NCT02617589

Brief Summary

The purpose of this study is to evaluate patients with glioblastoma that is MGMT-unmethylated (the MGMT gene is not altered by a chemical change). Patients will receive Nivolumab every two weeks in addition to radiation therapy, and then every four weeks. They will be compared to patients receiving standard therapy with temozolomide in addition to radiation therapy.

Trial Health

98
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Strong global presence with extensive site network
Enrollment
560

participants targeted

Target at P75+ for phase_3

Timeline
Completed

Started Mar 2016

Longer than P75 for phase_3

Geographic Reach
18 countries

120 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

November 26, 2015

Completed
5 days until next milestone

First Posted

Study publicly available on registry

December 1, 2015

Completed
3 months until next milestone

Study Start

First participant enrolled

March 1, 2016

Completed
2.9 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

January 17, 2019

Completed
2 years until next milestone

Results Posted

Study results publicly available

February 3, 2021

Completed
1.1 years until next milestone

Study Completion

Last participant's last visit for all outcomes

March 4, 2022

Completed
Last Updated

March 28, 2023

Status Verified

March 1, 2023

Enrollment Period

2.9 years

First QC Date

November 26, 2015

Results QC Date

November 30, 2020

Last Update Submit

March 1, 2023

Conditions

Outcome Measures

Primary Outcomes (1)

  • Overall Survival (OS)

    OS is defined as the time between the date of randomization and the date of death due to any cause. A participant who has not died will be censored at the last known alive date.

    up to 3 years

Secondary Outcomes (4)

  • Kaplan-Meier Plot of Progression Free Survival

    From randomization to the date of the first documented tumor progression or death due to any cause (up to approximately 6 years)

  • Overall Survival Rate at 24 Months

    At 24 Months

  • Overall Survival in Tumor Mutational Burden (TMB) High Population

    From randomization to the date of death due to any cause (up to approximately 6 years)

  • Progression Free Survival in Tumor Mutational Burden (TMB) High Population

    From randomization to the date of the first documented tumor progression or death due to any cause (up to approximately 6 years)

Study Arms (2)

Nivolumab + Radiotherapy Arm

EXPERIMENTAL

Nivolumab IV infusion + Radiotherapy dose as specified

Drug: NivolumabRadiation: Radiotherapy

Temozolomide + Radiotherapy Arm

ACTIVE COMPARATOR

Temozolomide + Radiotherapy dose as specified

Drug: TemozolomideRadiation: Radiotherapy

Interventions

Nivolumab + Radiotherapy Arm
Temozolomide + Radiotherapy Arm
RadiotherapyRADIATION
Nivolumab + Radiotherapy ArmTemozolomide + Radiotherapy Arm

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Males and Females, age ≥ 18 years old
  • Newly-diagnosed brain cancer or tumor called glioblastoma or GBM
  • Tumor test result shows MGMT unmethylated type
  • Karnofsky performance status of ≥ 70 (able to care for self)

You may not qualify if:

  • Prior treatment for GBM (other than surgical resection)
  • Any known tumor outside of the brain
  • Recurrent or secondary GBM
  • Active known or suspected autoimmune disease
  • Biopsy with less than 20% of tumor removed

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (125)

University of Alabama at Birmingham

Birmingham, Alabama, 35294-3410, United States

Location

Local Institution - 0083

Phoenix, Arizona, 85013, United States

Location

Cedars Sinai Medical Center

Los Angeles, California, 90048, United States

Location

Local Institution - 0019

Los Angeles, California, 90095-1769, United States

Location

Sutter Institute For Medical Research

Sacramento, California, 95816, United States

Location

Sharp Memorial Hospital

San Diego, California, 92123, United States

Location

The Regents of the University of California, San Francisco

San Francisco, California, 94143-0372, United States

Location

Yale Cancer Center

New Haven, Connecticut, 06520, United States

Location

Georgetown University Medical Center

Washington D.C., District of Columbia, 20007, United States

Location

University Of Miami Sylvester Comprehensive Cancer Center

Miami, Florida, 33136, United States

Location

Moffitt Cancer Center

Tampa, Florida, 33612, United States

Location

Emory University - Winship Cancer Institute

Atlanta, Georgia, 30322, United States

Location

The University Of Chicago

Chicago, Illinois, 60637, United States

Location

University Of Kansas Medical Center

Westwood, Kansas, 66205, United States

Location

Norton Cancer Institute

Louisville, Kentucky, 40202, United States

Location

Johns Hopkins University School Of Medicine

Baltimore, Maryland, 21287, United States

Location

Dana-Farber Cancer Institute

Boston, Massachusetts, 02215, United States

Location

Massachusetts General Hospital

Boston, Massachusetts, 02215, United States

Location

Local Institution - 0006

Detroit, Michigan, 48202, United States

Location

Washington University School OF Medicine-Siteman Cancer Center

St Louis, Missouri, 63110, United States

Location

JFK Medical Center

Edison, New Jersey, 08820, United States

Location

Local Institution - 0064

Hackensack, New Jersey, 07601, United States

Location

Columbia University Medical Center (Cumc)

New York, New York, 10032, United States

Location

Memorial Sloan Kettering Cancer Center

New York, New York, 10065, United States

Location

Levine Cancer Institute

Charlotte, North Carolina, 28204, United States

Location

Preston Robert Tisch Brain Tumor Center at Duke University

Durham, North Carolina, 27710, United States

Location

Local Institution - 0010

Cleveland, Ohio, 44195, United States

Location

Local Institution - 0095

Columbus, Ohio, 43210, United States

Location

Local Institution - 0132

Allentown, Pennsylvania, 18103, United States

Location

Local Institution - 0007

Philadelphia, Pennsylvania, 19107, United States

Location

Medical University Of South Carolina

Charleston, South Carolina, 29425, United States

Location

Local Institution - 0090

Chattanooga, Tennessee, 37404, United States

Location

Vanderbilt University Medical Center

Nashville, Tennessee, 37232, United States

Location

University Of Texas Southwestern Medical Center

Dallas, Texas, 75390-8852, United States

Location

University Of Texas Md Anderson Cancer Ctr

Houston, Texas, 77030, United States

Location

Local Institution - 0068

Salt Lake City, Utah, 84112, United States

Location

Swedish Neuroscience Institute

Seattle, Washington, 98122, United States

Location

Royal North Shore Hospital

St Leonards, New South Wales, 2065, Australia

Location

Local Institution - 0003

Heidelberg, Victoria, 3084, Australia

Location

Local Institution - 0004

Prahran, Victoria, 3181, Australia

Location

Local Institution - 0001

Nedlands, Western Australia, 6009, Australia

Location

Local Institution - 0002

New South Wales, 2170, Australia

Location

Local Institution - 0061

Linz, 4020, Austria

Location

Local Institution - 0060

Vienna, 1090, Austria

Location

Universitair Ziekenhuis Brussel

Brussels, 1090, Belgium

Location

Cliniques Universitaires Saint-Luc

Brussels, 1200, Belgium

Location

Uz Leuven

Leuven, 3000, Belgium

Location

BC Cancer - Vancouver

Vancouver, British Columbia, V5Z 4E6, Canada

Location

Princess Margaret Cancer Centre

Toronto, Ontario, M5G 2M9, Canada

Location

Montreal Neurological Institute and Hospital

Montreal, Quebec, H3A 2B4, Canada

Location

Local Institution

Copenhagen, 2100, Denmark

Location

Local Institution

Odense, 5000, Denmark

Location

Local Institution - 0032

Bron, 69677, France

Location

Local Institution

Lille, 59037, France

Location

Local Institution - 0024

Marseille, 13005, France

Location

Local Institution - 0101

Nancy, 54035, France

Location

Local Institution - 0023

Paris, 75010, France

Location

Local Institution - 0038

Paris, 75651, France

Location

Centre Eugene Marquis

Rennes, 35000, France

Location

Local Institution - 0106

Toulouse, 31100, France

Location

Local Institution - 0051

Bonn, 53105, Germany

Location

Local Institution - 0139

Cologne, 50937, Germany

Location

Local Institution - 0072

Erlangen, 91054, Germany

Location

Local Institution - 0049

Frankfurt am Main, 60528, Germany

Location

Local Institution - 0073

Freiburg im Breisgau, 79106, Germany

Location

Local Institution - 0054

Hamburg, 20246, Germany

Location

Local Institution - 0052

Heidelberg, 69120, Germany

Location

Local Institution - 0138

Munich, 81675, Germany

Location

Local Institution - 0050

Münster, 48149, Germany

Location

Local Institution - 0055

Regensburg, 93053, Germany

Location

Local Institution - 0056

Tübingen, 72076, Germany

Location

Local Institution - 0096

Petah Tikva, 49100, Israel

Location

Local Institution - 0097

Tel Aviv, 64239, Israel

Location

Local Institution - 0076

Bologna, 40139, Italy

Location

Local Institution - 0079

Milan, 20133, Italy

Location

Local Institution - 0126

Padua, 35128, Italy

Location

Local Institution - 0135

Rozzano (milano), 20089, Italy

Location

Local Institution - 0078

Siena, 53100, Italy

Location

Local Institution - 0077

Torino, 10126, Italy

Location

Local Institution - 0115

Nagoya, Aichi-ken, 4668560, Japan

Location

Local Institution - 0125

Chiba, Chiba, 2608677, Japan

Location

Local Institution - 0123

Hiroshima, Hiroshima, 7348551, Japan

Location

Local Institution - 0122

Sapporo, Hokkaido, 0608648, Japan

Location

Local Institution - 0129

Kobe, Hyōgo, 6500017, Japan

Location

Local Institution - 0111

Tsukuba, Ibaraki, 3058576, Japan

Location

Local Institution - 0121

Kanazawa, Ishikawa-ken, 9200934, Japan

Location

Local Institution - 0131

Kagoshima, Kagoshima-ken, 8908520, Japan

Location

Local Institution - 0133

Sagamihara-shi, Kanagawa, 2520375, Japan

Location

Local Institution - 0119

Kumamoto, Kumamoto, 8608556, Japan

Location

Local Institution - 0117

Kyoto, Kyoto, 606-8507, Japan

Location

Local Institution - 0116

Kyoto, Kyoto, 6128555, Japan

Location

Local Institution - 0134

Okayama, Okayama-ken, 7008558, Japan

Location

Local Institution

Hirakata-shi, Osaka, 5731191, Japan

Location

Local Institution - 0130

Suita-shi, Osaka, 565-0871, Japan

Location

Local Institution - 0113

Hidaka, Saitama, 350-1298, Japan

Location

Local Institution - 0128

Bunkyo-ku, Tokyo, 1138655, Japan

Location

Local Institution - 0114

Chuo-ku, Tokyo, 1040045, Japan

Location

Local Institution - 0118

Mitaka-shi, Tokyo, 181-8611, Japan

Location

Local Institution - 0110

Yamagata, Yamagata, 9909585, Japan

Location

Local Institution - 0112

Tokyo, 1628666, Japan

Location

NKI AVL

Amsterdam, 1066 CX, Netherlands

Location

Universitair Medisch Centrum Groningen

Groningen, 9713 AP, Netherlands

Location

Erasmus Mc

Rotterdam, 3015 CE, Netherlands

Location

Local Institution - 0063

Utrecht, 3584CX, Netherlands

Location

Local Institution

Oslo, 0379, Norway

Location

Local Institution - 0080

Gdansk, 80952, Poland

Location

Local Institution - 0081

Warsaw, 02-781, Poland

Location

Local Institution - 0070

Moscow, 105229, Russia

Location

Local Institution - 0105

Moscow, 115478, Russia

Location

Local Institution

Badalona-Barcelona, 08916, Spain

Location

Local Institution

Barcelona, 08035, Spain

Location

Local Institution - 0028

Barcelona, 08036, Spain

Location

Local Institution - 0029

Madrid, 28007, Spain

Location

Local Institution

Madrid, 28041, Spain

Location

Local Institution

Santiago de Compostela, 15706, Spain

Location

Local Institution - 0025

Valencia, 46014, Spain

Location

Local Institution

Lund, 221 85, Sweden

Location

Local Institution

Solna, 171 64, Sweden

Location

Local Institution - 0059

Geneva, 1211, Switzerland

Location

Local Institution - 0057

Lausanne, 1011, Switzerland

Location

Local Institution - 0053

Zurich, 8091, Switzerland

Location

University College Hospital

London, Greater London, NW1 2PG, United Kingdom

Location

Christie Hospital Nhs Found. Trust

Manchester, Greater Manchester, M20 4BX, United Kingdom

Location

Royal Marsden Hospital

Sutton, Surrey, SM2 5PT, United Kingdom

Location

Beaston West of Scotland Cancer Centre

Glasgow, G12 0YN, United Kingdom

Location

Related Publications (3)

  • Grkovski M, Daras M, Bale T, Lyashchenko S, Reiner AS, Mellinghoff IK, Schoder H, Dunphy MPS. 18F-BMS-986229 PET imaging of tumor PD-L1 expression in glioblastoma patients. EJNMMI Res. 2025 Sep 26;15(1):124. doi: 10.1186/s13550-025-01283-x.

  • Omuro A, Brandes AA, Carpentier AF, Idbaih A, Reardon DA, Cloughesy T, Sumrall A, Baehring J, van den Bent M, Bahr O, Lombardi G, Mulholland P, Tabatabai G, Lassen U, Sepulveda JM, Khasraw M, Vauleon E, Muragaki Y, Di Giacomo AM, Butowski N, Roth P, Qian X, Fu AZ, Liu Y, Potter V, Chalamandaris AG, Tatsuoka K, Lim M, Weller M. Radiotherapy combined with nivolumab or temozolomide for newly diagnosed glioblastoma with unmethylated MGMT promoter: An international randomized phase III trial. Neuro Oncol. 2023 Jan 5;25(1):123-134. doi: 10.1093/neuonc/noac099.

  • Woroniecka K, Fecci PE. Immuno-synergy? Neoantigen vaccines and checkpoint blockade in glioblastoma. Neuro Oncol. 2020 Sep 29;22(9):1233-1234. doi: 10.1093/neuonc/noaa170. No abstract available.

Related Links

MeSH Terms

Conditions

Brain Neoplasms

Interventions

NivolumabTemozolomideRadiotherapy

Condition Hierarchy (Ancestors)

Central Nervous System NeoplasmsNervous System NeoplasmsNeoplasms by SiteNeoplasmsBrain DiseasesCentral Nervous System DiseasesNervous System Diseases

Intervention Hierarchy (Ancestors)

Antibodies, Monoclonal, HumanizedAntibodies, MonoclonalAntibodiesImmunoglobulinsImmunoproteinsBlood ProteinsProteinsAmino Acids, Peptides, and ProteinsSerum GlobulinsGlobulinsDacarbazineTriazenesOrganic ChemicalsImidazolesAzolesHeterocyclic Compounds, 1-RingHeterocyclic CompoundsTherapeutics

Results Point of Contact

Title
Bristol-Myers Squibb Study Director
Organization
Bristol-Myers Squibb

Study Officials

  • Bristol-Myers Squibb

    Bristol-Myers Squibb

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
LTE60
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR
Expanded Access
Yes

Study Record Dates

First Submitted

November 26, 2015

First Posted

December 1, 2015

Study Start

March 1, 2016

Primary Completion

January 17, 2019

Study Completion

March 4, 2022

Last Updated

March 28, 2023

Results First Posted

February 3, 2021

Record last verified: 2023-03

Locations