NCT04643886

Brief Summary

This study is designed to investigate the safety, PK/PD, biomarker and early clinical effects of repeat GEM103 IVT injections.

Trial Health

57
Monitor

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
62

participants targeted

Target at P50-P75 for phase_2

Timeline
Completed

Started Jul 2020

Geographic Reach
1 country

29 active sites

Status
terminated

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

July 30, 2020

Completed
4 months until next milestone

First Submitted

Initial submission to the registry

November 16, 2020

Completed
9 days until next milestone

First Posted

Study publicly available on registry

November 25, 2020

Completed
1.2 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

February 18, 2022

Completed
1 month until next milestone

Study Completion

Last participant's last visit for all outcomes

March 21, 2022

Completed
Last Updated

September 23, 2022

Status Verified

September 1, 2022

Enrollment Period

1.6 years

First QC Date

November 16, 2020

Last Update Submit

September 22, 2022

Conditions

Outcome Measures

Primary Outcomes (1)

  • Safety of intravitreal (IVT) injections of GEM103, as measured by number of subjects with ocular adverse events.

    18 months

Secondary Outcomes (2)

  • To describe the clinical effect of GEM103 IVT injection, as the change from baseline in best corrected visual acuity (BCVA) scores as assessed by ETDRS scale.

    6 months

  • To evaluate the total CFH levels in aqueous humor after GEM103 IVT injection, whenever possible.

    6 months

Study Arms (2)

Cohort with Genetic Profile A

EXPERIMENTAL

Subjects will have Genetic Profile A. Intervention: Biological: GEM103.

Drug: GEM103

Cohort with Genetic Profile B

EXPERIMENTAL

Subjects will have Genetic Profile B. Intervention: Biological: GEM103

Drug: GEM103

Interventions

GEM103DRUG

Biological

Cohort with Genetic Profile ACohort with Genetic Profile B

Eligibility Criteria

Age50 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • At least 50 years old at the time of signed informed consent.
  • Must have one of the following genetic profiles:
  • Genetic Profile A.
  • Genetic Profile B.
  • BCVA in the study eye of 24 to 83 letters using ETDRS Chart Visual Acuity (VA) Scale (approximately equivalent to Snellen VA of 20/25 to 20/320).
  • Confirmed diagnosis of GA in the study eye where total size of all GA lesions in the study eye must be within 0.5 to 15.01- and 7- disc areas.
  • Sufficiently clear ocular media and able to cooperate with ophthalmic visual function testing and anatomic assessment in the study eye.
  • Understands the full nature and purpose of the study and provides informed consent prior to initiation of any study procedure; all subjects with a reproductive potential must agree to use effective contraceptive methods through the end of study (EOS) Visit.

You may not qualify if:

  • Presence of the following ocular conditions - in the study eye:
  • Any history of exudative Age-related Macular Degeneration or choroidal neovascularization.
  • Any active ocular disease or condition that could confound the assessment of the macula or be a contraindication to IVT injection.
  • Any intraocular surgery, with the exception of stable intraocular lens replacement surgery more than 3 months prior to consent.
  • Aphakia or complete absence of the posterior capsule.
  • History of laser therapy to the macula or fundus or extensive laser to the retina.
  • Prior corneal transplant.
  • Presence of any of the following ocular conditions - in either eye:
  • History of herpetic infection.
  • Concurrent disease that could require medical or surgical intervention during the study period.
  • Active uveitis and/or vitritis (grade: trace or above).
  • History of idiopathic or autoimmune-associated uveitis.
  • Active blepharitis, conjunctivitis, keratitis, episcleritis, scleritis, or endophthalmitis.
  • Any ophthalmologic condition that reduces the clarity of the media and that, in the opinion of the Investigator, interferes with ophthalmologic examination.
  • In the opinion of the Investigator, the subject has any prior or ongoing medical condition (e.g., ocular other than dry AMD, systemic, psychiatric) or clinically significant screening laboratory value that may present a safety risk, interfere with study compliance or study follow-up, or confound data interpretation throughout the follow-up period.
  • +3 more criteria

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (29)

Gemini Clinical Trial Site

Phoenix, Arizona, 85020, United States

Location

Gemini Clinical Trial Site

Bakersfield, California, 93309, United States

Location

Gemini Clinical Trial Site

Beverly Hills, California, 90211, United States

Location

Gemini Clinical Trial Site

Oxnard, California, 93036, United States

Location

Gemini Clinical Trial Site

Poway, California, 92064, United States

Location

Gemini Clinical Trial Site

Santa Barbara, California, 93103, United States

Location

Gemini Clinical Trial Site

Santa Maria, California, 93454, United States

Location

Gemini Clinical Trial Site

Golden, Colorado, 80401, United States

Location

Gemini Clinical Trial Site

New London, Connecticut, 06320, United States

Location

Gemini Clinical Trial Site

Palm Beach Gardens, Florida, 33410, United States

Location

Gemini Clinical Trial Site

St. Petersburg, Florida, 33711, United States

Location

Gemini Clinical Trial Site

Tallahassee, Florida, 32308, United States

Location

Gemini Clinical Trial Site

Winter Haven, Florida, 33880, United States

Location

Gemini Clinical Trial Site

Augusta, Georgia, 30909, United States

Location

Gemini Clinical Trial Site

Marietta, Georgia, 30060, United States

Location

Gemini Clinical Trial Site

Oak Park, Illinois, 60304, United States

Location

Gemini Clinical Trial Site

Indianapolis, Indiana, 46290, United States

Location

Gemini Clinical Trial Site

Chesterfield, Missouri, 63017, United States

Location

Gemini Clinical Trial Site

St Louis, Missouri, 63144, United States

Location

Gemini Clinical Trial Site

Reno, Nevada, 89502, United States

Location

Gemini Clinical Trial Site

Bloomfield, New Jersey, 07003, United States

Location

Gemini Clinical Trial Site

Asheville, North Carolina, 28803, United States

Location

Gemini Clinical Trial Site

Charlotte, North Carolina, 28210, United States

Location

Gemini Clinical Trial Site

Eugene, Oregon, 97401, United States

Location

Gemini Clinical Trial Site

Rapid City, South Dakota, 57701, United States

Location

Gemini Clinical Trial Site

Abilene, Texas, 79606, United States

Location

Gemini Clinical Trial Site

Dallas, Texas, 75231, United States

Location

Gemini Clinical Trial Site

The Woodlands, Texas, 77384, United States

Location

Gemini Clinical Trial Site

Virginia Beach, Virginia, 23454, United States

Location

Related Publications (1)

  • Tzoumas N, Riding G, Williams MA, Steel DH. Complement inhibitors for age-related macular degeneration. Cochrane Database Syst Rev. 2023 Jun 14;6(6):CD009300. doi: 10.1002/14651858.CD009300.pub3.

MeSH Terms

Conditions

Geographic AtrophyMacular DegenerationRetinal DiseasesRetinal Degeneration

Condition Hierarchy (Ancestors)

Eye DiseasesEye Diseases, Hereditary

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

November 16, 2020

First Posted

November 25, 2020

Study Start

July 30, 2020

Primary Completion

February 18, 2022

Study Completion

March 21, 2022

Last Updated

September 23, 2022

Record last verified: 2022-09

Data Sharing

IPD Sharing
Will not share

Locations