NCT04401748

Brief Summary

Myelodysplastic Syndrome (MDS) is a group of disorders that gradually affect the ability of a person's bone marrow (semi-liquid tissue present in many bones like backbones) to produce normal blood cells. Some people with MDS have a risk of the disease progressing to acute myeloid leukemia (AML), and a risk of death from the disease itself. Symptoms of MDS include fatigue, shortness of breath, unusual paleness due to anemia (low red blood cell count), easy or unusual bruising, and red spots just beneath the skin caused by bleeding. The purpose of this study is to see how safe and effective venetoclax and azacitidine (AZA) combination are when compared to AZA and a placebo (contains no medicine), in participants with newly diagnosed higher-risk MDS. Venetoclax is an investigational drug being developed for the treatment of MDS. The study consists of two treatment arms - In one arm, participants will receive venetoclax and AZA. In another arm, participants will receive AZA and placebo. Adult participants with newly diagnosed higher-risk MDS will be enrolled. Around 500 participants will be enrolled in approximately 220 sites worldwide. Participants in one arm will receive oral doses of venetoclax tablet and intravenous (infusion in the vein) or subcutaneous (given under the skin) AZA solution. Participants in another arm will receive oral doses of placebo tablet and intravenous or subcutaneous AZA solution. There may be higher treatment burden for participants in this trial compared to their standard of care. Participants will attend regular visits during the course of the study at a hospital or clinic. The effect of the treatment will be checked by medical assessments, blood and bone marrow tests, checking for side effects, and completing questionnaires.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Strong global presence with extensive site network
Enrollment
531

participants targeted

Target at P75+ for phase_3

Timeline
14mo left

Started Sep 2020

Longer than P75 for phase_3

Geographic Reach
22 countries

215 active sites

Status
active not recruiting

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Progress83%
Sep 2020Jul 2027

First Submitted

Initial submission to the registry

May 22, 2020

Completed
4 days until next milestone

First Posted

Study publicly available on registry

May 26, 2020

Completed
4 months until next milestone

Study Start

First participant enrolled

September 10, 2020

Completed
6.8 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

July 1, 2027

Expected
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

July 1, 2027

Last Updated

May 6, 2026

Status Verified

May 1, 2026

Enrollment Period

6.8 years

First QC Date

May 22, 2020

Last Update Submit

May 1, 2026

Conditions

Keywords

MDSMyelodysplastic SyndromeVenetoclaxAzacitidineAZAVenclexta

Outcome Measures

Primary Outcomes (1)

  • Overall survival (OS)

    OS is defined as the number of days from the date of randomization to the date of death of any cause, or last known date to be alive.

    Up To 5 Years

Secondary Outcomes (7)

  • Modified Overall Response (mOR)

    Up To 5 Years

  • Percentage of Participants Achieving Overall Hematological Improvement (HI)

    Up to 5 Years

  • Complete Remission (CR)

    Up To 36 Months

  • Percentage of Participants Achieving Transfusion Independence (TI) Who are Transfusion Dependent at Baseline

    Up To 5 Years

  • Time to Deterioration in Physical Functioning as Measured by Physical Functioning Domain of the European Organisation for Research and Treatment of Cancer Quality of Life Questionnaire (EORTC QLQ-C30) Scale

    Up To 5 Years

  • +2 more secondary outcomes

Study Arms (2)

Arm 1: Venetoclax + Azacitidine (AZA)

EXPERIMENTAL

Participants will receive venetoclax once daily (QD) (Days 1-14) in combination with AZA QD (7 days of the first 9 days) of each 28 day cycle.

Drug: VenetoclaxDrug: Azacitidine

Arm 2: Placebo + Azacitidine

ACTIVE COMPARATOR

Participants will receive placebo once daily (QD) (Days 1-14) in combination with AZA QD (7 days of the first 9 days) of each 28 day cycle.

Drug: AzacitidineDrug: Placebo

Interventions

Tablet: Oral

Also known as: ABT-199, GDC-0199, Venclexta
Arm 1: Venetoclax + Azacitidine (AZA)

Subcutaneous (SC) or Intravenous (IV) injection

Also known as: AZA
Arm 1: Venetoclax + Azacitidine (AZA)Arm 2: Placebo + Azacitidine

Tablet; Oral

Arm 2: Placebo + Azacitidine

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Participants with a diagnosis of Myelodysplastic Syndrome (MDS) according to the 2016 World Health Organization (WHO) classification wtih presence of \< 20% bone marrow blasts per marrow biopsy/aspirate at screening.
  • Participants must meet the following disease activity criteria:
  • Overall Revised International Prognostic Scoring System (IPSS-R) score \> 3 (intermediate, high or very high).
  • Eastern Cooperative Oncology Group (ECOG) performance status of \<= 2.
  • Hematopoietic stem cell transplant (HSCT) eligible with no pre-arranged HSCT at the time of Study Day 1, or HSCT ineligible without plan for HSCT at the time of Study Day 1.

You may not qualify if:

  • Prior therapy for MDS with any hypomethylating agent, chemotherapy, or allogenic stem cell transplantation.
  • Prior diagnosis of therapy-related MDS (t-MDS), MDS evolving from a pre-existing myeloproliferative neoplasm (MPN), MDS/MPN including chronic myelomonocytic leukemia (CMML), atypical chronic myeloid leukemia (aCML), juvenile myelomonocytic leukemia (JMML) and unclassifiable MDS/MPN.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (220)

Duplicate_Providence Medical Foundation /ID# 222633

Fullerton, California, 92835, United States

Location

University of California, Los Angeles /ID# 221760

Los Angeles, California, 90095, United States

Location

Torrance Memorial Physician Network Cancer Care /ID# 222702

Torrance, California, 90505-5004, United States

Location

PIH Health Whittier Hospital /ID# 222647

Whittier, California, 90602-1006, United States

Location

Rocky Mountain Cancer Centers - Boulder /ID# 223723

Boulder, Colorado, 80303, United States

Location

Yale University School of Medicine /ID# 222764

New Haven, Connecticut, 06510, United States

Location

Helen F. Graham Cancer Center & Research Institute /ID# 223731

Newark, Delaware, 19713-2055, United States

Location

Florida Cancer Specialists - Fort Myers /ID# 221319

Fort Myers, Florida, 33916, United States

Location

Memorial Healthcare System /ID# 222703

Hollywood, Florida, 33021-3513, United States

Location

Florida Cancer Specialists - North /ID# 221318

St. Petersburg, Florida, 33705-1449, United States

Location

Florida Cancer Specialists - Panhandle /ID# 221315

Tallahassee, Florida, 32308-5304, United States

Location

Florida Cancer Specialists - East /ID# 221317

West Palm Beach, Florida, 33401, United States

Location

St. Luke's Mountain State Tumor Institute /ID# 220838

Boise, Idaho, 83712-6267, United States

Location

Northwestern University Feinberg School of Medicine /ID# 220843

Chicago, Illinois, 60611-2927, United States

Location

Duplicate_Rush University Medical Center /ID# 221007

Chicago, Illinois, 60612, United States

Location

Ingalls Memorial Hosp /ID# 220844

Harvey, Illinois, 60426, United States

Location

Illinois Cancer Care, PC /ID# 220840

Peoria, Illinois, 61615, United States

Location

Duplicate_Parkview Cancer Institute /ID# 223620

Fort Wayne, Indiana, 46845-1739, United States

Location

Cancer Center of Kansas /ID# 222648

Wichita, Kansas, 67214, United States

Location

Hematology/Oncology Clinic /ID# 224257

Baton Rouge, Louisiana, 70809, United States

Location

Pontchartrain Cancer Center - Covington /ID# 221005

Covington, Louisiana, 70433-7512, United States

Location

Maryland Oncology Hematology /ID# 223776

Columbia, Maryland, 21044-3128, United States

Location

Massachusetts General Hospital /ID# 225068

Boston, Massachusetts, 02114, United States

Location

Beth Israel Deaconess Medical Center /ID# 225069

Boston, Massachusetts, 02215-5400, United States

Location

Dana-Farber Cancer Institute /ID# 219162

Boston, Massachusetts, 02215, United States

Location

VA Ann Arbor Healthcare System /ID# 221365

Ann Arbor, Michigan, 48105, United States

Location

Cancer & Hematology Centers /ID# 220848

Grand Rapids, Michigan, 49503, United States

Location

Metro Minnesota Community Oncology Research Consortium (MMCORC) /ID# 221321

Saint Louis Park, Minnesota, 55416, United States

Location

MidAmerica Division, Inc. /ID# 221895

Kansas City, Missouri, 64132, United States

Location

Comprehensive Cancer Centers of Nevada - Horizon Ridge /ID# 222635

Henderson, Nevada, 89052-2648, United States

Location

Titan Health Partners LLC, d/b/a Astera Cancer Care /ID# 221003

East Brunswick, New Jersey, 08816, United States

Location

The Valley Hospital /ID# 232337

Paramus, New Jersey, 07652, United States

Location

New York Oncology Hematology - Albany Cancer Center /ID# 223778

Albany, New York, 12206-5013, United States

Location

University at Buffalo /ID# 221206

Buffalo, New York, 14222, United States

Location

Weill Cornell Medical College /ID# 222898

New York, New York, 10065, United States

Location

Stony Brook University Hospital /ID# 224450

Stony Brook, New York, 11794-8183, United States

Location

Novant Health Presbyterian Medical Center /ID# 222561

Charlotte, North Carolina, 28204, United States

Location

Novant Health Forsyth Medical Center /ID# 221004

Winston-Salem, North Carolina, 27103, United States

Location

Oncology Hematology Care, Inc. /ID# 223724

Cincinnati, Ohio, 45236-2725, United States

Location

Bend Memorial Clinic /ID# 220999

Bend, Oregon, 97701, United States

Location

Willamette Valley Cancer Institute and Research Center /ID# 223733

Eugene, Oregon, 97401-6043, United States

Location

UPMC Hillman Cancer Ctr /ID# 223201

Pittsburgh, Pennsylvania, 15232, United States

Location

Avera Cancer Institute /ID# 243461

Sioux Falls, South Dakota, 57105, United States

Location

Tennessee Oncology - Chattanooga / McCallie /ID# 221311

Chattanooga, Tennessee, 37404-3230, United States

Location

Tennessee Oncology-Nashville Centennial /ID# 220854

Nashville, Tennessee, 37203-1632, United States

Location

Texas Oncology - Austin Midtown /ID# 223729

Austin, Texas, 78705, United States

Location

Duplicate_Texas Oncology - Medical City Dallas /ID# 223725

Dallas, Texas, 75230, United States

Location

Texas Oncology- Baylor Charles A. Sammons Cancer Center /ID# 223727

Dallas, Texas, 75246-2003, United States

Location

Texas Oncology - Forth Worth /ID# 223777

Fort Worth, Texas, 76104-2150, United States

Location

MD Anderson Cancer Center at Texas Medical Center /ID# 219163

Houston, Texas, 77030-4000, United States

Location

Texas Oncology - San Antonio Medical Center - Research Drive /ID# 223728

San Antonio, Texas, 78240, United States

Location

Baylor Scott & White Medical Center- Temple /ID# 221332

Temple, Texas, 76508-0001, United States

Location

Texas Oncology - Northeast Texas /ID# 223734

Tyler, Texas, 75702, United States

Location

Utah Cancer Specialists Salt Lake Clinic /ID# 219160

Salt Lake City, Utah, 84106, United States

Location

Virginia Cancer Specialists - Gainesville /ID# 223726

Gainesville, Virginia, 20155-3257, United States

Location

Virginia Commonwealth University Medical Center Main Hospital /ID# 221590

Richmond, Virginia, 23219, United States

Location

Virginia Cancer Institute at Reynolds Crossing /ID# 221002

Richmond, Virginia, 23230, United States

Location

VA Puget Sound Health Care System /ID# 221358

Seattle, Washington, 98108-1597, United States

Location

Duplicate_Blacktown Hospital /ID# 234079

Blacktown, New South Wales, 2148, Australia

Location

St George Hospital /ID# 221810

Kogarah, New South Wales, 2217, Australia

Location

Port Macquarie Base Hospital /ID# 234078

Port Macquarie, New South Wales, 2444, Australia

Location

Gold coast University Hospital /ID# 222606

Southport, Queensland, 4215, Australia

Location

Royal Adelaide Hospital /ID# 221805

Adelaide, South Australia, 5000, Australia

Location

St Vincent's Hospital Melbourne /ID# 221809

Fitzroy Melbourne, Victoria, 3065, Australia

Location

Austin Health /ID# 221807

Heidelberg, Victoria, 3084, Australia

Location

Medizinische Universitaet Wien /ID# 221446

Vienna, State of Vienna, 1090, Austria

Location

Ordensklinikum Linz GmbH Elisabethinen /ID# 221387

Linz, Upper Austria, 4010, Austria

Location

Klinikum Wels-Grieskirchen GmbH /ID# 221386

Wels, Upper Austria, 4600, Austria

Location

Landeskrankenhaus Salzburg-Universitaetsklinikum der PMU (LKH) /ID# 221092

Salzburg, 5020, Austria

Location

Hanusch Krankenhaus /ID# 221093

Vienna, 1140, Austria

Location

ZAS Middelheim /ID# 218907

Antwerp, Antwerpen, 2020, Belgium

Location

Cliniques Universitaires UCL Saint-Luc /ID# 219066

Brussels, Brussels Capital, 1200, Belgium

Location

Hospital La Louviere Site Jolimont - Helora /ID# 218921

La Louvière, Hainaut, 7100, Belgium

Location

Université Catholique de Louvain-Namur - Centre Hospitalier Universitaire Dinant /ID# 219064

Yvoir, Namur, 5530, Belgium

Location

UZ Gent /ID# 218767

Ghent, Oost-Vlaanderen, 9000, Belgium

Location

Universitair Ziekenhuis Leuven /ID# 218905

Leuven, Vlaams-Brabant, 3000, Belgium

Location

AZ Sint-Jan Brugge /ID# 218212

Bruges, West-Vlaanderen, 8000, Belgium

Location

Hospital Universitario Walter Cantidio /ID# 223434

Fortaleza, Ceará, 60430-372, Brazil

Location

Hospital Erasto Gaertner /ID# 221341

Curitiba, Puerto Rico, 81520-060, Brazil

Location

Sociedade Beneficente Israelita Brasileira Hospital Albert Einstein /ID# 221370

São Paulo, São Paulo, 05652-900, Brazil

Location

Hospital Universitário Pedro Ernesto /ID# 223080

Rio de Janeiro, 20551-030, Brazil

Location

Hospital das Clinicas da Faculdade de Medicina da Universidade de Sao /ID# 221339

São Paulo, 05403-000, Brazil

Location

BC Cancer - Surrey /ID# 219098

Surrey, British Columbia, V3V 1Z2, Canada

Location

Ottawa Hospital Research Institute /ID# 219105

Ottawa, Ontario, K1H 8L6, Canada

Location

Sunnybrook Health Sciences Centre /ID# 219103

Toronto, Ontario, M4N 3M5, Canada

Location

McGill University Health Centre - Glen Site /ID# 222519

Montreal, Quebec, H4A 3J1, Canada

Location

CIUSSS du Nord-de-l'ile-de-Montréal_Hopital du Sacré-Coeur de Montréal /ID# 218973

Montreal, Quebec, H4J 1C5, Canada

Location

CHUQ- Hôpital de l'Enfant-Jesus /ID# 221200

Québec, Quebec, G1J 1Z4, Canada

Location

Peking University International Hospital /ID# 222987

Beijing, Beijing Municipality, 102206, China

Location

Lanzhou University Second Hospital /ID# 225980

Lanzhou, Gansu, 730030, China

Location

Guangdong Provincial People's Hospital /ID# 221442

Guangzhou, Guangdong, 510080, China

Location

Zhujiang Hospital of Southern Medical University /ID# 222071

Guangzhou, Guangdong, 510280, China

Location

Nanfang Hospital of Southern Medical University /ID# 224566

Guangzhou, Guangdong, 510515, China

Location

The Second Hospital of Hebei Medical University /ID# 222919

Shijiazhuang, Hebei, 050000, China

Location

People's Hospital of Henan Province /ID# 225790

Zhengzhou, Henan, 450003, China

Location

Henan Cancer Hospital /ID# 221447

Zhengzhou, Henan, 450008, China

Location

Union Hospital affiliated to Tongji Medical College of Huazhong University of Sc /ID# 221475

Wuhan, Hubei, 430022, China

Location

Tongji Hospital Tongji Medical College of HUST /ID# 221474

Wuhan, Hubei, 430030, China

Location

Zhongda Hospital Southeast University /ID# 221849

Nanjing, Jiangsu, 210009, China

Location

Jiangsu Province Hospital /ID# 221342

Nanjing, Jiangsu, 210029, China

Location

The First Affiliated Hospital of Soochow University /ID# 221640

Suzhou, Jiangsu, 215031, China

Location

The First Affiliated Hospital of Nanchang University /ID# 225983

Nanchang, Jiangxi, 330006, China

Location

Shengjing Hospital of China Medical University /ID# 222945

Shenyang, Liaoning, 110022, China

Location

Shaanxi Provincial People'S Hospital /ID# 225728

Xi'an, Shaanxi, 710054, China

Location

Shanghai Sixth People's Hospital /ID# 221546

Shanghai, Shanghai Municipality, 200233, China

Location

West China Hospital, Sichuan University /ID# 221601

Chengdu, Sichuan, 610041, China

Location

Institute of Hematology & Blood Diseases Hospital, Chinese Academy of Medical Sc /ID# 221567

Tianjin, Tianjin Municipality, 300020, China

Location

Tianjin Medical University General Hospital /ID# 226810

Tianjin, Tianjin Municipality, 300052, China

Location

The First Affiliated Hospital, Zhejiang University School of Medicine /ID# 221494

Hangzhou, Zhejiang, 310003, China

Location

Sir Run Run Shaw Hospital Zhejiang University School of Medicine /ID# 225982

Hangzhou, Zhejiang, 310020, China

Location

The Fourth Affiliated Hospital Zhejiang University School of Medicine /ID# 225918

Yiwu, Zhejiang, 322000, China

Location

Fakultní Nemocnice Brno - Jihlavská /ID# 221351

Brno, Brno-mesto, 625 00, Czechia

Location

Fakultní nemocnice Hradec Králové - Sokolská /ID# 221163

Hradec Králové, Hradec Kralove, 500 05, Czechia

Location

Fakultni Nemocnice Ostrava /ID# 219143

Ostrava, Ostrava-mesto, 708 52, Czechia

Location

Fakultní Nemocnice Plzeň-Lochotín /ID# 221162

Pilsen, Plzen-jih, 323 00, Czechia

Location

Všeobecná Fakultní Nemocnice v Praze /ID# 221229

Prague, Praha 17, 128 00, Czechia

Location

Ustav hematologie a krevni transfuze /ID# 221350

Prague, 128 00, Czechia

Location

Chu de Nice-Hopital L'Archet Ii /Id# 220992

Nice, Alpes-Maritimes, 06202, France

Location

Centre Hospitalier Universitaire de Bordeaux /ID# 220989

Pessac, Gironde, 33604, France

Location

CHU Grenoble - Hopital Michallon /ID# 220988

La Tronche, Isere, 38700, France

Location

CHRU Lille - Hopital Claude Huriez /ID# 220991

Lille, Nord, 59037, France

Location

Centre Hospitalier Universitaire de Nantes, Hotel Dieu -HME /ID# 222074

Nantes, Pays de la Loire Region, 44000, France

Location

Hopital de la Conception /ID# 224882

Marseille, Provence-Alpes-Côte d'Azur Region, 13005, France

Location

Centre Henri Becquerel /ID# 220986

Rouen, Seine-Maritime, 76038, France

Location

CH Henri Duffaut /ID# 225185

Avignon, Vaucluse, 84902, France

Location

Hôpital Saint-Louis /ID# 222075

Paris, 75010, France

Location

Universitatsklinikum Mannheim /ID# 221172

Mannheim, Baden-Wurttemberg, 68167, Germany

Location

Stauferklinikum Schwaebisch Gmuend /ID# 224917

Mutlangen, Baden-Wurttemberg, 73557, Germany

Location

Klinikum rechts der Isar /ID# 221170

Munich, Bavaria, 81675, Germany

Location

Medizinische Hochschule Hannover /ID# 221173

Hanover, Lower Saxony, 30625, Germany

Location

Universitaetsklinikum Koeln /ID# 234219

Cologne, North Rhine-Westphalia, 50937, Germany

Location

Universitaetsklinikum Duesseldorf /ID# 221169

Düsseldorf, North Rhine-Westphalia, 40225, Germany

Location

Universitaetsklinikum Leipzig /ID# 221168

Leipzig, Saxony, 04103, Germany

Location

Charite Universitaetsklinikum Berlin - Campus Benjamin Franklin /ID# 221189

Berlin, 12203, Germany

Location

Fejér Vármegyei Szent György Egyetemi Oktató Kórház /ID# 222953

Székesfehérvár, Fejér, 8000, Hungary

Location

Duplicate_Debreceni Egyetem Klinikai Kozpont /ID# 221702

Debrecen, Hajdú-Bihar, 4032, Hungary

Location

Duplicate_Somogy Varmegyei Kaposi Mor Oktato Korhaz /ID# 221703

Kaposvár, Somogy County, 7400, Hungary

Location

Szabolcs-Szatmar-Bereg Varmegyei Oktatokorhaz /ID# 221704

Nyíregyháza, Szabolcs-Szatmár-Bereg, 4400, Hungary

Location

Szegedi Tudományegyetem /ID# 221705

Szeged, 6720, Hungary

Location

Shaare Zedek Medical Center /ID# 233181

Jerusalem, Jerusalem, 91031, Israel

Location

Hadassah Medical Center-Hebrew University /ID# 222006

Jerusalem, Jerusalem, 91120, Israel

Location

The Chaim Sheba Medical Center /ID# 221110

Ramat Gan, Tel Aviv, 5265601, Israel

Location

Tel Aviv Sourasky Medical Center /ID# 221896

Tel Aviv, Tel Aviv, 6423906, Israel

Location

Rambam Health Care Campus /ID# 221083

Haifa, 3109601, Israel

Location

Rabin Medical Center /ID# 221184

Petah Tikva, 4941492, Israel

Location

IRCCS Istituto Clinico Humanitas /ID# 220815

Rozzano, Lombardy, 20089, Italy

Location

Azienda Ospedaliera di Rilievo Nazionale Antonio Cardarelli /ID# 220816

Naples, Napoli, 80131, Italy

Location

Duplicate_Azienda Ospedaliero-Universitaria Sant'Andrea /ID# 220819

Rome, Roma, 00189, Italy

Location

IRCCS AOU di Bologna Policlinico Sant Orsola Malpighi /ID# 220810

Bologna, 40138, Italy

Location

Grande Ospedale Metropolitano Bianchi - Melacrino - Morelli P.O. Riuniti /ID# 220818

Reggio Calabria, 89125, Italy

Location

Nagoya University Hospital /ID# 221566

Nagoya, Aichi-ken, 466-8560, Japan

Location

University of Fukui Hospital /ID# 221568

Yoshida-gun, Fukui, 910-1104, Japan

Location

Kyushu University Hospital /ID# 223473

Fukuoka, Fukuoka, 812-8582, Japan

Location

Fukushima Medical University Hospital /ID# 222015

Fukushima, Fukushima, 960-1295, Japan

Location

Chugoku Central Hospital /ID# 222955

Fukuyama, Hiroshima, 720-0001, Japan

Location

Sapporo Hokuyu Hospital /ID# 222133

Sapporo, Hokkaido, 003-0006, Japan

Location

Aiiku Hospital /ID# 222351

Sapporo, Hokkaido, 064-0804, Japan

Location

Kobe City Medical Center General Hospital /ID# 221977

Kobe, Hyōgo, 650-0047, Japan

Location

NHO Mito Medical Center /ID# 222278

Higashiibaraki-gun, Ibaraki, 311-3193, Japan

Location

Tohoku University Hospital /ID# 221976

Sendai, Miyagi, 9808574, Japan

Location

Okayama Medical Center /ID# 222310

Okayama, Okayama-ken, 701-1192, Japan

Location

Kindai University Hospital /ID# 222284

Osakasayama-shi, Osaka, 589-8511, Japan

Location

Saitama Medical Center /ID# 222016

Kawagoe, Saitama, 350-8550, Japan

Location

NTT Medical Center Tokyo /ID# 222365

Shinagawa-ku, Tokyo, 141-8625, Japan

Location

Yamagata University Hospital /ID# 221574

Yamagata, Yamagata, 990-9585, Japan

Location

Nagasaki University Hospital /ID# 222241

Nagasaki, 852-8501, Japan

Location

Maastricht Universitair Medisch Centrum /ID# 221630

Maastricht, Limburg, 6229 HX, Netherlands

Location

Maxima Medisch Centrum /ID# 223010

Eindhoven, North Brabant, 5631 BM, Netherlands

Location

Medisch Spectrum Twente /ID# 223012

Enschede, Overijssel, 7512 KZ, Netherlands

Location

Isala /ID# 223011

Zwolle, Overijssel, 8025 AB, Netherlands

Location

Erasmus Medisch Centrum /ID# 218937

Rotterdam, South Holland, 3015 CE, Netherlands

Location

Szpital Uniwersytecki nr 2 im. dr. Jana Biziela /ID# 233321

Bydgoszcz, Kuyavian-Pomeranian Voivodeship, 85-168, Poland

Location

Uniwersytecki Szpital Kliniczny Nr 1 w Lublinie /ID# 221667

Lublin, Lublin Voivodeship, 20-081, Poland

Location

Lux Med Onkologia - Szpital Szamocka /Id# 222203

Warsaw, Masovian Voivodeship, 01-748, Poland

Location

MTZ Clinical Research Powered by Pratia /ID# 221354

Warsaw, Masovian Voivodeship, 02-172, Poland

Location

Uniwersyteckie Centrum Kliniczne /ID# 222069

Gdansk, Pomeranian Voivodeship, 80-214, Poland

Location

Pratia Onkologia Katowice /ID# 224728

Katowice, 40-519, Poland

Location

Wojewódzkie Wielospecjalistyczne Centrum Onkologii i Traumatologii im. M. Kopern /ID# 221784

Lodz, Łódź Voivodeship, 93-513, Poland

Location

Pan American Center for Oncology Trials, LLC /ID# 221010

Rio Piedras, 00935, Puerto Rico

Location

VA Caribbean Healthcare System /ID# 221012

San Juan, 00921-3201, Puerto Rico

Location

Kaluga Regional Clinical Hospital /ID# 221211

Kaluga, Kaluga Oblast, 248007, Russia

Location

Republican hospital named after V.A. Baranov /ID# 221214

Petrozavodsk, Murmansk Oblast, 185019, Russia

Location

Clinic UZI 4D /ID# 221215

Pyatigorsk, Stavropol Kray, 357502, Russia

Location

Hospital n.a. V.V. Veresaev /ID# 225435

Moscow, 127644, Russia

Location

MMCC Kommunarka /ID# 221213

Moscow, 129301, Russia

Location

Almazov National Medical Research Centre /ID# 221449

Saint Petersburg, 197341, Russia

Location

Duplicate_Pusan National University Hospital /ID# 232353

Busan, Busan Gwang Yeogsi, 49241, South Korea

Location

Seoul National University Bundang Hospital /ID# 221695

Seongnam-si, Gyeonggido, 13620, South Korea

Location

Seoul National University Hospital /ID# 221226

Seoul, Seoul Teugbyeolsi, 03080, South Korea

Location

Asan Medical Center /ID# 221227

Seoul, Seoul Teugbyeolsi, 05505, South Korea

Location

Samsung Medical Center /ID# 221224

Seoul, Seoul Teugbyeolsi, 06351, South Korea

Location

Yonsei University Health System Severance Hospital /ID# 233171

Seoul, 03722, South Korea

Location

Hospital Universitario Germans Trias i Pujol /ID# 221274

Badalona, Barcelona, 08916, Spain

Location

Hospital Universitario Reina Sofia /ID# 221273

Córdoba, Cordoba, 14004, Spain

Location

Hospital Universitario Quironsalud Madrid /ID# 221275

Pozuelo de Alarcón, Madrid, 28223, Spain

Location

Hospital Universitario Vall d'Hebron /ID# 221323

Barcelona, 08035, Spain

Location

Hospital General Universitario Gregorio Maranon /ID# 221271

Madrid, 28007, Spain

Location

Hospital Universitario 12 de Octubre /ID# 221272

Madrid, 28041, Spain

Location

Hospital Universitario de Salamanca /ID# 221297

Salamanca, 37711, Spain

Location

Hospital Universitario Virgen del Rocio /ID# 221276

Seville, 41013, Spain

Location

Hospital Universitario y Politecnico La Fe /ID# 221270

Valencia, 46026, Spain

Location

Duplicate_Kaohsiung Chang Gung Memorial Hospital /ID# 223573

Kaohsiung City, Kaohsiung, 833, Taiwan

Location

China Medical University Hospital /ID# 218987

Taichung, 40447, Taiwan

Location

National Cheng Kung University Hospital /ID# 218989

Tainan, 704, Taiwan

Location

Chi-Mei Medical Center /ID# 218991

Tainan, 71004, Taiwan

Location

Duplicate_Erciyes University Medical Fac /ID# 222090

Melikgazi, Kayseri, 38030, Turkey (Türkiye)

Location

Hacettepe University Faculty of Medicine /ID# 222094

Ankara, 06100, Turkey (Türkiye)

Location

Ankara City Hospital /ID# 222093

Ankara, 06800, Turkey (Türkiye)

Location

Akdeniz Universitesi Tip Fakul /ID# 222095

Antalya, 07059, Turkey (Türkiye)

Location

Ondokuz mayis University Facul /ID# 222091

Samsun, 55200, Turkey (Türkiye)

Location

Acibadem Maslak Hastanesi /ID# 222072

Tuzla, 34953, Turkey (Türkiye)

Location

Derriford Hospital and the Royal Eye Infirmary /ID# 222514

Plymouth, Devon, PL6 8DH, United Kingdom

Location

University Hospitals Dorset NHS Foundation Trust /ID# 221237

Poole, Dorset, BH15 2JB, United Kingdom

Location

University College London Hospital /ID# 221240

London, Greater London, NW1 2BU, United Kingdom

Location

Oxford University Hospitals NHS Foundation Trust /ID# 221231

Oxford, Oxfordshire, OX3 9DU, United Kingdom

Location

Cardiff & Vale University Health Board /ID# 221236

Cardiff, Wales, CF14 4XN, United Kingdom

Location

NHS Grampian /ID# 222509

Aberdeen, AB15 6RE, United Kingdom

Location

University Hospitals Birmingham NHS Foundation Trust /ID# 221233

Birmingham, B15 2TH, United Kingdom

Location

University Hospitals Bristol /ID# 222510

Bristol, BS1 3NU, United Kingdom

Location

The Royal Marsden NHS Foundation Trust /ID# 221232

London, SW3 6JJ, United Kingdom

Location

Related Publications (1)

  • Stahl M, DeZern AE. Is there a path forward for immunotherapy in patients with myelodysplastic syndromes? Lancet Haematol. 2024 Jan;11(1):e5-e7. doi: 10.1016/S2352-3026(23)00343-5. Epub 2023 Dec 5. No abstract available.

Related Links

MeSH Terms

Conditions

Myelodysplastic Syndromes

Interventions

venetoclaxAzacitidine

Condition Hierarchy (Ancestors)

Bone Marrow DiseasesHematologic DiseasesHemic and Lymphatic Diseases

Intervention Hierarchy (Ancestors)

Aza CompoundsOrganic ChemicalsCytidinePyrimidine NucleosidesPyrimidinesHeterocyclic Compounds, 1-RingHeterocyclic CompoundsNucleosidesNucleic Acids, Nucleotides, and NucleosidesRibonucleosides

Study Officials

  • ABBVIE INC.

    AbbVie

    STUDY DIRECTOR

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

May 22, 2020

First Posted

May 26, 2020

Study Start

September 10, 2020

Primary Completion (Estimated)

July 1, 2027

Study Completion (Estimated)

July 1, 2027

Last Updated

May 6, 2026

Record last verified: 2026-05

Data Sharing

IPD Sharing
Will share

AbbVie is committed to responsible clinical trial data sharing. This includes access to anonymized, individual and trial-level data (analysis data sets), as well as other information.

Shared Documents
STUDY PROTOCOL, SAP, CSR
Time Frame
For details on when studies are available for sharing visit https://vivli.org/ourmember/abbvie/
Access Criteria
To learn more about the process, or to submit a request, visit the following link https://www.abbvieclinicaltrials.com/hcp/data-sharing/
More information

Locations