NCT02870907

Brief Summary

Postoperative Treatment of Unilateral Retinoblastoma After Primary Enucleation according to histopathological risk factors of the International Retinoblastoma Staging Working Group.

Trial Health

75
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
195

participants targeted

Target at P75+ for phase_2

Timeline
57mo left

Started Mar 2010

Longer than P75 for phase_2

Geographic Reach
1 country

27 active sites

Status
active not recruiting

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Progress78%
Mar 2010Mar 2031

Study Start

First participant enrolled

March 18, 2010

Completed
6.4 years until next milestone

First Submitted

Initial submission to the registry

August 9, 2016

Completed
8 days until next milestone

First Posted

Study publicly available on registry

August 17, 2016

Completed
14.5 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

March 1, 2031

Expected
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

March 1, 2031

Last Updated

January 7, 2026

Status Verified

January 1, 2026

Enrollment Period

21 years

First QC Date

August 9, 2016

Last Update Submit

January 5, 2026

Conditions

Keywords

primary enucleationretinoblastoma

Outcome Measures

Primary Outcomes (1)

  • Rate of extra ocular relapses

    5 years

Secondary Outcomes (5)

  • Evaluate long term and acute toxicities of adjuvant chemotherapy and orbital irradiation if necessary.

    5 years

  • Number of patient with secondary bilateralisation

    5 years

  • Evaluate the different histopathological risk factors frequency

    5 years

  • To determine tumors genomic

    at the inclusion

  • Evaluate sensitivity of MRI in detecting extra ocular extension

    At the inclusion

Study Arms (4)

Low risk group

EXPERIMENTAL

No treatment

Other: Observation

Intermediate risk sub group 1

EXPERIMENTAL

2 cycles (4 courses): 2 courses of etoposide and Carboplatin from D1 to D5 and Vincristin at D22 and D26- Cyclophosphamide from D22 to D26.

Drug: EtoposideDrug: CarboplatinDrug: VincristineDrug: Cyclophosphamide

Intermediate risk sub group 2

EXPERIMENTAL

2 courses of Vincristin and Carboplatin

Drug: VincristineDrug: Carboplatin

High risk group

EXPERIMENTAL

* Orbital irradiation * 3 cycles of two different types of alternating chemotherapy courses (id 6 courses) : * Etoposide (100 mg/m²/d) and Carboplatin (160 mg/m²/d) with intrathecal Thiotepa injection. * Vincristin (1,5 mg/m²/d) - Cyclophosphamide (1000 mg/m²/d) * Cytapheresis for peripheral blood stem cells collection after the primary or the secondary courses of Vincristine- Cyclophosphamide. * High dose chemotherapy : * Carboplatin (AUC : 7/d) - etoposide (250 mg/m²/d) - Thiotepa (300 mg/m²/d) * Peripheral bood stem cell transplantation.

Radiation: Orbital irradiationDrug: EtoposideDrug: CarboplatinDrug: ThiotepaDrug: VincristineDrug: CyclophosphamideProcedure: CytapheresisProcedure: Peripheral bood stem cell transplantation

Interventions

no post operative chemotherapy

Also known as: Low risk group
Low risk group

100 mg/m²/d, IV (in the vein) from D1 to D5.

Also known as: Intermediate risk sub group 1
Intermediate risk sub group 1

1, 5 mg/m²/d, IV at D1.

Also known as: Intermediate risk sub group 2
Intermediate risk sub group 2

45 Grays (Standard or external beam radiotherapy).

Also known as: High risk group
High risk group

160 mg/m²/d, IV from D1 to D5.

Also known as: Intermediate risk sub group 1
Intermediate risk sub group 1

300 mg/m²/d, IV from D22 to D26.

Also known as: Intermediate risk sub group 1
Intermediate risk sub group 1

15 mg, intrathecal Thiotepa injection at D1.

Also known as: High risk group
High risk group
CytapheresisPROCEDURE

Cytapheresis for peripheral blood stem cells collection after the primary or the secondary courses of Vincristine- Cyclophosphamid.

Also known as: High risk group
High risk group

at D0

Also known as: High risk group
High risk group

Eligibility Criteria

Age2 Months - 10 Years
Sexall
Healthy VolunteersNo
Age GroupsChild (0-17)

You may qualify if:

  • Written informed consent - a signed informed consent and/or assent (as age appropriate) will be obtained according to institutional guidelines;
  • Male or female ≥2 months and \<10 years of age at the time of signing the informed consent form;
  • Diagnosis of non familial extensive unilateral retinoblastoma treated by primary enucleation
  • In case of post operative chemotherapy, patients must have adequate organ function:
  • Adequate hematopoietic function Neutrophils\>1.0x109/l, Platelets \>100 x 109/l.
  • Adequate hepatic function: grade II NCI CTC
  • Adequate renal function: serum creatinemia \<1.5 x ULN for age with normal creatinine clearance estimated by SCHWARTZ formula
  • Audiometry \< Grade II de Brock.
  • Echocardiography normal in case of high dose cyclophosphamide chemotherapy (3 g/m²).
  • Patients affiliated to a Social Security Regimen or beneficiary of the same
  • No chemotherapy or radiotherapy prior to administration of the first dose of study treatment for retinoblastoma or other tumor types
  • Without medical cons-indication to study drugs.

You may not qualify if:

  • Bilateral and/or familial or trilateral retinoblastoma.
  • Unilateral retinoblastoma with indication of primary chemotherapy before enucleation:
  • One or several surgical risk factors
  • Buphthalmia Exophthalmia.
  • Peri ocular inflammatory signs.
  • Extraocular extension :
  • Radiological retrolaminar extension (more than 3 mm behind the lamina cribrosa) and or meningeal sheat optic nerve extension.
  • Extrascleral extension
  • Lymp nodes extension
  • Unilateral retinoblastoma with possibility of conservative treatment:
  • Metastatic extension at diagnosis
  • Uncontrolled medical conditions, psychological, familial, sociological, or geographical conditions that do not permit compliance with the protocol

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (27)

Chr Felix Guyon

Saint-Denis, La Réunion, 97405, France

Location

Hopital Nord Chu Amiens

Amiens, 80054, France

Location

Chu Angers

Angers, 49033, France

Location

Hopital Jean Minioz

Besançon, 25030, France

Location

Chu R; Pellegrin

Bordeaux, 33076, France

Location

Chu Morvan

Brest, 29609, France

Location

CHU CAEN

Caen, 14033, France

Location

Chu Estaing

Clermont-Ferrand, 63003, France

Location

Chu Bocage

Dijon, 21079, France

Location

Chu de Grenoble

Grenoble, 38043, France

Location

Centre Oscar Lambret

Lille, 59020, France

Location

Chu Limoges

Limoges, 87042, France

Location

Centre Leon Berard

Lyon, 69373, France

Location

Hopital D'Enfants La Timone

Marseille, 13385, France

Location

Hopital Arnaud de Villeneuve

Montpellier, 34295, France

Location

Chu Nantes

Nantes, 44093, France

Location

Chu de Nice

Nice, 06202, France

Location

Institut Curie

Paris, 75005, France

Location

Chu de Poitiers

Poitiers, 86021, France

Location

Chur de Reims

Reims, 51100, France

Location

Chu de Rennes

Rennes, 35056, France

Location

Chu de Rouen

Rouen, 76031, France

Location

Chu Saint Etienne

Saint-Etienne, 420555, France

Location

Hoptial Hautepierre

Strasbourg, 67098, France

Location

Chu Toulouse

Toulouse, 31026, France

Location

Chu Tours

Tours, 37044, France

Location

Chu Nancy

Vandœuvre-lès-Nancy, 54500, France

Location

MeSH Terms

Conditions

Retinoblastoma

Interventions

ObservationEtoposideVincristineCarboplatinCyclophosphamideThiotepaCytapheresis

Condition Hierarchy (Ancestors)

Neoplasms, NeuroepithelialNeuroectodermal TumorsNeoplasms, Germ Cell and EmbryonalNeoplasms by Histologic TypeNeoplasmsNeoplasms, Glandular and EpithelialNeoplasms, Nerve TissueRetinal NeoplasmsEye NeoplasmsNeoplasms by SiteEye Diseases, HereditaryEye DiseasesRetinal Diseases

Intervention Hierarchy (Ancestors)

MethodsInvestigative TechniquesPodophyllotoxinTetrahydronaphthalenesNaphthalenesPolycyclic Aromatic HydrocarbonsHydrocarbons, AromaticHydrocarbons, CyclicHydrocarbonsOrganic ChemicalsPolycyclic CompoundsGlucosidesGlycosidesCarbohydratesVinca AlkaloidsSecologanin Tryptamine AlkaloidsIndole AlkaloidsAlkaloidsHeterocyclic CompoundsIndolesHeterocyclic Compounds, 2-RingHeterocyclic Compounds, Fused-RingIndolizidinesIndolizinesCoordination ComplexesPhosphoramide MustardsNitrogen Mustard CompoundsMustard CompoundsHydrocarbons, HalogenatedPhosphoramidesOrganophosphorus CompoundsTriethylenephosphoramideAziridinesAzirinesHeterocyclic Compounds, 1-RingBiological TherapyTherapeuticsBlood Component RemovalCell SeparationCytological TechniquesClinical Laboratory Techniques

Study Design

Study Type
interventional
Phase
phase 2
Allocation
NON RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
OTHER
Responsible Party
SPONSOR

Study Record Dates

First Submitted

August 9, 2016

First Posted

August 17, 2016

Study Start

March 18, 2010

Primary Completion (Estimated)

March 1, 2031

Study Completion (Estimated)

March 1, 2031

Last Updated

January 7, 2026

Record last verified: 2026-01

Data Sharing

IPD Sharing
Will share

Sponsor will share de-identified data sets. Documents generated under the project will be disseminated in accordance with Institut Curie policies.

Shared Documents
SAP
Time Frame
Data requests can be submitted starting 9 months after last article publication and will be made accessible for up to 12 months.
Access Criteria
Access to trial individual participant data can be requested by qualified researchers engaging in independent scientific research, and will be provided following review and approval of a research proposal and Statistical Analysis Plan (SAP) and execution of a data sharing agreement (DSA).

Locations