Research Impact

h-index

N/A

Research impact score

Publications

0

Total publications

Trial Results

0

Published trial results

Citations

0

Total citations

Drug Portfolio

Analytics

Trial Phases

Phase 18
Phase 27

Trial Status

Recruiting4
Terminated2
Other2

Role Distribution

Principal Investigator8
PI Rate100%

Activity Timeline

Clinical Trials (8)

NCT07775313Phase 1/2Enrolling By Invitation
Base-Edited Hematopoietic Stem/Progenitor Cell Gene Therapy for Treatment of CXCR4-WHIM
HypogammaglobulinemiaImmunodeficiencyMyelokathexis+2 more
PrincipalinvestigatorStart date: 2026-10-21
NCT06959771Phase 1/2Recruiting
Base Editing Hematopoietic Stem Cell and T Cell Gene Therapy for CD40L-HyperIgM Syndrome: Single Patient Study
CD40L-HyperIgM Syndrome
PrincipalinvestigatorStart date: 2025-07-16
NCT06851767Phase 1/2Enrolling By Invitation
Base-Edited Hematopoietic Stem/Progenitor Cell X-Linked Severe Combined Immunodeficiency Gene Therapy
X-linked Severe Combined ImmunodeficiencyXSCID
PrincipalinvestigatorStart date: 2025-05-09
NCT06325709Phase 1/2Recruiting
Base Editing for Mutation Repair in Hematopoietic Stem & Progenitor Cells for X-Linked Chronic Granulomatous Disease
Chronic Granulomatous Disease (CGD)X-Linked Chronic Granulomatous Disease
PrincipalinvestigatorStart date: 2024-04-17
NCT05189925Phase 1Recruiting
NADPH Oxidase Correction in mRNA-transfected Granulocyte-enriched Cells in Chronic Granulomatous Disease (CGD)
Chronic Granulomatous DiseaseInfection
PrincipalinvestigatorStart date: 2022-07-22
NCT01306019Phase 1/2Recruiting
Lentiviral Gene Transfer for Treatment of Children Older Than Two Years of Age With X-Linked Severe Combined Immunodeficiency (XSCID)
X-linked Severe Combined Immunodeficiency (XSCID)
PrincipalinvestigatorStart date: 2012-09-25
NCT00325078Phase 1/2Terminated
Infliximab to Treat Crohn'S-like Inflammatory Bowel Disease in Chronic Granulomatous Disease
Chronic Granulomatous DiseaseCrohn'S-like IBDInflammatory Bowel Disease (IBD)
Principalinvestigator
NCT00490100Phase 1/2Terminated
Treatment for Growth Failure in Patients With X-Linked Severe Combined Immunodeficiency: Phase 2 Study of Insulin-Like Growth Factor-1
Growth FailureGrowth Hormone ResistenceX-linked Severe Combined Immunodeficiency (XSCID)
Principalinvestigator

Research Network

Collaboration Network

1 collaborators·0 connections
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Publications (0)

No publications found for this investigator.

Clinical Trials (8)

Showing 8 of 8 trials

NCT07775313Phase 1/2PrincipalInvestigator

Base-Edited Hematopoietic Stem/Progenitor Cell Gene Therapy for Treatment of CXCR4-WHIM

HypogammaglobulinemiaImmunodeficiencyMyelokathexis+2 more
Enrolling By Invitation
NCT06959771Phase 1/2PrincipalInvestigator

Base Editing Hematopoietic Stem Cell and T Cell Gene Therapy for CD40L-HyperIgM Syndrome: Single Patient Study

CD40L-HyperIgM Syndrome
Recruiting
NCT06851767Phase 1/2PrincipalInvestigator

Base-Edited Hematopoietic Stem/Progenitor Cell X-Linked Severe Combined Immunodeficiency Gene Therapy

X-linked Severe Combined ImmunodeficiencyXSCID
Enrolling By Invitation
NCT06325709Phase 1/2PrincipalInvestigator

Base Editing for Mutation Repair in Hematopoietic Stem & Progenitor Cells for X-Linked Chronic Granulomatous Disease

Chronic Granulomatous Disease (CGD)X-Linked Chronic Granulomatous Disease
Recruiting
NCT05189925Phase 1PrincipalInvestigator

NADPH Oxidase Correction in mRNA-transfected Granulocyte-enriched Cells in Chronic Granulomatous Disease (CGD)

Chronic Granulomatous DiseaseInfection
Recruiting
NCT01306019Phase 1/2PrincipalInvestigator

Lentiviral Gene Transfer for Treatment of Children Older Than Two Years of Age With X-Linked Severe Combined Immunodeficiency (XSCID)

X-linked Severe Combined Immunodeficiency (XSCID)
Recruiting
NCT00325078Phase 1/2PrincipalInvestigator

Infliximab to Treat Crohn'S-like Inflammatory Bowel Disease in Chronic Granulomatous Disease

Chronic Granulomatous DiseaseCrohn'S-like IBDInflammatory Bowel Disease (IBD)
Terminated
NCT00490100Phase 1/2PrincipalInvestigator

Treatment for Growth Failure in Patients With X-Linked Severe Combined Immunodeficiency: Phase 2 Study of Insulin-Like Growth Factor-1

Growth FailureGrowth Hormone ResistenceX-linked Severe Combined Immunodeficiency (XSCID)
Terminated

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