NCT07087860

Brief Summary

This phase II trial compares therapeutic plasma exchange followed by enfortumab vedotin and pembrolizumab to standard of care next-line therapy for the treatment of patients with bladder or upper urinary tract cancers that have spread from where they first started (primary site) to other places in the body (metastatic) and that have not responded to previous treatment (refractory). TPE is a process that slowly removes a patient's blood through an intravenous or central line. The blood is sent through a machine that separates the plasma (the liquid part of blood) from other blood components (red cells, white cells, platelets). The plasma is then removed. The remaining blood components are combined with replacement fluid and returned to the patient's bloodstream through the intravenous or central line. Enfortumab vedotin is a monoclonal antibody, enfortumab, linked to an anticancer drug called vedotin. It works by helping the immune system to slow or stop the growth of cancer cells. Enfortumab attaches to a protein called nectin-4 on cancer cells in a targeted way and delivers vedotin to kill them. It is a type of antibody-drug conjugate. Immunotherapy with monoclonal antibodies, such as pembrolizumab, may help the body's immune system attack the cancer, and may interfere with the ability of tumor cells to grow and spread. Treatment with enfortumab vedotin and pembrolizumab is already approved by the Food and Drug Administration for the treatment of bladder cancer, but TPE is not. Combining TPE with enfortumab vedotin and pembrolizumab may work better than standard of care options for treating metastatic and refractory bladder and urinary tract cancers. This study also evaluates the effect of TPE with standard of care antibody drug conjugates (ADCs) in treating patients with refractory metastatic bladder cancer. ADC therapy is treatment with a monoclonal antibody linked to a chemotherapy drug. It is a form of targeted therapy because it attaches to specific molecules (receptors) on the surface of tumor cells, and delivers chemotherapy to kill them. Giving TPE with standard of care ADC therapy may be effective in treating patients with refractory metastatic bladder cancer.

Trial Health

77
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
70

participants targeted

Target at P50-P75 for phase_2

Timeline
28mo left

Started Aug 2025

Typical duration for phase_2

Geographic Reach
1 country

1 active site

Status
recruiting

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Progress25%
Aug 2025Aug 2028

First Submitted

Initial submission to the registry

July 16, 2025

Completed
12 days until next milestone

First Posted

Study publicly available on registry

July 28, 2025

Completed
4 days until next milestone

Study Start

First participant enrolled

August 1, 2025

Completed
3 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

August 7, 2028

Expected
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

August 7, 2028

Last Updated

December 9, 2025

Status Verified

December 1, 2025

Enrollment Period

3 years

First QC Date

July 16, 2025

Last Update Submit

December 2, 2025

Conditions

Outcome Measures

Primary Outcomes (2)

  • Overall response rate (ORR) (Groups A and B)

    ORR is defined as proportion of evaluable patients with complete response (CR) or partial response (PR) as measured by Response Evaluation Criteria in Solid Tumors (RECIST) 1.1.

    Up to 6 months

  • ORR (Cohort C)

    ORR is defined as proportion of evaluable patients with complete response (CR) or partial response (PR) as measured by Response Evaluation Criteria in Solid Tumors (RECIST) 1.1.

    Up to 6 months

Secondary Outcomes (10)

  • Duration of response (DOR) (Groups A and B)

    Up to 5 years

  • DOR (Cohort C)

    Up to 5 years

  • Overall survival (OS) (Groups A and B)

    Up to 5 years

  • OS (Cohort C)

    Up to 5 years

  • Progression-free survival (PFS) (Groups A and B)

    Up to 5 years

  • +5 more secondary outcomes

Study Arms (3)

Group A (TPE, EV, pembrolizumab)

EXPERIMENTAL

Patients undergo TPE via venous access or central line on days 1-3 of cycles 1-3 and receive enfortumab vedotin IV over 30 minutes on days 3 and 10 of cycles 1-3 and on days 1 and 8 of cycle 4 and beyond and pembrolizumab IV over 30 minutes on day 3 of cycles 1-3 and day 1 of cycles 4 and beyond. Cycles repeat every 21 days in the absence of disease progression of unacceptable toxicity. Patients also undergo CT, PET/CT, or MRI and collection of blood and urine samples throughout the study. Patients may undergo central line placement prior to TPE.

Procedure: Biospecimen CollectionProcedure: Central Venous Cannula InsertionProcedure: Computed TomographyDrug: Enfortumab VedotinProcedure: Magnetic Resonance ImagingBiological: PembrolizumabProcedure: PlasmapheresisProcedure: Positron Emission TomographyOther: Questionnaire Administration

Group B (standard of care)

ACTIVE COMPARATOR

Patients receive physician's choice of standard of care next-line therapy. Patients also undergo CT, PET/CT, or MRI and collection of blood and urine samples throughout the study.

Other: Best PracticeProcedure: Biospecimen CollectionProcedure: Magnetic Resonance ImagingProcedure: Positron Emission TomographyOther: Questionnaire Administration

Cohort C (TPE, ADC)

EXPERIMENTAL

Patients undergo TPE via venous access or central line on days 1-3 of cycles 1-3 only and receive physician's choice of standard of care ADC IV on day 3 of cycles 1-3 and on day 1 of cycles 4 and beyond. Cycles repeat every 21 days in the absence of disease progression or unacceptable toxicity. Patients also undergo CT, PET/CT, or MRI and collection of blood and urine samples throughout the study.

Procedure: Biospecimen CollectionProcedure: Central Venous Cannula InsertionProcedure: Computed TomographyProcedure: Magnetic Resonance ImagingProcedure: PlasmapheresisProcedure: Positron Emission TomographyOther: Questionnaire AdministrationBiological: Antibody-Drug Conjugate Therapy

Interventions

Receive standard of care

Also known as: standard of care, standard therapy
Group B (standard of care)

Undergo collection of blood and urine samples

Also known as: Biological Sample Collection, Biospecimen Collected, Specimen Collection
Cohort C (TPE, ADC)Group A (TPE, EV, pembrolizumab)Group B (standard of care)
PembrolizumabBIOLOGICAL

Given IV

Also known as: BCD-201, GME 751, GME751, Keytruda, Lambrolizumab, MK 3475, MK-3475, MK3475, Pembrolizumab Biosimilar BCD-201, Pembrolizumab Biosimilar GME751, Pembrolizumab Biosimilar QL2107, Pembrolizumab Biosimilar RPH-075, Pembrolizumab Biosimilar SB27, QL2107, RPH 075, RPH-075, RPH075, SB 27, SB-27, SB27, SCH 900475, SCH-900475, SCH900475
Group A (TPE, EV, pembrolizumab)

Undergo central line placement

Also known as: Central venous catheter, Central Venous Catheter Placement
Cohort C (TPE, ADC)Group A (TPE, EV, pembrolizumab)

Undergo CT or PET/CT

Also known as: CAT, CAT Scan, Computed Axial Tomography, Computerized Axial Tomography, Computerized axial tomography (procedure), Computerized Tomography, Computerized Tomography (CT) scan, CT, CT Scan, tomography
Cohort C (TPE, ADC)Group A (TPE, EV, pembrolizumab)

Given IV

Also known as: AGS 22ME, AGS-22M6E, Anti-Nectin 4 ADC ASG-22CE, Anti-nectin-4 Monoclonal Antibody-Drug Conjugate AGS-22M6E, ASG 22CE, ASG-22CE, ASG22CE, Enfortumab Vedotin-ejfv, Padcev
Group A (TPE, EV, pembrolizumab)

Undergo MRI

Also known as: Magnetic Resonance, Magnetic Resonance Imaging (MRI), Magnetic resonance imaging (procedure), Magnetic Resonance Imaging Scan, Medical Imaging, Magnetic Resonance / Nuclear Magnetic Resonance, MR, MR Imaging, MRI, MRI Scan, MRIs, NMR Imaging, NMRI, Nuclear Magnetic Resonance Imaging, sMRI, Structural MRI
Cohort C (TPE, ADC)Group A (TPE, EV, pembrolizumab)Group B (standard of care)

Undergo TPE

Also known as: Plasma Exchange, Therapeutic Plasma Exchange, Therapeutic Plasmapheresis
Cohort C (TPE, ADC)Group A (TPE, EV, pembrolizumab)

Undergo PET/CT

Also known as: Medical Imaging, Positron Emission Tomography, PET, PET Scan, Positron emission tomography (procedure), Positron Emission Tomography Scan, Positron-Emission Tomography, PT
Cohort C (TPE, ADC)Group A (TPE, EV, pembrolizumab)Group B (standard of care)

Ancillary studies

Cohort C (TPE, ADC)Group A (TPE, EV, pembrolizumab)Group B (standard of care)

Given IV

Cohort C (TPE, ADC)

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Age ≥ 18 years
  • GROPUS A and B (reCIPE-B1): Histologically proven urothelial carcinoma \[American Joint Committee on Cancer (AJCC) 2017\] of the bladder (BCa) or upper urothelial tract (UTUC), that has progressed despite enfortumab vedotin and pembrolizumab treatment
  • NOTE: Primary or secondary progression are allowed, therapies are not required to be concurrent or immediately antecedent to enrollment)
  • COHORT C (CAKE ReCIPE): Histologically proven urothelial carcinoma (AJCC 2017) of the bladder (BCa) or upper urothelial tract (UTUC), that has progressed despite ADC AND is otherwise not a candidate for Groups A and B
  • NOTE: Patients in Groups A and B who have progressed on that treatment are candidates for this cohort. Such patients must be re-consented and re- enrolled
  • Measurable disease per RECIST version (v)1.1
  • Eastern Cooperative Oncology Group (ECOG) performance status grade 0, 1, or 2
  • Hemoglobin \> 7.0 g/dL (obtained ≤ 30 days prior to registration)
  • Platelet count ≥ 75,000/mm\^3 (obtained ≤ 30 days prior to registration)
  • Alanine aminotransferase (ALT) OR aspartate transaminase (AST) ≤ 3.5 x upper limit of normal (ULN) OR total bilirubin ≤ 3 x ULN OR direct bilirubin ≤ 3 x ULN (obtained ≤ 30 days prior to registration)
  • Estimated glomerular filtration rate (GFR) ≥ 15 ml/min (obtained ≤ 30 days prior to registration)
  • Negative pregnancy test ≤ 8 days prior to registration, for persons of childbearing potential only
  • Provide written informed consent
  • Ability to complete questionnaire(s) by themselves or with assistance
  • Willingness to undergo treatment as assigned (group A: TPE + EV/pembro; OR group B: next line standard of care; OR Cohort C TPE + ADC)
  • +3 more criteria

You may not qualify if:

  • Any of the following because this study involves an investigational agent, the genotoxic, mutagenic, and teratogenic effects of which on the developing fetus and newborn are unknown
  • Pregnant persons
  • Nursing persons
  • Persons of childbearing potential or able to father a child who are unwilling to employ adequate contraception
  • Any of the following histologic variants/divergent differentiation: Any amount of neuroendocrine, micropapillary, or signet ring cell features
  • Active malignancies (i.e., progressing or requiring treatment change ≤ 24 months before registration) other than the disease being treated under study
  • EXCEPTIONS:
  • Skin cancer (melanoma or non-melanoma) that is considered completely cured
  • Non-invasive cervical cancer that is considered completely cured
  • Breast cancer: adequately treated lobular carcinoma in situ or ductal carcinoma in situ considered to have a very low risk of recurrence
  • Localized prostate cancer (T1c/T2N0M0):
  • Gleason score 6, treated by either surgery or ablation ≤ 24 months prior to registration or untreated and under active surveillance
  • Gleason score 3+4 that has been treated (may include surgery or ablation) ≤ 24 months prior to registration and considered to have a very low risk of recurrence (i.e., cT1c or pT2 on prostatectomy specimen)
  • History of uncontrolled cardiovascular disease including any of the following ≤ 6 months prior to registration:
  • Significant cardiovascular disease \[New York Heart Association (NYHA) class ≥ III\], symptomatic congestive heart failure, unstable angina pectoris, cardiac arrhythmia, myocardial infarction, ventricular fibrillation, Torsades de Pointes, cerebrovascular accident, or transient ischemic attack
  • +2 more criteria

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (1)

Mayo Clinic in Rochester

Rochester, Minnesota, 55905, United States

RECRUITING

Related Links

MeSH Terms

Conditions

Urinary Bladder NeoplasmsUreteral Neoplasms

Interventions

Practice Guidelines as TopicStandard of CareSpecimen HandlingCentral Venous Cathetersenfortumab vedotinMagnetic Resonance SpectroscopypembrolizumabPlasmapheresisPlasma Exchange

Condition Hierarchy (Ancestors)

Urologic NeoplasmsUrogenital NeoplasmsNeoplasms by SiteNeoplasmsFemale Urogenital DiseasesFemale Urogenital Diseases and Pregnancy ComplicationsUrogenital DiseasesUrinary Bladder DiseasesUrologic DiseasesMale Urogenital DiseasesUreteral Diseases

Intervention Hierarchy (Ancestors)

Guidelines as TopicQuality Assurance, Health CareQuality of Health CareHealth Services AdministrationHealth Care Quality, Access, and EvaluationQuality Indicators, Health CareClinical Laboratory TechniquesDiagnostic Techniques and ProceduresDiagnosisInvestigative TechniquesVascular Access DevicesCathetersEquipment and SuppliesSpectrum AnalysisChemistry Techniques, AnalyticalBlood Component RemovalTherapeuticsSorption DetoxificationExtracorporeal CirculationSurgical Procedures, OperativeBlood TransfusionBiological Therapy

Study Officials

  • Jacob J. Orme, MD, PhD

    Mayo Clinic

    PRINCIPAL INVESTIGATOR

Central Study Contacts

Clinical Trials Referral Office

CONTACT

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
OTHER
Responsible Party
SPONSOR

Study Record Dates

First Submitted

July 16, 2025

First Posted

July 28, 2025

Study Start

August 1, 2025

Primary Completion (Estimated)

August 7, 2028

Study Completion (Estimated)

August 7, 2028

Last Updated

December 9, 2025

Record last verified: 2025-12

Data Sharing

IPD Sharing
Will not share

Locations