NCT06340737

Brief Summary

This is a non-randomized clinical trial to evaluate the safety and efficacy of CD22CART administered after lymphodepleting chemotherapy in adults with relapsed / refractory B Cell Lymphomas. All evaluable participants will be followed for overall survival (OS), progression free survival (PFS), and duration of response (DOR). An evaluable participant is one who completes leukapheresis, lymphodepleting chemotherapy and CART infusion.

Trial Health

77
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
148

participants targeted

Target at P75+ for phase_1

Timeline
59mo left

Started Mar 2024

Longer than P75 for phase_1

Geographic Reach
1 country

1 active site

Status
recruiting

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

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Study Timeline

Key milestones and dates

Study Progress30%
Mar 2024Apr 2031

First Submitted

Initial submission to the registry

March 8, 2024

Completed
21 days until next milestone

Study Start

First participant enrolled

March 29, 2024

Completed
3 days until next milestone

First Posted

Study publicly available on registry

April 1, 2024

Completed
7 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

April 1, 2031

Expected
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

April 1, 2031

Last Updated

August 7, 2025

Status Verified

August 1, 2025

Enrollment Period

7 years

First QC Date

March 8, 2024

Last Update Submit

August 4, 2025

Conditions

Keywords

lymphomaleukemialymphodepleting chemotherapyrelapsedrefractorysystemic therapy

Outcome Measures

Primary Outcomes (3)

  • Determine the manufacturing feasibility of CD22 CART by assessing the target dose level and release specifications in each disease cohort.

    Rate of successful manufacture of CD22CART cells at the target dose level that meet required release specifications in Cohort 1, Cohort 2, and Cohort 3.

    6 years

  • Maximum tolerated dose (MTD)/recommended phase 2 dose (RP2D)

    Establish the maximum tolerated dose (MTD)/recommended phase 2 dose (RP2D) of CD22CART cells in 3 cohorts of adults with relapsed/refractory B Cell lymphoma.

    6 years

  • Determine the overall response rate (ORR) in adults with follicular lymphoma (FL) and mantle cell lymphoma (MCL)

    Assess the ORR at 3 months post CD22 CART infusion as defined by the disease specific response criteria for Cohort 1 (FL) and Cohort 2 (MCL)

    3 months CD22 CART infusion

Secondary Outcomes (4)

  • Evaluate Progression Free Survival (PFS)

    6 years

  • Evaluate Overall Survival (OS)

    6 years

  • Evaluate Duration of Response (DOR)

    6 years

  • Assess the response rate in adults with relapsed/refractory Hairy cell leukemia (HCL), Lymphoplasmacytic lymphoma (Waldenstrom macroglobulemia) (WM), Burkitt lymphoma (BL), and Marginal Zone lymphoma (MZL).

    3 months post CD22

Study Arms (4)

Cohort 1: Follicular lymphoma (FL)

EXPERIMENTAL

18-34 participants with FL will be administered the RP2D of CD22CART

Drug: CD22CART Infusion

Cohort 2: Mantle cell lymphoma (MCL)

EXPERIMENTAL

12-32 participants with MCL will be administered the RP2D of CD22CART.

Drug: CD22CART Infusion

Cohort 3: Other lymphomas

EXPERIMENTAL

Up to 30 participants with no more than 10 of any one type, including: Hairy cell leukemia, Lymphoplasmacytic lymphoma (Waldenstrom macroglobulinemia), Burkitt lymphoma, and Marginal zone lymphoma.

Drug: CD22CART Infusion

Cohort 4: Relapsed/refractory large B cell lymphoma (LBCL)

EXPERIMENTAL

14 - 19 participants will be administered the RP2D of CD22 CART

Drug: CD22CART Infusion

Interventions

Dosing and Administration Participants will be hospitalized to receive treatment with CD22CART, if not previously hospitalized, and will remain hospitalized for approximately 5 to 7 (±2) days. Patients may be discharged once all AEs have resolved to Grade 1 or better, or at the discretion of the treating physician. Participants may be discharged with non critical and clinically stable or slowly improving toxicities (e.g., renal insufficiency, cytopenias) even if \> Grade 1, if deemed appropriate by the investigator.

Cohort 1: Follicular lymphoma (FL)Cohort 2: Mantle cell lymphoma (MCL)Cohort 3: Other lymphomasCohort 4: Relapsed/refractory large B cell lymphoma (LBCL)

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Disease: Must have histologically confirmed disease as defined by WHO 2016\[117\] of one of the following:
  • Follicular Lymphoma, grade 1-3a
  • Relapsed or refractory disease after at least 2 lines of systemic therapy. Prior therapy must have included an anti-CD20 monoclonal antibody combined with systemic therapy (single-agent anti- CD20 antibody does not count as line of therapy for eligibility nor does local radiation). Anti-CD20 antibody is not required for participants with CD20 negative disease. A systemic therapy includes, but is not limited to: Bendamustine, CHOP, CVP, CART therapy, lenalidomide, or platinum-based chemotherapy.
  • Relapsed or progressive disease within 24 months of initiation of the initial course of chemotherapy (also known as progression of disease within 24 months POD24). Initial treatment must have included an anti-CD20 monoclonal antibody (unless CD20 negative) plus either Bendamustine, CHOP or CVP (R-Chemo). Must have completed 3 or more cycles of R-Chemo. Progression is measured from the initial day of treatment of the first cycle of R-Chemo. In the case of those who received anti-CD20 monoclonal antibody monotherapy previously and then received R-Chemo are also eligible if they are POD24, and progression is measured from the initial day of treatment of the first cycle of R-Chemo and not from the initial day of anti-CD20 monoclonal antibody monotherapy.
  • Mantle Cell Lymphoma 1. Relapsed or refractory disease after at least 2 lines of systemic therapy. Prior therapy must have included an anti-CD20 monoclonal antibody combined with systemic therapy. Anti-CD20 antibody is not required for participants with CD20negative disease.
  • \. Participants who have received an anti-CD20 monoclonal antibody in combination with chemotherapy AND a Bruton's Tyrosine Kinase inhibitor as a single line of therapy are also eligible.
  • Hairy cell leukemia (HCL)
  • Diagnosis of HCL and require treatment as defined by having HCL-related anemia (hemoglobin \<11 g/dL), thrombocytopenia (platelets\<100 x 10\^9 /L), or neutropenia (absolute neutrophil count below 1.5 x 10\^9/L); symptomatic splenomegaly or adenopathy; or other constitutional symptoms directly related to HCL;
  • Must have progressed or been refractory to 2 lines of therapy including a purine nucleoside analog.
  • Lymphoplasmacytic lymphoma (Waldenstrom macroglobulinemia (WM)) - participants must meet all eligibility criteria listed
  • \. Must have confirmed diagnosis of WM based on Second International Workshop on WM 2. Relapsed or refractory disease after 2 or more lines of therapy
  • \. Prior therapies must include a i. BTKi ii. either chemotherapy and/or proteasome inhibitor 3. Requires treatment based on the recommendations from the Second International Workshop on WM 4. Requires the presence of serum IgM that is at least 2 times the upper limit of normal 5. Patients cannot require plasmapheresis for symptomatic hyperviscosity. 6. Patients cannot have symptomatic central nervous system involvement (Bing-Neel syndrome) that would prevent the assessment of neurotoxicity 7. Patients cannot have transformed to large B cell lymphoma Burkitt lymphoma (BL)
  • \. Relapsed or refractory to front line chemoimmunotherapy; Participants with high-grade B-cell lymphoma with MYC and BCL2 and/orBCL6 rearrangements will be excluded.
  • Marginal zone lymphoma (MZL)
  • \. Must have received 2 prior lines of therapy including rituximab in combination with chemotherapy or a BTKi
  • +28 more criteria

You may not qualify if:

  • Presence rapidly progressive disease that in the estimation of the investigator and sponsor would compromise ability to complete study therapy.
  • \. History or current other malignancies, apart from non-melanoma skin cancer, low-grade untreated prostate cancer under observation, or carcinoma in situ, unless disease free for at least 3 years, or in remission 1-2 years and Principal Investigator assesses other malignancy as unlikely to return within 1 year or interfere with CAR T cell safety
  • \. Presence of active fungal, bacterial, viral or other infection requiring intravenous antimicrobials. Simple UTI or uncomplicated bacterial pharyngitis is permitted if responding to active treatment.
  • \. Ongoing HIV, HBV, or HCV infection. History of HBV or HCV is permitted if viral load is undetectable by qPCR and/or nucleic acid testing.
  • \. Active cerebrovascular ischemic/hemorrhage, dementia, cerebellar disease, or autoimmune disease with CNS involvement that in investigator's judgement impair ability to evaluate neurotoxicity.
  • \. History of MI, cardiac angioplasty or stenting, unstable angina or other clinically significant cardiac disease within 12 months of enrollment.
  • \. Severe, immediate hypersensitivity reaction attributed to compounds of similar chemical or biologic composition to any agents used in study.
  • \. Is pregnant or breastfeeding.
  • \. Active primary immunodeficiency or history of autoimmune disease (e.g. Crohn's disease, rheumatoid arthritis, systemic lupus) requiring systemic immunosuppression/systemic disease modifying agents within the last 2 years.
  • \. May NOT, in investigator's judgment, have any medical condition likely to interfere with assessment of safety or efficacy, or be likely to complete all protocol-required visits and procedures.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (1)

Stanford University

Palo Alto, California, 94304, United States

RECRUITING

MeSH Terms

Conditions

Lymphoma, FollicularLymphoma, Mantle-CellLeukemia, Hairy CellLymphoma, B-Cell, Marginal ZoneBurkitt LymphomaWaldenstrom MacroglobulinemiaLymphomaLeukemiaRecurrence

Condition Hierarchy (Ancestors)

Lymphoma, Non-HodgkinNeoplasms by Histologic TypeNeoplasmsLymphoproliferative DisordersLymphatic DiseasesHemic and Lymphatic DiseasesImmunoproliferative DisordersImmune System DiseasesHematologic DiseasesLymphoma, B-CellEpstein-Barr Virus InfectionsHerpesviridae InfectionsDNA Virus InfectionsVirus DiseasesInfectionsTumor Virus InfectionsNeoplasms, Plasma CellHemostatic DisordersVascular DiseasesCardiovascular DiseasesParaproteinemiasBlood Protein DisordersHemorrhagic DisordersDisease AttributesPathologic ProcessesPathological Conditions, Signs and Symptoms

Study Officials

  • Matthew Frank, MD, PhD

    Stanford University

    PRINCIPAL INVESTIGATOR

Central Study Contacts

Study Design

Study Type
interventional
Phase
phase 1
Allocation
NON RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
OTHER
Responsible Party
SPONSOR

Study Record Dates

First Submitted

March 8, 2024

First Posted

April 1, 2024

Study Start

March 29, 2024

Primary Completion (Estimated)

April 1, 2031

Study Completion (Estimated)

April 1, 2031

Last Updated

August 7, 2025

Record last verified: 2025-08

Locations