NCT04213794

Brief Summary

This early phase I trial studies how well heated intra-peritoneal chemotherapy with doxorubicin and cisplatin work for the treatment of abdominal or pelvic tumors that can be removed by surgery (resectable), does not respond to treatment (refractory), or has come back (recurrent). Heated intra-peritoneal chemotherapy is a procedure performed in combination with abdominal surgery for cancer that has spread to the abdomen. It involves the infusion of a heated chemotherapy solution that circulates into the abdominal cavity. Chemotherapy drugs, such as doxorubicin and cisplatin, work in different ways to stop the growth of tumor cells, either by killing the cells, by stopping them from dividing, or by stopping them from spreading. Heating a chemotherapy solution and infusing it directly into the abdomen may kill more cells.

Trial Health

57
Monitor

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
2

participants targeted

Target at below P25 for early_phase_1

Timeline
Completed

Started Nov 2019

Longer than P75 for early_phase_1

Geographic Reach
1 country

1 active site

Status
terminated

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

November 8, 2019

Completed
2 months until next milestone

First Submitted

Initial submission to the registry

December 27, 2019

Completed
3 days until next milestone

First Posted

Study publicly available on registry

December 30, 2019

Completed
4.2 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

March 4, 2024

Completed
7 months until next milestone

Study Completion

Last participant's last visit for all outcomes

October 3, 2024

Completed
Last Updated

February 20, 2025

Status Verified

February 1, 2025

Enrollment Period

4.3 years

First QC Date

December 27, 2019

Last Update Submit

February 18, 2025

Conditions

Outcome Measures

Primary Outcomes (1)

  • Incidence of adverse events of cytoreductive surgery (CRS) with heated intra-peritoneal chemotherapy (HIPEC) in this patient population

    To assess the feasibility of heated intra-peritoneal chemotherapy (HIPEC) with doxorubicin (DOXO) and cisplatin (CDDP) after surgical resection of pediatric pelvic and abdominal tumors.

    Up to 6 months

Secondary Outcomes (9)

  • Overall survival (OS)

    From the time of diagnosis of cancer up, assessed to 5 years

  • Disease-free survival (DFS)

    From the time of diagnosis of cancer up to 5 years

  • Peritoneal-free recurrence

    From the time of diagnosis of cancer up to 5 years

  • Incidence of morbidity

    30, 60, and, 90 days post-HIPEC procedure

  • Incidence of mortality

    30 days post-HIPEC procedure

  • +4 more secondary outcomes

Study Arms (1)

Treatment (cytoreduction, HIPEC)

EXPERIMENTAL

Patients undergo cytoreduction. Patients also undergo HIPEC over 60 minutes consisting of doxorubicin and cisplatin. Patients then receive sodium thiosulfate IV over 12 hours. Patients also undergo CT scan, MRI or PET/CT scan and blood sample collection throughout study.

Drug: CisplatinProcedure: Cytoreductive SurgeryDrug: DoxorubicinDrug: Hyperthermic Intraperitoneal ChemotherapyDrug: Sodium ThiosulfateProcedure: Computed TomographyProcedure: Magnetic Resonance ImagingProcedure: Positron Emission TomographyProcedure: Biospecimen Collection

Interventions

Undergo HIPEC with doxorubicin and cisplatin

Also known as: Abiplatin, Blastolem, Briplatin, CDDP, Cis-diammine-dichloroplatinum, Cis-diamminedichloridoplatinum, Cis-diamminedichloro Platinum (II), Cis-diamminedichloroplatinum, Cis-dichloroammine Platinum (II), Cis-platinous Diamine Dichloride, Cis-platinum, Cis-platinum II, Cis-platinum II Diamine Dichloride, Cismaplat, Cisplatina, Cisplatinum, Cisplatyl, Citoplatino, Citosin, Cysplatyna, DDP, Lederplatin, Metaplatin, Neoplatin, Peyrone's Chloride, Peyrone's Salt, Placis, Plastistil, Platamine, Platiblastin, Platiblastin-S, Platinex, Platinol, Platinol- AQ, Platinol-AQ, Platinol-AQ VHA Plus, Platinoxan, Platinum, Platinum Diamminodichloride, Platiran, Platistin, Platosin
Treatment (cytoreduction, HIPEC)

Undergo cytoreduction

Also known as: Cytoreduction
Treatment (cytoreduction, HIPEC)

Undergo HIPEC with doxorubicin and cisplatin

Also known as: Adriablastin, Hydroxydaunomycin, Hydroxyl Daunorubicin, Hydroxyldaunorubicin
Treatment (cytoreduction, HIPEC)

Undergo HIPEC with doxorubicin and cisplatin

Also known as: HIPEC
Treatment (cytoreduction, HIPEC)

Given IV

Also known as: Cyanide Antidote Package, Disodium Thiosulfate, S-Hydril, Sodium Hyposulfate, Sodium Thiosulfate Pentahydrate, Sodium Thiosulphate, Sodothiol, Thiosulfate, Sodium, Pentahydrate, Thiosulfuric Acid Disodium Salt
Treatment (cytoreduction, HIPEC)

Undergo CT scan

Also known as: CAT, CAT Scan, Computed Axial Tomography, computerized axial tomography, Computed Tomography (CT), CT Scan
Treatment (cytoreduction, HIPEC)

Undergo MRI

Also known as: Magnetic Resonance Imaging Scan, Magnetic Resonance / Nuclear Magnetic Resonance, MR, MRI, MRI Scan, Nuclear Magnetic Resonance Imaging, NMRI, Structural MRI, sMRI
Treatment (cytoreduction, HIPEC)

Undergo PET/CT

Also known as: Medical Imaging, PET, PET Scan, positron emission tomography scan, Positron-Emission Tomography, proton magnetic resonance spectroscopic imaging, PT
Treatment (cytoreduction, HIPEC)

Undergo blood sample collection

Also known as: Biological Sample Collection, Biospecimen Collected, Specimen Collection
Treatment (cytoreduction, HIPEC)

Eligibility Criteria

Age1 Year - 25 Years
Sexall
Healthy VolunteersNo
Age GroupsChild (0-17), Adult (18-64)

You may qualify if:

  • Patients must have resectable, primary refractory or recurrent intra-abdominal or pelvic tumors based on imaging studies with measurable disease (\>= 1 cm in 2 perpendicular planes), or primary tumor with peritoneal implants in whom no known other curative treatment exists, and/or patients not on up-front clinical trial
  • Evidence of macroscopic or microscopic intra-peritoneal seeding (separate from the primary tumor) identified at the time of exploratory surgery with or without primary tumor resection
  • Peritoneal cancer index (PCI) =\< 20 and surgeons deem high likelihood of complete residual tumor stage R0 (R0) resection
  • No evidence of distant metastases at the time of enrollment
  • Histologies to be considered include: rhabdomyosarcoma, liposarcoma, sarcoma (other), ovarian cancer, fallopian tube cancer, gastric cancer, colon cancer, rectal cancer, mesothelioma, and desmoplastic small-round-cell tumor
  • Patients must be 1-25 years of age at the time of entry into the study
  • Patients may be included in the study independent of the regimen of previous surgical, radiation, or chemotherapy treatments administered. Given the increased risk of entero-cutaneous fistulae observed in patients treated with HIPEC AFTER radiation therapy, patients will be assessed for risk by radiation oncology
  • Karnofsky / Lansky performance score of \>= 40 or Eastern Cooperative Oncology Group (ECOG) performance score of 3 or less
  • Platelet count \>= 50,000 (independent of transfusion) (performed no later than 14 days before surgery)
  • Prothrombin and partial thromboplastin times =\< 1.2 X normal (performed no later than 14 days before surgery)
  • Total bilirubin =\< 2 X normal (performed no later than 14 days before surgery)
  • Serum glutamic-oxaloacetic transaminase (SGOT) =\< 2 X normal (performed no later than 14 days before surgery)
  • Serum glutamate pyruvate transaminase (SGPT) =\< 2 X normal (performed no later than 14 days before surgery)
  • Lactate dehydrogenase (LDH) =\< 2 X normal (performed no later than 14 days before surgery)
  • Alkaline phosphatase =\< 2 X normal (performed no later than 14 days before surgery)
  • +6 more criteria

You may not qualify if:

  • Females who are pregnant or breast-feeding during the study period will be excluded
  • Distant metastatic disease not limited to peritoneum:
  • Solid organ metastases (liver, central nervous system, lung)
  • Known bone marrow involvement
  • No critical cumulative dose of previous chemotherapy (total anthracycline dose not \>= 435 mg / m\^2)
  • Prior HIPEC within 3 months
  • Patients with an active infection requiring treatment or having an unexplained febrile illness (Tmax \> 99.5 Fahrenheit \[F\]), patients with known immune deficiency disorder or known human immunodeficiency virus infection
  • Patients must not have any systemic illness which precludes them from being an operative candidate as determined by anesthesia preoperative evaluation. This includes but is not limited to, sepsis, liver failure, renal failure, cardiovascular failure, pulmonary failure
  • Subjects deemed unable to comply with study and/or follow-up procedures
  • Subjects with a known hypersensitivity to protocol systemic chemotherapy that was life-threatening, required hospitalization or prolongation of existing hospitalization, or resulted in persistent or significant disability or incapacitation

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (1)

Mayo Clinic in Rochester

Rochester, Minnesota, 55905, United States

Location

Related Links

MeSH Terms

Conditions

Pelvic NeoplasmsColonic NeoplasmsDesmoplastic Small Round Cell TumorFallopian Tube NeoplasmsStomach NeoplasmsLiposarcomaMesothelioma, MalignantOvarian NeoplasmsRectal NeoplasmsRhabdomyosarcomaSarcoma

Interventions

Cisplatin1,2-diaminocyclohexaneplatinum II citratePlatinumCytoreduction Surgical ProceduresDoxorubicinHyperthermic Intraperitoneal Chemotherapysodium thiosulfateMagnetic Resonance SpectroscopyX-RaysSpecimen Handling

Condition Hierarchy (Ancestors)

Neoplasms by SiteNeoplasmsColorectal NeoplasmsIntestinal NeoplasmsGastrointestinal NeoplasmsDigestive System NeoplasmsDigestive System DiseasesGastrointestinal DiseasesColonic DiseasesIntestinal DiseasesNeoplasms, Connective and Soft TissueNeoplasms by Histologic TypeGenital Neoplasms, FemaleUrogenital NeoplasmsFallopian Tube DiseasesAdnexal DiseasesGenital Diseases, FemaleFemale Urogenital DiseasesFemale Urogenital Diseases and Pregnancy ComplicationsUrogenital DiseasesGenital DiseasesStomach DiseasesNeoplasms, Adipose TissueMesotheliomaAdenomaNeoplasms, Glandular and EpithelialNeoplasms, MesothelialLung NeoplasmsRespiratory Tract NeoplasmsThoracic NeoplasmsPleural NeoplasmsLung DiseasesRespiratory Tract DiseasesEndocrine Gland NeoplasmsOvarian DiseasesEndocrine System DiseasesGonadal DisordersRectal DiseasesMyosarcomaNeoplasms, Muscle Tissue

Intervention Hierarchy (Ancestors)

Chlorine CompoundsInorganic ChemicalsNitrogen CompoundsPlatinum CompoundsMetals, HeavyElementsTransition ElementsMetalsSurgical Procedures, OperativeDaunorubicinAnthracyclinesNaphthacenesPolycyclic Aromatic HydrocarbonsHydrocarbons, AromaticHydrocarbons, CyclicHydrocarbonsOrganic ChemicalsPolycyclic CompoundsAminoglycosidesGlycosidesCarbohydratesChemotherapy, AdjuvantCombined Modality TherapyTherapeuticsDrug TherapyHyperthermia, InducedSpectrum AnalysisChemistry Techniques, AnalyticalInvestigative TechniquesElectromagnetic RadiationElectromagnetic PhenomenaMagnetic PhenomenaPhysical PhenomenaRadiationRadiation, IonizingClinical Laboratory TechniquesDiagnostic Techniques and ProceduresDiagnosis

Study Officials

  • Patricio C. Gargollo, M.D.

    Mayo Clinic

    PRINCIPAL INVESTIGATOR

Study Design

Study Type
interventional
Phase
early phase 1
Allocation
NA
Masking
NONE
Purpose
TREATMENT
Intervention Model
SINGLE GROUP
Sponsor Type
OTHER
Responsible Party
SPONSOR

Study Record Dates

First Submitted

December 27, 2019

First Posted

December 30, 2019

Study Start

November 8, 2019

Primary Completion

March 4, 2024

Study Completion

October 3, 2024

Last Updated

February 20, 2025

Record last verified: 2025-02

Locations