NCT02231723

Brief Summary

This is an open label, multi-center, multi-arm, dose-escalation study of BBI608 administered in combination with Gemcitabine and nab-Paclitaxel, mFOLFIRINOX, FOLFIRI, or MM-398 with 5-FU and leucovorin.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
139

participants targeted

Target at P75+ for phase_1

Timeline
Completed

Started Aug 2014

Longer than P75 for phase_1

Geographic Reach
1 country

12 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

August 1, 2014

Completed
29 days until next milestone

First Submitted

Initial submission to the registry

August 30, 2014

Completed
5 days until next milestone

First Posted

Study publicly available on registry

September 4, 2014

Completed
5.7 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

June 1, 2020

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

June 1, 2020

Completed
Last Updated

November 18, 2023

Status Verified

April 1, 2022

Enrollment Period

5.8 years

First QC Date

August 30, 2014

Last Update Submit

November 13, 2023

Conditions

Keywords

Digestive System NeoplasmsEndocrine Gland NeoplasmsPancreatic neoplasmsPancreatic cancer, adultPancreatic cancerPancreas cancerPancreatic diseasesAdenoma, Islet CellCarcinoma, Islet CellCarcinoma, Pancreatic DuctalGemcitabineGemzarNab-paclitaxelPaclitaxelAbraxaneOxaliplatinLeucovorinIrinotecanFluorouracil5-FUMM-398

Outcome Measures

Primary Outcomes (2)

  • Safety by reporting the adverse events and serious adverse events

    6 months

  • Determination of the Recommended Phase 2 Dose by assessing dose-limiting toxicities (DLTs)

    3 months

Secondary Outcomes (4)

  • Assess the preliminary anti-tumor activity of BBI608 when administered in combination with standard chemotherapies by performing tumor assessments every 8 weeks

    6 months

  • Assess the preliminary anti-tumor activity of BBI608 when administered in combination with standard chemotherapies by performing serum CA 19-9 level measurement

    6 months

  • Assess pharmacokinetic profile of BBI608 when administered in combination with standard chemotherapies

    On Day 1 and Day 15 of the first cycle prior to dosing and 1, 2, 3, 3.5, 4, 5, 5.5, 7, 8, 9, 10, 11 and 24 hours after first dose

  • Assess pharmacodynamic activity of BBI608 when administered in combination with standard chemotherapies

    During the first 28 days of treatment

Study Arms (4)

A: BBI608 in combination with Gemcitabine and nab-Paclitaxel

EXPERIMENTAL
Drug: BBI608Drug: Nab-paclitaxelDrug: Gemcitabine

B: BBI608 in combination with modified FOLFIRINOX

EXPERIMENTAL
Drug: BBI608Drug: OxaliplatinDrug: IrinotecanDrug: Fluorouracil

C: BBI608 in combination with FOLFIRI

EXPERIMENTAL
Drug: BBI608Drug: LeucovorinDrug: IrinotecanDrug: Fluorouracil

D: BBI608 in combination with MM-398, 5-FU and leucovorin

EXPERIMENTAL
Drug: BBI608Drug: LeucovorinDrug: FluorouracilDrug: MM-398

Interventions

BBI608DRUG

Administered continuously twice daily with doses separated by 12 hours

Also known as: Napabucasin, BB608, BBI-608
A: BBI608 in combination with Gemcitabine and nab-PaclitaxelB: BBI608 in combination with modified FOLFIRINOXC: BBI608 in combination with FOLFIRID: BBI608 in combination with MM-398, 5-FU and leucovorin

Nab-paclitaxel 125 mg/m\^2 I.V. infusion on Days 1, 8, and 15 of every 28-day cycle

Also known as: Abraxane, nanoparticle albumin-bound paclitaxel, paclitaxel, ABI-007
A: BBI608 in combination with Gemcitabine and nab-Paclitaxel

Gemcitabine 1000 mg/m\^2 I.V. infusion on Days 1, 8, and 15 of every 28-day cycle

Also known as: Gemzar
A: BBI608 in combination with Gemcitabine and nab-Paclitaxel

Oxaliplatin 85 mg/m\^2 I.V. infusion on Days 1 and 15 of every 28-day cycle

Also known as: Eloxatin
B: BBI608 in combination with modified FOLFIRINOX

Arm C, D: Leucovorin 400 mg/m\^2 I.V. infusion on Days 1 and 15 of every 28-day cycle

Also known as: Folinic Acid
C: BBI608 in combination with FOLFIRID: BBI608 in combination with MM-398, 5-FU and leucovorin

Arm B: Irinotecan 165 mg/m\^2 I.V. infusion on Days 1 and 15 of every 28-day cycle, Arm C: Irinotecan 165 mg/m\^2 I.V. infusion on Days 1 and 15 of every 28-day cycle

Also known as: Camptosar
B: BBI608 in combination with modified FOLFIRINOXC: BBI608 in combination with FOLFIRI

Arm B, D: Fluorouracil 2400 mg/m\^2 I.V. infusion on Days 1 and 15 of every 28-day cycle, Arm C: Fluorouracil 400 mg/m\^2 I.V. bolus followed by 2400 mg/m\^2 I.V. infusion on Days 1 and 15 of every 28-day cycle

Also known as: 5-FU, Carac, Efudex, Fluoroplex, Adrucil
B: BBI608 in combination with modified FOLFIRINOXC: BBI608 in combination with FOLFIRID: BBI608 in combination with MM-398, 5-FU and leucovorin
MM-398DRUG

MM-398 70 mg/m\^2 I.V. infusion on Days 1 and 15 of every 28-day cycle

Also known as: Onivyde
D: BBI608 in combination with MM-398, 5-FU and leucovorin

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Signed written informed consent must be obtained and documented according to International Conference on Harmonisation (ICH) - Good Clinical Practice (GCP), the local regulatory requirements, and permission to use private health information in accordance with the Health Insurance Portability and Accountability Act (HIPAA) prior to study-specific screening procedures.
  • Patients must have histologic or cytologic evidence of adenocarcinoma of the pancreas, such as a core tissue biopsy or a surgical resection specimen.
  • Patients must have metastatic disease. Baseline imaging of chest, abdomen and pelvis (CT or MRI) within 21 days prior to initiation of protocol therapy is required.
  • Patients must have measurable disease as defined by RECIST 1.1.
  • Patients with locally advanced unresectable pancreatic ductal adenocarcinoma are excluded.
  • Patients enrolling onto Arm A (Gemcitabine and nab-Paclitaxel) or Arm B (mFOLFIRINOX) are allowed to have up to two prior lines of systemic therapy, with adjuvant therapy counted as one line of therapy as long as disease recurrence occurred \> 6 months of last dose of therapy. Prior systemic therapy in the metastatic setting is allowed for as long as the therapy contained BBI608 in combination with either Gemcitabine and nab-Paclitaxel or mFOLFIRINOX. Toxicities related to prior therapy must have completely resolved (except for alopecia and anemia), or be deemed irreversible.
  • Patients who received Gemcitabine-based therapy in an adjuvant setting will be allowed to be enrolled on Arm A of the trial (Gemcitabine with nab-Paclitaxel) as long as their last Gemcitabine administration was at least 6 months prior to the first dose of BBI608.
  • Patients enrolling onto Arm A (Gemcitabine with nab-Paclitaxel) are allowed to have prior mFOLFIRINOX in combination with BBI608 in the metastatic setting.
  • Patients enrolling onto Arm B (mFOLFIRINOX) are allowed to have prior Gemcitabine with nab-Paclitaxel in combination with BBI608 in the metastatic setting.
  • Prior treatment with radiotherapy is allowed.
  • Patients enrolling onto Arm C (FOLFIRI) or Arm D (MM-398 with 5-FU and leucovorin) must have failed one prior line of gemcitabine-based therapy with or without BBI608 in the metastatic setting. No additional lines of therapy in the metastatic setting are allowed. Prior adjuvant therapy with gemcitabine is allowed as long as disease recurrence occurred \> 6 months of last dose of therapy. Toxicities related to prior therapy must have completely resolved (except for alopecia and anemia), or be deemed irreversible. Prior treatment with radiotherapy is allowed.
  • ≥ 18 years of age.
  • Patients must have an ECOG Performance Status ≤ 1.
  • Male or female patients of child-producing potential agree to use contraception or avoidance of pregnancy measures during the study and for 30 days after the last BBI608 dose.
  • Females of childbearing potential have a negative serum pregnancy test (preceding 72 hours of first day of BBI608 treatment).
  • +13 more criteria

You may not qualify if:

  • Anti-cancer chemotherapy, radiotherapy, immunotherapy, or investigational agents within 14 days of the first dose of BBI608, except for BBI608 for which a washout period is not required.
  • Patients may begin BBI608 on a date determined by the investigator and medical monitor for the sponsor after a minimum of 14 days since last receiving anti-cancer treatment which did not include BBI608, provided that all treatment-related adverse events have resolved or have been deemed irreversible (except for alopecia).
  • Patients who previously received BBI608 for treatment of PDAC on the BBI608-118 (BBI608-201PANC) study may continue with BBI608 in monotherapy between discontinuation of the first chemotherapy backbone and start of the second chemotherapy backbone. Patients may begin chemotherapy backbone on a date determined by the investigator and medical monitor for the sponsor after a minimum of 14 days and a maximum of 30 days since last receiving anti-cancer treatment which included BBI608, provided that all treatment-related adverse events have resolved or have been deemed irreversible (except for alopecia).
  • Patients with neuroendocrine neoplasms will be excluded.
  • Major surgery, other than diagnostic surgery (e.g., surgery done to obtain a biopsy for diagnosis without removal of an organ), within 4 weeks prior to first dose.
  • Any brain metastases including leptomeningeal metastases, are excluded, even if treated and stable.
  • History of posterior reversible encephalopathy syndrome.
  • Neurosensory neuropathy ≥ grade 2 at baseline.
  • Pregnant or breastfeeding.
  • Significant gastrointestinal disorder(s) that would, in the opinion of the Principal Investigator, prevent absorption of an orally available agent (e.g., Crohn's disease, ulcerative colitis, extensive gastric resection and small intestinal resection).
  • Unable or unwilling to swallow BBI608 capsules daily.
  • Uncontrolled chronic diarrhea ≥ grade 2 at baseline.
  • Uncontrolled intercurrent illness including, but not limited to uncontrolled active infection (including bacterial, viral or fungal requiring systemic therapy), clinically significant non-healing or healing wounds, symptomatic congestive heart failure, unstable angina pectoris, uncontrolled cardiac arrhythmia, significant pulmonary disease (shortness of breath at rest or mild exertion), uncontrolled infection or psychiatric illness/social situations that would limit compliance with study requirements.
  • Interstitial pneumonia or extensive and symptomatic interstitial fibrosis of the lung.
  • History of other active malignancies.
  • +20 more criteria

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (12)

Mayo Clinic Arizona

Phoenix, Arizona, 85054, United States

Location

Emory University Winship Cancer Institute

Atlanta, Georgia, 30322, United States

Location

Parkview Research Center

Fort Wayne, Indiana, 46845, United States

Location

Indiana University Health Goshen Center for Cancer Care

Goshen, Indiana, 46526, United States

Location

Indiana University Melvin and Bren Simon Cancer Center

Indianapolis, Indiana, 46202, United States

Location

Comprehensive Cancer Centers of Nevada

Henderson, Nevada, 89014, United States

Location

The Ohio State University Comprehensive Cancer Center

Columbus, Ohio, 43210, United States

Location

The University of Tennessee Medical Center

Knoxville, Tennessee, 37920, United States

Location

Texas Oncology - Austin Midtown

Austin, Texas, 78705, United States

Location

Texas Oncology - Baylor Charles A. Sammons Cancer Center

Dallas, Texas, 75246, United States

Location

Texas Oncology - SAT&BC

San Antonio, Texas, 78216, United States

Location

Virginia Oncology Associates

Norfolk, Virginia, 23502, United States

Location

MeSH Terms

Conditions

Digestive System NeoplasmsEndocrine Gland NeoplasmsPancreatic NeoplasmsPancreatic cancer, adultPancreatic DiseasesAdenoma, Islet CellCarcinoma, Islet CellCarcinoma, Pancreatic Ductal

Interventions

napabucasin130-nm albumin-bound paclitaxelAlbumin-Bound PaclitaxelTaxesPaclitaxelGemcitabineOxaliplatinLeucovorinIrinotecanFluorouracilirinotecan sucrosofate

Condition Hierarchy (Ancestors)

Neoplasms by SiteNeoplasmsDigestive System DiseasesEndocrine System DiseasesAdenomaNeoplasms, Glandular and EpithelialNeoplasms by Histologic TypeAdenocarcinomaCarcinomaCarcinoma, DuctalNeoplasms, Ductal, Lobular, and Medullary

Intervention Hierarchy (Ancestors)

TaxoidsCyclodecanesCycloparaffinsHydrocarbons, AlicyclicHydrocarbons, CyclicHydrocarbonsOrganic ChemicalsDiterpenesTerpenesAlbuminsProteinsAmino Acids, Peptides, and ProteinsEconomicsHealth Care Economics and OrganizationsHeterocyclic CompoundsDeoxycytidineCytidinePyrimidine NucleosidesPyrimidinesHeterocyclic Compounds, 1-RingCoordination ComplexesFormyltetrahydrofolatesTetrahydrofolatesFolic AcidPterinsPteridinesHeterocyclic Compounds, 2-RingHeterocyclic Compounds, Fused-RingCoenzymesEnzymes and CoenzymesCamptothecinAlkaloidsUracilPyrimidinones

Study Design

Study Type
interventional
Phase
phase 1
Allocation
NON RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

August 30, 2014

First Posted

September 4, 2014

Study Start

August 1, 2014

Primary Completion

June 1, 2020

Study Completion

June 1, 2020

Last Updated

November 18, 2023

Record last verified: 2022-04

Locations