TNM, UICC 2015)
  • Age ≥ 18 years.
  • Adequate biological function:
  • Creatinine clearance ≥ 30 ml/min;
  • Neutrophils ≥ 1500/mm3;
  • Platelets ≥100,000/mm3;
  • Haemoglobin ≥ 8 g/dL;
  • +7 more criteria

You may not qualify if:

  • Prior treatment with a MET inhibitor (including crizotinib).
  • ECOG Performance Status 4.
  • Known hypersensitivity to tepotinib or its excipients.
  • Inability to comply with study or follow-up procedures.
  • Pregnant, lactating, or breastfeeding women.
  • Any disease, metabolic dysfunction, physical examination finding, or clinical laboratory finding giving reasonable suspicion of a disease or condition that contraindicates the use of an investigational drug, that may affect the interpretation of the results, or that may render the patient at high risk from treatment complications.
  • History of idiopathic pulmonary fibrosis or active pneumonitis on chest computed tomography (CT) scan at screening. History of radiation pneumonitis in the radiation field (fibrosis) is permitted.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (29)

Besançon - CHU

Besançon, France

RECRUITING

Bordeaux - Institut Bergonie

Bordeaux, France

RECRUITING

Brest - CHU

Brest, France

RECRUITING

Caen - CRLCC

Caen, France

RECRUITING

Centre Hospitalier Intercommunal de Créteil

Créteil, 94000, France

RECRUITING

Dijon - Centre Georges-François Leclerc

Dijon, 21000, France

RECRUITING

Grenoble - CHU

Grenoble, France

RECRUITING

CHD Vendée

La Roche-sur-Yon, France

RECRUITING

Le Mans - CHG

Le Mans, France

RECRUITING

CHRU de Lille

Lille, France

RECRUITING

Centre Léon Bérard

Lyon, 69373, France

RECRUITING

Institut Paoli Calmette

Marseille, France

RECRUITING

Marseille - APHM

Marseille, France

RECRUITING

Montpellier - CHU

Montpellier, France

RECRUITING

Centre Antoine Lacassagne

Nice, France

RECRUITING

AP-HP Hôpital Cochin

Paris, 75014, France

RECRUITING

AP-HP Hôpital Tenon

Paris, 75970, France

RECRUITING

Paris - APHP Bichat

Paris, France

RECRUITING

Centre Hospitalier Général - Pau

Pau, 64000, France

RECRUITING

Bordeaux - CHU

Pessac, France

RECRUITING

Institut de Cancérologie de l'Ouest - René Gauducheau

Saint-Herblain, 44805, France

RECRUITING

Sens - CH

Sens, 89100, France

RECRUITING

Strasbourg - NHC

Strasbourg, 63000, France

RECRUITING

Toulon - CHI

Toulon, 83000, France

RECRUITING

CHU Toulouse

Toulouse, France

RECRUITING

CHRU de Tours

Tours, France

RECRUITING

CH de Valence

Valence, France

RECRUITING

Nancy - CHU

Vandœuvre-lès-Nancy, 54500, France

RECRUITING

Gustave Roussy

Villejuif, France

RECRUITING

Related Links

MeSH Terms

Conditions

Carcinoma, Non-Small-Cell Lung

Interventions

tepotinibPemetrexedVinorelbineGemcitabineDocetaxelPaclitaxelpembrolizumabNivolumabatezolizumab

Condition Hierarchy (Ancestors)

Carcinoma, BronchogenicBronchial NeoplasmsLung NeoplasmsRespiratory Tract NeoplasmsThoracic NeoplasmsNeoplasms by SiteNeoplasmsLung DiseasesRespiratory Tract Diseases

Intervention Hierarchy (Ancestors)

GuanineHypoxanthinesPurinonesPurinesHeterocyclic Compounds, 2-RingHeterocyclic Compounds, Fused-RingHeterocyclic CompoundsGlutamatesAmino Acids, AcidicAmino AcidsAmino Acids, Peptides, and ProteinsAmino Acids, DicarboxylicVinca AlkaloidsSecologanin Tryptamine AlkaloidsIndole AlkaloidsAlkaloidsIndolesIndolizidinesIndolizinesDeoxycytidineCytidinePyrimidine NucleosidesPyrimidinesHeterocyclic Compounds, 1-RingTaxoidsCyclodecanesCycloparaffinsHydrocarbons, AlicyclicHydrocarbons, CyclicHydrocarbonsOrganic ChemicalsDiterpenesTerpenesAntibodies, Monoclonal, HumanizedAntibodies, MonoclonalAntibodiesImmunoglobulinsImmunoproteinsBlood ProteinsProteinsSerum GlobulinsGlobulins

Central Study Contacts

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
OTHER
Responsible Party
SPONSOR

Study Record Dates

First Submitted

March 27, 2025

First Posted

April 3, 2025

Study Start

December 9, 2025

Primary Completion (Estimated)

March 15, 2028

Study Completion (Estimated)

July 15, 2028

Last Updated

December 17, 2025

Record last verified: 2025-12

Data Sharing

IPD Sharing
Will share

The individual participant data underlying the results reported in this article, as well as the study protocol and statistical analysis plan, will be made available after deidentification immediately following publication and for three years. Researchers who provide a methodologically sound proposal for any purpose may direct proposals to contact@ifct.fr. To gain access, data requestors will need to sign a data access agreement that requires approval by the French Cooperative Thoracic Intergroup.

Locations