NCT05079230

Brief Summary

The goal of this clinical study is to compare the study drugs, magrolimab + venetoclax + azacitidine, versus placebo + venetoclax + azacitidine in participants with untreated acute myeloid leukemia (AML) who are not able to have chemotherapy.

Trial Health

68
Monitor

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Strong global presence with extensive site network
Enrollment
378

participants targeted

Target at P50-P75 for phase_3

Timeline
Completed

Started Jul 2022

Geographic Reach
19 countries

161 active sites

Status
terminated

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

October 4, 2021

Completed
11 days until next milestone

First Posted

Study publicly available on registry

October 15, 2021

Completed
9 months until next milestone

Study Start

First participant enrolled

July 7, 2022

Completed
1.8 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

April 11, 2024

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

April 11, 2024

Completed
12 months until next milestone

Results Posted

Study results publicly available

April 4, 2025

Completed
Last Updated

April 4, 2025

Status Verified

April 1, 2025

Enrollment Period

1.8 years

First QC Date

October 4, 2021

Results QC Date

February 25, 2025

Last Update Submit

April 3, 2025

Conditions

Outcome Measures

Primary Outcomes (1)

  • Overall Survival (OS)

    OS was measured from the date of randomization to the date of death from any cause. Participants were censored at last known alive date. Kaplan-Meier (KM) estimates were used in outcome measure analysis.

    Up to 1.6 years

Secondary Outcomes (16)

  • Rate of Complete Remission (CR) + Complete Remission With Partial Hematologic Recovery (CRh)

    Up to 1.6 years

  • Rate of Complete Remission (CR)

    Up to 1.6 years

  • Event-Free Survival (EFS)

    Up to 1.6 years

  • Duration of CR + CRh in Participants Who Achieved Complete Remission (CR) or Complete Remission With Partial Hematologic Recovery (CRh)

    Up to 1.6 years

  • Duration of Complete Remission (DCR) in Participants Who Achieved Complete Remission (CR)

    Up to 1.6 years

  • +11 more secondary outcomes

Study Arms (2)

Magrolimab + Venetoclax + Azacitidine

EXPERIMENTAL

Participants will receive * magrolimab: 1 mg/kg priming dose on Days 1 and 4; 15 mg/kg on Day 8; and 30 mg/kg on Days 11, 15, and then every week for 5 doses and every 2 weeks thereafter * venetoclax: 100 mg on Cycle 1 Day 1, 200 mg on Cycle 1 Day 2, 400 mg on Cycle 1 Day 3 and daily thereafter * azacitidine: 75 mg/m\^2 on Days 1-7 or Days 1-5 and 8-9 of each cycle Each cycle is 28 days.

Drug: MagrolimabDrug: VenetoclaxDrug: Azacitidine

Magrolimab Matching Placebo + Venetoclax + Azacitidine

PLACEBO COMPARATOR

Participants will receive * magrolimab matching placebo: Days 1, 4, 8, 11, and 15, then every week for 5 doses and every 2 weeks thereafter * venetoclax: 100 mg on Cycle 1 Day 1, 200 mg on Cycle 1 Day 2, 400 mg on Cycle 1 Day 3 and daily thereafter * azacitidine: 75 mg/m\^2 on Days 1-7 or Days 1-5 and 8-9 of each cycle Each cycle is 28 days.

Drug: VenetoclaxDrug: AzacitidineDrug: Placebo

Interventions

Administered intravenously (IV)

Also known as: GS-4721
Magrolimab + Venetoclax + Azacitidine

Tablets administered orally

Also known as: VENCLEXTA®
Magrolimab + Venetoclax + AzacitidineMagrolimab Matching Placebo + Venetoclax + Azacitidine

Administered according to region-specific drug labeling, either subcutaneously (SC) or intravenously (IV)

Magrolimab + Venetoclax + AzacitidineMagrolimab Matching Placebo + Venetoclax + Azacitidine

Administered intravenously (IV)

Magrolimab Matching Placebo + Venetoclax + Azacitidine

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Previously untreated individuals with histological confirmation of acute myeloid leukemia (AML) by World Health Organization (WHO) criteria who are ineligible for treatment with a standard cytarabine and anthracycline induction regimen due to age, or comorbidity. Individuals must be considered ineligible for intensive chemotherapy, defined by the following:
  • ≥ 75 years of age; Or
  • ≥ 18 to 74 years of age with at least 1 of the following comorbidities:
  • Eastern Cooperative Oncology Group (ECOG) performance status of 2 or 3
  • Diffusing capacity of the lung of carbon monoxide ≤ 65% or forced expiratory volume in 1 second ≤ 65%
  • Left ventricular ejection fraction ≤ 50%
  • Baseline creatinine clearance ≥ 30 mL/min to \< 45 mL/min calculated by the Cockcroft Gault formula or measured by 24-hour urine collection
  • Hepatic disorder with total bilirubin \> 1.5 x upper limit of normal (ULN)
  • Any other comorbidity that the investigator judges to be incompatible with intensive chemotherapy
  • ECOG performance status:
  • Of 0 to 2 for individuals ≥ 75 years of age Or
  • Of 0 to 3 for individuals ≥ 18 to 74 years of age
  • Individuals with white blood cell (WBC) count ≤ 20 x 10\^3/μL prior to randomization. If the individual's WBC is \> 20 x10\^3/μL prior to randomization, the individual can be enrolled, assuming all other eligibility criteria are met. However, the WBC should be ≤ 20 x 10\^3/μL prior to the first dose of study treatment and prior to each magrolimab/placebo dose during Cycle 1.
  • Note: Individuals can be treated with hydroxyurea and/or leukapheresis prior to randomization and throughout the study to reduce the WBC to ≤ 20 x 10\^3/μL to enable eligibility for study drug dosing
  • Hemoglobin must be ≥ 9 g/dL prior to initial dose of study treatment
  • +2 more criteria

You may not qualify if:

  • Prior treatment with any of the following:
  • cluster of differentiation 47 (CD47) or signal regulatory protein alpha (SIRPα)-targeting agents
  • Antileukemic therapy for the treatment of AML (eg, hypomethylating agents (HMAs), low-dose cytarabine, and/or venetoclax), excluding hydroxyurea
  • Note: Individuals with prior MDS who have not received prior HMAs or venetoclax or chemotherapeutic agents for MDS may be enrolled in the study. Prior treatment with myelodysplastic syndrome (MDS) therapies including, but not limited to lenalidomide, erythroid-stimulating agents, or similar red blood cell negative (RBC-), white blood cell negative (WBC-), or platelet-direct therapies or growth factors is allowed for these individuals.
  • Clinical suspicion of or documented active central nervous system (CNS) involvement with AML
  • Individuals who have acute promyelocytic leukemia
  • Second malignancy, except MDS, treated basal cell or localized squamous skin carcinomas, localized prostate cancer, or other malignancies for which individuals are not on active anticancer therapies and have had no evidence of active malignancy for at least 1 year

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (164)

University of Arkansas for Medical Sciences

Little Rock, Arkansas, 72205, United States

Location

City of Hope (City of Hope National Medical Center, City of Hope Medical Center)

Duarte, California, 91010, United States

Location

Community Cancer Institute

Fresno, California, 93730, United States

Location

UC Irvine Health- Chao Family Comprehensive Cancer Center

Orange, California, 92868, United States

Location

Baptist MD Anderson Cancer Center

Jacksonville, Florida, 32207, United States

Location

Moffitt Cancer Center

Tampa, Florida, 33612, United States

Location

Loyola University Medical Center

Maywood, Illinois, 60153, United States

Location

Parkview Research Center

Fort Wayne, Indiana, 46845, United States

Location

Indiana Blood and Marrow Transplantation - Clinic

Indianapolis, Indiana, 46237, United States

Location

The University of Iowa Hospitals and Clinics

Iowa City, Iowa, 52242, United States

Location

University of Maryland, Greenebaum Comprehensive Cancer Center

Baltimore, Maryland, 21201, United States

Location

University of Massachusetts Worcester

Worcester, Massachusetts, 01655, United States

Location

MidAmerica Division, Inc., c/o Research Medical Center

Kansas City, Missouri, 64132, United States

Location

SSM Health Saint Louis University Hospital

St Louis, Missouri, 63110, United States

Location

John Theurer Cancer Center at Hackensack University Medical Center

Hackensack, New Jersey, 07601, United States

Location

Rutgers Cancer Institute of New Jersey

New Brunswick, New Jersey, 08901, United States

Location

New York-Presbyterian/Weill Cornell Medical Center

New York, New York, 10021, United States

Location

Icahn School of Medicine at Mount Sinai and The Mount Sinai Hospital

New York, New York, 10029, United States

Location

University of Rochester Medical Center

Rochester, New York, 14642, United States

Location

UNC Hospitals, The University of North Carolina at Chapel Hill

Chapel Hill, North Carolina, 27514, United States

Location

Novant Health Cancer Institute Hematology- Charlotte

Charlotte, North Carolina, 28204, United States

Location

Novant Health Cancer Institute Hematology - Forsyth

Winston-Salem, North Carolina, 27103, United States

Location

Wake Forest Baptist Health

Winston-Salem, North Carolina, 27103, United States

Location

University Hospitals Cleveland Medical Center

Cleveland, Ohio, 44106, United States

Location

Cleveland Clinic Foundation

Cleveland, Ohio, 44195, United States

Location

OU Health Stephenson Cancer Center

Oklahoma City, Oklahoma, 73104, United States

Location

Providence Cancer Institute Franz Clinic

Portland, Oregon, 97213, United States

Location

Penn State Hershey Medical Center

Hershey, Pennsylvania, 17033, United States

Location

Fox Chase Cancer Center

Philadelphia, Pennsylvania, 19111, United States

Location

West Penn Hospital

Pittsburgh, Pennsylvania, 15224, United States

Location

Rhode Island Hospital

Providence, Rhode Island, 02903, United States

Location

Baylor University Medical Center

Dallas, Texas, 75246, United States

Location

Brooke Army Medical Center

Fort Sam Houston, Texas, 78234, United States

Location

Houston Methodist Hospital Cancer Center

Houston, Texas, 77030, United States

Location

MD Anderson Cancer Center

Houston, Texas, 77030, United States

Location

Intermountain Health - LDS Hospital

Salt Lake City, Utah, 84143, United States

Location

Virginia Mason Franciscan Health

Seattle, Washington, 98101, United States

Location

Fred Hutchinson Cancer Center

Seattle, Washington, 98109, United States

Location

Froedtert Hospital and the Medical College of Wisconsin

Milwaukee, Wisconsin, 53226, United States

Location

Canberra Hospital

Woden, Australian Capital Territory, 2606, Australia

Location

Border Medical Oncology Research Unit

Albury, New South Wales, 2640, Australia

Location

Concord Repatriation General Hospital

Concord, New South Wales, 2139, Australia

Location

Liverpool Hospital

Liverpool, New South Wales, 2170, Australia

Location

St George Hospital, Clinical Research Unit Haemotology, Division of Cancer Services

Sydney, New South Wales, 2217, Australia

Location

Gold Coast University Hospital

Southport, Queensland, 4215, Australia

Location

Monash University, Eastern Health-Box Hill Hospital

Box Hill, Victoria, 3128, Australia

Location

Northern Health

Epping, Victoria, 3076, Australia

Location

Peter MacCallum Cancer Centre

Melbourne, Victoria, 3000, Australia

Location

Ordensklinikum Linz GmbH Elisabethinen

Linz, Austria

Location

Wiener Gesundheitsverbund, Klinik Hietzing

Vienna, 1130, Austria

Location

Hanusch Krankenhaus

Vienna, 1140, Austria

Location

Ziekenhuis Netwerk Antwerp (ZNA) - Stuivenberg

Antwerp, 2060, Belgium

Location

Cliniques Universitaires Saint-Luc

Brussels, 1200, Belgium

Location

University Hospital Gent

Ghent, 9000, Belgium

Location

Hopital de Jolimont

Haine-Saint-Paul, 7100, Belgium

Location

University Hospital Leuven (UZ Leuven) - Campus Gasthuisberg

Leuven, 3000, Belgium

Location

Centre Hospitalier Universitaire de Liege

Liège, 4000, Belgium

Location

Queen Elizabeth II (QEII) Health Sciences Centre

Halifax, B3H 1V7, Canada

Location

Centre Integre Universitaire de Sante et de Services Sociaux(CIUSSS) de l'Est-de-L'Ile-de- Montreal - Hopital Maisonneuve-Rosemont

Montreal, H1T 2M4, Canada

Location

Princess Margaret Cancer Centre - University Health Network

Toronto, M5G 2M9, Canada

Location

CancerCare Manitoba

Winnipeg, R3E 0V9, Canada

Location

Fakultni nemocnice Brno, Interni hematologicka a onkologicka klinika FN Brno a LF MU

Jihormoravsky KRAJ, 625 00, Czechia

Location

Fakultni nemocine Olomouc, Hemato-onkologicka klinika

Olomouc, 77520, Czechia

Location

Fakultni nemocnice Ostrava, Klinika hematoonkologie

Ostrava, 70852, Czechia

Location

Fakulti nemocnice Kralovske Vinohrady, Internf hematologicka klinika FNKV a 3. LF UK

Prague, 100 34, Czechia

Location

Vseobecna fakultni nemocnice v Praze, Fakultni poliklinika, Hematologicka ambulance

Prague, 128 08, Czechia

Location

CHU Amiens Picardie

Amiens, 80054, France

Location

CHU d'Angers

Angers, 49033, France

Location

Hopital Avicenne

Bobigny, 93000, France

Location

Hopitaux Universitaires Henri Mondor

Créteil, 94010, France

Location

Centre Hospitalier Universitaire Grenoble Alpes

La Tronche, 38700, France

Location

Centre Hospitalier de Versailles

Le Chesnay, 78157, France

Location

Hôpital Claude Huriez (CHRU de Lillle)

Lille, 59037, France

Location

Centre Leon Berard

Lyon, 69373, France

Location

Centre Hospitalier Universitaire Nantes - Hotel Dieu

Nantes, 44093, France

Location

Hopital Saint-Louis

Paris, 75010, France

Location

Centre Hospitalier Lyon-Sud (CHLS)

Pierre-Bénite, 69495, France

Location

Institut de Cancérologie Strasbourg Europe (ICANS)

Strasbourg, 67033, France

Location

Institut Universitaire du Cancer de Toulouse (IUCT)-Oncopole

Toulouse, 31059, France

Location

CHU de Nancy - Hopitaux de Brabois

Vandœuvre-lès-Nancy, 54500, France

Location

Charite - Universitatsmedizin Berlin, Campus Virchow Klinikum, Medizinische Klinik mit Schwerpunkt Hamatologie, Onkologie und Tumorimmunologie

Berlin, 13353, Germany

Location

Universitätsklinikum Bonn

Bonn, 53127, Germany

Location

Städtisches Klinikum Braunschweig GmbH Medizinische Klinik III/Hämatologie und Onkologie

Braunschweig, 38114, Germany

Location

Universitatsklinikum Dusseldorf, Klink fur Hamatologie, Onkologie und Klinische Immunologie

Düsseldorf, 40225, Germany

Location

Marien Hospital Dusseldorf GmbH, Klinik Fur Onkologie, Hamatologie Und Palliativmedizin

Düsseldorf, 40479, Germany

Location

Malteser Krankenhaus St. Franziskus Hospital,Med.Klinik I

Flensburg, 24939, Germany

Location

Universitatsklinikum Frankfurt Goethe Universitat Med. Klink II

Frankfurt, 60590, Germany

Location

Asklepios Klink St.Georg

Hamburg, 20099, Germany

Location

Medizinische Hochschule Hannover, Hamatologie, Hamostaseologie, Onkologie und Stammzelltrandsplantation

Hanover, 30625, Germany

Location

Universitätsklinikum Magdeburg

Magdeburg, 39120, Germany

Location

Johannes Wesling Klinikum Minden Universitätsklinik fur Hämatologie, Onkologie, Hämostaseologie und Pastativrndezin, Universitatsklinik der Ruhr-Unive

Minden, 32429, Germany

Location

Klinikum rechts der Isar Technischen Universitat Munchen

München, 81675, Germany

Location

Klinikum Oldenburg, Rahel-Straus-Straße 10

Oldenburg, 26133, Germany

Location

Universitatsklinikum Regensburg, Klink fur Innere Medizin III

Regensburg, 93053, Germany

Location

Universitatsklinikum Ulm, Zentrum fur Innere Medizin, Klinik fur Innere Medizin III

Ulm, 89070, Germany

Location

Department of Medicine and Therapeutics, The Chinese University of Hong Kong, Prince of Wales Hospital

Hong Kong, Hong Kong

Location

Princess Margaret Hospital

Hong Kong, Hong Kong

Location

Queen Mary Hospital

Hong Kong, Hong Kong

Location

Tuen Mun Hospital

Hong Kong, Hong Kong

Location

Semmelweis Egyetem Belgyogyaszati es Hematologiai Klinika

Budapest, 1083, Hungary

Location

Petz Aladár Egyetemi Oktató Kórház II. Belgyógyaszat - Haematológia

Győr, 9024, Hungary

Location

Debreceni Egyetem Klinikai Központ Belgyogyaszati Klinika B epulet Hematologia

Hajdu-bihar, 4032, Hungary

Location

Szegedi Tudomanyegyetem Szent-Gyorgyi Albert Kozpont

Szeged, 6725, Hungary

Location

Rambam Health Care Campus

Haifa, 31096, Israel

Location

Shaare Zedek Medical Center

Jerusalem, 9103102, Israel

Location

Hadassah University Hospital Ein Kerem

Jerusalem, 91120, Israel

Location

Rabin Medical Center

Petah Tikva, 49100, Israel

Location

The Chaim Sheba Medical Center

Ramat Gan, 52621, Israel

Location

Azienda Ospedaliero Universitaria delle Marche - SOD Clinica di Ematologia

Ancona, I-60126, Italy

Location

ASST Papa Giovanni XXIII

Bergamo, 24127, Italy

Location

Azienda Ospedaliero Universitaria di Bologna Policlinico Sant'Orsola-Malpighi

Bologna, 40138, Italy

Location

IRCCS Istituto Clinico Humanitas

Milan, 20089, Italy

Location

ASST Monza-Ospedale San Gerardo

Monza, 20052, Italy

Location

Azienda Ospedaliera di Perugia - Santa Maria della Misericordia

Perugia, Italy

Location

Azienda Sanitaria Territoriale Pesaro e Urbino - "Stabilimento Ospedaliero San Salvatore - Muraglia" - U.O. Ematologia e Centro Trapianti

Pesaro, 61122, Italy

Location

Jeroen Bosch Ziekenhuis

's-Hertogenbosch, 5223GZ, Netherlands

Location

Meander Medisch Centrum

Amersfoort, 3813 TZ, Netherlands

Location

Amsterdam Universitair Medische Centra-Locatie Vrije Universiteit Medisch Centrum

Amsterdam, 1081 HV, Netherlands

Location

Amphia Hospital, department Oncologie, Route 43

Breda, 4818 CK, Netherlands

Location

Medisch Spectrum Twente - Enschede Koningsplein

Enschede, 7512 KZ, Netherlands

Location

Universitair Medisch Centrum Groningen

Groningen, 9700 RB, Netherlands

Location

Medisch Centrum Leeuwarden

Leeuwarden, 8934 AD, Netherlands

Location

Masstricht Universitair Medisch Centrum

Maastricht, 62002, Netherlands

Location

St. Antonius Ziekenhuis, Nieuwegein

Nieuwegein, 3435 CM, Netherlands

Location

Canisius Wilhelmina Ziekenhuis

Nijmegen, 6532 SZ, Netherlands

Location

Erasmus Medisch Centrum

Rotterdam, 3000 CA, Netherlands

Location

HagaZiekenhuis

The Hague, 2545AA, Netherlands

Location

Oslo University Hospital, Department of Hematology

Oslo, 0424, Norway

Location

Wojewódzkie Wielospecjalistyczne Centrum Onkologii i Traumatologii im. M.Kopernika w Lodzi, Oddzial Hematologii Ogolnej

Lodz, 93-510, Poland

Location

Centrum Onkologii Ziemi Lubelskiej im. Sw. Jana z Dukli, Oddzial Hematologiczny

Lublin, 20090, Poland

Location

Szpital Wojewodozki w Opolu Sp. z 0.0. Oddzial Klinixzny Hematologii, Onkologii Hematologicznej i Chorob Wemnetrznych

Opole, 45-372, Poland

Location

Seoul National University Hospital

Seoul, 03080, South Korea

Location

Samsung Medical Center

Seoul, 06351, South Korea

Location

Severance Hospital

Seoul, 120-752, South Korea

Location

Asan Medical Center

Seoul, 138-736, South Korea

Location

The Catholic University of Korea Seoul Saint Mary's Hospital

Seoul, 6591, South Korea

Location

Hospital Universitario Araba

Alava, Spain

Location

Hospital Clinic de Barcelona

Barcelona, 08036, Spain

Location

Hospital Universitario Reina Sofia

Córdoba, 14004, Spain

Location

Hospital General Universitario Gregorio Maranon

Madrid, 28009, Spain

Location

Hospital Universitario 12 de Octubre

Madrid, 28041, Spain

Location

Hospital Universitario La Paz

Madrid, 28041, Spain

Location

Hospital Universitario Quironsalud Madrid

Madrid, Spain

Location

Hospital Universitario Ramon y Cajal

Madrid, Spain

Location

Hospital Regional Universitario de Malaga

Málaga, 29010, Spain

Location

Complejo Asistencial Universitario de Salamanca - Hospital Clinico

Salamanca, 37007, Spain

Location

Complejo Hospitalario Universitario de Santiago de Compostela

Santiago de Compostela, 15706, Spain

Location

Hospital Universitari I Politecnic La Fe

Valencia, 46026, Spain

Location

Inselspital Universitätsspital Bern

Bern, 3010, Switzerland

Location

Kaohsiung Chang Gung Memorial Hospital

Kaohsiung City, 83301, Taiwan

Location

China Medical University Hospital

Taichung, 404, Taiwan

Location

National Taiwan University Hospital

Taipei, 10002, Taiwan

Location

National Cheng Kung University Hospital

Taipei, 11490, Taiwan

Location

Blackpool Teaching Hospitals NHS Foundation Trust

Blackpool, FY3 8NR, United Kingdom

Location

University Hospitals Bristol and Weston NHS Foundation Trust

Bristol, BS2 8ED, United Kingdom

Location

Leeds Teaching Hospitals NHS Trust

Leeds, LS9 7TF, United Kingdom

Location

Clatterbridge Cancer Centre NHS Foundation Trust

Liverpool, L7 8YA, United Kingdom

Location

Barts Health NHS Trust

London, EC1A 7BE, United Kingdom

Location

King's College Hospital

London, SE5 9RS, United Kingdom

Location

The Christie NHS Foundation Trust

Manchester, M20 4BX, United Kingdom

Location

Newcastle upon Tyne Hospitals Foundation Trust

Newcastle upon Tyne, NE7 7DN, United Kingdom

Location

Oxford University Hospitals NHS Foundation Trust, Churchill Hospital

Oxford, OX3 7LE, United Kingdom

Location

South Warwickshire University NHS Foundation Trust

Warwick, CV34 5BW, United Kingdom

Location

The Royal Wolverhampton NHS Trust

Wolverhampton, WV10 0QP, United Kingdom

Location

Related Publications (2)

  • Daver N, Vyas P, Huls G, Dohner H, Maury S, Novak J, Papayannidis C, Martinez Chamorro C, Montesinos P, Niroula R, Fenaux P, Esteve J, Wu SJ, De Voeght A, Mayer J, Valk PJM, Johnson L, Dong M, Liu K, Kuwahara S, Caldwell K, Guru Murthy GS. The ENHANCE-3 study: venetoclax and azacitidine plus magrolimab or placebo for untreated AML unfit for intensive therapy. Blood. 2025 Jul 31;146(5):601-611. doi: 10.1182/blood.2024027506.

  • Daver NG, Vyas P, Kambhampati S, Al Malki MM, Larson RA, Asch AS, Mannis G, Chai-Ho W, Tanaka TN, Bradley TJ, Jeyakumar D, Wang ES, Sweet K, Kantarjian HM, Garcia-Manero G, Komrokji R, Xing G, Ramsingh G, Renard C, Zeidner JF, Sallman DA. Tolerability and Efficacy of the Anticluster of Differentiation 47 Antibody Magrolimab Combined With Azacitidine in Patients With Previously Untreated AML: Phase Ib Results. J Clin Oncol. 2023 Nov 1;41(31):4893-4904. doi: 10.1200/JCO.22.02604. Epub 2023 Sep 13.

Related Links

MeSH Terms

Conditions

Leukemia, Myeloid, Acute

Interventions

magrolimabvenetoclaxAzacitidine

Condition Hierarchy (Ancestors)

Leukemia, MyeloidLeukemiaNeoplasms by Histologic TypeNeoplasmsHematologic DiseasesHemic and Lymphatic Diseases

Intervention Hierarchy (Ancestors)

Aza CompoundsOrganic ChemicalsCytidinePyrimidine NucleosidesPyrimidinesHeterocyclic Compounds, 1-RingHeterocyclic CompoundsNucleosidesNucleic Acids, Nucleotides, and NucleosidesRibonucleosides

Results Point of Contact

Title
Gilead Clinical Study Information Center
Organization
Gilead Sciences

Study Officials

  • Gilead Study Director

    Gilead Sciences

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
DOUBLE
Who Masked
PARTICIPANT, INVESTIGATOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR
Expanded Access
Yes

Study Record Dates

First Submitted

October 4, 2021

First Posted

October 15, 2021

Study Start

July 7, 2022

Primary Completion

April 11, 2024

Study Completion

April 11, 2024

Last Updated

April 4, 2025

Results First Posted

April 4, 2025

Record last verified: 2025-04

Data Sharing

IPD Sharing
Will not share

Locations