NCT05048797

Brief Summary

DESTINY-Lung04 will investigate the efficacy and safety of Trastuzumab Deruxtecan (T-DXd) versus Standard of Care (SoC) as first-line treatment of Non-Small Cell Lung Cancer (NSCLC) with HER2 Exon 19 or 20 mutations

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Strong global presence with extensive site network
Enrollment
454

participants targeted

Target at P50-P75 for phase_3

Timeline
15mo left

Started Oct 2021

Longer than P75 for phase_3

Geographic Reach
20 countries

130 active sites

Status
active not recruiting

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Progress79%
Oct 2021Jul 2027

First Submitted

Initial submission to the registry

September 9, 2021

Completed
8 days until next milestone

First Posted

Study publicly available on registry

September 17, 2021

Completed
1 month until next milestone

Study Start

First participant enrolled

October 28, 2021

Completed
4.4 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

March 30, 2026

Completed
1.3 years until next milestone

Study Completion

Last participant's last visit for all outcomes

July 30, 2027

Expected
Last Updated

December 23, 2025

Status Verified

December 1, 2025

Enrollment Period

4.4 years

First QC Date

September 9, 2021

Last Update Submit

December 22, 2025

Conditions

Keywords

DS-8201aHER2 exon 19 or 20 mutationsERBB2 gene (coding for the HER2 protein)T-DXdTrastuzumab DeruxtecanLocally advanced and unresectable non-squamous NSCLCMetastatic non-squamous NSCLCNon-small cell lung cancer

Outcome Measures

Primary Outcomes (1)

  • Progression Free Survival (PFS) by Blinded Independent Central Review (BICR)

    Defined as time from randomization until progression per RECIST 1.1 as assessed by Blinded Independent Central Review (BICR), or death due to any cause.

    Until progression or death, assessed up to approximately 12 months

Secondary Outcomes (15)

  • Overall Survival (OS)

    Until death, assessed up to approximately 28 months.

  • Progression Free Survival (PFS) by investigator assessment

    Until progression, assessed up to approximately 12 months

  • Objective Response Rate (ORR)

    Until progression, assessed up to approximately 12 months

  • Duration of Response (DoR)

    Until progression, assessed up to approximately 12 months

  • Time to second progression or death (PFS2)

    Assessed up to approximately 20 months

  • +10 more secondary outcomes

Study Arms (2)

Arm 1

EXPERIMENTAL

Trastuzumab Deruxtecan (T-DXd)

Drug: Trastuzumab Deruxtecan

Arm 2

ACTIVE COMPARATOR

Standard of Care Treatment (platinum, pemetrexed and pembrolizumab)

Drug: CisplatinDrug: CarboplatinDrug: PembrolizumabDrug: Pemetrexed

Interventions

Trastuzumab Deruxtecan administered by intravenous infusion

Also known as: DS-8201a; T-DXd
Arm 1

Investigator's choice of platinum chemotherapy (cisplatin) administered by intravenous infusion

Arm 2

Investigator's choice of platinum chemotherapy (carboplatin) administered by intravenous infusion

Arm 2

Pembrolizumab administered by intravenous infusion

Arm 2

Pemetrexed administered by intravenous infusion

Arm 2

Eligibility Criteria

Age18 Years - 123 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Participants at least 18 years of age
  • Locally advanced and unresectable NSCLC, not amenable to curative therapy, or metastatic disease
  • Histologically documented non-squamous NSCLC with HER2 mutation in exons 19 or 20 by tissue NGS or ctDNA
  • Treatment-naïve for palliative intent systemic therapy for locally advanced or metastatic disease
  • Left ventricular ejection fraction (LVEF) ≥ 50%
  • Measurable disease assessed by Investigator based on RECIST 1.1
  • Protocol-defined adequate organ function including cardiac, renal, hepatic function
  • ECOG 0-1
  • Having tumour tissue available for central testing

You may not qualify if:

  • Tumors with targetable alterations to EGFR (or other targetable mutations including but not limited to ALK, if routinely tested as a targetable alteration with approved available therapy)
  • Any untreated brain metastases, including asymptomatic or clinically inactive brain metastases
  • Active autoimmune or inflammatory disorders
  • Medical history of myocardial infarction within 6 months prior to randomization
  • History of non-infectious pneumonitis/ILD, current or suspected ILD
  • Lung-specific intercurrent clinical significant severe illness
  • Contraindication to platinum-based doublet chemotherapy or pembrolizumab

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (130)

Research Site

Anchorage, Alaska, 99508, United States

Location

Research Site

Los Alamitos, California, 90720, United States

Location

Research Site

Los Angeles, California, 90048, United States

Location

Research Site

Orange, California, 92868, United States

Location

Research Site

San Francisco, California, 94143, United States

Location

Research Site

Santa Monica, California, 90404, United States

Location

Research Site

Silver Spring, Maryland, 20910, United States

Location

Research Site

Boston, Massachusetts, 02215, United States

Location

Research Site

Ann Arbor, Michigan, 48109, United States

Location

Research Site

Basking Ridge, New Jersey, 07920, United States

Location

Research Site

Middletown, New Jersey, 07748, United States

Location

Research Site

Montvale, New Jersey, 07645, United States

Location

Research Site

New Brunswick, New Jersey, 08901, United States

Location

Research Site

Commack, New York, 11725, United States

Location

Research Site

Harrison, New York, 10604, United States

Location

Research Site

New York, New York, 10065, United States

Location

Research Site

Uniondale, New York, 11553, United States

Location

Research Site

Pittsburgh, Pennsylvania, 15232, United States

Location

Research Site

Dallas, Texas, 75246, United States

Location

Research Site

Linz, 4020, Austria

Location

Research Site

Vienna, 1210, Austria

Location

Research Site

Ghent, 9000, Belgium

Location

Research Site

Leuven, 3000, Belgium

Location

Research Site

Barretos, 14784-400, Brazil

Location

Research Site

Blumenau, 89010-340, Brazil

Location

Research Site

Brasília, 70200-730, Brazil

Location

Research Site

Natal, 59075-740, Brazil

Location

Research Site

Salvador, 40170-110, Brazil

Location

Research Site

São Paulo, 01321-001, Brazil

Location

Research Site

São Paulo, 01327-001, Brazil

Location

Research Site

Uberlândia, 38408-150, Brazil

Location

Research Site

Vancouver, British Columbia, V5Z 4E6, Canada

Location

Research Site

Brampton, Ontario, L6R 3J7, Canada

Location

Research Site

Toronto, Ontario, M5G 1Z5, Canada

Location

Research Site

Montreal, Quebec, H4A 3J1, Canada

Location

Research Site

Beijing, 100142, China

Location

Research Site

Beijing, 100730, China

Location

Research Site

Changchun, 130021, China

Location

Research Site

Changsha, 410008, China

Location

Research Site

Changsha, 410013, China

Location

Research Site

Chengdu, 610041, China

Location

Research Site

Fuzhou, 350014, China

Location

Research Site

Guangzhou, 510080, China

Location

Research Site

Hangzhou, 310020, China

Location

Research Site

Jinan, 250117, China

Location

Research Site

Kunming, 650101, China

Location

Research Site

Kunming, 650118, China

Location

Research Site

Linhai, 317000, China

Location

Research Site

Nanchang, 330006, China

Location

Research Site

Nanjing, 210029, China

Location

Research Site

Shanghai, 200032, China

Location

Research Site

Shenyang, 110016, China

Location

Research Site

Shenzhen, 518020, China

Location

Research Site

Wenzhou, CN-325000, China

Location

Research Site

Wuhan, 430022, China

Location

Research Site

Xi'an, 710061, China

Location

Research Site

Xiamen, 361003, China

Location

Research Site

Yangzhou, 225001, China

Location

Research Site

Vejle, 7100, Denmark

Location

Research Site

Bordeaux, 33000, France

Location

Research Site

Dijon, 21079, France

Location

Research Site

Le Mans, 72037, France

Location

Research Site

Lyon, 69373, France

Location

Research Site

Marseille, 13915, France

Location

Research Site

Nantes, 44093, France

Location

Research Site

Toulouse, 31059, France

Location

Research Site

Villejuif, 94805, France

Location

Research Site

Cologne, 50937, Germany

Location

Research Site

Dresden, 01307, Germany

Location

Research Site

Mainz, 55131, Germany

Location

Research Site

München, 81377, Germany

Location

Research Site

Oldenburg, 26121, Germany

Location

Research Site

Hong Kong, HKG, Hong Kong

Location

Research Site

Hong Kong, Hong Kong

Location

Research Site

Jordan, HKG, Hong Kong

Location

Research Site

Bangalore, 560027, India

Location

Research Site

Delhi, 110085, India

Location

Research Site

Hyderabad, 500032, India

Location

Research Site

Mumbai, 400012, India

Location

Research Site

Nashik, 422002, India

Location

Research Site

Milan, 20141, Italy

Location

Research Site

Monza, 20090, Italy

Location

Research Site

Orbassano, 10043, Italy

Location

Research Site

Parma, 43100, Italy

Location

Research Site

Roma, 00168, Italy

Location

Research Site

Verona, 37126, Italy

Location

Research Site

Chūōku, 104-0045, Japan

Location

Research Site

Fukuoka, 812-8582, Japan

Location

Research Site

Kashiwa, 277-8577, Japan

Location

Research Site

Matsuyama, 791-0280, Japan

Location

Research Site

Niigata, 951-8566, Japan

Location

Research Site

Okayama, 700-8558, Japan

Location

Research Site

Osaka, 541-8567, Japan

Location

Research Site

Osakasayama-shi, 589-8511, Japan

Location

Research Site

Sapporo, 060-8638, Japan

Location

Research Site

Sendai, 980-0873, Japan

Location

Research Site

Sunto-gun, 411-8777, Japan

Location

Research Site

Yokohama, 241-8515, Japan

Location

Research Site

Yonago-shi, 683-8504, Japan

Location

Research Site

Mexico City, '14080, Mexico

Location

Research Site

Mexico City, 03810, Mexico

Location

Research Site

Amsterdam, 1081 HV, Netherlands

Location

Research Site

Groningen, 9700 RB, Netherlands

Location

Research Site

Nijmegen, 6525 GA, Netherlands

Location

Research Site

Gdansk, 80-952, Poland

Location

Research Site

Olsztyn, 10-357, Poland

Location

Research Site

Przemyśl, 37-700, Poland

Location

Research Site

Warsaw, 02-781, Poland

Location

Research Site

Cheongju-si, 28644, South Korea

Location

Research Site

Goyang-si, 10408, South Korea

Location

Research Site

Gyeonggi-do, 13620, South Korea

Location

Research Site

Seoul, 03080, South Korea

Location

Research Site

Seoul, 05505, South Korea

Location

Research Site

Seoul, 06351, South Korea

Location

Research Site

L'Hospitalet de Llobregat, 08908, Spain

Location

Research Site

Madrid, 28041, Spain

Location

Research Site

Málaga, 29730, Spain

Location

Research Site

Valencia, 46026, Spain

Location

Research Site

Kaohsiung City, 833, Taiwan

Location

Research Site

Taichung, 40201, Taiwan

Location

Research Site

Taichung, 40705, Taiwan

Location

Research Site

Tainan, 70403, Taiwan

Location

Research Site

Taipei, 10048, Taiwan

Location

Research Site

Taipei, 235, Taiwan

Location

Research Site

Taipei, TAIWAN, Taiwan

Location

Research Site

Taoyuan District, 333, Taiwan

Location

Research Site

Çankaya, 06680, Turkey (Türkiye)

Location

Research Site

Edirne, 22030, Turkey (Türkiye)

Location

Research Site

Izmir, 35040, Turkey (Türkiye)

Location

Research Site

Kadıkoy/Istanbul, 34722, Turkey (Türkiye)

Location

Related Links

MeSH Terms

Conditions

Carcinoma, Non-Small-Cell Lung

Interventions

trastuzumab deruxtecanCisplatinCarboplatinpembrolizumabPemetrexed

Condition Hierarchy (Ancestors)

Carcinoma, BronchogenicBronchial NeoplasmsLung NeoplasmsRespiratory Tract NeoplasmsThoracic NeoplasmsNeoplasms by SiteNeoplasmsLung DiseasesRespiratory Tract Diseases

Intervention Hierarchy (Ancestors)

Chlorine CompoundsInorganic ChemicalsNitrogen CompoundsPlatinum CompoundsCoordination ComplexesOrganic ChemicalsGuanineHypoxanthinesPurinonesPurinesHeterocyclic Compounds, 2-RingHeterocyclic Compounds, Fused-RingHeterocyclic CompoundsGlutamatesAmino Acids, AcidicAmino AcidsAmino Acids, Peptides, and ProteinsAmino Acids, Dicarboxylic

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Model Details: This study consists of two open-label treatment arms: Arm 1: Trastuzumab Deruxtecan Arm 2: Standard of Care treatment (platinum, pemetrexed and pembrolizumab)
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

September 9, 2021

First Posted

September 17, 2021

Study Start

October 28, 2021

Primary Completion

March 30, 2026

Study Completion (Estimated)

July 30, 2027

Last Updated

December 23, 2025

Record last verified: 2025-12

Data Sharing

IPD Sharing
Will share

Qualified researchers can request access to anonymized individual patient-level data from AstraZeneca group of companies sponsored clinical trials via the request portal. All request will be evaluated as per the AZ disclosure commitment: https://astrazenecagrouptrials.pharmacm.com/ST/Submission/Disclosure.

Shared Documents
STUDY PROTOCOL, SAP
Time Frame
AstraZeneca will meet or exceed data availability as per the commitments made to the EFPIA Pharma Data Sharing Principles. For details of our timelines, please rerefer to our disclosure commitment at https://astrazenecagrouptrials.pharmacm.com/ST/Submission/Disclosure.
Access Criteria
When a request has been approved AstraZeneca will provide access to the de-identified individual patient-level data in an approved sponsored tool . Signed Data Sharing Agreement (non-negotiable contract for data accessors) must be in place before accessing requested information. Additionally, all users will need to accept the terms and conditions of the SAS MSE to gain access. For additional details, please review the Disclosure Statements at https://astrazenecagrouptrials.pharmacm.com/ST/Submission/Disclosure.
More information

Locations