NCT00506948

Brief Summary

The goal of this clinical research study is to learn if the combination of rabbit anti-thymocyte globulin (Thymoglobulin®), sirolimus (Rapamune®), and mycophenolate mofetil (Cellcept®) can help to prevent graft versus host disease (GVHD). The safety of this drug combination will also be studied. Primary Objective: To determine efficacy and toxicity of a regimen of thymoglobulin, sirolimus and mycophenolate mofetil for prevention of acute GVHD after allogeneic stem cell transplantation from human leukocyte antigen (HLA) identical related or unrelated donors. Secondary Objective: To assess engraftment, chronic GVHD, relapse and survival.

Trial Health

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Monitor

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
13

participants targeted

Target at below P25 for phase_2

Timeline
Completed

Started Sep 2006

Typical duration for phase_2

Geographic Reach
1 country

1 active site

Status
terminated

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

September 1, 2006

Completed
11 months until next milestone

First Submitted

Initial submission to the registry

July 20, 2007

Completed
5 days until next milestone

First Posted

Study publicly available on registry

July 25, 2007

Completed
3.2 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

October 1, 2010

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

October 1, 2010

Completed
3.4 years until next milestone

Results Posted

Study results publicly available

February 20, 2014

Completed
Last Updated

September 24, 2020

Status Verified

September 1, 2020

Enrollment Period

4.1 years

First QC Date

July 20, 2007

Results QC Date

January 7, 2014

Last Update Submit

September 1, 2020

Conditions

Keywords

Hematological MalignanciesMyelodysplastic SyndromeGraft Versus Host DiseaseGVHDAllogeneic Hematopoietic Stem Cell TransplantationAHSCTLeukemiaLymphomaT-CellsThymoglobulinATGrATGRabbit Antithymocyte GlobulinRapamuneSirolimusMycophenolate MofetilCellceptMMF

Outcome Measures

Primary Outcomes (2)

  • Failure Rate

    Efficacy failure defined as a participants who had either grade 3-4 acute graft-versus-host disease (aGVHD) or treatment related mortality (TRM) within 100 days post transplant. Failure Rate calculated as (# of failures) / (# participants evaluated). Physical exam and bloodwork every week (for the first 90-100 days after the transplant).

    Baseline to 100 days post transplant

  • Number of Participants With Acute Graft-versus-host Disease (aGVHD)

    Participants who had acute graft-versus-host disease (aGVHD) within 100 days post transplant. Physical exam and bloodwork every week (for the first 90-100 days after the transplant).

    Baseline to 100 days post transplant

Study Arms (1)

Thymoglobulin + Sirolimus + MMF

EXPERIMENTAL

Thymoglobulin 1.5 mg/kg intravenous (IV) days -4, -3, -2, -1 before Stem Cell Transplant (Day 0); Sirolimus 6 mg IV on day -2 followed by 2 mg daily to maintain therapeutic levels and Mycophenolate Mofetil (MMF) 15 mg/kg IV or orally every 12 hours starting on day 0 until day+27.

Drug: Mycophenolate Mofetil (MMF)Drug: ThymoglobulinDrug: SirolimusProcedure: Stem Cell Transplant

Interventions

15 mg/kg by vein or by mouth every 12 hours.

Also known as: CellCept, MMF
Thymoglobulin + Sirolimus + MMF

1.5 mg/kg by vein daily for 4 days

Also known as: Antithymocyte Globulin, rATG, ATG
Thymoglobulin + Sirolimus + MMF

6 mg daily by mouth for 1 day, followed by 2 mg daily for 1 day.

Also known as: Rapamune
Thymoglobulin + Sirolimus + MMF

Stem cell infusion on Day 0.

Also known as: hematopoietic stem cell transplantation, HSCT, transplantation
Thymoglobulin + Sirolimus + MMF

Eligibility Criteria

Age18 Years - 75 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Patients with high risk hematological malignancies, including those with induction failure and after treated or untreated relapse. High risk hematological malignancies include: Acute myelogenous or lymphocytic leukemia with induction failure of after relapse, myelodysplastic syndrome of intermediate and high risk according to Greenberg criteria, chronic myelogenous leukemia in accelerated phase or blast crisis, non-Hodgkin's and Hodgkin's lymphoma with induction failure or relapse after chemotherapy and refractory or relapsed chronic lymphocytic leukemia.
  • HLA-identical sibling or matched unrelated donor transplants not eligible for protocols of higher priority.
  • Age 18-75 years.
  • Bilirubin \</=1.5 mg/dl, serum glutamic-pyruvic transaminase (SGPT) \</= 200 IU/ml.
  • Creatinine \</=1.6 mg/dl.

You may not qualify if:

  • Regimens including rituximab or alemtuzumab in the preparative regimen.
  • Patients can not have received prior treatment with gemtuzumab.
  • Planned conditioning chemotherapy for transplant can not include gemtuzumab.
  • Planned conditioning chemotherapy for transplant can not include the busulfan and cyclophosphamide regimen.
  • HIV seropositivity
  • Uncontrolled infection, not responding to adequate antimicrobial therapy after 7 days of treatment. The protocol PI is the final arbiter of eligibility.
  • Pregnancy
  • Inability to sign consent.
  • Patients who are past recipients of allogeneic or autologous stem cell transplants from any source.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (1)

UT MD Anderson Cancer Center

Houston, Texas, 77030, United States

Location

Related Links

MeSH Terms

Conditions

Hematologic NeoplasmsMyelodysplastic SyndromesLeukemiaLymphomaGraft vs Host Disease

Interventions

Mycophenolic AcidthymoglobulinAntilymphocyte SerumSirolimusStem Cell TransplantationHematopoietic Stem Cell TransplantationTransplantation

Condition Hierarchy (Ancestors)

Neoplasms by SiteNeoplasmsHematologic DiseasesHemic and Lymphatic DiseasesBone Marrow DiseasesNeoplasms by Histologic TypeLymphoproliferative DisordersLymphatic DiseasesImmunoproliferative DisordersImmune System Diseases

Intervention Hierarchy (Ancestors)

CaproatesAcids, AcyclicCarboxylic AcidsOrganic ChemicalsFatty AcidsLipidsImmune SeraAntibodiesImmunoglobulinsImmunoproteinsBlood ProteinsProteinsAmino Acids, Peptides, and ProteinsSerum GlobulinsGlobulinsBiological ProductsComplex MixturesMacrolidesLactonesCell TransplantationCell- and Tissue-Based TherapyBiological TherapyTherapeuticsSurgical Procedures, Operative

Limitations and Caveats

A decision to terminate this trial was made due to the high incidence of veno-occlusive disease of the liver in participants receiving this graft-versus-host disease (GVHD) prophylaxis regimen.

Results Point of Contact

Title
Amin Alousi, MD /Professor, Stem Cell Transplantation
Organization
University of Texas (UT) MD Anderson Cancer Center

Study Officials

  • Amin Alousi, MD

    M.D. Anderson Cancer Center

    PRINCIPAL INVESTIGATOR

Publication Agreements

PI is Sponsor Employee
Yes
Restrictive Agreement
No

Study Design

Study Type
interventional
Phase
phase 2
Allocation
NA
Masking
NONE
Purpose
TREATMENT
Intervention Model
SINGLE GROUP
Sponsor Type
OTHER
Responsible Party
SPONSOR

Study Record Dates

First Submitted

July 20, 2007

First Posted

July 25, 2007

Study Start

September 1, 2006

Primary Completion

October 1, 2010

Study Completion

October 1, 2010

Last Updated

September 24, 2020

Results First Posted

February 20, 2014

Record last verified: 2020-09

Locations