NCT02734277

Brief Summary

This is a multi-center, prospective, non-interventional study that focuses on the long- term effects following participation in selected ITN new-onset Type1 Diabetes Mellitus studies with immunomodulatory agents (T1DM, T1D). This observational study will:

  • follow participants to determine how long they continue to produce insulin, and
  • will also assess how changes in the immune system over time relate to the ability to produce insulin. This information could help design better therapies for type 1 diabetes in the future.

Trial Health

77
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
111

participants targeted

Target at P50-P75 for all trials

Timeline
28mo left

Started Aug 2016

Longer than P75 for all trials

Geographic Reach
1 country

12 active sites

Status
recruiting

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Progress81%
Aug 2016Aug 2028

First Submitted

Initial submission to the registry

April 6, 2016

Completed
6 days until next milestone

First Posted

Study publicly available on registry

April 12, 2016

Completed
4 months until next milestone

Study Start

First participant enrolled

August 18, 2016

Completed
12 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

August 1, 2028

Expected
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

August 1, 2028

Last Updated

March 10, 2026

Status Verified

March 1, 2026

Enrollment Period

12 years

First QC Date

April 6, 2016

Last Update Submit

March 6, 2026

Conditions

Keywords

InsulinGlucose Intolerance

Outcome Measures

Primary Outcomes (1)

  • Change in Beta Cell Function by MMTT-Stimulated Mean C-peptide Area Under the Curve (AUC)

    Evaluation of changes in beta cell function over time will be measured by mixed-meal tolerance test (MMTT) -Stimulated mean C-Peptide area under the curve (AUC). C-peptide is released by the pancreas into the bloodstream in equal amounts to insulin and reflects how much insulin pancreatic beta cells are making. The standardized MMTT evaluates whether beta cells are producing endogenous insulin. Detectable C-peptide is defined as any value during a MMTT of ≥0.15 ng/mL.

    Baseline (Visit 0) to Month 60 (Year 5)

Secondary Outcomes (6)

  • Change in Insulin Use in Units per Kilogram Body Weight Per Day

    Baseline (Visit 0) to Month 60 (Year 5)

  • Change in HbA1C

    Baseline (Visit 0) to Month 60 (Year 5)

  • Count of Participant-Reported Major Hypoglycemic Events

    Baseline (Visit 0) to Month 60 (Year 5)

  • Time to Undetectable C-Peptide

    Baseline (Visit 0) to Month 60 (Year 5)

  • Frequency of Grade 3 or Higher Adverse Events (AEs) of Interest

    Baseline (Visit 0) to Month 60 (Year 5)

  • +1 more secondary outcomes

Study Arms (2)

Group 1: Detectable C-peptide by MMTT

Participants with detectable C-peptide at their: * Last Immune Tolerance Network (ITN) T1DM week 104 study visit, * Last AbATE (NCT00129259) follow-up visit, or * Last ITN066AI T1DES visit Detectable C-peptide is defined as a value above the lower limit of detection.

Group 2:Undetectable C-peptide by MMTT

Participants without detectable C-peptide at their: * Last ITN T1DM week 104 study visit, * Last AbATE follow-up visit, or last * ITN066AI T1DES visit Undetectable C-peptide is defined as a value below the lower limit of detection.

Eligibility Criteria

Age8 Years - 35 Years
Sexall
Healthy VolunteersNo
Age GroupsChild (0-17), Adult (18-64)
Sampling MethodNon-Probability Sample
Study Population

Former participants in Immune Tolerance Network (ITN) new-onset Type 1 Diabetes Mellitus (T1DM) studies with immunomodulatory agents as the intervention.

You may qualify if:

  • Prior participant in an Immune Tolerance Network (ITN) executive committee approved T1DM study.
  • Ability to sign informed consent/assent (as applicable for children).

You may not qualify if:

  • Any medical condition that in the opinion of the principal investigator would interfere with safe completion of the trial; or
  • Inability to comply with the study visit schedule and required assessments.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (12)

UCSF School of Medicine

San Francisco, California, 94143, United States

RECRUITING

Stanford University

Stanford, California, 94305, United States

RECRUITING

University of Colorado School of Medicine: Barbara Davis Center for Diabetes

Aurora, Colorado, 80045, United States

RECRUITING

Yale University

New Haven, Connecticut, 06519, United States

COMPLETED

Emory University

Atlanta, Georgia, 30322, United States

WITHDRAWN

Indiana University Riley Hospital for Children

Indianapolis, Indiana, 46202, United States

RECRUITING

University of Iowa Health Care Division of Pediatric Endocrinology

Iowa City, Iowa, 52242, United States

RECRUITING

Joslin Diabetes Center

Boston, Massachusetts, 02215, United States

RECRUITING

University of Minnesota

Minneapolis, Minnesota, 55454, United States

RECRUITING

Children's Mercy Hospital

Kansas City, Missouri, 64108, United States

RECRUITING

Sanford Research

Sioux Falls, South Dakota, 57104, United States

COMPLETED

Benaroya Research Institute

Seattle, Washington, 98101, United States

RECRUITING

Related Publications (3)

  • Herold KC, Gitelman SE, Ehlers MR, Gottlieb PA, Greenbaum CJ, Hagopian W, Boyle KD, Keyes-Elstein L, Aggarwal S, Phippard D, Sayre PH, McNamara J, Bluestone JA; AbATE Study Team. Teplizumab (anti-CD3 mAb) treatment preserves C-peptide responses in patients with new-onset type 1 diabetes in a randomized controlled trial: metabolic and immunologic features at baseline identify a subgroup of responders. Diabetes. 2013 Nov;62(11):3766-74. doi: 10.2337/db13-0345. Epub 2013 Jul 8.

    PMID: 23835333BACKGROUND
  • Rigby MR, Harris KM, Pinckney A, DiMeglio LA, Rendell MS, Felner EI, Dostou JM, Gitelman SE, Griffin KJ, Tsalikian E, Gottlieb PA, Greenbaum CJ, Sherry NA, Moore WV, Monzavi R, Willi SM, Raskin P, Keyes-Elstein L, Long SA, Kanaparthi S, Lim N, Phippard D, Soppe CL, Fitzgibbon ML, McNamara J, Nepom GT, Ehlers MR. Alefacept provides sustained clinical and immunological effects in new-onset type 1 diabetes patients. J Clin Invest. 2015 Aug 3;125(8):3285-96. doi: 10.1172/JCI81722. Epub 2015 Jul 20.

    PMID: 26193635BACKGROUND
  • Rigby MR, DiMeglio LA, Rendell MS, Felner EI, Dostou JM, Gitelman SE, Patel CM, Griffin KJ, Tsalikian E, Gottlieb PA, Greenbaum CJ, Sherry NA, Moore WV, Monzavi R, Willi SM, Raskin P, Moran A, Russell WE, Pinckney A, Keyes-Elstein L, Howell M, Aggarwal S, Lim N, Phippard D, Nepom GT, McNamara J, Ehlers MR; T1DAL Study Team. Targeting of memory T cells with alefacept in new-onset type 1 diabetes (T1DAL study): 12 month results of a randomised, double-blind, placebo-controlled phase 2 trial. Lancet Diabetes Endocrinol. 2013 Dec;1(4):284-94. doi: 10.1016/S2213-8587(13)70111-6. Epub 2013 Sep 23.

    PMID: 24622414BACKGROUND

Related Links

Biospecimen

Retention: SAMPLES WITHOUT DNA

* Blood or urine tests as needed to follow-up on potential long term safety concerns with a particular therapeutic agent * Blood and urine samples for additional studies related to your diabetes

MeSH Terms

Conditions

Diabetes Mellitus, Type 1Insulin ResistanceGlucose Intolerance

Condition Hierarchy (Ancestors)

Diabetes MellitusGlucose Metabolism DisordersMetabolic DiseasesNutritional and Metabolic DiseasesEndocrine System DiseasesAutoimmune DiseasesImmune System DiseasesHyperinsulinismHyperglycemia

Study Officials

  • Linda A. DiMeglio, MD, MPH,MA

    Riley Hospital for Children at Indiana University Health

    STUDY CHAIR

Study Design

Study Type
observational
Observational Model
COHORT
Time Perspective
PROSPECTIVE
Sponsor Type
NIH
Responsible Party
SPONSOR

Study Record Dates

First Submitted

April 6, 2016

First Posted

April 12, 2016

Study Start

August 18, 2016

Primary Completion (Estimated)

August 1, 2028

Study Completion (Estimated)

August 1, 2028

Last Updated

March 10, 2026

Record last verified: 2026-03

Data Sharing

IPD Sharing
Will share

The plan is to share data in: 1.)ImmPort, a long-term archive of clinical and mechanistic data from DAIT-funded grants and contracts that also provides data analysis tools that are available to researchers who register online and subsequently receive DAIT approval; and 2.)TrialShare, a clinical trials research portal developed by the Immune Tolerance Network that makes data from the consortium's clinical trials publicly available without charge.

Time Frame
After completion of the study.
Access Criteria
Will be available to the public.
More information

Locations