NCT04616248

Brief Summary

This phase I trial evaluates the safety and effectiveness of in situ immunomodulation with CDX-301, radiotherapy, CDX-1140 and Poly-ICLC (Cohort A) and these with intravenous (IV) pembrolizumab and subcutaneous (SC) tocilizumab (Cohort B) in treating patients with unresectable and measurable metastatic melanoma, cutaneous squamous cell carcinoma (SCC), basal cell carcinoma (BCC), Merkel cell carcinoma, high-grade bone and soft tissue sarcoma or HER2/neu(-) breast cancer. CDX-301 may induce cross-presenting dendritic cells, master regulators in the immune system. Radiation therapy uses high energy to kill tumor cells and release antigens that may be picked up, processed and presented by cross-presenting dendritic cells. CDX-1140 and Poly-ICLC may activate tumor antigen-loaded,cross-presenting dendritic cells, and generate tumor-specific T lymphocytes, a type of immune cells, that can search out and attack cancers. Giving immune modulators and radiation therapy may stimulate tumor cell death and activate the immune system.

Trial Health

75
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
14

participants targeted

Target at below P25 for phase_1

Timeline
21mo left

Started Jan 2023

Longer than P75 for phase_1

Geographic Reach
1 country

2 active sites

Status
active not recruiting

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Progress67%
Jan 2023Jan 2028

First Submitted

Initial submission to the registry

October 26, 2020

Completed
9 days until next milestone

First Posted

Study publicly available on registry

November 4, 2020

Completed
2.2 years until next milestone

Study Start

First participant enrolled

January 9, 2023

Completed
4 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

January 9, 2027

Expected
1 year until next milestone

Study Completion

Last participant's last visit for all outcomes

January 9, 2028

Last Updated

January 7, 2026

Status Verified

January 1, 2026

Enrollment Period

4 years

First QC Date

October 26, 2020

Last Update Submit

January 6, 2026

Conditions

Keywords

High-grade bone sarcomaHigh-grade soft tissue sarcomaBasal Cell Carcinoma

Outcome Measures

Primary Outcomes (2)

  • Incidence of adverse events

    Up to 30 days

  • Maximum tolerated dose or maximum administered dose

    The dose limiting toxicity rate will be estimated by cohort and dose-level (if appropriate) using 90% confidence intervals obtained by Jeffrey's prior method.

    Up to 30 days

Secondary Outcomes (4)

  • Changes in Immune signatures in the tumor microenvironment

    Baseline up to 2 years

  • Changes in the levels of infiltrating CD4+ and CD8+ T cells

    Baseline up to 2 years

  • Changes in the levels of infiltrating myeloid cell subsets

    Baseline up to 2 years

  • Changes in the levels of PD-L1 expression

    Baseline up to 2 years

Other Outcomes (4)

  • Overall response rate (ORR)

    Up to 2 years

  • Overall survival

    From treatment initiation until death due to any cause (event) or last follow-up, assessed up to 2 years

  • Progression free survival

    From treatment initiation until disease progression, death due to disease (events), or last follow-up, assessed at 1 year

  • +1 more other outcomes

Study Arms (2)

Cohort A (immunomodulators, radiation therapy)

EXPERIMENTAL

Patients receive recombinant Flt3 ligand IT on days 1-5 and undergo radiation therapy on day 8 or 9. Patients also receive agonistic anti-CD40 monoclonal antibody CDX-1140 IT and Poly-ICLC IT on day 9 or 10. Treatment repeats every 21 days for 4 cycles in the absence of disease progression or unacceptable toxicity.

Biological: Anti-CD40 Agonist Monoclonal Antibody CDX-1140Drug: Poly ICLCRadiation: Radiation TherapyBiological: Recombinant Flt3 Ligand

Cohort B (immunomodulators, radiation therapy)

EXPERIMENTAL

Patients receive recombinant Flt3 ligand IT on days 1-5 and also receive pembrolizumab (IV), tocilizumab (SC) as well as undergo radiation therapy on day 8 or 9. Patients also receive agonistic anti-CD40 monoclonal antibody IT and IV over 90 minutes and Poly-ICLC IT on day 9 or 10. Treatment repeats every 21 days for 4 cycles in the absence of disease progression or unacceptable toxicity.

Biological: Anti-CD40 Agonist Monoclonal Antibody CDX-1140Drug: Poly ICLCRadiation: Radiation TherapyBiological: Recombinant Flt3 LigandDrug: PembrolizumabDrug: Tocilizumab

Interventions

Given IT

Also known as: Agonist CD40 Antibody CDX-1140, Anti-CD40 Agonistic Monoclonal Antibody CDX-1140, CDX 1140, CDX-1140
Cohort A (immunomodulators, radiation therapy)Cohort B (immunomodulators, radiation therapy)

Given IT

Also known as: Hiltonol, Poly I:Poly C with Poly-L-Lysine Stabilizer, poly-ICLC, PolyI:PolyC with Poly-L-Lysine Stabilizer, Polyinosinic-Polycytidylic Acid Stabilized with Polylysine and Carboxymethylcellulose, Polyriboinosinic-Polyribocytidylic Acid-Polylysine Carboxymethylcellulose, Stabilized Polyriboinosinic/Polyribocytidylic Acid
Cohort A (immunomodulators, radiation therapy)Cohort B (immunomodulators, radiation therapy)

Undergo radiation therapy

Also known as: Cancer Radiotherapy, Irradiate, Irradiated, Irradiation, Radiation, Radiation Therapy, NOS, Radiotherapeutics, Radiotherapy, RT, Therapy, Radiation
Cohort A (immunomodulators, radiation therapy)Cohort B (immunomodulators, radiation therapy)

Given IT

Also known as: CDX-301, FLT 3 Ligand, FLT3 Ligand, Flt3-Ligand, Flt3L, Mobist, Mobista, rhuFlt3L
Cohort A (immunomodulators, radiation therapy)Cohort B (immunomodulators, radiation therapy)

Given IV

Also known as: Keytruda
Cohort B (immunomodulators, radiation therapy)

Given SC

Also known as: Actemra
Cohort B (immunomodulators, radiation therapy)

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Have clinically or pathologically confirmed diagnosis of unresectable and metastatic melanoma, cutaneous SCC, basal cell carcinoma, Merkel cell carcinoma, high-grade bone and soft tissue sarcoma or HER2/neu (-) breast cancer with no curative treatment options.
  • The unresectable disease to be irradiated and injected with medications must be located in breast, dermal, subcutaneous, or soft tissue, or lymph nodes with the longest axis of the tumor 2-7 centimeters, and should be considered safe for injection by the investigator.
  • The metastatic disease must be measured per irRECIST criteria.
  • Patient must have lesion that can be biopsied and is willing to undergo the procedure as part of the protocol.
  • Have an Eastern Cooperative Oncology Group (ECOG) performance status of =\< 1.
  • Participants of child-bearing potential and men must agree to use adequate contraceptive methods (e.g., hormonal or barrier method of birth control; abstinence) prior to study entry. Should a woman become pregnant or suspect she is pregnant while she or her partner is participating in this study, she should inform her treating physician immediately.
  • For patients with history of radiotherapy to the same location that will be treated on study, he/she will be eligible only if the prior radiation dose was under or equal to 68 Gy total and delivered more than 6 months prior to planned re-treatment. (The cumulative dose received to the irradiated area will be no more than 87 Gy total, including a maximum of 68 Gy allowed from prior treatment course.)
  • Patient requires the use of radiation therapy to the target lesion of palliation of symptoms and/or achieving local control as part of standard of care as deemed appropriate by treating radiation oncologist.
  • Patients must agree to radiation to the tumor.
  • Any line of therapy allowed, radiologically or clinically confirmed progression on prior therapy
  • Must have adequate organ and marrow function present as defined below:
  • Platelets \>= 100,000/uL
  • Hemoglobin \>= 8.0 g/dL
  • Absolute neutrophil count (ANC) \>= 1500/uL
  • Total bilirubin =\< 1.5 X institutional upper limit of normal (ULN)
  • +7 more criteria

You may not qualify if:

  • Patients currently treated with systemic immunosuppressive agents, including steroids, are ineligible until 3 weeks after removal from immunosuppressive treatment. (inhaled steroids are allowed)
  • Patients with HER2+ breast cancer
  • Concurrent use of targeted therapy including CDK4/6, mTOR, PIK3CA, PARP, BRAF, MEK, hedgehog inhibitors or chemotherapy (endocrine therapy is allowed).
  • Targeted therapy including CDK4/6, mTOR, PIK3CA, PARP, BRAF, MEK, hedgehog inhibitors, chemotherapy, or immunotherapy within 2 weeks prior to first dosing of study agent. (endocrine therapy is allowed).
  • Patients with active or history of autoimmune disease or history of transplantation except for the patients with Graves' disease with ablative therapy of total thyroidectomy.
  • Patients with history of (non-infectious) pneumonitis/interstitial lung disease, including grade 1 pneumonitis (asymptomatic; clinical or diagnostic observations only; intervention not indicated).
  • Patients with prior history of acute myeloid leukemia (AML) or known FLT3 aberrations
  • Pregnant or nursing female participants.
  • Unwilling or unable to follow protocol requirements.
  • Cardiac risk factors including:
  • Patients experiencing cardiac event(s) (acute coronary syndrome, myocardial infarction, or ischemia) within 3 months of signing consent.
  • Patients with a New York Heart Association classification of III or IV.
  • Patients with uveal melanoma.
  • Patients with uncontrolled diseases other than cancer may be excluded if after consultation with PI and research team it is decided it might affect the treatment efficacy or toxicity.
  • Evidence of current drug or alcohol abuse or psychiatric impairment, which in the investigator's opinion will prevent completion of the protocol therapy or follow-up. Specific testing is not required, however may be done as clinically indicated.
  • +12 more criteria

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (2)

Los Angeles General Medical Center

Los Angeles, California, 90033, United States

Location

USC/Norris Comprehensive Cancer Center

Los Angeles, California, 90033, United States

Location

MeSH Terms

Conditions

Breast NeoplasmsMelanomaCarcinoma, Merkel CellSarcomaBone NeoplasmsOsteosarcomaCarcinoma, Basal Cell

Interventions

poly ICLCRadiotherapyRadiationflt3 ligand proteinpembrolizumabtocilizumab

Condition Hierarchy (Ancestors)

Neoplasms by SiteNeoplasmsBreast DiseasesSkin DiseasesSkin and Connective Tissue DiseasesNeuroendocrine TumorsNeuroectodermal TumorsNeoplasms, Germ Cell and EmbryonalNeoplasms by Histologic TypeNeoplasms, Nerve TissueNevi and MelanomasSkin NeoplasmsPolyomavirus InfectionsDNA Virus InfectionsVirus DiseasesInfectionsTumor Virus InfectionsCarcinoma, NeuroendocrineAdenocarcinomaCarcinomaNeoplasms, Glandular and EpithelialNeoplasms, Connective and Soft TissueBone DiseasesMusculoskeletal DiseasesNeoplasms, Bone TissueNeoplasms, Connective TissueNeoplasms, Basal Cell

Intervention Hierarchy (Ancestors)

TherapeuticsPhysical Phenomena

Study Officials

  • Fumito Ito, MD

    University of Southern California

    PRINCIPAL INVESTIGATOR

Study Design

Study Type
interventional
Phase
phase 1
Allocation
NON RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
SEQUENTIAL
Sponsor Type
OTHER
Responsible Party
SPONSOR

Study Record Dates

First Submitted

October 26, 2020

First Posted

November 4, 2020

Study Start

January 9, 2023

Primary Completion (Estimated)

January 9, 2027

Study Completion (Estimated)

January 9, 2028

Last Updated

January 7, 2026

Record last verified: 2026-01

Locations