NCT04711252

Brief Summary

The study is intended to show superiority of AZD9833 in combination with palbociclib (a CDK4/6 inhibitor) versus anastrozole (an aromatase inhibitor) and palbociclib as the initial treatment of patients with hormone receptor-positive (ER-positive), human epidermal growth factor 2-negative (HER2-negative) advanced/metastatic breast cancer. INFORMATION FOR TRIAL PARTICIPANTS In this trial, the researchers will look at how well camizestrant with palbociclib works, compared with anastrozole with palbociclib, in participants with breast cancer that has either spread into other parts of the body at the time of diagnosis, or has come back after at least 2 years of standard endocrine treatment. Participants in this trial will have breast cancer that has ER proteins but does not have overexpression of HER2 protein.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Strong global presence with extensive site network
Enrollment
1,370

participants targeted

Target at P75+ for phase_3

Timeline
34mo left

Started Jan 2021

Longer than P75 for phase_3

Geographic Reach
27 countries

263 active sites

Status
active not recruiting

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Progress66%
Jan 2021Feb 2029

First Submitted

Initial submission to the registry

December 23, 2020

Completed
23 days until next milestone

First Posted

Study publicly available on registry

January 15, 2021

Completed
13 days until next milestone

Study Start

First participant enrolled

January 28, 2021

Completed
5.6 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

August 24, 2026

Expected
2.4 years until next milestone

Study Completion

Last participant's last visit for all outcomes

February 1, 2029

Last Updated

October 14, 2025

Status Verified

October 1, 2025

Enrollment Period

5.6 years

First QC Date

December 23, 2020

Last Update Submit

October 10, 2025

Conditions

Keywords

MetastaticBreast NeoplasmsNeoplasms by SiteNeoplasmsBreast DiseasesSkin DiseasesHormones, Hormone Substitutes, and HormonePhysiological Effects of DrugsRandomisedMulticentreDouble-BlindPhase IIIAZD9833Next Generation Oral SERDAnastrozolePalbociclibAntagonistsAntineoplastic AgentsEstrogen Receptor AntagonistsHormone Antagonistscamizestrant

Outcome Measures

Primary Outcomes (1)

  • Progression-free survival (PFS) assessed by the Investigator as defined by response evaluation criteria in solid tumors (RECIST) version 1.1

    PFS is defined as the time from randomization to objective disease progression (as assessed by RECIST) or death.

    From randomization until progression per RECIST 1.1 as assessed by the investigator at local site or death due to any cause (up to 5 years)

Secondary Outcomes (11)

  • Overall survival (OS)

    From randomization until the date of death due to any cause (up to 8 years)

  • Second progression-free survival (PFS2)

    From randomization to the earliest of the progression event (following the initial progression), subsequent to first subsequent therapy or death (up to 5 years)

  • Objective response rate (ORR) assessed by the Investigator as defined by RECIST version 1.1

    From randomization until a response or in the absence of a response from randomization up until progression, or the last evaluable assessment in the absence of progression (up to 5 years)

  • Duration of response (DoR) assessed by the Investigator as defined by RECIST version 1.1

    From the date of first documented response until date of documented progression per RECIST 1.1 as assessed by the investigator at local site or death due to any cause (up to 5 years)

  • Time to chemotherapy (TTC)

    From randomization until the earlier of the start date of chemotherapy or death due to any cause (up to 5 years)

  • +6 more secondary outcomes

Study Arms (2)

AZD9833 + palbociclib

EXPERIMENTAL

The patients will receive AZD9833 (75 mg, PO, once daily) + palbociclib (PO, once daily, 125 mg for 21 consecutive days followed by 7 days off treatment) + anastrozole placebo (1 mg, PO, once daily)

Drug: AZD9833Drug: Anastrozole placeboDrug: PalbociclibDrug: Luteinizing hormone-releasing hormone (LHRH) agonist

Anastrozole + palbociclib

ACTIVE COMPARATOR

The patients will recieve Anastrozole (1 mg, PO, once daily) + palbociclib (PO, once daily, 125 mg for 21 consecutive days followed by 7 days off treatment) + AZD9833 placebo (PO, once daily)

Drug: AnastrozoleDrug: AZD9833 placeboDrug: PalbociclibDrug: Luteinizing hormone-releasing hormone (LHRH) agonist

Interventions

Dosage formulation: AZD9833 tablets will be administered orally

AZD9833 + palbociclib

Dosage formulation: Anastrozole tablets will be administered orally.

Anastrozole + palbociclib

Dosage formulation: anastrozole placebo tablets will be administrated orally.

AZD9833 + palbociclib

Dosage formulation: AZD9833 placebo tablets will be administrated orally.

Anastrozole + palbociclib

Dosage formulation: palbociclib tablets/capsules will be administered orally

AZD9833 + palbociclibAnastrozole + palbociclib

Men (when medically applicable) and pre- or peri-menopausal women are required to receive a monthly LHRH agonist.

AZD9833 + palbociclibAnastrozole + palbociclib

Eligibility Criteria

Age18 Years - 130 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Pre-/peri-menopausal women or men can be enrolled if amenable to be treated with concomitant, approved LHRH agonists for the duration of the study treatment.
  • De novo Stage 4 disease, or recurrence from early stage disease after at least 24 months of standard adjuvant endocrine therapy. Note that at least 12 months must have elapsed since the patient's last dose of adjuvant AI therapy without disease progression on treatment. Note that a 2-week washout period is required after the last dose of tamoxifen prior to randomisation.
  • Histologically or cytologically documented diagnosis of ER+, HER2-negative breast cancer based on local laboratory results.
  • Previously untreated with any systemic anti-cancer therapy for their locoregionally recurrent or metastatic ER+ disease.
  • Measurable disease as defined per RECIST v.1.1 OR at least one lytic or mixed (lytic + sclerotic) bone lesion with a soft tissue component that can be assessed by CT or MRI.
  • Eastern Cooperative Oncology Group performance status of 0 or 1.
  • Adequate organ and marrow function.
  • Willingness and ability to comply with scheduled visits, treatment plan, laboratory tests, and other study procedures.
  • INFORMATION FOR TRIAL PARTICIPANTS
  • Participants can join the trial if they:
  • Have breast cancer that cannot be treated with surgery or radiation
  • Have breast cancer that has already spread into other parts of the body at the time of diagnosis, or has come back after at least 2 years of a standard endocrine treatment
  • Have ER proteins but not overexpression of HER2 protein in their tumors
  • Have never received any type of cancer therapy that affects the whole body for advanced breast cancer
  • Are able to do their daily activities

You may not qualify if:

  • Previous neoadjuvant or adjuvant treatment with an AI treatment +/- CDK4/6 inhibitor with disease recurrence while on or within 12 months of completing treatment.
  • Prior exposure to AZD9833, other investigational SERDs/endocrine agents or fulvestrant.
  • Participation in another clinical study with a study treatment or investigational medicinal device administered in the last 4 weeks prior to randomization or concurrent enrollment in another clinical study, unless it is an observational (non-interventional) clinical study or during the follow-up period of an interventional study.
  • Advanced, symptomatic, visceral spread, that are at risk of life-threatening complications in the short term and/or impending visceral crisis
  • Known active uncontrolled or symptomatic CNS metastases, carcinomatous meningitis, or leptomeningeal disease.
  • Any clinically important and symptomatic heart disease .
  • Currently pregnant (confirmed with positive pregnancy test) or breast-feeding.
  • As judged by the investigator, any evidence of diseases (such as severe or uncontrolled systemic diseases, renal transplant and active bleeding diseases) which, in the investigator's opinion, makes it undesirable for the participant to participate in the study or that would jeopardize compliance with the protocol.
  • Any concurrent anti-cancer treatment.
  • Active infection including tuberculosis, HBV and HCV.
  • INFORMATION FOR TRIAL PARTICIPANTS
  • Participants cannot join the trial if they:
  • Have uncontrolled cancer that has spread to the brain or the spinal cord
  • Have received certain treatments for cancer in the past but the cancer came back within 1 year
  • Had certain types of tumors in the past, which the study doctors think could come back
  • +3 more criteria

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (263)

Research Site

Mobile, Alabama, 36604, United States

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Springdale, Arkansas, 72762, United States

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Harbor City, California, 90710, United States

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Solvang, California, 93463, United States

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Lone Tree, Colorado, 80124, United States

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Fort Myers, Florida, 33901-8101, United States

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Jacksonville, Florida, 32256, United States

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West Palm Beach, Florida, 33401, United States

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Indianapolis, Indiana, 46256, United States

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Baton Rouge, Louisiana, 70809, United States

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Silver Spring, Maryland, 20904, United States

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Boston, Massachusetts, 02114, United States

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Detroit, Michigan, 48202, United States

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Hattiesburg, Mississippi, 39401, United States

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Omaha, Nebraska, 68130, United States

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Cincinnati, Ohio, 45219, United States

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Cincinnati, Ohio, 45267, United States

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Portland, Oregon, 97239, United States

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West Columbia, South Carolina, 29169, United States

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Sioux Falls, South Dakota, 57105, United States

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Chattanooga, Tennessee, 37404, United States

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Nashville, Tennessee, 37203, United States

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Austin, Texas, 78731, United States

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Houston, Texas, 77030, United States

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Houston, Texas, 77090, United States

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Tyler, Texas, 75702, United States

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Fairfax, Virginia, 22031, United States

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Kennewick, Washington, 99336, United States

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Renton, Washington, 98055, United States

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Morgantown, West Virginia, 26505, United States

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Feldkirch, 6807, Austria

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Salzburg, 5020, Austria

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Vienna, 1130, Austria

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Anderlecht, 1070, Belgium

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Edegem, 2650, Belgium

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Ghent, 9000, Belgium

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Leuven, 3000, Belgium

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Liège, 4000, Belgium

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Namur, 5000, Belgium

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Sint-Niklaas, 9100, Belgium

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Plovdiv, 4000, Bulgaria

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Plovdiv, 4109, Bulgaria

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Shumen, 9700, Bulgaria

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Sofia, 1330, Bulgaria

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Sofia, 1431, Bulgaria

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Sofia, 1527, Bulgaria

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Edmonton, Alberta, T6G 1Z2, Canada

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Vancouver, British Columbia, V5Z 1H7, Canada

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Kitchener, Ontario, N2G 1G3, Canada

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London, Ontario, N6A 5W9, Canada

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Toronto, Ontario, M5G 2M9, Canada

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Montreal, H3T 1E2, Canada

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Concepción, 4070196, Chile

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La Serena, 1720430, Chile

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Santiago, 7630370, Chile

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Santiago, 8241479, Chile

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Baoding, 071000, China

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Beijing, 100039, China

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Beijing, 100142, China

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Beijing, China

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Bengbu, 233060, China

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Changchun, 130000, China

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Changchun, 130021, China

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Changsha, 410013, China

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Chengdu, 610042, China

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Chongqing, 400042, China

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Dalian, 116011, China

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Guangzhou, 510060, China

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Guangzhou, 510100, China

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Guiyang, 550004, China

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Haikou, 570311, China

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Hangzhou, 310020, China

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Hangzhou, 310022, China

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Hefei, 230031, China

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Jinan, 250117, China

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Lanzhou, 730000, China

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Linyi, 276000, China

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Nanchang, 330009, China

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Nanjing, 210008, China

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Shanghai, 200025, China

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Shanghai, 200032, China

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Shenyang, 110001, China

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Tianjin, 300060, China

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Wuhan, 430000, China

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Wuhan, 430022, China

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Xi'an, 710061, China

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Zhengzhou, 450008, China

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Hořovice, 268 01, Czechia

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Hradec Králové, 500 05, Czechia

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Nový Jičín, 741 01, Czechia

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Prague, 100 34, Czechia

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Prague, 140 00, Czechia

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Prague, 150 06, Czechia

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Besançon, 25030, France

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Bordeaux, 33030, France

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Brest, 29609, France

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Caen, 14076, France

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Dijon, 21079, France

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Le Mans, 72000, France

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Lille, 59000, France

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Montpellier, 34070, France

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Pierre-Bénite, 69495, France

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Plerin SUR MER, 22190, France

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Saint-Cloud, 92210, France

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Vandœuvre-lès-Nancy, 54000, France

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Villejuif, 94805, France

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Berlin, 13125, Germany

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Dessau-RoBlau, 06847, Germany

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Essen, 45136, Germany

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Freiburg im Breisgau, 79110, Germany

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Mönchengladbach, 41061, Germany

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München, 81675, Germany

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Münster, 48145, Germany

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Regensburg, 93053, Germany

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Velbert, 42551, Germany

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Budapest, 1062, Hungary

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Budapest, 1088, Hungary

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Budapest, 1122, Hungary

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Győr, 9024, Hungary

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Miskolc, 3526, Hungary

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Nyíregyháza, 4400, Hungary

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Szekszárd, 7100, Hungary

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Zalaegerszeg, 8900, Hungary

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Ahmedabad, 380060, India

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Calicut, 673601, India

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Delhi, 110085, India

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Faridabad, 121001, India

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Gūrgaon, 122001, India

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Karamsad, 388325, India

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Kolkata, 700160, India

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Madurai, 625107, India

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Nagpur, 440001, India

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Nashik, 422009, India

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Nashik, 422011, India

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New Delhi, 11029, India

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Bergamo, 24127, Italy

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Florence, 50139, Italy

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Milan, 20141, Italy

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Modena, 41124, Italy

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Napoli, 80131, Italy

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Novara, 28100, Italy

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Padua, 35128, Italy

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Parma, 43100, Italy

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Prato, 59100, Italy

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Roma, 00168, Italy

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Roma, 161, Italy

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Rozzano, 20089, Italy

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Chiba, 260-8717, Japan

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Chūōku, 104-0045, Japan

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Chūōku, 862-8655, Japan

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Hidaka-shi, 350-1298, Japan

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Hirakata-shi, 573-1191, Japan

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Isehara-shi, 259-1193, Japan

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Kitaadachi-gun, 362-0806, Japan

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Kōtoku, 135-8550, Japan

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Kumamoto, 860-8556, Japan

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Kurashiki Shi, 701 0192, Japan

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Kurume-shi, 830-0013, Japan

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Kyoto, 606-8507, Japan

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Nagoya, 464-8681, Japan

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Nagoya, 467-8602, Japan

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Nishinomiya-shi, 663-8501, Japan

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Osaka, 540-0006, Japan

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Osaka, 541-8567, Japan

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Ota-shi, 373-8550, Japan

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Sapporo, 003-0804, Japan

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Sendai, 980-8574, Japan

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Shimotsuke-shi, 329-0498, Japan

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Shinagawa-ku, 142-8666, Japan

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Shinjuku-ku, 162-8655, Japan

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Suita-shi, 565-0871, Japan

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Takasaki-shi, 370-0829, Japan

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Tsu, 514-8507, Japan

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Tsukuba, 305-8576, Japan

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Yokohama, 241-8515, Japan

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George Town, 10450, Malaysia

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Johor Bahru, 81100, Malaysia

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Kuala Lumpur, 50586, Malaysia

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Kuala Lumpur, 59100, Malaysia

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Kuala Selangor, 62250, Malaysia

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Kuching, 93586, Malaysia

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Del. Cuauhtemoc, 06700, Mexico

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Estado de México, 50080, Mexico

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La Paz, 23040, Mexico

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Mexico City, 0 3100, Mexico

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Monterrey, 64710, Mexico

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Puebla City, 72424, Mexico

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Drammen, 3004, Norway

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Oslo, N-0379, Norway

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Gdynia, 81-519, Poland

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Konin, 62-500, Poland

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Koszalin, 75-581, Poland

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Lodz, 90-302, Poland

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Lublin, 20-090, Poland

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Olsztyn, 10-513, Poland

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Poznan, 60-192, Poland

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Braga, 4710, Portugal

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Guimarães, 4835-044, Portugal

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Lisbon, 1400-038, Portugal

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Lisbon, 1500-650, Portugal

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Lisbon, 1998-018, Portugal

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Loures, 2674-514, Portugal

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Porto, 4099-001, Portugal

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Porto, 4200-319, Portugal

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Vila Nova de Gaia, 4434-502, Portugal

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Kaluga, 248007, Russia

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Kislino Village, Ryshkovsky Ru, 305524, Russia

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Moscow, 111123, Russia

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Moscow, 115478, Russia

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Moscow, 117997, Russia

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Moscow, 121467, Russia

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Saint Petersburg, 190103, Russia

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Saint Petersburg, 195067, Russia

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Saint Petersburg, 196603, Russia

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Saint Petersburg, 197758, Russia

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Banská Bystrica, 974 01, Slovakia

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Bratislava, 81250, Slovakia

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Bratislava, 833 01, Slovakia

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Prešov, 081 81, Slovakia

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Trenčín, 91171, Slovakia

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Busan, 49201, South Korea

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Daegu, 41404, South Korea

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Goyang-si, 10408, South Korea

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Seoul, 03080, South Korea

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Seoul, 03722, South Korea

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Seoul, 05505, South Korea

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Seoul, 06273, South Korea

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Seoul, 06351, South Korea

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Barcelona, 08908, Spain

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Barcelona, 8035, Spain

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Jaén, 23007, Spain

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Lleida, 25198, Spain

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Madrid, 28040, Spain

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Madrid, 28046, Spain

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Málaga, 29010, Spain

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Pamplona, 31008, Spain

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Santander, 39008, Spain

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Seville, 41013, Spain

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Valencia, 46015, Spain

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Liestal, CH- 4410, Switzerland

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Zurich, 8008, Switzerland

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Kaohsiung City, 82445, Taiwan

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Kaohsiung City, Taiwan

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Taichung, 40443, Taiwan

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Tainan, 70403, Taiwan

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Taipei, 10048, Taiwan

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Taipei, 104, Taiwan

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Taipei, 110, Taiwan

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Taipei, 235, Taiwan

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Taoyuan District, 333, Taiwan

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Adana, 01120, Turkey (Türkiye)

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Ankara, 06010, Turkey (Türkiye)

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Ankara, 06230, Turkey (Türkiye)

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Ankara, 06340, Turkey (Türkiye)

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Ankara, 6100, Turkey (Türkiye)

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Izmir, 35100, Turkey (Türkiye)

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Izmir, 35620, Turkey (Türkiye)

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Kayseri, 38039, Turkey (Türkiye)

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Cambridge, CB2 2QQ, United Kingdom

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Colchester, CO4 5JL, United Kingdom

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Leeds, LS9 7TF, United Kingdom

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Nottingham, NG5 1PB, United Kingdom

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Surrey, GU2 7XX, United Kingdom

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Related Links

MeSH Terms

Conditions

Neoplasm MetastasisBreast NeoplasmsNeoplasms by SiteNeoplasmsBreast DiseasesSkin Diseases

Interventions

AZD9833AnastrozolepalbociclibGonadotropin-Releasing Hormone

Condition Hierarchy (Ancestors)

Neoplastic ProcessesPathologic ProcessesPathological Conditions, Signs and SymptomsSkin and Connective Tissue Diseases

Intervention Hierarchy (Ancestors)

NitrilesOrganic ChemicalsTriazolesAzolesHeterocyclic Compounds, 1-RingHeterocyclic CompoundsPituitary Hormone-Releasing HormonesHypothalamic HormonesPeptide HormonesHormonesHormones, Hormone Substitutes, and Hormone AntagonistsNeuropeptidesPeptidesAmino Acids, Peptides, and ProteinsOligopeptidesNerve Tissue ProteinsProteins

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
TRIPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

December 23, 2020

First Posted

January 15, 2021

Study Start

January 28, 2021

Primary Completion (Estimated)

August 24, 2026

Study Completion (Estimated)

February 1, 2029

Last Updated

October 14, 2025

Record last verified: 2025-10

Data Sharing

IPD Sharing
Will share

Qualified researchers can request access to anonymized individual patient-level data from AstraZeneca group of companies sponsored clinical trials via the request portal. All request will be evaluated as per the AZ disclosure commitment: https://astrazenecagrouptrials.pharmacm.com/ST/Submission/Disclosure. Yes, indicates that AZ are accepting requests for IPD, but this does not mean all requests will be shared.

Shared Documents
STUDY PROTOCOL, SAP
Time Frame
AstraZeneca will meet or exceed data availability as per the commitments made to the EFPIA Pharma Data Sharing Principles. For details of our timelines, please rerefer to our disclosure commitment at https://astrazenecagrouptrials.pharmacm.com/ST/Submission/Disclosure.
Access Criteria
When a request has been approved AstraZeneca will provide access to the deidentified individual patient-level data in an approved sponsored tool. Signed Data Sharing Agreement (non-negotiable contract for data accessors) must be in place before accessing requested information. Additionally, all users will need to accept the terms and conditions of the SAS MSE to gain access. For additional details, please review the Disclosure Statements at https://astrazenecagrouptrials.pharmacm.com/ST/Submission/Disclosure.
More information

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