Immunodeficiency
36
10
11
15
Key Insights
Highlights
Success Rate
79% trial completion
Clinical Risk Assessment
Based on trial outcomes
High Risk
Score: 62/100
11.1%
4 terminated out of 36 trials
78.9%
-7.6% vs benchmark
14%
5 trials in Phase 3/4
33%
5 of 15 completed with results
Key Signals
Data Visualizations
Phase Distribution
Trial Status
Trial Success Rate
Benchmark: 86.6%
Based on 15 completed trials
Clinical Trials (36)
Base-Edited Hematopoietic Stem/Progenitor Cell Gene Therapy for Treatment of CXCR4-WHIM
Allogeneic Hematopoietic Stem Cell Transplant for GATA2 Mutations
Genetic Analysis of Immune Disorders
Sample Collection for Systems Evaluation of Patients With Unknown or Incompletely Characterized Immune Defects
Allogeneic Hematopoietic Stem Cell Transplantation With Briquilimab-Based Conditioning in Participants With GATA2 Deficiency
Impact of a Strategy Based on Bacterial DNA Detection to Optimize Antibiotics in Immunocompromised Patients With Hospital-acquired Pneumonia Requiring Mechanical Ventilation
A Phase II Study of Allogeneic Hematopoietic Stem Cell Transplant for Subjects With VEXAS (Vacuoles, E1 Enzyme, X-linked, Autoinflammatory, Somatic) Syndrome
Vaccine-induced Immunity in Immunocompromised Patients
Phase 1/2: CD45RA Depleted Stem Cell Addback to Prevent Viral or Fungal Infections Post TCRab/CD19 Depleted HSCT
OPtimisation of Antiviral Therapy in Immunocompromised COVID-19 Patients: a Randomized Factorial Controlled Strategy Trial
OPtimisation of Antiviral Therapy in Immunocompromised COVID-19 Patients
The Sequestration of Holistic Stress Management Techniques for Adults
Immunogenicity and Safety of Inactivated Hepatitis A Vaccine in HIV-infected People
Determination of Adequate Tuberculosis Regimen in Patients Hospitalized With HIV-associated Severe Immune Suppression
Clozapine-related Immunodeficiency in Parkinsons Disease
Omega-3, Nigella Sativa, Indian Costus, Quinine, Anise Seed, Deglycyrrhizinated Licorice, Artemisinin, Febrifugine on Immunity of Patients With (COVID-19)
ImmunoCARE: Rapid, Accurate COVID Testing to Reduce Hospitalization of Immunocompromised Individuals
Blood Samples to Identify Biomarkers of Busulfan
Expanded Access Protocol Thymus Transplantation
Evaluation of Post-SARS-CoV-2 Vaccinal Response in Immunocompromised Patients