NCT01049633

Brief Summary

Type 1 diabetes is an autoimmune disease in which the insulin-producing pancreatic beta cells are destroyed, resulting in poor blood sugar control. The purpose of this study is to determine the safety and effectiveness of islet transplantation, combined with immunosuppressive medications and medications to support islet survival for treating type 1 diabetes in individuals experiencing hypoglycemia unawareness and severe hypoglycemic episodes.

Trial Health

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Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Geographic Reach
1 country

1 active site

Status
unknown

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

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Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

January 12, 2010

Completed
2 days until next milestone

First Posted

Study publicly available on registry

January 14, 2010

Completed
Last Updated

June 11, 2014

Status Verified

June 1, 2014

First QC Date

January 12, 2010

Last Update Submit

June 9, 2014

Conditions

Keywords

Insulin dependenceHypoglycemiaHypoglycemia unawarenessIslet transplantation

Interventions

200mL sterile suspension of allogeneic human pancreatic islets

Dosed to maintain whole blood 24-hr trough levels 10-15ng/mL for first 3 months and 8-12ng/mL thereafter daily. Sirolimus is used to prevent transplant rejection.

BasiliximabBIOLOGICAL

20mg intravenously (IV) 2hrs prior to islet infusion and on Day 4 post-transplant. Basiliximab is used to prevent transplant rejection

Initial dose of 0.015mg/kg p.o. daily on Day 1 post transplant, and adjusted to maintain 12-hr trough levels 3-6ng/mL. Tacrolimus lowers the risk of organ rejection

Broad spectrum antimicrobial prophylaxis administered preoperatively

80mg/400mg by mouth once a day starting on Day 1 for duration of the study follow-up. This medication is used to prevent bacterial infections.

Also known as: Septra SS

1 troche by mouth 4 times daily starting two days prior to transplant until 3 months after the transplant. This medication is used to prevent fungal infections.

Also known as: Mycelex Troche

450mg dose by mouth once a day starting two days pre-transplant and increasing to 900 mg once a day by Day 12 and continuing for 14 weeks post-transplant. This medication is used to prevent cytomegalovirus infections.

Also known as: Valcyte

70U/kg body weight of recipient given with islet infusion, followed by 3U/kg/hr for the next 4hrs. From 5th through 48th hr post-transplant heparin will be titrated to achieve and maintain a Partial Thromboplastin Time (PTT) of 50-60 seconds. This medication is used to prevent the formation of blood clots.

Also known as: Anticoagulation and Hematological Agent

30mg subcutaneously twice a day from 48 hrs post-transplant through Day 7 post-transplant. This medication is used to prevent the formation of blood clots.

Also known as: Lovenox; Anticoagulation and Hematological Agent

400mg slow release tablet by mouth three times a day beginning 2 days prior to transplant and continue for 7 days post transplant. This medication improves blood flow.

Also known as: Anticoagulation and Hematological Agent

81mg enteric coated aspirin by mouth every night, starting 24hrs post-transplant. This medication prevents blood clots.

Also known as: ASA, Anticoagulation and Hematological Agent

Eligibility Criteria

Sexall
Healthy VolunteersNo
Age GroupsChild (0-17), Adult (18-64), Older Adult (65+)

You may qualify if:

  • Enrolled in clinical trial DAIT CIT-05 (NCT00468442)
  • Islet graft failure: absent stimulated C-peptide (\<0.3ng/mL) in response to mixed meal tolerance test

You may not qualify if:

  • Untreated proliferative diabetic retinopathy
  • Blood Pressure: systolic blood pressure\>160mmHg or diastolic blood pressure\>100mmHg
  • Measured glomerular filtration rate (GFR) using iohexol \< 80ml/min/1.73m\^2 Strict vegetarians with a calculated GFR \< 70ml/min/1.73m\^2
  • Presence or history of macroalbuminuria \> 300mg/g of creatinine
  • Presence or history of panel-reactive anti-HLA antibodies above background by flow cytometry
  • For female participants: Positive Pregnancy Test, presently breast-feeding, or unwillingness to use effective contraceptive measures for the duration of the study and 3 months after discontinuation. For male participants: intent to procreate during the duration of the study or within 3 months after discontinuation or unwillingness to use effective measures of contraception. Oral contraceptives, Norplant, Depo-Provera and barrier devices with spermicide are acceptable contraceptive methods; condoms used alone are not acceptable.
  • Active infection including hepatitis B, hepatitis C, HIV, or TB as determined by a positive skin test or clinical presentation, or under treatment for suspected TB. Positive tests are acceptable only if associated with a history of previous vaccination in the absence of any sign of active infection. Positive tests are otherwise not acceptable, even in the absence of any active infection at the time of evaluation.
  • Negative screen for Epstein-Barr Virus (EBV) by IgG determination
  • Invasive aspergillus, histoplasmosis, or coccidiomycosis infection within one year prior to study enrollment
  • Any history of malignancy except for completely resected squamous or basal cell carcinoma of the skin
  • Known active alcohol or substance abuse
  • Anemia (Hgb \< 11 g/dL),neutropenia (\<1,500/µL), or thrombocytopenia (platelets \<100,000/µL)
  • A history of Factor V deficiency
  • Any coagulopathy or medical condition requiring long-term anticoagulant therapy (e.g., warfarin) after transplantation (low-dose aspirin treatment is allowed) or patients with an International Normalized Ratio (INR) \>1.5
  • Severe co-existing cardiac disease, characterized by any one of these conditions:
  • +15 more criteria

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (1)

Hospital of the University of Pennsylvania

Philadelphia, Pennsylvania, 19104, United States

Location

Related Links

MeSH Terms

Conditions

Diabetes Mellitus, Type 1Hypoglycemia

Interventions

SirolimusBasiliximabTacrolimusAnti-Infective AgentsAntifungal AgentsTrimethoprim, Sulfamethoxazole Drug CombinationClotrimazoleValganciclovirHeparinEnoxaparinPentoxifyllineAspirin

Condition Hierarchy (Ancestors)

Diabetes MellitusGlucose Metabolism DisordersMetabolic DiseasesNutritional and Metabolic DiseasesEndocrine System DiseasesAutoimmune DiseasesImmune System Diseases

Intervention Hierarchy (Ancestors)

MacrolidesLactonesOrganic ChemicalsAntibodies, Monoclonal, HumanizedAntibodies, MonoclonalAntibodiesImmunoglobulinsImmunoproteinsBlood ProteinsProteinsAmino Acids, Peptides, and ProteinsSerum GlobulinsGlobulinsTherapeutic UsesPharmacologic ActionsChemical Actions and UsesSulfamethoxazoleBenzenesulfonamidesSulfonamidesAmidesSulfanilamidesAniline CompoundsAminesBenzene DerivativesHydrocarbons, AromaticHydrocarbons, CyclicHydrocarbonsSulfonesSulfur CompoundsTrimethoprimPyrimidinesHeterocyclic Compounds, 1-RingHeterocyclic CompoundsDrug CombinationsPharmaceutical PreparationsImidazolesAzolesGanciclovirAcyclovirGuanineHypoxanthinesPurinonesPurinesHeterocyclic Compounds, 2-RingHeterocyclic Compounds, Fused-RingGlycosaminoglycansPolysaccharidesCarbohydratesHeparin, Low-Molecular-WeightTheobromineXanthinesSalicylatesHydroxybenzoatesPhenols

Study Design

Study Type
expanded access
Sponsor Type
NIH
Responsible Party
SPONSOR

Study Record Dates

First Submitted

January 12, 2010

First Posted

January 14, 2010

Last Updated

June 11, 2014

Record last verified: 2014-06

Locations