NCT03374254

Brief Summary

The purpose of this study is to determine safety and tolerability and to establish a preliminary recommended Phase 2 dose (RP2D) for the following combinations: pembrolizumab plus binimetinib (Cohort A), pembrolizumab plus mFOLFOX7 (oxaliplatin 85 mg/m\^2; leucovorin \[calcium folinate\] 400 mg/m\^2; fluorouracil \[5-FU\] 2400 mg/m\^2) (Cohort B), pembrolizumab plus mFOLFOX7 and binimetinib (Cohort C), pembrolizumab plus FOLFIRI (irinotecan 180 mg/m\^2; leucovorin \[calcium folinate\]400 mg/m\^2; 5-FU 2400 mg/m\^2 over 46-48 hours) (Cohort D), and pembrolizumab plus FOLFIRI and binimetinib (Cohort E).

Trial Health

90
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
116

participants targeted

Target at P75+ for phase_1

Timeline
Completed

Started Feb 2018

Longer than P75 for phase_1

Geographic Reach
2 countries

14 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

December 12, 2017

Completed
3 days until next milestone

First Posted

Study publicly available on registry

December 15, 2017

Completed
2 months until next milestone

Study Start

First participant enrolled

February 16, 2018

Completed
3.6 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

September 8, 2021

Completed
1.9 years until next milestone

Study Completion

Last participant's last visit for all outcomes

July 18, 2023

Completed
1.2 years until next milestone

Results Posted

Study results publicly available

October 15, 2024

Completed
Last Updated

November 21, 2024

Status Verified

November 1, 2024

Enrollment Period

3.6 years

First QC Date

December 12, 2017

Results QC Date

July 11, 2024

Last Update Submit

November 5, 2024

Conditions

Keywords

CRC, MSS, non-MSI-H, PD-1, anti-PD-1, anti PD-1, MEK, MEK inhibitor

Outcome Measures

Primary Outcomes (1)

  • Percentage of Participants Who Experienced Dose-Limiting Toxicity (DLT)

    The occurrence of any of the following toxicities during Part 1 of the study (the first 21 days for Cohort A, first 28 days for Cohorts B,C, D, \& E), if possibly, probably or definitely related to study treatment, was considered a DLT: Grade (Gr) 4 non hematologic toxicity, Gr 4 hematologic toxicity lasting \>7 days, Gr 3 thrombocytopenia, Any non-hematologic AE ≥Gr 3 in severity, Any Gr 3 or Gr 4 non-hematologic laboratory value, Febrile neutropenia Gr 3 or Gr 4, Any prolonged delay in initiating study therapy due to a treatment-related AE that started during the DLT period, Any treatment-related toxicity that causes the participant to discontinue treatment during the DLT period, Missing \>25% of binimetinib doses as a result of drug-related AE(s), Gr 5 toxicity, Cardiac disorders and vascular disorders, Eye disorders (Retinopathy or retinal detachment Gr ≥ 3).

    Up to approximately first 28 days of treatment

Secondary Outcomes (1)

  • Objective Response Rate (ORR) Per Response Evaluation Criteria In Solid Tumors Version 1.1 (RECIST 1.1)

    Up to Approximately 64 months

Study Arms (9)

Cohort A Part 1: Pembrolizumab +Binimetinib 30 mg

EXPERIMENTAL

Participants in Cohort A will receive pembrolizumab (200 mg) intravenous (IV) every 3 weeks (Q3W) plus binimetinib orally at of 30 mg twice a day (BID) until disease progression or discontinuation.

Biological: PembrolizumabDrug: Binimetinib

Cohort A Part 1: Pembrolizumab +Binimetinib 45 mg

EXPERIMENTAL

Participants in Cohort A will receive pembrolizumab (200 mg) IV Q3W plus binimetinib orally at 45 mg BID (Dose Level 2 \[DL2\]) until disease progression or discontinuation.

Biological: PembrolizumabDrug: Binimetinib

Cohort B Part 1: Pembrolizumab + mFOLFOX7

EXPERIMENTAL

Participants in Cohort B will receive pembrolizumab (200 mg) IV Q3W plus mFOLFOX7 (oxaliplatin 85 mg/m\^2; leucovorin \[calcium folinate\] 400 mg/m\^2; fluorouracil \[5-FU\] 2400 mg/m\^2 over 46-48 hours) IV Q2W until disease progression or discontinuation.

Biological: PembrolizumabDrug: OxaliplatinDrug: LeucovorinDrug: 5-Fluorouracil [5-FU]

Cohort B Part 2: Pembrolizumab + mFOLFOX

EXPERIMENTAL

During Part 2, participants in Cohort B will receive pembrolizumab (200 mg) IV Q3W plus mFOLFOX7 (oxaliplatin 85mg/m\^2; leucovorin \[calcium folinate\] 400 mg/m\^2; fluorouracil \[5-FU\] 2400 mg/m\^2 over 46-48 hours) IV Q2W until disease progression or discontinuation.

Biological: PembrolizumabDrug: OxaliplatinDrug: LeucovorinDrug: 5-Fluorouracil [5-FU]

Cohort C Part 1: Pembrolizumab + mFOLFOX7 + Binimetinib 30 mg

EXPERIMENTAL

Participants in Cohort C will receive pembrolizumab 200 mg IV Q3W plus mFOLFOX7 (oxaliplatin 85mg/m\^2; leucovorin \[calcium folinate\] 400 mg/m\^2; fluorouracil \[5-FU\] 2400 mg/m\^2 over 46-48 hours) IV Q2W in combination with binimetinib orally at a starting dose of 30 mg BID until disease progression or discontinuation.

Biological: PembrolizumabDrug: BinimetinibDrug: OxaliplatinDrug: LeucovorinDrug: 5-Fluorouracil [5-FU]

Cohort D Part 1: Pembrolizumab + FOLFIRI

EXPERIMENTAL

Participants in Cohort D will receive a standard dose (DL1) of pembrolizumab 200 mg IV Q3W plus FOLFIRI (irinotecan 180 mg/m\^2; leucovorin \[calcium folinate\] 400 mg/m\^2; 5-FU 2400 mg/m\^2 over 46-48 hours) IV Q2W until disease progression or discontinuation.

Biological: PembrolizumabDrug: LeucovorinDrug: 5-Fluorouracil [5-FU]Drug: Irinotecan

Cohort D Part 2: Pembrolizumab + FOLFIRI

EXPERIMENTAL

During Part 2, participants in Cohort D will receive pembrolizumab 200 mg IV Q3W plus FOLFIRI (irinotecan 180 mg/m\^2; leucovorin \[calcium folinate\] 400 mg/m\^2; 5-FU 2400 mg/m\^2 over 46-48 hours) until disease progression or discontinuation.

Biological: PembrolizumabDrug: LeucovorinDrug: 5-Fluorouracil [5-FU]Drug: Irinotecan

Cohort E Part 1: Pembrolizumab + FOLFIRI + Binimetinib 30 mg

EXPERIMENTAL

Participants in Cohort E will receive pembrolizumab 200 mg IV Q3W plus FOLFIRI (irinotecan 180 mg/m\^2; leucovorin \[calcium folinate\] 400 mg/m\^2; 5-FU 2400 mg/m\^2 over 46-48 hours) Q2W in combination with binimetinib orally at a starting dose of 30 mg BID until disease progression or discontinuation.

Biological: PembrolizumabDrug: BinimetinibDrug: LeucovorinDrug: 5-Fluorouracil [5-FU]Drug: Irinotecan

Cohort E Part 1: Pembrolizumab + FOLFIRI + Binimetinib 45 mg

EXPERIMENTAL

During Part 2, participants in Cohort E received pembrolizumab 200 mg IV Q3W plus FOLFIRI (irinotecan 180 mg/m\^2; leucovorin \[calcium folinate\] 400 mg/m\^2; 5-FU 2400 mg/m\^2 over 46-48 hours) Q2W plus binimetinib orally at the starting dose of 45 mg BID until disease progression or discontinuation. Cohort A During Part 2, participants in Cohort E received pembrolizumab 200 mg IV Q3W plus FOLFIRI (irinotecan 180 mg/m\^2; leucovorin \[calcium folinate\] 400 mg/m\^2; 5-FU 2400 mg/m\^2 over 46-48 hours) Q2W plus binimetinib orally at the starting dose of 45 mg BID until disease progression or discontinuation.

Biological: PembrolizumabDrug: BinimetinibDrug: LeucovorinDrug: 5-Fluorouracil [5-FU]Drug: Irinotecan

Interventions

PembrolizumabBIOLOGICAL

200 mg Pembrolizumab solution for IV infusion Q3W

Also known as: MK-3475
Cohort A Part 1: Pembrolizumab +Binimetinib 30 mgCohort A Part 1: Pembrolizumab +Binimetinib 45 mgCohort B Part 1: Pembrolizumab + mFOLFOX7Cohort B Part 2: Pembrolizumab + mFOLFOXCohort C Part 1: Pembrolizumab + mFOLFOX7 + Binimetinib 30 mgCohort D Part 1: Pembrolizumab + FOLFIRICohort D Part 2: Pembrolizumab + FOLFIRICohort E Part 1: Pembrolizumab + FOLFIRI + Binimetinib 30 mgCohort E Part 1: Pembrolizumab + FOLFIRI + Binimetinib 45 mg

tablet orally BID at 30 or 45 mg depending upon DLT profile

Also known as: MEK162, ARRY-162, ARRY-438162
Cohort A Part 1: Pembrolizumab +Binimetinib 30 mgCohort A Part 1: Pembrolizumab +Binimetinib 45 mgCohort C Part 1: Pembrolizumab + mFOLFOX7 + Binimetinib 30 mgCohort E Part 1: Pembrolizumab + FOLFIRI + Binimetinib 30 mgCohort E Part 1: Pembrolizumab + FOLFIRI + Binimetinib 45 mg

85 mg/m\^2 as IV infusion. Administered Q2W as part of mFOLFOX7 cocktail. Dose may be de-escalated to 70 mg/m\^2 if the standard dose of mFOLFOX7 is deemed too toxic per mTPI, based upon occurrence of DLTs.

Cohort B Part 1: Pembrolizumab + mFOLFOX7Cohort B Part 2: Pembrolizumab + mFOLFOXCohort C Part 1: Pembrolizumab + mFOLFOX7 + Binimetinib 30 mg

400 mg/m\^2 as IV infusion. Administered Q2W as part of mFOLFOX7 or FOLFIRI cocktail, depending upon allocation.

Also known as: calcium folinate
Cohort B Part 1: Pembrolizumab + mFOLFOX7Cohort B Part 2: Pembrolizumab + mFOLFOXCohort C Part 1: Pembrolizumab + mFOLFOX7 + Binimetinib 30 mgCohort D Part 1: Pembrolizumab + FOLFIRICohort D Part 2: Pembrolizumab + FOLFIRICohort E Part 1: Pembrolizumab + FOLFIRI + Binimetinib 30 mgCohort E Part 1: Pembrolizumab + FOLFIRI + Binimetinib 45 mg

2400 mg/m\^2 over 46-48 hours as IV infusion. Administered Q2W as part of mFOLFOX7 or FOLFIRI cocktail, depending upon allocation. Dose may be de-escalated to 2000 mg/m\^2 if the standard dose of mFOLFOX7 or FOLFIRI is deemed too toxic per mTPI, based upon occurrence of DLTs.

Cohort B Part 1: Pembrolizumab + mFOLFOX7Cohort B Part 2: Pembrolizumab + mFOLFOXCohort C Part 1: Pembrolizumab + mFOLFOX7 + Binimetinib 30 mgCohort D Part 1: Pembrolizumab + FOLFIRICohort D Part 2: Pembrolizumab + FOLFIRICohort E Part 1: Pembrolizumab + FOLFIRI + Binimetinib 30 mgCohort E Part 1: Pembrolizumab + FOLFIRI + Binimetinib 45 mg

180 mg/m\^2 as IV infusion. Administered Q2W as part of FOLFIRI cocktail. Dose may be de-escalated to 150 mg/m\^2 if the standard dose of FOLFIRI is deemed too toxic per mTPI, based upon occurrence of DLTs.

Cohort D Part 1: Pembrolizumab + FOLFIRICohort D Part 2: Pembrolizumab + FOLFIRICohort E Part 1: Pembrolizumab + FOLFIRI + Binimetinib 30 mgCohort E Part 1: Pembrolizumab + FOLFIRI + Binimetinib 45 mg

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • At least 18 years of age
  • Has a histologically-confirmed, unresectable or metastatic (Stage IV American Joint Committee on Cancer \[AJCC seventh edition\]) colorectal cancer (CRC)
  • Has a locally determined non microsatellite instability high/ proficient mismatch repair (non-MSI-H/pMMR) tumor status
  • Has at least 1 radiologically measurable lesion as defined by RECIST 1.1
  • Has an Eastern Cooperative Oncology Group (ECOG) performance status of 0 or 1
  • Has a life expectancy of at least 3 months
  • Has the ability to swallow and retain oral medication and not have any clinically significant gastrointestinal abnormalities that might alter absorption.
  • Has adequate organ function
  • Male participants must agree to use contraception during the treatment period and for ≥180 days, after the last dose of study treatment and refrain from donating sperm during this period. Male participants with pregnant partners must agree to use a condom
  • Female participants eligible to participate if not pregnant, not breastfeeding, and is not a woman of childbearing potential (WOCBP) or is a WOCBP who agrees to follow contraceptive guidance during the treatment period and for ≥180 days after the last dose of study treatment
  • Participants for Cohort A:
  • Has been previously treated with fluoropyrimidine, irinotecan, and oxaliplatin
  • Participants for Cohorts B and C:
  • Must not have received prior systemic chemotherapy for Stage IV CRC
  • Participants for Cohorts D and E:
  • +3 more criteria

You may not qualify if:

  • Is currently participating and receiving study therapy in a study of an investigational agent or has participated and received study therapy in a study of an investigational agent or has used an investigational device within 28 days of administration of MK-3475
  • Has had chemotherapy, definitive radiation, or biological cancer therapy within 4 weeks (prior to the first dose of study therapy, or has not recovered to Common Terminology Criteria for Adverse Events (CTCAE) Gr 1 or better from any AEs that were due to cancer therapeutics administered more than 4 weeks earlier
  • Has history of a second malignancy, unless potentially curative treatment has been completed with no evidence of malignancy for 2 years
  • Has clinically active central nervous system (CNS) metastases and/or carcinomatous meningitis
  • Has a known hypersensitivity, intolerability or contraindication to any component of study treatment, including premedication
  • Has any active infection requiring systemic therapy
  • Has a history of (non-infectious) pneumonitis that required steroids or has current pneumonitis
  • Has received prior therapy with compounds targeting programmed death (PD)-1, PD-L1, PD-L2, or a mitogen-activated protein kinase (MAPK) pathway inhibitor
  • Has an autoimmune disease that has required systemic treatment in the past 2 years with use of disease modifying agents, corticosteroids, or immunosuppressive drugs
  • Has a diagnosis of immunodeficiency or is receiving systemic steroid therapy or any other form of immunosuppressive therapy within 7 days prior to randomization
  • Has known history of human immunodeficiency virus (HIV) infection
  • Has a known history of Hepatitis B
  • Has received live vaccine within 30 days of the planned start of study therapy
  • Has undergone major surgery and has not recovered adequately from any toxicity and/or complications from the intervention prior to starting study therapy
  • Has baseline peripheral neuropathy/paresthesia
  • +15 more criteria

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (14)

City of Hope National Medical Center ( Site 0102)

Duarte, California, 91010, United States

Location

Anschutz Medical Campus, Anschutz Cancer Pavilion ( Site 0106)

Aurora, Colorado, 80045, United States

Location

Yale Cancer Center ( Site 0108)

New Haven, Connecticut, 06520, United States

Location

Moffitt Cancer Center ( Site 0111)

Tampa, Florida, 33612, United States

Location

University of Chicago ( Site 0105)

Chicago, Illinois, 60637, United States

Location

Rutgers Cancer Institute of New Jersey ( Site 0107)

New Brunswick, New Jersey, 08903-2681, United States

Location

UPMC Cancer Center/Hillman Cancer Center ( Site 0113)

Pittsburgh, Pennsylvania, 15232, United States

Location

Baylor Scott and White ( Site 0110)

Temple, Texas, 76508, United States

Location

Seattle Cancer Care Alliance ( Site 0104)

Seattle, Washington, 98109, United States

Location

Northwest Medical Specialties, PLLC ( Site 0101)

Tacoma, Washington, 98405, United States

Location

Cross Cancer Institute ( Site 0123)

Edmonton, Alberta, T6G 1Z2, Canada

Location

Princess Margaret Cancer Centre ( Site 0122)

Toronto, Ontario, M5G 2M9, Canada

Location

Centre Hospitalier de l Universite de Montreal - CHUM ( Site 0124)

Montreal, Quebec, H2X 3E4, Canada

Location

Jewish General Hospital ( Site 0121)

Montreal, Quebec, H3T 1E2, Canada

Location

Related Publications (2)

  • Chen EX, Kavan P, Tehfe M, Kortmansky JS, Sawyer MB, Chiorean EG, Lieu CH, Polite B, Wong L, Fakih M, Spencer K, Chaves J, Li C, Leconte P, Adelberg D, Kim R. Pembrolizumab Plus Binimetinib With or Without Chemotherapy for MSS/pMMR Metastatic Colorectal Cancer: Outcomes From KEYNOTE-651 Cohorts A, C, and E. Clin Colorectal Cancer. 2024 Jun;23(2):183-193. doi: 10.1016/j.clcc.2024.03.002. Epub 2024 Apr 1.

  • Kim R, Tehfe M, Kavan P, Chaves J, Kortmansky JS, Chen EX, Lieu CH, Wong L, Fakih M, Spencer K, Zhao Q, Predoiu R, Li C, Leconte P, Adelberg D, Chiorean EG. Pembrolizumab Plus mFOLFOX7 or FOLFIRI for Microsatellite Stable/Mismatch Repair-Proficient Metastatic Colorectal Cancer: KEYNOTE-651 Cohorts B and D. Clin Colorectal Cancer. 2024 Jun;23(2):118-127.e6. doi: 10.1016/j.clcc.2024.03.001. Epub 2024 Apr 1.

Related Links

MeSH Terms

Conditions

Colorectal NeoplasmsSpinocerebellar DegenerationsParkinson Disease 4, Autosomal Dominant Lewy Body

Interventions

pembrolizumabbinimetinibOxaliplatinLeucovorinFluorouracilIrinotecan

Condition Hierarchy (Ancestors)

Intestinal NeoplasmsGastrointestinal NeoplasmsDigestive System NeoplasmsNeoplasms by SiteNeoplasmsDigestive System DiseasesGastrointestinal DiseasesColonic DiseasesIntestinal DiseasesRectal DiseasesCerebellar DiseasesBrain DiseasesCentral Nervous System DiseasesNervous System DiseasesSpinal Cord DiseasesHeredodegenerative Disorders, Nervous SystemNeurodegenerative DiseasesGenetic Diseases, InbornCongenital, Hereditary, and Neonatal Diseases and Abnormalities

Intervention Hierarchy (Ancestors)

Coordination ComplexesOrganic ChemicalsFormyltetrahydrofolatesTetrahydrofolatesFolic AcidPterinsPteridinesHeterocyclic Compounds, 2-RingHeterocyclic Compounds, Fused-RingHeterocyclic CompoundsCoenzymesEnzymes and CoenzymesUracilPyrimidinonesPyrimidinesHeterocyclic Compounds, 1-RingCamptothecinAlkaloids

Results Point of Contact

Title
Senior Vice President, Global Clinical Development
Organization
Merck Sharp & Dohme LLC

Study Officials

  • Medical Director

    Merck Sharp & Dohme LLC

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 1
Allocation
NON RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

December 12, 2017

First Posted

December 15, 2017

Study Start

February 16, 2018

Primary Completion

September 8, 2021

Study Completion

July 18, 2023

Last Updated

November 21, 2024

Results First Posted

October 15, 2024

Record last verified: 2024-11

Data Sharing

IPD Sharing
Will share

http://engagezone.msd.com/doc/ProcedureAccessClinicalTrialData.pdf

More information

Locations