NCT03594747

Brief Summary

An open-label, randomized, multicenter Phase 3 study designed to compare the efficacy and safety of tislelizumab combined with chemotherapy versus chemotherapy only as first-line treatment in advanced squamous non-small cell lung cancer (NSCLC).

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
360

participants targeted

Target at P25-P50 for phase_3 nonsmall-cell-lung-cancer

Timeline
Completed

Started Jul 2018

Geographic Reach
1 country

43 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

July 3, 2018

Completed
17 days until next milestone

First Posted

Study publicly available on registry

July 20, 2018

Completed
10 days until next milestone

Study Start

First participant enrolled

July 30, 2018

Completed
2.2 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

September 30, 2020

Completed
2.6 years until next milestone

Study Completion

Last participant's last visit for all outcomes

April 28, 2023

Completed
6 months until next milestone

Results Posted

Study results publicly available

October 17, 2023

Completed
Last Updated

October 26, 2024

Status Verified

October 1, 2024

Enrollment Period

2.2 years

First QC Date

July 3, 2018

Results QC Date

September 19, 2023

Last Update Submit

October 23, 2024

Conditions

Outcome Measures

Primary Outcomes (2)

  • Progression Free Survival (PFS) by Independent Review Committee (IRC) Assessment as of Data Cut-off Date of 06DEC2019

    PFS is defined as the time from randomization until first documentation of disease progression as assessed by the IRC per Response Evaluation Criteria in Solid Tumors (RECIST) v1.1 or death from any cause, whichever occurs first

    Through primary analysis data cut-off date of 06DEC2019 (up to approximately 1 year and 4 months)

  • PFS by IRC Assessment as of Data Cut-off Date of 30SEP2020

    PFS is defined as the time from randomization until first documentation of disease progression as assessed by the IRC per RECIST v1.1 or death from any cause, whichever occurs first

    Through primary analysis data cut-off date of 30SEP2020 (up to approximately 2 years and 2 months)

Secondary Outcomes (10)

  • Overall Survival (OS)

    Through study completion data cut-off date of 28APR2023 (up to approximately 4 years and 9 months)

  • Objective Response Rate (ORR) by IRC Assessment

    Through study completion data cut-off date of 28APR2023 (up to approximately 4 years and 9 months)

  • ORR by Investigator Assessment

    Through study completion data cut-off date of 28APR2023 (up to approximately 4 years and 9 months)

  • Duration of Response (DOR) by IRC Assessment

    Through study completion data cut-off date of 28APR2023 (up to approximately 4 years and 9 months)

  • DOR by Investigator Assessment

    Through study completion data cut-off date of 28APR2023 (up to approximately 4 years and 9 months)

  • +5 more secondary outcomes

Study Arms (3)

Tislelizumab + Paclitaxel + Carboplatin

EXPERIMENTAL

Tislelizumab 200 milligrams (mg) plus paclitaxel 175 mg/m\^2 and carboplatin area under the plasma or serum concentration-time curve (AUC) 5 on Day 1 administered intravenously once every 3 weeks until unacceptable toxicity, withdrawal of consent, loss of clinical benefit, or disease progression; paclitaxel and carboplatin were administered for 4 to 6 cycles (each cycle is 21 days)

Drug: TislelizumabDrug: PaclitaxelDrug: Carboplatin

Tislelizumab + Nab-paclitaxel + Carboplatin

EXPERIMENTAL

Tislelizumab 200 mg on Day 1 plus Nab-paclitaxel 100 mg/m\^2 on Days 1, 8, and 15 and carboplatin AUC 5 on Day 1 administered intravenously once every 3 weeks until unacceptable toxicity, withdrawal of consent, loss of clinical benefit, or disease progression; Nab-paclitaxel and carboplatin were administered for 4 to 6 cycles (each cycle is 21 days)

Drug: TislelizumabDrug: Nab-paclitaxelDrug: Carboplatin

Paclitaxel + Carboplatin

ACTIVE COMPARATOR

Paclitaxel 175 mg/m\^2 and carboplatin AUC 5 on Day 1 administered intravenously once every 3 weeks for 4 to 6 cycles (each cycle is 21 days)

Drug: PaclitaxelDrug: Carboplatin

Interventions

Administered intravenously as described

Also known as: BGB-A317, Tevimbra
Tislelizumab + Nab-paclitaxel + CarboplatinTislelizumab + Paclitaxel + Carboplatin

Administered intravenously as described

Paclitaxel + CarboplatinTislelizumab + Paclitaxel + Carboplatin

Administered intravenously as described

Tislelizumab + Nab-paclitaxel + Carboplatin

Administered intravenously as described

Paclitaxel + CarboplatinTislelizumab + Nab-paclitaxel + CarboplatinTislelizumab + Paclitaxel + Carboplatin

Eligibility Criteria

Age18 Years - 75 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Age 18-75 years old, male or female, and signed informed consent form (ICF)
  • Advanced NSCLC diagnosed by pathological or clinical physicians
  • Eastern Cooperative Oncology Group (ECOG) performance status (PS) ≤ 1
  • Participants must have ≥ 1 measurable lesion as defined per Response Evaluation Criteria in Solid Tumors (RECIST) v1.1
  • Must be treatment-naive for locally advanced or metastatic squamous NSCLC
  • Life expectancy ≥ 12 weeks
  • Participants must have adequate organ function
  • Male/Female is willing to use a highly effective method of birth control

You may not qualify if:

  • Diagnosed with NSCLC but with epidermal growth factor receptors (EGFR)-sensitizing mutation or anaplastic lymphoma kinase (ALK) gene translocation
  • Received any approved systemic anticancer therapy
  • Received prior treatment with EGFR inhibitors or ALK inhibitors
  • Received prior therapies targeting programmed death 1 (PD-1) or programmed death ligand 1 (PD-L1)
  • With history of interstitial lung disease
  • Clinically significant pericardial effusion
  • Severe infections, active leptomeningeal disease or uncontrolled, untreated brain metastasis
  • Any major surgical procedure before randomization
  • Human immunodeficiency virus infection
  • Untreated hepatitis B virus (HBV)/hepatitis C virus (HCV)
  • Active autoimmune diseases or history of autoimmune diseases
  • History of allergic reactions to chemotherapy

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (43)

Anhui Provincial Hospital

Hefei, Anhui, 230000, China

Location

The First Affiliated Hospital of Anhui Medical University

Hefei, Anhui, 230000, China

Location

Cancer Hospital Chinese Academy of Medical Sciences

Beijing, Beijing Municipality, 100021, China

Location

Beijing Cancer Hospital

Beijing, Beijing Municipality, 100142, China

Location

Peking Union Medical College Hospital

Beijing, Beijing Municipality, 100730, China

Location

Chinese Pla General Hospital

Beijing, Beijing Municipality, 100853, China

Location

Beijing Chest Hospital, Capital Medical University

Beijing, Beijing Municipality, 101149, China

Location

The Second Affiliated Hospital of Chongqing Medical University

Chongqing, Chongqing Municipality, 400010, China

Location

Southwest Hospital

Chongqing, Chongqing Municipality, 400038, China

Location

Daping Hospital, Third Military Medical University

Chongqing, Chongqing Municipality, 400042, China

Location

Chongqing Three Gorges Central Hospital

Chongqing, Chongqing Municipality, 404000, China

Location

Fujian Cancer Hospital

Fuzhou, Fujian, 350014, China

Location

The First Affiliated Hospital of Xiamen University

Xiamen, Fujian, 361003, China

Location

Nanfang Hospital of Southern Medical University

Guangzhou, Guangdong, 510515, China

Location

Cancer Hospital of Shantou University Medical College

Shantou, Guangdong, 515031, China

Location

The Peoples Hospital of Guangxi Zhuang Autonomous Region

Nanning, Guangxi, 530021, China

Location

The Affiliated Hospital of Zunyi Medical College

Zunyi, Guizhou, 563000, China

Location

Harbin Medical University Cancer Hospital

Harbin, Heilongjiang, 150000, China

Location

Henan Cancer Hospital

Zhengzhou, Henan, 450000, China

Location

The First Affiliated Hospital of Zhengzhou University

Zhengzhou, Henan, 450052, China

Location

Union Hospital of Tongji Medical College, Huazhong University of Science and Technology

Wuhan, Hubei, 430022, China

Location

Hubei Cancer Hospital

Wuhan, Hubei, 430079, China

Location

The Second Xiangya Hospital of Central South University

Changsha, Hunan, 410011, China

Location

Hunan Cancer Hospital

Changsha, Hunan, 410013, China

Location

General Hospital of Eastern Theater Command

Nanjing, Jiangsu, 210002, China

Location

The First Affiliated Hospital of Soochow University

Suzhou, Jiangsu, 215006, China

Location

Xuzhou Central Hospital

Xuzhou, Jiangsu, 221000, China

Location

The First Hospital of Jilin University

Changchun, Jilin, 130021, China

Location

Liaoning Cancer Hospital and Institute

Shenyang, Liaoning, 110042, China

Location

The First Affiliated Hospital of Xian Jiaotong University

Xi'an, Shaanxi, 710061, China

Location

Qilu Hospital of Shandong University

Jinan, Shandong, 250000, China

Location

Jinan Central Hospital

Jinan, Shandong, 250013, China

Location

Jinan Military General Hospital

Jinan, Shandong, 250031, China

Location

Shandong Cancer Hospital

Jinan, Shandong, 250117, China

Location

Weifang Peoples Hospital

Weifang, Shandong, 261000, China

Location

Shanghai Chest Hospital

Shanghai, Shanghai Municipality, 200030, China

Location

West China Hospital, Sichuan University

Chengdu, Sichuan, 610041, China

Location

Tianjin Medical University General Hospital

Tianjin, Tianjin Municipality, 300052, China

Location

Tianjin Medical University Cancer Institute and Hospital

Tianjin, Tianjin Municipality, 300060, China

Location

The First Affiliated Hospital, Zhejiang University School of Medicine

Hangzhou, Zhejiang, 310003, China

Location

Hangzhou First Peoples Hospital

Hangzhou, Zhejiang, 310006, China

Location

Sir Run Run Shaw Hospital, Zhejiang University School of Medicine

Hangzhou, Zhejiang, 310016, China

Location

Zhejiang Cancer Hospital

Hangzhou, Zhejiang, 310022, China

Location

Related Publications (3)

  • Wang J, Lu S, Yu X, Hu Y, Sun Y, Wang Z, Zhao J, Yu Y, Hu C, Yang K, Feng G, Ying K, Zhuang W, Zhou J, Wu J, Leaw SJ, Zhang J, Lin X, Liang L, Yang N. Tislelizumab Plus Chemotherapy vs Chemotherapy Alone as First-line Treatment for Advanced Squamous Non-Small-Cell Lung Cancer: A Phase 3 Randomized Clinical Trial. JAMA Oncol. 2021 May 1;7(5):709-717. doi: 10.1001/jamaoncol.2021.0366.

    PMID: 33792623BACKGROUND
  • Wang, J, S. Lu, et al. Randomized Phase III Study of Tislelizumab plus Chemotherapy versus Chemotherapy Alone as First-Line Treatment for Advanced Squamous Non-Small Cell Lung Cancer (Sq-NSCLC): RATIONALE-307 Updated Analysis. IOTECH Abstract, Vol. 16 Supplement 1, Dec. 2022. doi.org/10.1016/j.iotech.2022.100244.

    BACKGROUND
  • Duan J, Zhang Y, Chen R, Liang L, Huo Y, Lu S, Zhao J, Hu C, Sun Y, Yang K, Chen M, Yu Y, Ying J, Huang R, Ma X, Leaw S, Bai F, Shen Z, Cai S, Gao D, Wang J, Wang Z. Tumor-immune microenvironment and NRF2 associate with clinical efficacy of PD-1 blockade combined with chemotherapy in lung squamous cell carcinoma. Cell Rep Med. 2023 Dec 19;4(12):101302. doi: 10.1016/j.xcrm.2023.101302. Epub 2023 Dec 4.

MeSH Terms

Conditions

Carcinoma, Non-Small-Cell Lung

Interventions

tislelizumabPaclitaxel130-nm albumin-bound paclitaxelCarboplatin

Condition Hierarchy (Ancestors)

Carcinoma, BronchogenicBronchial NeoplasmsLung NeoplasmsRespiratory Tract NeoplasmsThoracic NeoplasmsNeoplasms by SiteNeoplasmsLung DiseasesRespiratory Tract Diseases

Intervention Hierarchy (Ancestors)

TaxoidsCyclodecanesCycloparaffinsHydrocarbons, AlicyclicHydrocarbons, CyclicHydrocarbonsOrganic ChemicalsDiterpenesTerpenesCoordination Complexes

Results Point of Contact

Title
Study Director
Organization
BeiGene

Study Officials

  • Study Director

    BeiGene

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

July 3, 2018

First Posted

July 20, 2018

Study Start

July 30, 2018

Primary Completion

September 30, 2020

Study Completion

April 28, 2023

Last Updated

October 26, 2024

Results First Posted

October 17, 2023

Record last verified: 2024-10

Data Sharing

IPD Sharing
Will share

Locations