NCT05156281

Brief Summary

To compare the efficacy and safety of remibrutinib versus teriflunomide in patients with relapsing multiple sclerosis (RMS)

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Strong global presence with extensive site network
Enrollment
1,011

participants targeted

Target at P75+ for phase_3

Timeline
54mo left

Started Dec 2021

Longer than P75 for phase_3

Geographic Reach
25 countries

205 active sites

Status
active not recruiting

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Progress50%
Dec 2021Oct 2030

First Submitted

Initial submission to the registry

December 1, 2021

Completed
12 days until next milestone

Study Start

First participant enrolled

December 13, 2021

Completed
1 day until next milestone

First Posted

Study publicly available on registry

December 14, 2021

Completed
4.4 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

April 30, 2026

Completed
4.5 years until next milestone

Study Completion

Last participant's last visit for all outcomes

October 30, 2030

Expected
Last Updated

March 30, 2026

Status Verified

March 1, 2026

Enrollment Period

4.4 years

First QC Date

December 1, 2021

Last Update Submit

March 27, 2026

Conditions

Keywords

MSRMSRRMSactive secondary progressive multiple sclerosis SPMSremibrutinibLOU064teriflunomideadultrelapseExpanded Disability Status ScaleT2 lesionsT1 lesionsGD- enhancing MRINeurofilament light chainMcDonald diagnostic criteria

Outcome Measures

Primary Outcomes (1)

  • Annualized relapse rate (ARR) of confirmed relapses [Core Part]

    ARR is the average number of confirmed MS relapses in a year

    From Baseline, up to 30 months

Secondary Outcomes (24)

  • Time to 3-month confirmed disability progression (3mCDP) on Expanded Disability Status Scale (EDSS) [Core Part] (pooled data)

    Baseline up to 30 months

  • Time to 6-month confirmed disability progression (6mCDP) on EDSS [Core Part] (pooled data)

    Baseline up to 30 months

  • Annualized rate of new or enlarging T2 lesion [Core Part]

    Baseline up to 30 months

  • Neurofilament light chain (Nfl) [Core Part]

    Baseline up to 30 months

  • Number of Gd-enhancing T1 lesions per MRI scan [Core Part]

    Baseline up to 30 months

  • +19 more secondary outcomes

Study Arms (4)

Remibrutinib - Core

EXPERIMENTAL

Remibrutinib tablet and matching placebo of teriflunomide capsule

Drug: Remibrutinib

Teriflunomide - Core

ACTIVE COMPARATOR

Teriflunomide capsule and matching placebo remibrutinib tablet

Drug: Teriflunomide

Remibrutinib - Extension

EXPERIMENTAL

Participants on remibrutinib in Core will continue on remibrutinib tablet

Drug: Remibrutinib

Remibrutinib - Extension (on teriflunomide in Core)

EXPERIMENTAL

Participants on teriflunomide in Core will switch to remibrutinib tablet

Drug: Remibrutinib

Interventions

tablet taken orally

Also known as: LOU064
Remibrutinib - CoreRemibrutinib - ExtensionRemibrutinib - Extension (on teriflunomide in Core)

capsule taken orally

Teriflunomide - Core

Eligibility Criteria

Age18 Years - 55 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64)

You may qualify if:

  • to 55 years of age
  • Diagnosis of RMS according to the 2017 McDonald diagnostic criteria
  • At least: 1 documented relapse within the previous year. OR 2 documented relapses within the previous 2 years, OR 1 active Gadolinium (Gd)-enhancing lesion in the 12 months.
  • EDSS score of 0 to 5.5 (inclusive)
  • Neurologically stable within 1 month

You may not qualify if:

  • Diagnosis of primary progressive multiple sclerosis (PPMS)
  • Disease duration of more than 10 years in participants with EDSS score of 2 or less at screening
  • History of clinically significant CNS disease other than MS
  • Ongoing substance abuse (drug or alcohol)
  • History of malignancy of any organ system (other than complete resection of localized basal cell carcinoma of the skin or in situ cervical cancer),
  • Participants with history of confirmed Progressive Multifocal Leukoencephalopathy (PML) or Neurological symptoms consistent with PML
  • suicidal ideation or behavior
  • Evidence of clinically significant cardiovascular, neurological, psychiatric, pulmonary , renal, hepatic, endocrine, metabolic, hematological disorders or gastrointestinal disease that can interfere with interpretation of the study results or protocol adherence
  • Participants who have had a splenectomy
  • Active clinically significant systemic bacterial, viral, parasitic or fungal infections
  • Positive results for syphilis or tuberculosis testing
  • Uncontrolled disease states, such as asthma, or inflammatory bowel disease, where flares are commonly treated with oral or parenteral corticosteroids
  • Active, chronic disease of the immune system (including stable disease treated with immune therapy (e.g. Leflunomide, Methotrexate)) other than MS (e.g. rheumatoid arthritis, systemic lupus erythematosus, etc.) with the exception of well-controlled diabetes or thyroid disorder.
  • Participants with a known immunodeficiency syndrome (AIDS, hereditary immune deficiency, drug induced immune deficiency), or tested positive for HIV antibody
  • History or current treatment for hepatic disease including but not limited to acute or chronic hepatitis, cirrhosis (including all Child-Pugh classes) or hepatic failure or any chronic liver or biliary disease.
  • +22 more criteria

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (225)

Ctr for Neurology and Spine

Phoenix, Arizona, 85018, United States

Location

Vladimir Royter MD APMC

Hanford, California, 93230, United States

Location

VA Greater LA Healthcare System

Los Angeles, California, 90073, United States

Location

Regina Berkovich MD PhD Inc

West Hollywood, California, 90048, United States

Location

CU Anschutz Med Campus

Aurora, Colorado, 80045, United States

Location

Colorado Neurological Research PC

Denver, Colorado, 80210, United States

Location

New England Institute for Clinical Research

Stamford, Connecticut, 06905, United States

Location

Georgetown University Hospital Research

Washington D.C., District of Columbia, 20007, United States

Location

Georgetown University Hospital

Washington D.C., District of Columbia, 20007, United States

Location

Nova Clinical Research LLC

Bradenton, Florida, 34209, United States

Location

University of Florida

Gainesville, Florida, 32610, United States

Location

Memorial Healthcare System

Hollywood, Florida, 33021, United States

Location

Neurology Associates PA

Maitland, Florida, 32751, United States

Location

Gables Neurology

Miami, Florida, 33133, United States

Location

UM Department Of Neurology

Miami, Florida, 33136, United States

Location

Aqualane Clinical Research

Naples, Florida, 34105, United States

Location

Advent Health Orlando

Orlando, Florida, 32803, United States

Location

Humanity Clinical Research

Pembroke Pines, Florida, 33024, United States

Location

Emerald Coast Neurology

Pensacola, Florida, 32514, United States

Location

Brain and Spine Institute

Port Orange, Florida, 32127, United States

Location

Vero Beach Neurology

Vero Beach, Florida, 32960, United States

Location

Conquest Research

Winter Park, Florida, 32789, United States

Location

Methodist Neuroscience Institute

Merrillville, Indiana, 46410, United States

Location

University of Kansas Hospital

Kansas City, Kansas, 66160, United States

Location

Baptist Physicians Lexington

Nicholasville, Kentucky, 40356, United States

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Ochsner Clinic Foundation

New Orleans, Louisiana, 70121, United States

Location

Clinre Comprehensive Neurology

Frederick, Maryland, 21702, United States

Location

Tufts Medical Center

Boston, Massachusetts, 02111, United States

Location

Kansas City VA Medical Center

Kansas City, Missouri, 64128, United States

Location

South Shore Neurologic Associates

Patchogue, New York, 11772, United States

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True North Neurology

Port Jefferson, New York, 11776, United States

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University Of NC At Chapel Hill

Chapel Hill, North Carolina, 27599 9500, United States

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Piedmont HealthCare

Charlotte, North Carolina, 28210, United States

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The Boster Ctr for MS

Columbus, Ohio, 43235, United States

Location

Neurology Diagnostics Inc

Dayton, Ohio, 45408, United States

Location

Penn State Hershey Medical Center

Hershey, Pennsylvania, 17033, United States

Location

Premier Neurology

Greenville, South Carolina, 29605, United States

Location

Metrolina Neurological Associates PA

Old Point Station, South Carolina, 29707, United States

Location

Sibyl Wray MD Neurology PC

Knoxville, Tennessee, 37922, United States

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Neurology Consultants Of Dallas PA

Dallas, Texas, 75231, United States

Location

Med Research Inc

El Paso, Texas, 79935, United States

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Lone Star Neurology

Frisco, Texas, 75035, United States

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UT Health MARC Medical Arts and Research Center

San Antonio, Texas, 78229, United States

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Lonestar Neurology of San Antonio

San Antonio, Texas, 78258, United States

Location

Texas Institute for Neurological Disorders

Sherman, Texas, 75092, United States

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Baylor Scott and White

Temple, Texas, 76508, United States

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Virginia Mason Medical Centre

Seattle, Washington, 98101, United States

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University of Washington MS Clinic

Seattle, Washington, 98133, United States

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Elligo Health Research

Crab Orchard, West Virginia, 25827, United States

Location

Ascension St Francis Center

Milwaukee, Wisconsin, 53215, United States

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Medical College of Wisconsin

Milwaukee, Wisconsin, 53226, United States

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Novartis Investigative Site

Bombal, Mendoza Province, M5500DXO, Argentina

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Novartis Investigative Site

Rosario, Santa Fe Province, S2000BZL, Argentina

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Rosario, Santa Fe Province, S2000DSW, Argentina

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San Miguel de, Tucumán Province, T4000, Argentina

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Buenos Aires, C1012AAR, Argentina

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CABA, C1181ACH, Argentina

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Córdoba, X5004CDT, Argentina

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Vitória, Espírito Santo, 29055-450, Brazil

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Brasília, Federal District, 70200-730, Brazil

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Curitiba, Paraná, 81210-310, Brazil

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Porto Alegre, Rio Grande do Sul, 90430-001, Brazil

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Porto Alegre, Rio Grande do Sul, 90560-032, Brazil

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Porto Alegre, Rio Grande do Sul, 90620-130, Brazil

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Joinville, Santa Catarina, 89202-165, Brazil

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São Paulo, 01240-020, Brazil

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Plovdiv, 4002, Bulgaria

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Sofia, 1309, Bulgaria

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Sofia, 1407, Bulgaria

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Sofia, 1431, Bulgaria

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Edmonton, Alberta, T6G 2B7, Canada

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Burnaby, British Columbia, V5G 2X6, Canada

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Halifax, Nova Scotia, B3H 4K4, Canada

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Ottawa, Ontario, K1H 8L6, Canada

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Lévis, Quebec, G6W 0M5, Canada

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Montreal, Quebec, H4A 3T2, Canada

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Québec, Quebec, G1J 1Z4, Canada

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Saint-Jérôme, Quebec, J7Z 5T3, Canada

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Wuhan, Hubei, 430030, China

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Wuhan, Hubei, 430060, China

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Nanjing, Jiangsu, 210029, China

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Yinchuan, Ningxia, 750004, China

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Taiyuan, Shanxi, 030001, China

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Hangzhou, Zhejiang, 310006, China

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Hangzhou, Zhejiang, 310016, China

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Wenzhou, Zhejiang, 325000, China

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Beijing, 100034, China

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Shanghai, 200025, China

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Shanghai, 200040, China

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Split, HRV, 21000, Croatia

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Varaždin, HRV, 42000, Croatia

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Vukovar, 32000, Croatia

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Zagreb, 10000, Croatia

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Brno, 602 00, Czechia

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Hradec Králové, 500 05, Czechia

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Teplice, 415 29, Czechia

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Tallinn, 11315, Estonia

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Tartu, 50406, Estonia

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Limoges, Haute Vienne, 87000, France

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Toulon, Val De Marne, 83800, France

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Caen, 14033, France

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Clermont-Ferrand, 63003, France

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Dijon, 21000, France

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Gonesse, 95500, France

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Grenoble, 38043, France

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Lille, 59000, France

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Lille, 59037, France

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Nice, 06001, France

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Nîmes, 30029, France

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Poissy, 78303, France

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Toulouse, 31059, France

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Freiburg im Breisgau, Baden-Wurttemberg, 79106, Germany

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Essen, 45147, Germany

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Hamburg, 22179, Germany

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Ulm, 89073, Germany

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Athens, 115 28, Greece

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Athens, 11526, Greece

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Chaïdári, 124 62, Greece

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Ioannina, 455 00, Greece

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Larissa, 411 10, Greece

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Thessaloniki, 53246, Greece

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Thessaloniki, 54636, Greece

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Kochi, Kerala, 682025, India

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Pune, Maharashtra, 411013, India

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New Delhi, National Capital Territory of Delhi, 110060, India

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Amritsar, Punjab, 143006, India

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Hyderabad, Telangana, 500082, India

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Lucknow, Uttar Pradesh, 226007, India

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Kolkata, West Bengal, 700017, India

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Brindisi, BR, 72100, Italy

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Foggia, FG, 71122, Italy

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Pozzilli, IS, 86077, Italy

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Messina, ME, 98124, Italy

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Modena, MO, 41126, Italy

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Pavia, PV, 27100, Italy

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Orbassano, TO, 10043, Italy

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Naples, 80138, Italy

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Nagoya, Aichi-ken, 4668560, Japan

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Ichihara, Chiba, 2990111, Japan

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Sapporo, Hokkaido, 0630005, Japan

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Nishinomiya, Hyōgo, 663 8501, Japan

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Isehara, Kanagawa, 259-1193, Japan

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Sagamihara, Kanagawa, 252-0375, Japan

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Sendai, Miyagi, 9838512, Japan

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Kashihara, Nara, 634 8522, Japan

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Moriguchi, Osaka, 570-8507, Japan

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Suita, Osaka, 5650871, Japan

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Higashi-Matsuyama, Saitama, 355-0005, Japan

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Itabashi-ku, Tokyo, 1738610, Japan

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Kodaira, Tokyo, 187-8551, Japan

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Shinjuku Ku, Tokyo, 160-0023, Japan

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Shinjuku Ku, Tokyo, 1628666, Japan

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Shinjuku-ku, Tokyo, 1608582, Japan

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Chiba, 2608677, Japan

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Fukuoka, 810-0022, Japan

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Fukuoka, 8128582, Japan

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Kobe, 650-0017, Japan

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Kyoto, 616-8255, Japan

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Niigata, 9518520, Japan

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Mexico City, Mexico City, 06700, Mexico

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Novartis Investigative Site

Chihuahua City, 31203, Mexico

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Novartis Investigative Site

Mexico City, 14050, Mexico

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Querétaro, 76070, Mexico

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Plewiska, Poznan, 62-064, Poland

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Bialystok, 15-704, Poland

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Glogow Wielkopolski, 36-060, Poland

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Katowice, 40-081, Poland

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Katowice, 40-571, Poland

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Katowice, 40-686, Poland

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Katowice, 40-689, Poland

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Lublin, 20-701, Poland

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Wroclaw, 51-685, Poland

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Zabrze, 41-800, Poland

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Braga, 4710243, Portugal

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Coimbra, 3004-561, Portugal

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Leiria, 2410-197, Portugal

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Lisbon, 1169-050, Portugal

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Novartis Investigative Site

Lisbon, 1649-035, Portugal

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Novartis Investigative Site

Matosinhos Municipality, 4454-513, Portugal

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Novartis Investigative Site

Santa Maria da Feira, 4520-211, Portugal

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Caribbean Center for Clinical Research, Inc

Guaynabo, 00968, Puerto Rico

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Novartis Investigative Site

Brasov, ROM, 500123, Romania

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Constanța, ROM, 900123, Romania

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Campulung Muscel, 115100, Romania

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Constanța, 900591, Romania

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Banská Bystrica, 974 04, Slovakia

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Banská Bystrica, 975 17, Slovakia

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Bratislava, 833 05, Slovakia

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Celje, 3000, Slovenia

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Ljubljana, 1000, Slovenia

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Maribor, 2000, Slovenia

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Bloemfontein, Free State, 9301, South Africa

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Pretoria, 0041, South Africa

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Rosebank, 2196, South Africa

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Santiago Compostela, A Coruna, 15706, Spain

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Vitoria-Gasteiz, Araba, 01009, Spain

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L'Hospitalet de Llobregat, Barcelona, 08907, Spain

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Albacete, Castille-La Mancha, 02006, Spain

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Barcelona, Catalonia, 08003, Spain

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Logroño, La Rioja, 26006, Spain

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Pozuelo de Alarcón, Madrid, 28223, Spain

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Torrejón de Ardoz, Madrid, 28850, Spain

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Gijón, Principality of Asturias, 33394, Spain

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Valencia, Valencia, 46017, Spain

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Barcelona, 08041, Spain

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Lleida, 25198, Spain

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Madrid, 28009, Spain

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Madrid, 28040, Spain

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Málaga, 29016, Spain

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Seville, 41009, Spain

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Valencia, 46026, Spain

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Stockholm, 102 35, Sweden

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Samsun, Atakum, 55200, Turkey (Türkiye)

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Izmir, Balcova, 35340, Turkey (Türkiye)

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Istanbul, Fatih, 34093, Turkey (Türkiye)

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Istanbul, Fatih, 34098, Turkey (Türkiye)

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Izmir, Karabaglar, 35150, Turkey (Türkiye)

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Kayseri, Melikgazi, 38039, Turkey (Türkiye)

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Bursa, Nilufer, 16140, Turkey (Türkiye)

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Istanbul, Pendik, 34899, Turkey (Türkiye)

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Istanbul, Sancaktepe, 34785, Turkey (Türkiye)

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Kocaeli, 41380, Turkey (Türkiye)

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Konya, 42130, Turkey (Türkiye)

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Inverness, Invernesshire, IV2 3RE, United Kingdom

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Canterbury, Kent, CT1 3NG, United Kingdom

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MeSH Terms

Conditions

RecurrenceCharcot-Marie-Tooth disease, Type 1F

Interventions

remibrutinibteriflunomide

Condition Hierarchy (Ancestors)

Disease AttributesPathologic ProcessesPathological Conditions, Signs and Symptoms

Study Officials

  • Novartis Pharmaceuticals

    Novartis Pharmaceuticals

    STUDY DIRECTOR

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
DOUBLE
Who Masked
PARTICIPANT, INVESTIGATOR
Masking Details
In order to maintain blinding, a double-dummy design will be used
Purpose
TREATMENT
Intervention Model
PARALLEL
Model Details: Eligible participants will be randomized in a 1:1 ratio
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

December 1, 2021

First Posted

December 14, 2021

Study Start

December 13, 2021

Primary Completion

April 30, 2026

Study Completion (Estimated)

October 30, 2030

Last Updated

March 30, 2026

Record last verified: 2026-03

Data Sharing

IPD Sharing
Will share

Novartis is committed to sharing with qualified external researchers, access to patient-level data and supporting clinical documents from eligible studies. These requests are reviewed and approved by an independent review panel on the basis of scientific merit. All data provided is anonymized to respect the privacy of patients who have participated in the trial in line with applicable laws and regulations. This trial data availability is according to the criteria and process described on www.clinicalstudydatarequest.com

Locations