NCT04877522

Brief Summary

This is a long term safety study for patients who have completed a Novartis sponsored asciminib study and are judged by the investigator to benefit from continued treatment

Trial Health

88
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
347

participants targeted

Target at P75+ for phase_4

Timeline
52mo left

Started Aug 2022

Longer than P75 for phase_4

Geographic Reach
29 countries

84 active sites

Status
recruiting

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Progress46%
Aug 2022Aug 2030

First Submitted

Initial submission to the registry

May 4, 2021

Completed
3 days until next milestone

First Posted

Study publicly available on registry

May 7, 2021

Completed
1.3 years until next milestone

Study Start

First participant enrolled

August 30, 2022

Completed
8 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

August 29, 2030

Expected
1 day until next milestone

Study Completion

Last participant's last visit for all outcomes

August 30, 2030

Last Updated

March 6, 2026

Status Verified

March 1, 2026

Enrollment Period

8 years

First QC Date

May 4, 2021

Last Update Submit

March 5, 2026

Conditions

Keywords

Chronic Myelogenous LeukemiaCMLALLCML-APCML-BPCML-CPmyeloproliferative neoplasmchronic phaseaccelerated phaseblast phaseABL001asciminib

Outcome Measures

Primary Outcomes (1)

  • Number of participants with adverse events (AEs) and serious adverse events (SAEs)

    All AEs and SAEs will be tabulated and listed for participants in the Safety Set by treatment group. From day of first administration of study treatment to 30 days after the last study treatment.

    8 years

Secondary Outcomes (1)

  • Percentage of participants with clinical benefit as assessed by Investigator

    8 years

Study Arms (11)

Asciminib single agent group

EXPERIMENTAL

Participants with CML or ALL, from Novartis sponsored asciminib studies, including but not limited to CABL001A2301, CABL001A2302, CABL001X2101, CABL001A2202, CABL001AUS04 and CABL001AUS08 studies, that were receiving asciminib

Drug: Asciminib single agent

Bosutinib single agent group

OTHER

Participants with CML-CP, from Novartis sponsored asciminib study CABL001A2301, that were receiving bosutinib

Drug: Bosutinib

Bosutinib-Asciminib switch group

EXPERIMENTAL

Participants with CML-CP, from Novartis sponsored asciminib study CABL001A2301 that were receiving bosutinib treatment and switched to asciminib when entering this study or during the course of this study

Drug: Asciminib single agent

Asciminib in combination with imatinib group

EXPERIMENTAL

Participants with CML from Novartis sponsored asciminib studies CABL001E2201 or CABL001X2101 that were receiving asciminib combined with imatinib

Drug: Imatinib

Asciminib in combination with nilotinib group

EXPERIMENTAL

Participants with CML or ALL from Novartis sponsored asciminib studies CABL001E2201or CABL001X2101 that were receiving asciminib combined with nilotinib

Drug: Nilotinib

Imatinib single agent group

OTHER

Participants with CML-CP, from Novartis sponsored asciminib study CABL001E2201 that were receiving imatinib

Drug: Imatinib

Nilotinib single agent group

OTHER

Participants with CML-CP, from Novartis sponsored asciminib study CABL001E2201 and CABL001J12302 that were receiving nilotinib

Drug: Nilotinib

Asciminib in combination with dasatinib group

EXPERIMENTAL

Participants with CML from Novartis sponsored study CABL001X2101 that were receiving asciminib with dasatinib

Drug: Dasatinib

Dasatinib single agent group

OTHER

Participant with CML-CP , from Novartis sponsored asciminib study CABL001A2202, CABL001J12301, that were receiving Dasatinib.

Drug: Dasatinib

Dasatinib-Asciminib switch group

EXPERIMENTAL

Participants with CML-CP, from Novartis sponsored asciminib study CABL001A2202 that were receiving best available therapy (dasatinib) and switched to asciminib when entering this study or during the course of this study

Drug: Asciminib single agent

Asciminib single agent formulation for Pediatric

EXPERIMENTAL

Participants with CML, from Novartis sponsored asciminib studies, including but not limited to CABL001I12201 study, that were receiving asciminib

Drug: Asciminib single agent pediatric formulation

Interventions

Taken orally, once daily, in the morning with low-fat meal

Also known as: STI571
Asciminib in combination with imatinib groupImatinib single agent group

Taken orally, twice daily (BID) or once daily (QD), in fasting state

Also known as: ABL001
Asciminib single agent groupBosutinib-Asciminib switch groupDasatinib-Asciminib switch group

Taken orally, twice daily, on an empty stomach

Also known as: AMN107
Asciminib in combination with nilotinib groupNilotinib single agent group

Taken orally, once daily, with food

Bosutinib single agent group

Taken orally, once daily in a fasted state, 1 or 2 hours before a meal

Also known as: Sprycel
Asciminib in combination with dasatinib groupDasatinib single agent group

Pediatric participants receive a body weight adjusted dose of 1.3 mg/kg of pediatric film coated granules with food twice daily (b.i.d.) or 2.6 mg/kg once daily (q.d.) in the morning.

Also known as: ABL001
Asciminib single agent formulation for Pediatric

Eligibility Criteria

Age7 Years - 100 Years
Sexall
Healthy VolunteersNo
Age GroupsChild (0-17), Adult (18-64), Older Adult (65+)

You may qualify if:

  • Participant with PH+ CML or PH+ ALL currently receiving treatment with asciminib (single agent or in combination with imatinib, nilotinib or dasatinib), imatinib, nilotinib or bosutinib alone within a Novartis-sponsored study and, in the opinion of the Investigator, would benefit from continued treatment.
  • Participant has demonstrated compliance on the parent study protocol and is willing and able to comply with scheduled visits, treatment plans and any other study procedures.

You may not qualify if:

  • Participant has been discontinued from parent study treatment.
  • Participant currently has unresolved toxicities reported as possibly related to study treatment in the parent study.
  • Participant's ongoing treatment is currently approved and reimbursed at country level.
  • Pregnant or nursing (lactating) women.
  • Women of child-bearing potential, unless they are using highly effective methods of contraception and willing to continue while taking study treatment.
  • Sexually active males receiving imatinib, nilotinib, bosutinib or dasatinib unwilling to follow the relevant contraception requirements in the local prescribing information.
  • Applicable for participants on bosutinib treatment at the end of the CABL001A2301 and on other TKIs for CABL001A2202 study that switch to asciminib treatment:
  • Asymptomatic (grade 2) pancreatitis if not resolved within 28 days
  • QTcF\>480msec or inability to determine QTc interval
  • any grade 3 or 4 toxicity not resolved to grade 2 or lower within 28 days before starting asciminib treatment

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (84)

Michigan Med University of Michigan

Ann Arbor, Michigan, 48109 5271, United States

RECRUITING

Memorial Sloan Kettering

New York, New York, 10017, United States

RECRUITING

Oregon Health Sciences University

Portland, Oregon, 97239, United States

ACTIVE NOT RECRUITING

Texas Oncology

Dallas, Texas, 75251, United States

RECRUITING

Uni Of TX MD Anderson Cancer Cntr

Houston, Texas, 77030, United States

RECRUITING

Novartis Investigative Site

CABA, Buenos Aires, C1221ADC, Argentina

RECRUITING

Novartis Investigative Site

Capital Federal, C1114AAN, Argentina

RECRUITING

Novartis Investigative Site

Graz, 8036, Austria

RECRUITING

Novartis Investigative Site

Vienna, 1140, Austria

RECRUITING

Novartis Investigative Site

Rio de Janeiro, Rio de Janeiro, 20211-030, Brazil

RECRUITING

Novartis Investigative Site

São Paulo, São Paulo, 05403 000, Brazil

RECRUITING

Novartis Investigative Site

São Paulo, São Paulo, 08270-070, Brazil

RECRUITING

Novartis Investigative Site

Varna, 9000, Bulgaria

RECRUITING

Novartis Investigative Site

Montreal, Quebec, H1T 2M4, Canada

RECRUITING

Novartis Investigative Site

Chongqing, Chongqing Municipality, 400010, China

RECRUITING

Novartis Investigative Site

Guangzhou, Guangdong, 510515, China

RECRUITING

Novartis Investigative Site

Zhengzhou, Henan, 450008, China

RECRUITING

Novartis Investigative Site

Wuhan, Hubei, 430022, China

RECRUITING

Novartis Investigative Site

Changchun, Jilin, 130021, China

RECRUITING

Novartis Investigative Site

Xian, Shanxi, 710004, China

RECRUITING

Novartis Investigative Site

Chengdu, Sichuan, 610041, China

COMPLETED

Novartis Investigative Site

Beijing, 100044, China

ACTIVE NOT RECRUITING

Novartis Investigative Site

Beijing, 100730, China

RECRUITING

Novartis Investigative Site

Shanghai, 200025, China

ACTIVE NOT RECRUITING

Novartis Investigative Site

Shenyang, 110004, China

RECRUITING

Novartis Investigative Site

Tianjin, 300020, China

RECRUITING

Novartis Investigative Site

Ostrava, Poruba, 708 52, Czechia

RECRUITING

Novartis Investigative Site

Brno, 625 00, Czechia

RECRUITING

Novartis Investigative Site

Copenhagen, DK-2100, Denmark

COMPLETED

Novartis Investigative Site

Bordeaux, 33076, France

RECRUITING

Novartis Investigative Site

Lyon, 69373, France

RECRUITING

Novartis Investigative Site

Marseille, 13273, France

RECRUITING

Novartis Investigative Site

Nantes, 44093, France

RECRUITING

Novartis Investigative Site

Paris, 75475, France

RECRUITING

Novartis Investigative Site

Vandœuvre-lès-Nancy, 54511, France

RECRUITING

Novartis Investigative Site

Frankfurt am Main, Hesse, 60590, Germany

RECRUITING

Novartis Investigative Site

Jena, Thuringia, 07740, Germany

RECRUITING

Novartis Investigative Site

Berlin, 13353, Germany

RECRUITING

Novartis Investigative Site

Kiel, 24116, Germany

RECRUITING

Novartis Investigative Site

Milan, MI, 20162, Italy

RECRUITING

Novartis Investigative Site

Roma, RM, 00161, Italy

RECRUITING

Novartis Investigative Site

Naples, 80131, Italy

COMPLETED

Novartis Investigative Site

Kobe, 650-0017, Japan

ACTIVE NOT RECRUITING

Novartis Investigative Site

Beirut, 113-0236, Lebanon

COMPLETED

Novartis Investigative Site

George Town, Pulau Pinang, 10450, Malaysia

RECRUITING

Novartis Investigative Site

Johor Bahru, 80100, Malaysia

RECRUITING

Novartis Investigative Site

Kuala Selangor, 68000, Malaysia

RECRUITING

Novartis Investigative Site

Monterrey, Nuevo León, 64460, Mexico

RECRUITING

Novartis Investigative Site

Khoudh, 123, Oman

RECRUITING

Novartis Investigative Site

Katowice, 40-519, Poland

RECRUITING

Novartis Investigative Site

Krakow, 30-688, Poland

COMPLETED

Novartis Investigative Site

Warsaw, 00-791, Poland

RECRUITING

Novartis Investigative Site

Wroclaw, 50 367, Poland

COMPLETED

Novartis Investigative Site

Lisbon, 1099-023, Portugal

ACTIVE NOT RECRUITING

Novartis Investigative Site

Porto, 4200-072, Portugal

RECRUITING

Novartis Investigative Site

Timișoara, 300079, Romania

RECRUITING

Novartis Investigative Site

Moscow, 125167, Russia

ACTIVE NOT RECRUITING

Novartis Investigative Site

Moscow, 125284, Russia

ACTIVE NOT RECRUITING

Novartis Investigative Site

Saint Petersburg, 191024, Russia

RECRUITING

Novartis Investigative Site

Saint Petersburg, 197341, Russia

RECRUITING

Novartis Investigative Site

Riyadh, 11211, Saudi Arabia

COMPLETED

Novartis Investigative Site

Singapore, 169608, Singapore

ACTIVE NOT RECRUITING

Novartis Investigative Site

Uijeongbu-si, Gyeonggi-do, 11759, South Korea

ACTIVE NOT RECRUITING

Novartis Investigative Site

Seoul, Korea, 03080, South Korea

RECRUITING

Novartis Investigative Site

Busan, 49201, South Korea

COMPLETED

Novartis Investigative Site

Jeollanam, 519763, South Korea

COMPLETED

Novartis Investigative Site

Santiago Compostela, A Coruna, 15706, Spain

RECRUITING

Novartis Investigative Site

Badalona, Barcelona, 08916, Spain

RECRUITING

Novartis Investigative Site

L'Hospitalet de Llobregat, Barcelona, 08907, Spain

RECRUITING

Novartis Investigative Site

Bilbao, Bizkaia, 48013, Spain

RECRUITING

Novartis Investigative Site

Santa Cruz, Santa Cruz De Tenerife, 38009, Spain

RECRUITING

Novartis Investigative Site

Barcelona, 08035, Spain

RECRUITING

Novartis Investigative Site

Barcelona, 08036, Spain

RECRUITING

Novartis Investigative Site

Madrid, 28006, Spain

RECRUITING

Novartis Investigative Site

Madrid, 28034, Spain

COMPLETED

Novartis Investigative Site

Madrid, 28041, Spain

RECRUITING

Novartis Investigative Site

Seville, 41009, Spain

RECRUITING

Novartis Investigative Site

Valencia, 46026, Spain

RECRUITING

Novartis Investigative Site

Taoyuan District, 33305, Taiwan

ACTIVE NOT RECRUITING

Novartis Investigative Site

Samsun, Atakum, 55200, Turkey (Türkiye)

RECRUITING

Novartis Investigative Site

London, W12 0HS, United Kingdom

RECRUITING

Novartis Investigative Site

Oxford, OX3 7LE, United Kingdom

RECRUITING

Novartis Investigative Site

Hanoi, 100000, Vietnam

RECRUITING

Novartis Investigative Site

Ho Chi Minh City, 70000, Vietnam

RECRUITING

MeSH Terms

Conditions

Leukemia, Myelogenous, Chronic, BCR-ABL PositiveMyeloproliferative DisordersBlast Crisis

Interventions

asciminibImatinib MesylatenilotinibbosutinibDasatinib

Condition Hierarchy (Ancestors)

Leukemia, MyeloidLeukemiaNeoplasms by Histologic TypeNeoplasmsBone Marrow DiseasesHematologic DiseasesHemic and Lymphatic DiseasesChronic DiseaseDisease AttributesPathologic ProcessesPathological Conditions, Signs and SymptomsCell Transformation, NeoplasticCarcinogenesisNeoplastic Processes

Intervention Hierarchy (Ancestors)

BenzamidesAmidesOrganic ChemicalsBenzoatesAcids, CarbocyclicCarboxylic AcidsBenzene DerivativesHydrocarbons, AromaticHydrocarbons, CyclicHydrocarbonsPiperazinesHeterocyclic Compounds, 1-RingHeterocyclic CompoundsPyrimidinesThiazolesSulfur CompoundsAzoles

Study Officials

  • Novartis Pharmaceuticals

    Novartis Pharmaceuticals

    STUDY DIRECTOR

Central Study Contacts

Novartis Pharmaceuticals

CONTACT

Novartis Pharmaceuticals

CONTACT

Study Design

Study Type
interventional
Phase
phase 4
Allocation
NON RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR
Expanded Access
Yes

Study Record Dates

First Submitted

May 4, 2021

First Posted

May 7, 2021

Study Start

August 30, 2022

Primary Completion (Estimated)

August 29, 2030

Study Completion (Estimated)

August 30, 2030

Last Updated

March 6, 2026

Record last verified: 2026-03

Data Sharing

IPD Sharing
Will share

Novartis is committed to sharing with qualified external researchers, access to patient-level data and supporting clinical documents from eligible studies. These requests are reviewed and approved by an independent review panel on the basis of scientific merit. All data provided is anonymized to respect the privacy of patients who have participated in the trial in line with applicable laws and regulations. This trial data availability is according to the criteria and process described on www.clinicalstudydatarequest.com

Shared Documents
CSR

Locations