NCT04784715

Brief Summary

The study will evaluate the efficacy and safety of trastuzumab deruxtecan (also known as T-DXd, DS-8201a), either alone or in combination with pertuzumab, in treating patients with Human epidermal growth factor receptor 2 (HER2)-positive breast cancer as a first line of treatment in the metastatic setting.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Strong global presence with extensive site network
Enrollment
1,157

participants targeted

Target at P75+ for phase_3

Timeline
45mo left

Started Apr 2021

Longer than P75 for phase_3

Geographic Reach
27 countries

283 active sites

Status
active not recruiting

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Progress58%
Apr 2021Dec 2029

First Submitted

Initial submission to the registry

February 19, 2021

Completed
14 days until next milestone

First Posted

Study publicly available on registry

March 5, 2021

Completed
2 months until next milestone

Study Start

First participant enrolled

April 26, 2021

Completed
5.2 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

July 6, 2026

Expected
3.5 years until next milestone

Study Completion

Last participant's last visit for all outcomes

December 30, 2029

Last Updated

February 20, 2026

Status Verified

February 1, 2026

Enrollment Period

5.2 years

First QC Date

February 19, 2021

Last Update Submit

February 18, 2026

Conditions

Keywords

Breast Neoplasms; Breast Diseases; Trastuzumab; Antineoplastic Agents, Phytogenic; Anti-drug conjugate; Molecular Mechanisms of Pharmacological Action;

Outcome Measures

Primary Outcomes (1)

  • Progression Free Survival (PFS) by Blinded Independent Central Review (BICR) assessment

    Defined as time from date of randomisation until the date of objective radiological disease progression according to Blinded Independent Central Review (BICR) using RECIST 1.1 or death by any cause.

    Until progression or death, assessed up to approximately 60 months

Secondary Outcomes (14)

  • Progression Free Survival (PFS) by Investigator assessment

    Until progression or death, assessed up to approximately 60 months

  • Overall Survival (OS)

    Until death, assessed up to approximately 104 months

  • Objective Response Rate (ORR) by BICR and Investigator assessment

    Until progression or death (in the absence of progression), assessed up to approximately 60 months

  • Duration of Response (DoR) by BICR and Investigator Assessment

    Until progression or death (in the absence of progression), assessed up to approximately 60 months

  • Time to second progression or death (PFS2) by Investigator assessment

    Assessed up to approximately 104 months

  • +9 more secondary outcomes

Study Arms (3)

Arm A

EXPERIMENTAL

Trastuzumab deruxtecan (T-DXd) plus pertuzumab-matching placebo

Drug: Trastuzumab deruxtecanDrug: Placebo

Arm B

EXPERIMENTAL

Trastuzumab deruxtecan (T-DXd) plus pertuzumab

Drug: Trastuzumab deruxtecanDrug: Pertuzumab

Arm C

ACTIVE COMPARATOR

Standard of care (Taxane (paclitaxel or docetaxel), trastuzumab, and pertuzumab)

Drug: TaxaneDrug: PertuzumabDrug: Trastuzumab

Interventions

Administered by intravenous infusion

Also known as: DS-8201a; T-DXd
Arm AArm B

Administered by intravenous infusion

Arm A
TaxaneDRUG

Investigator's choice of docetaxel or paclitaxel administered by intravenous infusion

Arm C

Administered by intravenous infusion

Arm BArm C

Administered by intravenous infusion

Arm C

Eligibility Criteria

Age18 Years - 130 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Patients must be ≥18 years of age
  • Pathologically documented breast cancer that:
  • is advanced or metastatic
  • is locally assessed and prospectively centrally confirmed as HER2-positive (IHC3+ or ISH+)
  • is documented by local testing as hormone receptor (HR)-positive or HR-negative disease in the metastatic setting
  • No prior chemotherapy or HER2-targeted therapy for advanced or metastatic breast cancer or only 1 previous line of endocrine therapy in the metastatic setting. Participants who have received chemotherapy or HER2-targeted therapy in the neo-adjuvant or adjuvant setting are eligible if \> 6 months from treatment to metastatic diagnosis.
  • Has protocol-defined adequate organ and bone marrow function
  • ECOG performance status 0 or 1

You may not qualify if:

  • Ineligible for any of the agents on the study.
  • Any substance abuse or other medical conditions that, in the investigator's opinion, may interfere with subject's participation or study results
  • Patients with spinal cord compression or clinically active central nervous system metastases. Participants with clinically inactive brain metastases or treated brain metastases that are no longer symptomatic may be included in the study.
  • Active or prior documented interstitial lung disease (ILD)/pneumonitis or suspected ILD/pneumonitis that cannot be ruled out by imaging at screening
  • Prior randomization or treatment in a previous trastuzumab deruxtecan study regardless of treatment arm assignment

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (283)

Research Site

Tucson, Arizona, 85711, United States

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Springdale, Arkansas, 72762, United States

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Glendale, California, 91204, United States

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Glendale, California, 91206, United States

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Longmont, Colorado, 80501, United States

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Miami, Florida, 33176, United States

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Palm Bay, Florida, 32909, United States

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Plantation, Florida, 33324, United States

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Atlanta, Georgia, 30318, United States

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Louisville, Kentucky, 40241, United States

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Silver Spring, Maryland, 20904, United States

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Boston, Massachusetts, 02215, United States

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Detroit, Michigan, 48202, United States

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Jackson, Mississippi, 39213, United States

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Las Vegas, Nevada, 89128, United States

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Summit, New Jersey, 07901, United States

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New York, New York, 10065, United States

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Shirley, New York, 11967, United States

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York, Pennsylvania, 17403, United States

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Germantown, Tennessee, 38138, United States

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Dallas, Texas, 75203, United States

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Dallas, Texas, 75246, United States

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Denton, Texas, 76201, United States

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Houston, Texas, 77090, United States

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San Antonio, Texas, 78240, United States

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Shenandoah, Texas, 77380, United States

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Tyler, Texas, 75702, United States

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Norfolk, Virginia, 23502, United States

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Roanoke, Virginia, 24014, United States

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Tacoma, Washington, 98405, United States

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Buenos Aires, C1125ABD, Argentina

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CABA, 1414, Argentina

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CABA, C1012AAR, Argentina

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Caba, C1118AAT, Argentina

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Capital Federal, C1417DTB, Argentina

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Cipolletti, 8234, Argentina

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Ciudad de Buenos Aires, 1280, Argentina

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La Plata, 1900, Argentina

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Mar del Plata, 7600, Argentina

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Rosario, S2000DEJ, Argentina

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Rosario, S2002KDS, Argentina

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San Salvador de Jujuy, 4600, Argentina

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Brussels, 1160, Belgium

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Brussels, 1200, Belgium

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Charleroi, 6060, Belgium

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Edegem, 2650, Belgium

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Ghent, 9000, Belgium

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Leuven, 3000, Belgium

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Liège, 4000, Belgium

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Namur, 5000, Belgium

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Florianópolis, 88034-000, Brazil

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Goiânia, 74000-000, Brazil

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Londrina, 86015-520, Brazil

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Natal, 59075-740, Brazil

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Porto Alegre, 90035-003, Brazil

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Ribeirão Preto, 14015-130, Brazil

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São Paulo, 03102-002, Brazil

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Sorocaba, 18030-005, Brazil

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Vitória, 29043-260, Brazil

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Calgary, Alberta, T2N 5G2, Canada

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Halifax, Nova Scotia, B3H 2Y9, Canada

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Barrie, Ontario, L4M 6M2, Canada

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Kitchener, Ontario, N2G 1G3, Canada

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Newmarket, Ontario, L3Y 2P9, Canada

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North York, Ontario, M2K 1E1, Canada

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Toronto, Ontario, M5G 1X5, Canada

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Montreal, Quebec, H1T 2M4, Canada

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Montreal, Quebec, H2X 3E4, Canada

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Montreal, Quebec, H3T 1M5, Canada

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Montreal, Quebec, H4A 3J1, Canada

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Ste-Foy, Quebec, G1V 4G2, Canada

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Saskatoon, Saskatchewan, S7N 4H4, Canada

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Beijing, 100039, China

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Beijing, 100044, China

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Beijing, 100191, China

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Changchun, 130021, China

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Changsha, 410008, China

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Changsha, 410013, China

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Chengdu, 610041, China

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Chongqing, 400016, China

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Chongqing, 400030, China

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Dalian, 116011, China

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Guangzhou, 510060, China

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Guangzhou, 510080, China

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Guangzhou, 510120, China

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Hangzhou, 310003, China

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Hangzhou, 310022, China

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Harbin, 150049, China

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Kunming, 650118, China

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Nanchang, 330009, China

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Nanjing, 210008, China

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Nanjing, 210029, China

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Nanning, 530021, China

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Qingdao, 266100, China

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Shanghai, 200025, China

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Shanghai, 200032, China

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Shenyang, 110001, China

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Shenzhen, 518036, China

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Tianjin, 300060, China

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Wuhan, 430022, China

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Wuhan, 430030, China

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Wuhan, 430060, China

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Xi'an, 710004, China

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Xi'an, 710061, China

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Yinchuan, 750004, China

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Zhengzhou, 450008, China

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Copenhagen O, 2100, Denmark

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Sønderborg, 6400, Denmark

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Vejle, 7100, Denmark

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Avignon, 84000, France

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Besançon, 25000, France

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Bordeaux, 33030, France

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Caen, 14076, France

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Le Mans, 72000, France

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Montpellier, 34070, France

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Montpellier, 34298, France

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Nice, 06189, France

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Paris, 75005, France

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Pierre-Bénite, 69495, France

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Rennes, 35042, France

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Saint-Cloud, 92210, France

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Saint-Herblain, 44805, France

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Toulouse, 31059, France

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Vandœuvre-lès-Nancy, 54519, France

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Berlin, 10117, Germany

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Dresden, 1307, Germany

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Erlangen, 91054, Germany

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Essen, 45136, Germany

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Frankfurt am Main, 60431, Germany

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Freiburg im Breisgau, 79110, Germany

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Hamburg, 20357, Germany

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Heidelberg, 69120, Germany

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Leipzig, 04103, Germany

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Münster, 48149, Germany

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Paderborn, 33161, Germany

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Budapest, 1062, Hungary

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Budapest, 1082, Hungary

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Budapest, 1115, Hungary

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Budapest, 1122, Hungary

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Budapest, 1145, Hungary

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Győr, 9024, Hungary

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Kecskemét, 6000, Hungary

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Nyíregyháza, 4400, Hungary

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Szolnok, 5000, Hungary

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Ahmedabad, 380060, India

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Bangalore, 560027, India

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Bengaluru, 560099, India

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Calicut, 673601, India

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Gūrgaon, 122001, India

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Mysuru, 570017, India

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Nashik, 422009, India

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Nashik, 422011, India

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New Delhi, 110075, India

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New Delhi, 110085, India

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Haifa, 31096, Israel

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Jerusalem, 9112001, Israel

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Petah Tikva, 4941492, Israel

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Ramat Gan, 5266202, Israel

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Tel Aviv, 64239, Israel

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Bergamo, 24127, Italy

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Candiolo, 10060, Italy

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Genova, 16132, Italy

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Livorno, 57100, Italy

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Milan, 20141, Italy

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Naples, 80131, Italy

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Padua, 35128, Italy

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Rozzano, 20089, Italy

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Udine, 33100, Italy

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Akashi-shi, 673-8558, Japan

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Aomori, 030-8553, Japan

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Bunkyō City, 113-8431, Japan

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Chiba, 260-8717, Japan

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Chūōku, 104-0045, Japan

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Fukushima, 960-1295, Japan

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Hidaka-shi, 350-1298, Japan

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Hiroshima, 730-8518, Japan

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Hiroshima, 734-8551, Japan

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Isehara-shi, 259-1193, Japan

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Kagoshima, 892-0833, Japan

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Kawasaki-shi, 216-8511, Japan

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Kobe, 650-0047, Japan

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Kōtoku, 135-8550, Japan

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Kurume-shi, 830-0011, Japan

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Kyoto, 606-8507, Japan

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Matsuyama, 791-0280, Japan

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Nagoya, 464-8681, Japan

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Nagoya, 467-8602, Japan

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Niigata, 951-8566, Japan

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Nishinomiya-shi, 663-8501, Japan

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Okayama, 700-8558, Japan

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Osaka, 541-8567, Japan

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Ota-shi, 373-8550, Japan

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Sapporo, 003-0804, Japan

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Sendai, 980-8574, Japan

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Shinagawa-ku, 142-8666, Japan

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Shinjuku-ku, 160-0023, Japan

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Shinjuku-ku, 162-8655, Japan

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Shizuoka, 420-8527, Japan

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Tsu, 514-8507, Japan

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Yokohama, 241-8515, Japan

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Alc. Cuauhtémoc, 06700, Mexico

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Estado de México, 50080, Mexico

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Guadalajara, 44680, Mexico

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Metepec, 52140, Mexico

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Nuevo León, 66278, Mexico

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Veracruz, 91910, Mexico

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Arequipa, AREQUIPA01, Peru

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Lima, 15033, Peru

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Lima, 15036, Peru

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Lima, LIMA 29, Peru

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Lima, LIMA 34, Peru

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Baguio City, 2600, Philippines

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Cebu City, 6000, Philippines

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Davao City, 8000, Philippines

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Iloilo City, 5000, Philippines

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Manila, 1000, Philippines

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Quezon City, 1112, Philippines

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San Juan City, 1500, Philippines

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Bucharest, 011461, Romania

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Floreşti, 407280, Romania

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Moscow, 121205, Russia

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Moscow, 129090, Russia

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Moscow, 143442, Russia

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Saint Petersburg, 190020, Russia

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Saint Petersburg, 197758, Russia

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Yaroslavl, 150054, Russia

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Dammam, 31444, Saudi Arabia

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Jeddah, 22384, Saudi Arabia

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Jeddah, 23214, Saudi Arabia

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Riyadh, 11211, Saudi Arabia

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Riyadh, 11426, Saudi Arabia

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Cape Town, 7570, South Africa

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Cape Town, 7925, South Africa

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George, 6529, South Africa

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Johannesburg, 2193, South Africa

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Johannesburg, 2196, South Africa

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Port Elizabeth, 6045, South Africa

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Pretoria, 0081, South Africa

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Rondebosch, 7700, South Africa

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Soweto, 2013, South Africa

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Cheonan-si, 31151, South Korea

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Daegu, 41404, South Korea

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Goyang-si, 10408, South Korea

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Seoul, 03080, South Korea

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Seoul, 03722, South Korea

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Seoul, 05505, South Korea

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Seoul, 06273, South Korea

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Seoul, 06351, South Korea

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Seoul, 06591, South Korea

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Seoul, 08308, South Korea

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Alicante, 03010, Spain

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Barcelona, 08028, Spain

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Barcelona, 08036, Spain

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Barcelona, 8035, Spain

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Madrid, 28041, Spain

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Madrid, 28046, Spain

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Majadahonda, 28222, Spain

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Seville, 41009, Spain

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Gothenburg, 413 45, Sweden

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Örebro, 701 85, Sweden

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Stockholm, 118 83, Sweden

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Uppsala, 75185, Sweden

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Vaxjo, 35185, Sweden

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Taichung, 40443, Taiwan

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Tainan, 70403, Taiwan

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Taipei, 100, Taiwan

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Taipei, 10449, Taiwan

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Taipei, 11217, Taiwan

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Taipei, 235, Taiwan

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Taoyuan District, 333, Taiwan

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Adana, 01330, Turkey (Türkiye)

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Ankara, 06520, Turkey (Türkiye)

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Ankara, 06800, Turkey (Türkiye)

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Cordaleo, 35575, Turkey (Türkiye)

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Malatya, 44280, Turkey (Türkiye)

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Samsun, 55200, Turkey (Türkiye)

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Buckhurst Hill, IG9 5HX, United Kingdom

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Edinburgh, EH4 2XU, United Kingdom

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Guildford, GU2 7WG, United Kingdom

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London, NW1 2PG, United Kingdom

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Manchester, M20 4BX, United Kingdom

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Swansea, SA2 8QA, United Kingdom

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Taunton, TA1 5DA, United Kingdom

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Related Publications (1)

  • Tolaney SM, Jiang Z, Zhang Q, Barroso-Sousa R, Park YH, Rimawi MF, Saura C, Schneeweiss A, Toi M, Chae YS, Kemal Y, Chaudhari M, Sendur MAN, Yamashita T, Casalnuovo M, Danso MA, Liu J, Shetty J, Herbolsheimer P, Loibl S; DESTINY-Breast09 Trial Investigators. Trastuzumab Deruxtecan plus Pertuzumab for HER2-Positive Metastatic Breast Cancer. N Engl J Med. 2026 Feb 5;394(6):551-562. doi: 10.1056/NEJMoa2508668. Epub 2025 Oct 29.

Related Links

MeSH Terms

Conditions

Breast NeoplasmsNeoplasm MetastasisBreast Diseases

Interventions

trastuzumab deruxtecantaxanepertuzumabTrastuzumab

Condition Hierarchy (Ancestors)

Neoplasms by SiteNeoplasmsSkin DiseasesSkin and Connective Tissue DiseasesNeoplastic ProcessesPathologic ProcessesPathological Conditions, Signs and Symptoms

Intervention Hierarchy (Ancestors)

Antibodies, Monoclonal, HumanizedAntibodies, MonoclonalAntibodiesImmunoglobulinsImmunoproteinsBlood ProteinsProteinsAmino Acids, Peptides, and ProteinsSerum GlobulinsGlobulins

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
NONE
Masking Details
This study is open-label with respect to the control arm. Pertuzumab/placebo in the experimental arms will be blinded to the investigator and patients. The study will be "Sponsor-blind". To maintain the integrity of the study, Sponsor personnel directly involved in study conduct will not undertake or have access to efficacy data aggregated by treatment group prior to final data readout for the primary endpoint.
Purpose
TREATMENT
Intervention Model
PARALLEL
Model Details: Study will consist of three arms: Arm A - trastuzumab deruxtecan with pertuzumab-matching placebo Arm B - trastuzumab deruxtecan with pertuzumab Arm C - standard of care (taxane \[docetaxel or paclitaxel\], trastuzumab and pertuzumab)
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

February 19, 2021

First Posted

March 5, 2021

Study Start

April 26, 2021

Primary Completion (Estimated)

July 6, 2026

Study Completion (Estimated)

December 30, 2029

Last Updated

February 20, 2026

Record last verified: 2026-02

Data Sharing

IPD Sharing
Will share

Qualified researchers can request access to anonymized individual patient-level data from AstraZeneca group of companies sponsored clinical trials via the request portal. All request will be evaluated as per the AZ disclosure commitment: https://astrazenecagrouptrials.pharmacm.com/ST/Submission/Disclosure.

Shared Documents
STUDY PROTOCOL, SAP
Time Frame
AstraZeneca will meet or exceed data availability as per the commitments made to the EFPIA Pharma Data Sharing Principles. For details of our timelines, please rerefer to our disclosure commitment at https://astrazenecagrouptrials.pharmacm.com/ST/Submission/Disclosure.
Access Criteria
When a request has been approved AstraZeneca will provide access to the de-identified individual patient-level data in an approved sponsored tool . Signed Data Sharing Agreement (non-negotiable contract for data accessors) must be in place before accessing requested information. Additionally, all users will need to accept the terms and conditions of the SAS MSE to gain access. For additional details, please review the Disclosure Statements at https://astrazenecagrouptrials.pharmacm.com/ST/Submission/Disclosure.
More information

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