NCT04964934

Brief Summary

The study is intended to show superiority of AZD9833 in combination with CDK4/6 inhibitor (palbociclib, abemaciclib or ribociclib) versus aromatase inhibitors (anastrozole or letrozole) in combination with CDK4/6 inhibitor in patients with hormone receptor-positive (HR-positive), human epidermal growth factor receptor 2-negative (HER2-negative) metastatic breast cancer with detectable ESR1 mutation.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Strong global presence with extensive site network
Enrollment
315

participants targeted

Target at P50-P75 for phase_3

Timeline
28mo left

Started Jun 2021

Longer than P75 for phase_3

Geographic Reach
22 countries

263 active sites

Status
active not recruiting

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Progress68%
Jun 2021Sep 2028

First Submitted

Initial submission to the registry

June 30, 2021

Completed
Same day until next milestone

Study Start

First participant enrolled

June 30, 2021

Completed
16 days until next milestone

First Posted

Study publicly available on registry

July 16, 2021

Completed
4 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

June 30, 2025

Completed
3.2 years until next milestone

Study Completion

Last participant's last visit for all outcomes

September 1, 2028

Expected
Last Updated

April 21, 2026

Status Verified

April 1, 2026

Enrollment Period

4 years

First QC Date

June 30, 2021

Last Update Submit

April 20, 2026

Conditions

Keywords

MetastaticBreast NeoplasmsNeoplasms by SiteNeoplasmsBreast DiseasesPhysiological Effects of DrugsRandomisedMulticentreDouble-BlindPhase IIIAZD9833Next Generation Oral SERDAnastrozoleLetrozolePalbociclibAbemaciclibRibociclibAntagonistsAntineoplastic AgentsEstrogen Receptor AntagonistsHormone AntagonistscamizestrantESR1mSwitch TreatmentEndocrine TherapyEndocrine Resistance

Outcome Measures

Primary Outcomes (1)

  • Progression-free survival (PFS) assessed by the Investigator as defined by response evaluation criteria in solid tumors (RECIST version 1.1)

    PFS is defined as the time from randomization to objective disease progression (as assessed by RECIST 1.1) or death.

    From randomization until the earlier of the progression event or death (approximately 2 years)

Secondary Outcomes (8)

  • Progression-free survival 2 (PFS2)

    From randomization to the earliest of the progression event (following the initial progression), subsequent to first subsequent therapy or death (approximately 3.5 years)

  • Overall survival (OS)

    From randomization until the date of death due to any cause (approximately 5 years)

  • Chemotherapy free survival

    From randomization until the earlier of the start date of chemotherapy or death due to any cause (approximately 5 years)

  • Objective response rate (ORR) assessed by the Investigator as defined by RECIST version 1.1

    From randomization until a response or in the absence of a response from randomization up until progression, or the last evaluable assessment in the absence of progression (approximately 5 years)

  • Clinical benefit rate at 24 weeks (CBR24)

    At least 23 weeks after randomisation for each patient (1 week window for RECIST assessment)

  • +3 more secondary outcomes

Study Arms (2)

AZD9833 + palbociclib, abemaciclib or ribociclib

EXPERIMENTAL

The patients will receive AZD9833 (75 mg, PO, once daily) + palbociclib (PO, once daily, 125, 100 or 75 mg for 21 consecutive days followed by 7 days off treatment), abemaciclib (PO, twice daily, 150,100 or 50 mg) or ribociclib (To Be Determined, PO, once daily for 21 consecutive days followed by 7 days off treatment) + anastrozole placebo (PO, once daily) or letrozole placebo (PO, once daily)

Drug: AZD9833Drug: Anastrozole placeboDrug: Letrozole placeboDrug: PalbociclibDrug: AbemaciclibDrug: Luteinizing hormone-releasing hormone (LHRH) agonistDrug: Ribociclib

Anastrozole or letrozole + palbociclib, abemaciclib or ribociclib

ACTIVE COMPARATOR

The patients will recieve anastrozole (1 mg, PO, once daily) or letrozole (2.5 mg, PO, once daily) + palbociclib (PO, once daily, 125, 100 or 75 mg for 21 consecutive days followed by 7 days off treatment), abemaciclib (PO, twice daily, 150, 100 or 50 mg) or ribociclib (To Be Determined, PO, once daily for 21 consecutive days followed by 7 days off treatment) + AZD9833 placebo (PO, once daily)

Drug: AZD9833 PlaceboDrug: AnastrozoleDrug: LetrozoleDrug: PalbociclibDrug: AbemaciclibDrug: Luteinizing hormone-releasing hormone (LHRH) agonistDrug: Ribociclib

Interventions

Dosage formulation: abemaciclib tablets will be administered orally

AZD9833 + palbociclib, abemaciclib or ribociclibAnastrozole or letrozole + palbociclib, abemaciclib or ribociclib

Men (when medically applicable) and pre- or peri-menopausal women are required to receive a monthly LHRH agonist.

AZD9833 + palbociclib, abemaciclib or ribociclibAnastrozole or letrozole + palbociclib, abemaciclib or ribociclib

Dosage formulation: ribociclib tablets will be administered orally

AZD9833 + palbociclib, abemaciclib or ribociclibAnastrozole or letrozole + palbociclib, abemaciclib or ribociclib

Dosage formulation: AZD9833 tablets will be administered orally

AZD9833 + palbociclib, abemaciclib or ribociclib

Dosage formulation: AZD9833 placebo tablets will be administrated orally.

Anastrozole or letrozole + palbociclib, abemaciclib or ribociclib

Dosage formulation: anastrozole tablets will be administered orally.

Anastrozole or letrozole + palbociclib, abemaciclib or ribociclib

Dosage formulation: letrozole tablets will be administered orally.

Anastrozole or letrozole + palbociclib, abemaciclib or ribociclib

Dosage formulation: anastrozole placebo tablets will be administrated orally.

AZD9833 + palbociclib, abemaciclib or ribociclib

Dosage formulation: letrozole placebo tablets will be administered orally.

AZD9833 + palbociclib, abemaciclib or ribociclib

Dosage formulation: palbociclib tablets/capsules will be administered orally

AZD9833 + palbociclib, abemaciclib or ribociclibAnastrozole or letrozole + palbociclib, abemaciclib or ribociclib

Eligibility Criteria

Age18 Years - 130 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • INFORMATION FOR TRIAL PARTICIPANTS - Participants can join the trial if they:
  • Have advanced breast cancer that is not able to be treated with surgery or radiation;
  • Have an ESR1 mutation in their cancer;
  • Have breast cancer that is HR-positive and HER2-negative;
  • Are currently being treated with a CDK4/6 inhibitor and an AI and have been taking these drugs for at least 6 months;
  • Have not had their cancer get worse after taking an AI and CDK4/6 inhibitor;
  • Are able to do their daily activities;
  • Are at least 18.
  • Proven diagnosis of adenocarcinoma of the breast with evidence of locoregionally recurrent or metastatic disease not amenable to resection or radiation therapy with curative intent;
  • Documentation of histologically confirmed diagnosis of estrogen receptor positive (ER+) /HER2- breast cancer based on local laboratory results;
  • Currently on AI (letrozole or anastrozole) + CDK4/6 inhibitor (palbociclib, abemaciclib or ribociclib) ± LHRH as the initial endocrine based treatment for advanced disease;
  • Eastern Cooperative Oncology Group performance status of 0 or 1;
  • ESR1m detected by central testing of ctDNA with Guardant360® CDx;
  • Willingness and ability to comply with scheduled visits, treatment plan, laboratory tests, and other study procedures;
  • Adequate organ and marrow function.

You may not qualify if:

  • INFORMATION FOR TRIAL PARTICIPANTS - Participants cannot join the trial if they:
  • Had certain types of tumors in the past that may come back;
  • Are currently taking any other treatments for their cancer or other conditions including hormone replacements, medications, or supplements that could interfere with the trial treatment;
  • Have or have had any major health problem, infection, or recent surgery that could make it difficult or dangerous to participate in this trial.
  • Advanced, symptomatic, visceral spread, that are at risk of life-threatening complications in the short term;
  • Known active uncontrolled or symptomatic CNS metastases, carcinomatous meningitis, or leptomeningeal disease;
  • Any evidence of severe or uncontrolled systemic diseases which, in the investigator's opinion, makes it undesirable for the participant to participate in the study or that would jeopardize compliance with the protocol;
  • Patient with known or family history of severe heart disease;
  • Previous treatment with AZD9833, investigational SERDs or fulvestrant;
  • Currently pregnant (confirmed with positive pregnancy test) or breastfeeding;
  • Persistent non-haematological toxicities (CTCAE Grade \> 2) caused by CDK4/6 inhibitor and/or AI treatment.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (265)

Research Site

Phoenix, Arizona, 85054, United States

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Hot Springs, Arkansas, 71913, United States

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Little Rock, Arkansas, 72205, United States

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Long Beach, California, 90806, United States

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San Diego, California, 92123, United States

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Santa Rosa, California, 92805, United States

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Grand Junction, Colorado, 81501, United States

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Lone Tree, Colorado, 80124, United States

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Fort Myers, Florida, 33901, United States

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Jacksonville, Florida, 32224, United States

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Jacksonville, Florida, 32256, United States

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St. Petersburg, Florida, 33705, United States

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Atlanta, Georgia, 30318, United States

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Atlanta, Georgia, 30322, United States

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Atlanta, Georgia, 30342, United States

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Park Ridge, Illinois, 60068, United States

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Fort Wayne, Indiana, 46804, United States

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Indianapolis, Indiana, 46250, United States

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Baltimore, Maryland, 21202, United States

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Boston, Massachusetts, 02215, United States

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Fairhaven, Massachusetts, 02719, United States

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Foxborough, Massachusetts, 02035, United States

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Milford, Massachusetts, 01757, United States

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South Weymouth, Massachusetts, 02190, United States

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Detroit, Michigan, 48202, United States

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Grand Rapids, Michigan, 49503, United States

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Rochester, Minnesota, 55905, United States

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Oxford, Mississippi, 38655, United States

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Kansas City, Missouri, 64111, United States

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St Louis, Missouri, 63110, United States

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Billings, Montana, 59101, United States

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Omaha, Nebraska, 68130, United States

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Camden, New Jersey, 08103, United States

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Ridgewood, New Jersey, 07450, United States

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Brooklyn, New York, 11215, United States

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East Syracuse, New York, 13057, United States

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New Hyde Park, New York, 11042, United States

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New York, New York, 10065, United States

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New York, New York, 11355, United States

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Shirley, New York, 11967, United States

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Goldsboro, North Carolina, 27534, United States

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Canton, Ohio, 44710, United States

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Cincinnati, Ohio, 45220, United States

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Columbus, Ohio, 43219, United States

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Portland, Oregon, 97213, United States

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Philadelphia, Pennsylvania, 19104, United States

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Pittsburgh, Pennsylvania, 15213, United States

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York, Pennsylvania, 17403, United States

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Greenville, South Carolina, 29607, United States

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West Columbia, South Carolina, 29169, United States

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Knoxville, Tennessee, 37916, United States

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Memphis, Tennessee, 38120, United States

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Nashville, Tennessee, 37203, United States

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Bedford, Texas, 76022, United States

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Dallas, Texas, 75246, United States

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Houston, Texas, 77024, United States

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Houston, Texas, 77030, United States

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Irving, Texas, 75063, United States

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Longview, Texas, 75601, United States

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San Antonio, Texas, 78240, United States

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Salt Lake City, Utah, 84106, United States

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Midlothian, Virginia, 23114, United States

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Norfolk, Virginia, 23502, United States

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Tacoma, Washington, 98405, United States

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Waukesha, Wisconsin, 53226, United States

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Birtinya, 4575, Australia

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Darlinghurst, 2010, Australia

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Graz, 8036, Austria

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Innsbruck, 6020, Austria

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Salzburg, 5020, Austria

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Vienna, 1130, Austria

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Leuven, 3000, Belgium

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Liège, 4000, Belgium

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Namur, 5000, Belgium

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Haskovo, 6300, Bulgaria

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Panagyurishte, 4500, Bulgaria

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Pleven, 5804, Bulgaria

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Plovdiv, 4004, Bulgaria

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Sofia, 1303, Bulgaria

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Sofia, 1330, Bulgaria

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Sofia, 1407, Bulgaria

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Sofia, 1431, Bulgaria

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Sofia, 1527, Bulgaria

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Calgary, Alberta, T2N 5G2, Canada

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Vancouver, British Columbia, V5Z 4E6, Canada

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Ottawa, Ontario, K1H 8L6, Canada

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Lévis, Quebec, G6V 3Z1, Canada

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Montreal, Quebec, H1T 2M4, Canada

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Montreal, Quebec, H2X 0C1, Canada

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Montreal, Quebec, H3T 1E2, Canada

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Québec, Quebec, G1S 4L8, Canada

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Avignon, 84918, France

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Brest, 29200, France

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Clermont-Ferrand, 63050, France

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Dijon, 21079, France

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Limoges, 83000, France

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Lorient, 56322, France

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Lyon, 69373, France

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Marseille, 13273, France

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Metz-Tessy, 74370, France

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Nîmes, 30029, France

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Paris, 75248, France

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Rouen, 76021, France

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Saint-Cloud, 92210, France

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Saint-Herblain, 44805, France

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Toulouse, 31100, France

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Tours, 37000, France

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Vandœuvre-lès-Nancy, 54519, France

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Vantoux, 57070, France

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Villejuif, 94805, France

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Ansbach, 91522, Germany

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Aschaffenburg, 63739, Germany

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Augsburg, 86156, Germany

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Bonn, 53111, Germany

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Chemnitz, 09116, Germany

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Dresden, 01307, Germany

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Erlangen, 91054, Germany

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Essen, 45130, Germany

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Freiburg im Breisgau, 79110, Germany

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Immenstadt im Allgäu, 87509, Germany

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Koblenz, 56068, Germany

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Leipzig, 4103, Germany

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Mannheim, 68167, Germany

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München, 80634, Germany

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Paderborn, 33098, Germany

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Ratingen, 40878, Germany

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Ravensburg, 88212, Germany

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Regensburg, 93053, Germany

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Stade, 21680, Germany

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Tübingen, 72076, Germany

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Ulm, 89075, Germany

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Budapest, 1062, Hungary

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Budapest, 1122, Hungary

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Miskolc, 3526, Hungary

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Szekszárd, 7100, Hungary

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Szolnok, 5000, Hungary

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Zalaegerszeg, 8900, Hungary

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Beersheba, 8410101, Israel

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Haifa, 3109601, Israel

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Jerusalem, 91120, Israel

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Petah Tikva, 494142, Israel

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Ramat Gan, 5262000, Israel

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Bergamo, 24127, Italy

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Bologna, 40138, Italy

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Florence, 50134, Italy

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Meldola, 47014, Italy

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Milan, 20132, Italy

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Milan, 20141, Italy

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Misterbianco, 95045, Italy

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Naples, 80131, Italy

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Padova, 35128, Italy

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Roma, 00168, Italy

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Rozzano, 20089, Italy

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Chiba, 260-8717, Japan

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Chūōku, 104-0045, Japan

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Hidaka-shi, 350-1298, Japan

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Hirakata-shi, 573-1191, Japan

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Kitaadachi-gun, 362-0806, Japan

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Kōtoku, 135-8550, Japan

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Kumamoto, 860-8556, Japan

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Matsuyama, 791-0280, Japan

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Nagoya, 464-8681, Japan

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Nagoya, 467-8602, Japan

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Niigata, 951-8566, Japan

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Osaka, 540-0006, Japan

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Osaka, 541-8567, Japan

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Ota-shi, 373-8550, Japan

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Sapporo, 003-0804, Japan

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Shinagawa-ku, 142-8666, Japan

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Shinjuku-ku, 162-8655, Japan

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Takasaki-shi, 370-0829, Japan

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Takatsuki-shi, 569-8686, Japan

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Tsukuba, 305-8577, Japan

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Yokohama, 241-8515, Japan

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Drammen, 3004, Norway

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Oslo, 0450, Norway

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Bydgoszcz, 85-796, Poland

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Gdynia, 81-519, Poland

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Koszalin, 75-581, Poland

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Lodz, 90-302, Poland

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Poznan, 60-693, Poland

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Rzeszów, 35-001, Poland

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Tomaszów Mazowiecki, 97-200, Poland

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Warsaw, 02-781, Poland

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Guimarães, 4835-044, Portugal

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Lisbon, 1400-038, Portugal

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Lisbon, 1449-005, Portugal

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Lisbon, 1500-650, Portugal

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Lisbon, 1649-035, Portugal

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Loures, 2674-514, Portugal

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Porto, 4099-001, Portugal

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Porto, 4200-072, Portugal

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Porto, 4200-319, Portugal

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Vila Nova de Gaia, 4434-502, Portugal

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Moscow, 111123, Russia

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Moscow, 129090, Russia

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Moscow, 143423, Russia

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Nizhny Novgorod, 603126, Russia

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Podolsk, 142100, Russia

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Saint Petersburg, 194017, Russia

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Saint Petersburg, 197758, Russia

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Banská Bystrica, 974 01, Slovakia

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Bratislava, 833 01, Slovakia

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Košice, 041 91, Slovakia

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Michalovce, 07101, Slovakia

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Partizánske, 958 01, Slovakia

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Cheonan-si, 31151, South Korea

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Daegu, 42415, South Korea

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Goyang-si, 10408, South Korea

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Seongnam-si, 13620, South Korea

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Seongnam-si, 463-712, South Korea

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Seoul, 02841, South Korea

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Seoul, 03080, South Korea

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Seoul, 03722, South Korea

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Seoul, 05505, South Korea

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Seoul, 06273, South Korea

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Seoul, 06351, South Korea

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Seoul, 06591, South Korea

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A Coruña, 15009, Spain

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Badalona, 08003, Spain

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Barcelona, 8035, Spain

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L'Hospitalet de Llobregat, 08908, Spain

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Madrid, 28040, Spain

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Madrid, 28041, Spain

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Málaga, 29010, Spain

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Murcia, 30008, Spain

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Sant Joan Despí, 08970, Spain

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Seville, 41013, Spain

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Valencia, 46010, Spain

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Bern, CH-3010, Switzerland

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Chur, CH-7000, Switzerland

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Winterthur, 8401, Switzerland

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Kaohsiung City, 833, Taiwan

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Taichung, 40705, Taiwan

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Tainan, 70403, Taiwan

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Tainan, 710, Taiwan

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Taipei, 100, Taiwan

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Taipei, 110, Taiwan

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Taipei, 11259, Taiwan

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Taipei, 11490, Taiwan

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Taipei, 23561, Taiwan

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Taipei, Taiwan

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Taoyuan District, 333, Taiwan

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Adana, 01120, Turkey (Türkiye)

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Ankara, 06010, Turkey (Türkiye)

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Ankara, 06100, Turkey (Türkiye)

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Ankara, 06340, Turkey (Türkiye)

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Ankara, 06520, Turkey (Türkiye)

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Cordaleo, 35575, Turkey (Türkiye)

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Izmir, 35100, Turkey (Türkiye)

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Izmir, 35360, Turkey (Türkiye)

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Kadıkoy/Istanbul, 34722, Turkey (Türkiye)

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Kayseri, 38039, Turkey (Türkiye)

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Blackpool, FY3 8NR, United Kingdom

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Cambridge, CB2 0QQ, United Kingdom

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London, SW3 6JJ, United Kingdom

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London, WC1N 3BG, United Kingdom

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Manchester, M20 4BX, United Kingdom

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Newport, NP10 8FZ, United Kingdom

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Nottingham, NG5 1PB, United Kingdom

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Portsmouth, PO6 3LY, United Kingdom

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Reading, RG2 9LH, United Kingdom

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Sheffield, S10 2SJ, United Kingdom

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Sutton, SM2 5PT, United Kingdom

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Taunton, TA1 5DA, United Kingdom

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Related Publications (2)

  • Bidard FC, Mayer EL, Park YH, Janni W, Ma C, Cristofanilli M, Bianchini G, Kalinsky K, Iwata H, Chia S, Fasching PA, Brufsky A, Nowecki Z, Pascual J, Moreau L, Chen SC, Karadurmus N, Gal-Yam EN, Jung KH, Pernas S, McClain S, He W, Klinowska T, Huang-Bartlett C, Turner NC; SERENA-6 Study Group. First-Line Camizestrant for Emerging ESR1-Mutated Advanced Breast Cancer. N Engl J Med. 2025 Aug 7;393(6):569-580. doi: 10.1056/NEJMoa2502929. Epub 2025 Jun 1.

  • Turner N, Huang-Bartlett C, Kalinsky K, Cristofanilli M, Bianchini G, Chia S, Iwata H, Janni W, Ma CX, Mayer EL, Park YH, Fox S, Liu X, McClain S, Bidard FC. Design of SERENA-6, a phase III switching trial of camizestrant in ESR1-mutant breast cancer during first-line treatment. Future Oncol. 2023 Mar;19(8):559-573. doi: 10.2217/fon-2022-1196. Epub 2023 Apr 18.

Related Links

MeSH Terms

Conditions

Neoplasm MetastasisBreast NeoplasmsNeoplasms by SiteNeoplasmsBreast Diseases

Interventions

AZD9833AnastrozoleLetrozolepalbociclibabemaciclibGonadotropin-Releasing Hormoneribociclib

Condition Hierarchy (Ancestors)

Neoplastic ProcessesPathologic ProcessesPathological Conditions, Signs and SymptomsSkin DiseasesSkin and Connective Tissue Diseases

Intervention Hierarchy (Ancestors)

NitrilesOrganic ChemicalsTriazolesAzolesHeterocyclic Compounds, 1-RingHeterocyclic CompoundsPituitary Hormone-Releasing HormonesHypothalamic HormonesPeptide HormonesHormonesHormones, Hormone Substitutes, and Hormone AntagonistsNeuropeptidesPeptidesAmino Acids, Peptides, and ProteinsOligopeptidesNerve Tissue ProteinsProteins

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
TRIPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

June 30, 2021

First Posted

July 16, 2021

Study Start

June 30, 2021

Primary Completion

June 30, 2025

Study Completion (Estimated)

September 1, 2028

Last Updated

April 21, 2026

Record last verified: 2026-04

Data Sharing

IPD Sharing
Will share

Qualified researchers can request access to anonymized individual patient-level data from AstraZeneca group of companies sponsored clinical trials via the request portal. All request will be evaluated as per the AZ disclosure commitment: https://astrazenecagrouptrials.pharmacm.com/ST/Submission/Disclosure. Yes, indicates that AZ are accepting requests for IPD, but this does not mean all requests will be shared.

Shared Documents
STUDY PROTOCOL, SAP
Time Frame
AstraZeneca will meet or exceed data availability as per the commitments made to the EFPIA Pharma Data Sharing Principles. For details of our timelines, please rerefer to our disclosure commitment at https://astrazenecagrouptrials.pharmacm.com/ST/Submission/Disclosure.
Access Criteria
When a request has been approved AstraZeneca will provide access to the deidentified individual patient-level data in an approved sponsored tool. Signed Data Sharing Agreement (non-negotiable contract for data accessors) must be in place before accessing requested information. Additionally, all users will need to accept the terms and conditions of the SAS MSE to gain access. For additional details, please review the Disclosure Statements at https://astrazenecagrouptrials.pharmacm.com/ST/Submission/Disclosure.
More information

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