NCT05999994

Brief Summary

The main purpose of the master is to help the research sites and sponsor carry out several clinical trials more efficiently by providing a common research protocol. Individual clinical trials under this master protocol define drug/disease-specific research goals and activities to test them. New studies will be added as new drugs emerge against different cancers. Participation in the trial will depend on how long the benefit lasts.

Trial Health

88
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
105

participants targeted

Target at P50-P75 for phase_2

Timeline
11mo left

Started Jan 2020

Longer than P75 for phase_2

Geographic Reach
10 countries

73 active sites

Status
recruiting

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Progress88%
Jan 2020May 2027

Study Start

First participant enrolled

January 22, 2020

Completed
3.6 years until next milestone

First Submitted

Initial submission to the registry

August 14, 2023

Completed
7 days until next milestone

First Posted

Study publicly available on registry

August 21, 2023

Completed
3.7 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

May 1, 2027

Expected
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

May 1, 2027

Last Updated

March 27, 2026

Status Verified

March 1, 2026

Enrollment Period

7.3 years

First QC Date

August 14, 2023

Last Update Submit

March 26, 2026

Conditions

Outcome Measures

Primary Outcomes (1)

  • Number of Participants Allocated to Each ISA

    Number of Participants Allocated to Each ISA

    Baseline up to Week 4

Study Arms (6)

Ramucirumab + Cyclophosphamide + Vinorelbine (DSRCT ISA)

EXPERIMENTAL

Ramucirumab given intravenously (IV), cyclophosphamide given orally and vinorelbine given IV in 28-day cycles for desmoplastic small round cell tumor (DSRCT) intervention-specific appendix (ISA).

Drug: RamucirumabDrug: CyclophosphamideDrug: Vinorelbine

Cyclophosphamide + Vinorelbine (DSRCT ISA)

ACTIVE COMPARATOR

Cyclophosphamide given orally and vinorelbine given IV in 28-day cycles for DSRCT ISA.

Drug: CyclophosphamideDrug: Vinorelbine

Ramucirumab + Gemcitabine + Docetaxel (SS ISA)

EXPERIMENTAL

Ramucirumab and gemcitabine given IV in 21-day cycles for synovial sarcoma (SS) ISA.

Drug: RamucirumabDrug: GemcitabineDrug: Docetaxel

Gemcitabine + Docetaxel (SS ISA)

ACTIVE COMPARATOR

Gemcitabine and docetaxel given IV in 21-day cycles for SS ISA.

Drug: GemcitabineDrug: Docetaxel

Abemaciclib + Irinotecan + Temozolomide (ES ISA)

EXPERIMENTAL

Abemaciclib given orally, irinotecan given IV, and temozolomide given orally in 21-day cycles for Ewing's sarcoma (ES) ISA.

Drug: AbemaciclibDrug: IrinotecanDrug: Temozolomide

Irinotecan + Temozolomide (ES ISA)

ACTIVE COMPARATOR

Irinotecan given IV and temozolomide given orally in 21-day cycles for ES ISA.

Drug: IrinotecanDrug: Temozolomide

Interventions

Administered IV

Also known as: LY3009806
Ramucirumab + Cyclophosphamide + Vinorelbine (DSRCT ISA)Ramucirumab + Gemcitabine + Docetaxel (SS ISA)

Administered orally

Cyclophosphamide + Vinorelbine (DSRCT ISA)Ramucirumab + Cyclophosphamide + Vinorelbine (DSRCT ISA)

Administered IV

Cyclophosphamide + Vinorelbine (DSRCT ISA)Ramucirumab + Cyclophosphamide + Vinorelbine (DSRCT ISA)

Administered IV

Also known as: LY188011
Gemcitabine + Docetaxel (SS ISA)Ramucirumab + Gemcitabine + Docetaxel (SS ISA)

Administered IV

Gemcitabine + Docetaxel (SS ISA)Ramucirumab + Gemcitabine + Docetaxel (SS ISA)

Administered orally

Also known as: LY2835219
Abemaciclib + Irinotecan + Temozolomide (ES ISA)

Administered IV

Abemaciclib + Irinotecan + Temozolomide (ES ISA)Irinotecan + Temozolomide (ES ISA)

Administered orally

Abemaciclib + Irinotecan + Temozolomide (ES ISA)Irinotecan + Temozolomide (ES ISA)

Eligibility Criteria

Age1 Year - 39 Years
Sexall
Healthy VolunteersNo
Age GroupsChild (0-17), Adult (18-64)

You may qualify if:

  • Have either measurable or evaluable disease using standard techniques by the Response Evaluation Criteria in Solid Tumors, Version 1.1 (RECIST 1.1).
  • The participant has a Lansky (\<16 years of age) or Karnofsky (≥16 years of age) performance score of at least 50.
  • Participants must have discontinued all previous treatments for cancer or investigational agents greater than or equal to (≥)7 days after the last dose and must have recovered from clinically significant side effects.
  • The participant has adequate hematologic and organ function.
  • Female participants of childbearing potential must have a negative urine or serum pregnancy test within 7 days prior to first dose.
  • Both female and male participants of childbearing potential must agree to use highly effective contraceptive precautions during the trial and for at least 3 months following the last dose of study drug.

You may not qualify if:

  • Participants with severe and/or uncontrolled concurrent medical disease or psychiatric illness/social situation that, in the opinion of the investigator, could cause unacceptable safety risks or compromise compliance with the protocol.
  • Participants who have active infections requiring therapy.
  • Participants who have had allogeneic bone marrow or solid organ transplant.
  • Participants who have had, or are planning to have, certain invasive procedures.
  • Female participants who are pregnant or breastfeeding.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (73)

Childrens Hospital of Alabama

Birmingham, Alabama, 35233, United States

NOT YET RECRUITING

Phoenix Children's Hospital

Phoenix, Arizona, 85016, United States

RECRUITING

Phoenix Children's Hospital

Phoenix, Arizona, 85016, United States

RECRUITING

Childrens Hospital of Los Angeles

Los Angeles, California, 90027, United States

COMPLETED

UCLA Medical Center

Los Angeles, California, 90095, United States

NOT YET RECRUITING

Children's Hospital of Orange County

Orange, California, 92868, United States

RECRUITING

Children's Hospital of Colorado

Denver, Colorado, 80218, United States

RECRUITING

Children's National Medical Center

Washington D.C., District of Columbia, 20010, United States

RECRUITING

Golisano Children's Hospital of Southwest Florida

Fort Myers, Florida, 33908, United States

RECRUITING

Mayo Clinic in Florida

Jacksonville, Florida, 32224, United States

RECRUITING

Children's Healthcare of Atlanta, Inc. at Egleston

Atlanta, Georgia, 30322, United States

NOT YET RECRUITING

Ann & Robert H Lurie Children's Hospital of Chicago

Chicago, Illinois, 60611, United States

RECRUITING

Riley Hospital for Children

Indianapolis, Indiana, 46202-5225, United States

ACTIVE NOT RECRUITING

Dana-Farber Cancer Institute

Boston, Massachusetts, 02215, United States

NOT YET RECRUITING

C.S. Mott Children's Hospital

Ann Arbor, Michigan, 48109, United States

NOT YET RECRUITING

University of Minnesota Hospital

Minneapolis, Minnesota, 55455, United States

NOT YET RECRUITING

Children's Mercy Hospital

Kansas City, Missouri, 64108, United States

RECRUITING

Washington University Medical School

St Louis, Missouri, 63110, United States

COMPLETED

Memorial Sloan Kettering Cancer Center

New York, New York, 10065, United States

RECRUITING

Nationwide Children's Hosp

Columbus, Ohio, 43205-2664, United States

RECRUITING

Oregon Health and Science University

Portland, Oregon, 97201, United States

NOT YET RECRUITING

Children's Hospital of Philadelphia

Philadelphia, Pennsylvania, 19104, United States

COMPLETED

UPMC Children's Hospital of Pittsburgh

Pittsburgh, Pennsylvania, 15224, United States

RECRUITING

Lifespan Cancer Institute

Providence, Rhode Island, 02906, United States

RECRUITING

University of Texas Southwestern Medical Center at Dallas

Dallas, Texas, 75390-9063, United States

RECRUITING

Cook Children's Hospital

Fort Worth, Texas, 76104-2724, United States

ACTIVE NOT RECRUITING

Texas Childrens Hospital

Houston, Texas, 77025, United States

NOT YET RECRUITING

University of Texas MD Anderson Cancer Center

Houston, Texas, 77030, United States

RECRUITING

Seattle Children's Hospital Research Foundation

Seattle, Washington, 98105, United States

RECRUITING

Medical College of Wisconsin

Milwaukee, Wisconsin, 53226, United States

NOT YET RECRUITING

Chris O'Brien Lifehouse

Camperdown, 2050, Australia

RECRUITING

Peter MacCallum Cancer Centre

Melbourne, 3000, Australia

RECRUITING

Royal Children's Hospital

Melbourne, 3052, Australia

RECRUITING

The Sydney Children's Hospitals Network

Westmead, 2145, Australia

NOT YET RECRUITING

UCL- Saint Luc

Brussels, 1200, Belgium

RECRUITING

Universitair Ziekenhuis Gent

Ghent, 9000, Belgium

COMPLETED

Institut Bergonié - Centre Régional de Lutte Contre Le Cancer de Bordeaux et Sud Ouest

Bordeaux, 33076, France

RECRUITING

Centre Leon Berard

Lyon, 69008, France

NOT YET RECRUITING

Centre Leon Berard

Lyon, 69008, France

RECRUITING

Institut Curie

Paris, 75248, France

NOT YET RECRUITING

Universitaetsklinikum Essen

Essen, 45147, Germany

RECRUITING

Universitaetsklinikum Freiburg

Freiburg im Breisgau, 79106, Germany

RECRUITING

Universitaetsklinikum Hamburg-Eppendorf

Hamburg, 20251, Germany

RECRUITING

IRCCS Istituto Ortopedico Rizzoli

Bologna, 40136, Italy

RECRUITING

Istituto di Candiolo IRCCS - Fondazione del Piemonte per l'Oncologia

Candiolo, 10060, Italy

RECRUITING

Istituto Nazionale dei Tumori

Milan, 20133, Italy

RECRUITING

Azienda Ospedaliera Di Padova

Padua, 35128, Italy

RECRUITING

Ospedale Bambino Gesu

Roma, 00165, Italy

RECRUITING

Fondazione Policlinico Universitario Agostino Gemelli IRCCS - Università Cattolica del Sacro Cuore

Roma, 00168, Italy

RECRUITING

Istituto Clinico Humanitas

Rozzano, 20089, Italy

RECRUITING

National Cancer Center Hospital

Chūōku, 104-0045, Japan

RECRUITING

Kyushu University Hospital

Fukuoka, 812-8582, Japan

RECRUITING

Hyogo Prefectural Kobe Children's Hospital

Kobe, 650-0047, Japan

RECRUITING

Leids Universitair Medisch Centrum

Leiden, 2333 ZA, Netherlands

RECRUITING

Prinses Maxima Centrum

Utrecht, 3584 CS, Netherlands

RECRUITING

Hospital de la Santa Creu i Sant Pau

Barcelona, 08025, Spain

RECRUITING

Hospital Universitari Vall d'Hebron

Barcelona, 08035, Spain

RECRUITING

Hospital Universitari Vall d'Hebron

Barcelona, 8035, Spain

RECRUITING

Hospital Sant Joan de Déu

Esplugues de Llobregat, 8950, Spain

RECRUITING

Hospital General Universitario Gregorio Marañon

Madrid, 28007, Spain

RECRUITING

Hospital General Universitario Gregorio Marañon

Madrid, 28007, Spain

RECRUITING

Hospital Infantil Universitario Niño Jesús

Madrid, 28009, Spain

RECRUITING

Hospital Universitario La Paz

Madrid, 28046, Spain

RECRUITING

Hospital Universitario La Paz

Madrid, 28046, Spain

RECRUITING

Hospital Universitario de Canarias

San Cristóbal de La Laguna, 38320, Spain

RECRUITING

Hospital Universitario Virgen Del Rocio

Seville, 41013, Spain

RECRUITING

Hospital Universitario Virgen Del Rocio

Seville, 41013, Spain

RECRUITING

Hospital Universitari i Politecnic La Fe

Valencia, 46026, Spain

RECRUITING

University College Hospital - London

London, NW1 2PG, United Kingdom

RECRUITING

Royal Marsden Hospital

London, SW3 6JJ, United Kingdom

RECRUITING

Royal Marsden Hospital

London, SW3 6JJ, United Kingdom

RECRUITING

Royal Manchester Children's Hospital

Manchester, M13 9WL, United Kingdom

RECRUITING

The Christie NHS Foundation Trust

Manchester, M20 4BX, United Kingdom

RECRUITING

MeSH Terms

Conditions

Neoplasms

Interventions

RamucirumabCyclophosphamideVinorelbineGemcitabineDocetaxelabemaciclibIrinotecanTemozolomide

Intervention Hierarchy (Ancestors)

Antibodies, Monoclonal, HumanizedAntibodies, MonoclonalAntibodiesImmunoglobulinsImmunoproteinsBlood ProteinsProteinsAmino Acids, Peptides, and ProteinsSerum GlobulinsGlobulinsPhosphoramide MustardsNitrogen Mustard CompoundsMustard CompoundsHydrocarbons, HalogenatedHydrocarbonsOrganic ChemicalsPhosphoramidesOrganophosphorus CompoundsVinca AlkaloidsSecologanin Tryptamine AlkaloidsIndole AlkaloidsAlkaloidsHeterocyclic CompoundsIndolesHeterocyclic Compounds, 2-RingHeterocyclic Compounds, Fused-RingIndolizidinesIndolizinesDeoxycytidineCytidinePyrimidine NucleosidesPyrimidinesHeterocyclic Compounds, 1-RingTaxoidsCyclodecanesCycloparaffinsHydrocarbons, AlicyclicHydrocarbons, CyclicDiterpenesTerpenesCamptothecinDacarbazineTriazenesImidazolesAzoles

Study Officials

  • Call 1-877-CTLILLY (1-877-285-4559) or 1-317-615-4559 Mon - Fri 8 AM - 8 PM Eastern time (UTC/GMT - 5 hours, EST)

    Eli Lilly and Company

    STUDY DIRECTOR

Central Study Contacts

Trial questions or participation questions: 1-877-CTLILLY (1-877-285-4559) or

CONTACT

Physicians interested in becoming principal investigators please contact

CONTACT

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR
Expanded Access
Yes

Study Record Dates

First Submitted

August 14, 2023

First Posted

August 21, 2023

Study Start

January 22, 2020

Primary Completion (Estimated)

May 1, 2027

Study Completion (Estimated)

May 1, 2027

Last Updated

March 27, 2026

Record last verified: 2026-03

Data Sharing

IPD Sharing
Will share

Anonymized individual patient level data will be provided in a secure access environment upon approval of a research proposal and a signed data sharing agreement.

Shared Documents
STUDY PROTOCOL
Time Frame
Data are available 6 months after the primary publication and approval of the indication studied in the US and European Union (EU), whichever is later. Data will be indefinitely available for requesting.
Access Criteria
A research proposal must be approved by an independent review panel and researchers must sign a data sharing agreement.
More information

Locations