NCT06533579

Brief Summary

This is a Phase 1/2, first-in-human, open-label, dose-escalating trial designed to assess the safety and efficacy of VNX-101 in patients with relapsed or refractory CD19-positive hematologic malignancies.

Trial Health

77
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
32

participants targeted

Target at P50-P75 for phase_1

Timeline
65mo left

Started May 2025

Longer than P75 for phase_1

Geographic Reach
1 country

9 active sites

Status
recruiting

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Progress15%
May 2025Sep 2031

First Submitted

Initial submission to the registry

July 24, 2024

Completed
8 days until next milestone

First Posted

Study publicly available on registry

August 1, 2024

Completed
10 months until next milestone

Study Start

First participant enrolled

May 30, 2025

Completed
2 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

June 1, 2027

Expected
4.3 years until next milestone

Study Completion

Last participant's last visit for all outcomes

September 1, 2031

Last Updated

March 30, 2026

Status Verified

March 1, 2026

Enrollment Period

2 years

First QC Date

July 24, 2024

Last Update Submit

March 24, 2026

Conditions

Keywords

CD19-positiveLeukemiaLymphoma

Outcome Measures

Primary Outcomes (1)

  • Treatment emergent adverse events (TEAEs) and treatment-emergent serious events (TESAEs)

    Change from Baseline to Year 5 post dosing

Secondary Outcomes (4)

  • Change from baseline in B-cell counts

    Change from baseline to year 5 post dosing

  • Change baseline in immunoglobulin levels

    Change from baseline to year 5 post dosing

  • Change baseline in antitumor activity

    Change from baseline to year 5 post dosing

  • Proportion/duration of subjects achieving response, progression free survival, and disease free survival.

    Change from baseline to year 5 post dosing

Other Outcomes (2)

  • Exploratory Measure: Change in VNX-101 gene product levels

    Change from baseline to year 5 post dosing

  • Exploratory Measure: Change in VNX-101 vector shedding

    Change from baseline to year 5 post dosing

Study Arms (1)

Group 1/Group 2/Group 3/Group 4

EXPERIMENTAL
Genetic: Dose Level 1, VNX-101Genetic: Dose Level 2, VNX-101Genetic: Dose Level 3, VNX-101Genetic: Dose Level 4, VNX-101

Interventions

Adeno-associated viral vector encoding the CD3/CD19 Bi-Specific T-Cell Engager (AAV.CD3/CD19), Single IV infusion

Group 1/Group 2/Group 3/Group 4

Adeno-associated viral vector encoding the CD3/CD19 Bi-Specific T-Cell Engager (AAV.CD3/CD19), Single IV infusion

Group 1/Group 2/Group 3/Group 4

Adeno-associated viral vector encoding the CD3/CD19 Bi-Specific T-Cell Engager (AAV.CD3/CD19), Single IV infusion

Group 1/Group 2/Group 3/Group 4

Adeno-associated viral vector encoding the CD3/CD19 Bi-Specific T-Cell Engager (AAV.CD3/CD19), Single IV infusion

Group 1/Group 2/Group 3/Group 4

Eligibility Criteria

Age13 Years - 90 Years
Sexall
Healthy VolunteersNo
Age GroupsChild (0-17), Adult (18-64), Older Adult (65+)

You may qualify if:

  • Age: Part 1: 18-90 years of age, Part 2: 13-90 years of age
  • Relapsed or refractory CD-19 positive leukemia or lymphoma as defined in the protocol
  • CD19-positive expression
  • AAV specified capsid total antibody \<1:400
  • Protocol-specified ranges for renal, liver, cardiac and pulmonary function
  • Protocol-specified ranges for hematology parameters

You may not qualify if:

  • Hepatoxicity (AST or ALT \> 2x upper limit of normal)
  • History of thrombotic microangiopathy or cardiomyopathy, or evidence of sensory neuropathy
  • Pregnant or nursing (lactating) women
  • Acute Graft versus Host Disease (GvHD): Grade 2-4 or chronic GvHD of any grade
  • History of hypersensitivity to corticosteroids or history of corticosteroid-related toxicity
  • Chemotherapy given within the protocol-specified discontinuation timelines

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (9)

City of Hope

Duarte, California, 91010, United States

RECRUITING

Valkyrie Clinical Trials

Los Angeles, California, 90067, United States

RECRUITING

Colorado Blood Cancer Institute

Denver, Colorado, 80218, United States

RECRUITING

New York Medical College

Valhalla, New York, 10595, United States

RECRUITING

University of North Carolina at Chapel Hill/ University of North Carolina Medical Center

Chapel Hill, North Carolina, 27599, United States

RECRUITING

The Ohio State University Wexner Medical Center

Columbus, Ohio, 43210, United States

RECRUITING

Oregon Health & Science University

Portland, Oregon, 97239, United States

RECRUITING

TriStar BMT

Nashville, Tennessee, 37203, United States

RECRUITING

University of Texas MD Anderson Cancer Center

Houston, Texas, 77030, United States

RECRUITING

Related Links

MeSH Terms

Conditions

Burkitt LymphomaLeukemia, Lymphocytic, Chronic, B-CellLymphoma, B-Cell, Marginal ZoneLymphoma, FollicularLymphoma, Mantle-CellLymphoma, Large B-Cell, DiffuseLymphoma, Non-HodgkinLeukemia, Biphenotypic, AcuteLeukemiaLymphoma

Condition Hierarchy (Ancestors)

Epstein-Barr Virus InfectionsHerpesviridae InfectionsDNA Virus InfectionsVirus DiseasesInfectionsTumor Virus InfectionsLymphoma, B-CellNeoplasms by Histologic TypeNeoplasmsLymphoproliferative DisordersLymphatic DiseasesHemic and Lymphatic DiseasesImmunoproliferative DisordersImmune System DiseasesLeukemia, B-CellLeukemia, LymphoidHematologic DiseasesChronic DiseaseDisease AttributesPathologic ProcessesPathological Conditions, Signs and Symptoms

Study Officials

  • Vironexis Clinical Trials

    Vironexis Biotherapeutics Inc.

    STUDY DIRECTOR

Central Study Contacts

Recruitment Partner: PatientWing

CONTACT

Study Design

Study Type
interventional
Phase
phase 1
Allocation
NA
Masking
NONE
Purpose
TREATMENT
Intervention Model
SINGLE GROUP
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

July 24, 2024

First Posted

August 1, 2024

Study Start

May 30, 2025

Primary Completion (Estimated)

June 1, 2027

Study Completion (Estimated)

September 1, 2031

Last Updated

March 30, 2026

Record last verified: 2026-03

Data Sharing

IPD Sharing
Will not share

Locations