Chronic Granulomatous Disease
47
4
9
22
Key Insights
Highlights
Success Rate
71% trial completion
Clinical Risk Assessment
Based on trial outcomes
High Risk
Score: 72/100
19.1%
9 terminated out of 47 trials
71.0%
-15.5% vs benchmark
4%
2 trials in Phase 3/4
32%
7 of 22 completed with results
Key Signals
Data Visualizations
Phase Distribution
Trial Status
Trial Success Rate
Benchmark: 86.5%
Based on 22 completed trials
Clinical Trials (47)
Safety and Efficacy of Tofacitinib for Chronic Granulomatous Disease With Inflammatory Complications
Analysis of Patients Treated for Chronic Granulomatous Disease Since January 1, 1995
Hematopoietic Stem Cell Transplantation (HSCT) for Common Variable Immunodeficiency (CVID) and Other Autoimmune Manifestations of Primary Immune Regulatory Disorders (PIRD)
Allogeneic Hematopoietic Stem Cell Transplantation for Chronic Granulomatous Disease (CGD) With an Alemtuzumab, Busulfan and TBI-based Conditioning Regimen Combined With Cytokine (IL-6, +/- IFN-gamma) Antagonists
Study of Voicing My CHOiCES as a Tool for Advanced Care Planning in Young Adults With Cancer
Haploidentical Transplant for People With Chronic Granulomatous Disease (CGD) Using Alemtuzumab, Busulfan and TBI With Post-Transplant Cyclophosphamide
Genetic Disorders of Mucociliary Clearance in Nontuberculous Mycobacterial Lung Disease
Lentiviral Gene Therapy for CGD
NADPH Oxidase Correction in mRNA-transfected Granulocyte-enriched Cells in Chronic Granulomatous Disease (CGD)
pCCLCHIM-p47 (Lentiviral Vector Transduced CD34 Plus Cells) in Patients With p47 Autosomal Recessive Chronic Granulomatous Disease (AR-CGD)
Immune Disorder HSCT Protocol
Allogeneic Hematopoietic Stem Cell Transplant for Patients With Primary Immune Deficiencies
Elemental Diet for Treatment of Inflammatory Bowel Disease in Patients With Chronic Granulomatous Disease
Gene Therapy for Chronic Granulomatous Disease in Korea
Study to Assess the Use of JSP191 in Matched Unrelated Donor Transplantation for Chronic Granulomatous Disease (CGD)
Baby Detect : Genomic Newborn Screening
Fludarabine Phosphate, Cyclophosphamide, Total Body Irradiation, and Donor Stem Cell Transplant in Treating Patients With Blood Cancer
A Study of the Safety and Efficacy of Prime Editing (PM359) in Participants With p47phox Autosomal Recessive Chronic Granulomatous Disease (CGD )
Early Check: Expanded Screening in Newborns
Whole Blood Biospecimen Collection for Subjects With Chronic Granulomatous Disease (CGD)