NCT02696993

Brief Summary

This phase I/II trial studies the side effects and best dose of nivolumab when giving together with stereotactic radiosurgery or whole brain radiotherapy with or without ipilimumab and to see how well they work in treating patients with non-small cell lung cancer that has spread to the brain. Monoclonal antibodies, such as nivolumab and ipilimumab, may interfere with the ability of tumor cells to grow and spread. Stereotactic radiosurgery is a specialized radiation therapy that delivers a single, high dose of radiation directly to the tumor and may cause less damage to normal tissue. Radiation therapy, such as whole-brain radiotherapy, uses high energy x-rays to kill tumor cells and shrink tumors. Giving nivolumab together with stereotactic radiosurgery or whole brain radiotherapy with or without ipilimumab may work better in treating patients with non-small cell lung cancer that has spread to the brain.

Trial Health

75
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
80

participants targeted

Target at P75+ for phase_1

Timeline
20mo left

Started Dec 2016

Longer than P75 for phase_1

Geographic Reach
1 country

1 active site

Status
active not recruiting

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Progress85%
Dec 2016Dec 2027

First Submitted

Initial submission to the registry

February 26, 2016

Completed
5 days until next milestone

First Posted

Study publicly available on registry

March 2, 2016

Completed
10 months until next milestone

Study Start

First participant enrolled

December 16, 2016

Completed
11 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

December 31, 2027

Expected
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

December 31, 2027

Last Updated

November 10, 2025

Status Verified

November 1, 2025

Enrollment Period

11 years

First QC Date

February 26, 2016

Last Update Submit

November 5, 2025

Conditions

Outcome Measures

Primary Outcomes (3)

  • Recommended phase 2 dose (RP2D) of nivolumab defined as the probability of > 15% intracranial or > 30% extracranial dose limiting toxicities (DLT) (Phase I)

    Assessed using a Bayesian model.

    Up to 6 weeks

  • RP2D of nivolumab in combination with ipilimumab defined as the probability of > 15% intracranial or > 30% extracranial DLT (Phase I)

    Assessed using a Bayesian model.

    Up to 8 weeks

  • Intracranial progression free survival (PFS) (Phase II)

    Up to 4 months

Secondary Outcomes (1)

  • Neurocognitive changes assessed by the Hopkins Verbal Learning Revised (HVLT-R) total recall test (Phase II)

    1 month after radiation to 3 years

Study Arms (4)

Group A (nivolumab, SRS)

EXPERIMENTAL

Patients receive nivolumab IV over 90 minutes every 2 weeks in the absence of disease progression or unacceptable toxicity. Patients undergo SRS once the day after nivolumab administration.

Procedure: Cognitive AssessmentOther: Laboratory Biomarker AnalysisBiological: NivolumabRadiation: Stereotactic Radiosurgery

Group B (nivolumab, WBRT)

EXPERIMENTAL

Patients then receive nivolumab as in Group A. Patients undergo WBRT once daily for 10 days.

Procedure: Cognitive AssessmentOther: Laboratory Biomarker AnalysisBiological: NivolumabRadiation: Whole-Brain Radiotherapy

Group C (nivolumab, ipilimumab, SRS)

EXPERIMENTAL

Patients receive nivolumab as in Group A and ipilimumab IV over 90 minutes every 6 weeks in the absence of disease progression or unacceptable toxicity. Patients undergo SRS once the day after nivolumab administration.

Procedure: Cognitive AssessmentBiological: IpilimumabOther: Laboratory Biomarker AnalysisBiological: NivolumabRadiation: Stereotactic Radiosurgery

Group D (nivolumab, ipilimumab, WBRT)

EXPERIMENTAL

GROUP D: Patients receive nivolumab as in Group A and ipilimumab as in Group C. Patients undergo WBRT once daily for 10 days.

Procedure: Cognitive AssessmentBiological: IpilimumabOther: Laboratory Biomarker AnalysisBiological: NivolumabRadiation: Whole-Brain Radiotherapy

Interventions

Ancillary studies

Group A (nivolumab, SRS)Group B (nivolumab, WBRT)Group C (nivolumab, ipilimumab, SRS)Group D (nivolumab, ipilimumab, WBRT)
IpilimumabBIOLOGICAL

Given IV

Also known as: Anti-Cytotoxic T-Lymphocyte-Associated Antigen-4 Monoclonal Antibody, BMS-734016, MDX-010, MDX-CTLA4, Yervoy
Group C (nivolumab, ipilimumab, SRS)Group D (nivolumab, ipilimumab, WBRT)

Correlative studies

Group A (nivolumab, SRS)Group B (nivolumab, WBRT)Group C (nivolumab, ipilimumab, SRS)Group D (nivolumab, ipilimumab, WBRT)
NivolumabBIOLOGICAL

Given IV

Also known as: BMS-936558, MDX-1106, NIVO, ONO-4538, Opdivo
Group A (nivolumab, SRS)Group B (nivolumab, WBRT)Group C (nivolumab, ipilimumab, SRS)Group D (nivolumab, ipilimumab, WBRT)

Undergo SRS

Also known as: Stereotactic External Beam Irradiation, stereotactic external-beam radiation therapy, stereotactic radiation therapy, Stereotactic Radiotherapy, stereotaxic radiation therapy, stereotaxic radiosurgery
Group A (nivolumab, SRS)Group C (nivolumab, ipilimumab, SRS)

Undergo WBRT

Also known as: WBRT, whole-brain radiation therapy
Group B (nivolumab, WBRT)Group D (nivolumab, ipilimumab, WBRT)

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Pathologically confirmed non-small lung cancer
  • Stage IV metastatic disease with intracranial disease visible with magnetic resonance image (MRI)
  • At least one brain lesion size \>= 0.3 cm in the longest axis amenable to radiation therapy (either via SRS or WBRT)
  • Be willing and able to provide written informed consent/assent for the trial
  • Have a performance status of 0 or 1 on the Eastern Cooperative Oncology Group (ECOG) performance scale
  • Absolute neutrophil count (ANC) \>= 1,000 /mcL (performed 28 days prior to study registration up to the first dose of study drug)
  • Platelets \>= 100,000 /mcL (performed 28 days prior to study registration up to the first dose of study drug)
  • Hemoglobin \>= 9 g/dL or \>= 5.6 mmol/L (performed 28 days prior to study registration up to the first dose of study drug)
  • Serum creatinine or measured or calculated creatinine clearance (glomerular filtration rate \[GFR\] can also be used in place of creatinine or creatinine clearance \[CrCl\]) =\< 1.5 X upper limit of normal (ULN) or \>= 40 mL/min CrCl using the Cockroft-Gault formula (performed 28 days prior to study registration up to the first dose of study drug)
  • Serum total bilirubin =\< 1.5 X ULN (except for subjects with Gilbert syndrome, who may have total bilirubin \< 3.0 mg/dl) or direct bilirubin =\< ULN for subjects with total bilirubin levels \> 1.5 x ULN (performed 28 days prior to study registration up to the first dose of study drug)
  • Aspartate aminotransferase (AST \[serum glutamic-oxaloacetic transaminase (SGOT)\]) and alanine aminotransferase (ALT \[serum glutamate pyruvate transaminase (SGPT)\]) =\< 3 X ULN or =\< 5 X ULN for subjects with the liver metastases (performed 28 days prior to study registration up to the first dose of study drug)
  • International normalized ratio (INR) or prothrombin time (PT) =\< 1.5 X ULN unless subject is receiving anticoagulant therapy as long as PT or partial thromboplastin time (PTT) is within therapeutic range of intended use of anticoagulants (performed 28 days prior to study registration up to the first dose of study drug)
  • Activated partial thromboplastin time (aPTT) =\< 1.5 X ULN unless subject is receiving anticoagulant therapy as long as PT or PTT is within therapeutic range of intended use of anticoagulants (performed 28 days prior to study registration up to the first dose of study drug)
  • Female subject of childbearing potential should have a negative urine or serum pregnancy within 24 hours of study enrollment up to administration of the dose of study drug; if the urine test is positive or cannot be confirmed as negative, a serum pregnancy test will be required
  • Female subjects of childbearing potential should be willing to use 2 methods of birth control or be surgically sterile, or abstain from heterosexual activity for the course of the study through 31 weeks after the last dose of study medication; subjects of childbearing potential are those who have not been surgically sterilized or have not been free from menses for \> 1 year
  • +3 more criteria

You may not qualify if:

  • Is currently participating in or has participated in a study of an investigational agent or using an investigational device within 4 weeks of the first dose of treatment or 5 half-lives, whichever is shorter
  • Has a diagnosis of severe active scleroderma, lupus, other rheumatologic or autoimmune disease within the past 3 months; patients with a documented history of clinically severe autoimmune disease or a syndrome requiring systemic steroids or immunosuppressive agents will not be allowed on this study; subjects with vitiligo or resolved childhood asthma/atopy are an exception to this rule; subjects that require intermittent use of bronchodilators or local steroid injections are not excluded from the study; subjects with hypothyroidism stable on hormone replacement are not excluded from this study
  • Has had a prior monoclonal antibody within 4 weeks or 5 half-lives, whichever is shorter, prior to study day 1 or who has not recovered (i.e., =\< grade 1 or at baseline) from adverse events due to agents administered more than 4 weeks earlier
  • For the nivolumab only arm patients who received anti PD1 or anti PD-L1 therapies will be excluded, for ipilimumab and nivolumab arms patients who received anti PD1 or anti PD L1 therapies will be eligible
  • Has had prior chemotherapy or targeted small molecule therapy within 3 weeks prior to administration of the study drug or who has not recovered (i.e., =\< grade 1 or at baseline) from adverse events due to a previously administered agent; \*Note: Subjects with permanent =\< grade 2 toxicities (e.g. neuropathy) or toxicities corrected through routine medical management (e.g. thyroid replacement for hypothyroidism), are an exception to this criterion and may qualify for the study; \*Note: If subject received major surgery, they must have recovered adequately from the toxicity and/or complications from the intervention prior to starting therapy; \*Note: Subjects with =\< grade 2 amylase or lipase elevations abnormalities that have no corresponding clinical manifestations (e.g. manifestation of pancreatitis), are an exception to this criterion and may qualify for the study
  • Has a known additional malignancy that is progressing or requires active treatment; exceptions include basal cell carcinoma of the skin, squamous cell carcinoma of the skin, indolent lymphomas, or in situ cervical cancer that has undergone potentially curative therapy
  • Has known carcinomatous meningitis (also known as leptomeningeal disease)
  • Has an active infection requiring intravenous systemic therapy or hospital admission
  • Has a history or current evidence of any condition, therapy, or laboratory abnormality, including psychiatric or substance abuse disorder, that might confound the results of the trial, interfere with the subject's participation for the full duration of the trial, or is not in the best interest of the subject to participate, in the opinion of the treating investigator
  • Is pregnant or breastfeeding, or expecting to conceive or father children within the projected duration of the trial, starting with the screening visit through 31 weeks after the last dose of trial treatment
  • Has a known history of human immunodeficiency virus (HIV) (HIV 1/2 antibodies)
  • Patients should be excluded if they are positive test for hepatitis B virus surface antigen (HBV sAg) or hepatitis C virus ribonucleic acid (hepatitis C virus \[HCV\] antibody) indicating acute or chronic infection
  • Has received a live vaccine 30 days prior to the first dose of trial treatment
  • Has experienced grade 4 toxicity on treatment with prior radiation
  • Has experienced grade 3-4 intracranial toxicity (hypophysitis or CNS toxicity) with either prior intracranial radiation, anti programmed cell death-1 (PD-1), or cytotoxic t-lymphocyte-associated protein 4 (CTLA-4) inhibitor therapy
  • +5 more criteria

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (1)

M D Anderson Cancer Center

Houston, Texas, 77030, United States

Location

Related Links

MeSH Terms

Conditions

Brain NeoplasmsCarcinoma, Non-Small-Cell Lung

Interventions

Mental Status and Dementia TestsIpilimumabCTLA-4 AntigenNivolumabRadiosurgery

Condition Hierarchy (Ancestors)

Central Nervous System NeoplasmsNervous System NeoplasmsNeoplasms by SiteNeoplasmsBrain DiseasesCentral Nervous System DiseasesNervous System DiseasesCarcinoma, BronchogenicBronchial NeoplasmsLung NeoplasmsRespiratory Tract NeoplasmsThoracic NeoplasmsLung DiseasesRespiratory Tract Diseases

Intervention Hierarchy (Ancestors)

Neuropsychological TestsPsychological TestsBehavioral Disciplines and ActivitiesAntibodies, Monoclonal, HumanizedAntibodies, MonoclonalAntibodiesImmunoglobulinsImmunoproteinsBlood ProteinsProteinsAmino Acids, Peptides, and ProteinsSerum GlobulinsGlobulinsImmune Checkpoint ProteinsCostimulatory and Inhibitory T-Cell ReceptorsReceptors, ImmunologicReceptors, Cell SurfaceMembrane ProteinsAntigens, Differentiation, T-LymphocyteAntigens, DifferentiationAntigens, SurfaceAntigensBiological FactorsBiomarkersRadiotherapyTherapeuticsStereotaxic TechniquesNeurosurgical ProceduresSurgical Procedures, OperativeInvestigative Techniques

Study Officials

  • Jing Li

    M.D. Anderson Cancer Center

    PRINCIPAL INVESTIGATOR

Study Design

Study Type
interventional
Phase
phase 1
Allocation
NON RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
OTHER
Responsible Party
SPONSOR

Study Record Dates

First Submitted

February 26, 2016

First Posted

March 2, 2016

Study Start

December 16, 2016

Primary Completion (Estimated)

December 31, 2027

Study Completion (Estimated)

December 31, 2027

Last Updated

November 10, 2025

Record last verified: 2025-11

Locations