NCT01721876

Brief Summary

To investigate the efficacy, safety, and pharmacokinetics of intravenous volasertib + subcutaneous low dose cytarabine in patients \>= 65 years of age with previously untreated acute myeloid leukaemia, ineligible for intensive remission induction therapy

Trial Health

98
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Strong global presence with extensive site network
Enrollment
666

participants targeted

Target at P75+ for phase_3

Timeline
Completed

Started Jan 2013

Longer than P75 for phase_3

Geographic Reach
25 countries

122 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

November 2, 2012

Completed
4 days until next milestone

First Posted

Study publicly available on registry

November 6, 2012

Completed
3 months until next milestone

Study Start

First participant enrolled

January 29, 2013

Completed
1.5 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

August 12, 2014

Completed
6.8 years until next milestone

Study Completion

Last participant's last visit for all outcomes

May 28, 2021

Completed
6 months until next milestone

Results Posted

Study results publicly available

November 19, 2021

Completed
Last Updated

February 8, 2023

Status Verified

February 1, 2023

Enrollment Period

1.5 years

First QC Date

November 2, 2012

Results QC Date

September 9, 2021

Last Update Submit

February 6, 2023

Conditions

Outcome Measures

Primary Outcomes (1)

  • Objective Response (OR)

    OR is the number of patients who achieved complete remission (CR) or complete remission with incomplete blood count recovery (CRi), where OR was based on the best response attained during the treatment period.

    Response assessment was performed at the end of every 2nd cycle, (i.e. at the end of Cycle 2, 4, 6, 8, etc., and at end of treatment), i.e. up to 52 months.

Secondary Outcomes (3)

  • Overall Survival (OS)

    From randomization until death due to any cause, up to 1557 days.

  • Event-free Survival (EFS)

    From randomization until disease progression or relapse or death from any cause, up to 1557 days.

  • Relapse-free Survival (RFS)

    From randomization until disease progression or relapse or death from any cause, up to 1557 days.

Study Arms (2)

Volasertib and Cytarabine

EXPERIMENTAL
Drug: VolasertibDrug: Cytarabine

Placebo and Cytarabine

PLACEBO COMPARATOR
Drug: PlaceboDrug: Cytarabine

Interventions

Placebo matching Volasertib

Placebo and Cytarabine

Volasertib

Volasertib and Cytarabine

Cytarabine

Placebo and CytarabineVolasertib and Cytarabine

Eligibility Criteria

Age65 Years+
Sexall
Healthy VolunteersNo
Age GroupsOlder Adult (65+)

You may qualify if:

  • Age \>= 65years.
  • Cytologically/histologically confirmed acute myeloid leukaemia (AML) according to WHO classification; (except for acute promyelocytic leukaemia (APL).
  • Previously untreated AML (except for hydroxyurea and/or corticosteroid therapy for no more than 28 days (cumulative)). Previous therapy for Myelodysplastic Syndrome (MDS) is allowed.
  • Investigator considers patient ineligible for intensive remission induction therapy based on documented medical reasons (e.g. disease characteristics like AML genetics, type of AML (de novo or secondary), and patient characteristics like performance score, concomitant diagnoses, organ dysfunctions).
  • Patient is eligible for Low-Dose Cytarabine (LDAC) treatment.
  • Eastern co-operative oncology group (ECOG) performance score \<= 2 at screening.
  • Signed and dated written informed consent by start date of Screening visit in accordance with Good Clinical Practice (GCP) and local legislation.

You may not qualify if:

  • Prior or concomitant chemotherapy for AML (with the exception of hydroxyurea and/or corticosteroid therapy for no more than 28 days (cumulative)). Please note that any prior therapy for MDS is allowed.
  • Treatment with any investigational drug within 2 weeks before first administration of present trial drug.
  • Acute promyelocytic leukaemia (French-American-British (FAB) classification subtype M3).
  • Current clinical central nervous system (CNS) symptoms deemed by the investigator to be related to leukaemic CNS involvement (no lumbar puncture required, clinical assessment per investigator´s judgement is sufficient).
  • Hypersensitivity to one of the trial drugs or the excipients.
  • Severe illness or organ dysfunction involving the heart, kidney, liver or other organ system (e.g. active infection, clinically relevant impairment of cardiac function, severe heart failure/cardiac insufficiency, unstable angina pectoris or history of recent myocardial infarction), which in the opinion of the investigator precludes treatment with LDAC.
  • Corrected QT interval according to Fridericia (QTcF) prolongation \> 470 ms or QT prolongation deemed clinically relevant by the investigator (e.g., congenital long QT syndrome).The QTcF will be calculated as the mean of the 3 Electrocardiogram (ECGs) taken at screening.
  • Total bilirubin \> 3 x upper limit of normal (ULN).
  • Creatinine clearance (CLcr) \< 30 ml/min (estimated creatinine clearance by the Cockcroft-Gault (C-G) equation) .
  • Active hepatitis B or hepatitis C, or laboratory evidence for a chronic infection.
  • HIV infection.
  • Second malignancy currently requiring active therapy (except for hormonal/anti-hormonal treatment e.g. in prostate or breast cancer).
  • Any significant concurrent psychiatric disorder or social situation that according to the investigator´s judgement would compromise patient´s safety or compliance, interfere with consent, study participation, or interpretation of study results.
  • Known or suspected active alcohol or drug abuse.
  • Patient unable to comply with the protocol, in the opinion of the investigator.
  • +1 more criteria

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (122)

University of California

Los Angeles, California, 90095-1678, United States

Location

St. Luke's Hospital Association of Duluth, Inc.

Duluth, Minnesota, 55805, United States

Location

Henry-Joyce Cancer Clinic

Nashville, Tennessee, 37232, United States

Location

The University of Texas MD Anderson Cancer Center

Houston, Texas, 77030, United States

Location

Fundacion COIR

Mendoza, M5500AYB, Argentina

Location

Hospital Central de Salud Zenón Santillan

San Miguel de Tucumán, T4000HXU, Argentina

Location

LKH-Univ. Hospital Graz

Graz, 8036, Austria

Location

LKH Leoben

Leoben, 8700, Austria

Location

Hospital Hietzing

Vienna, 1130, Austria

Location

AZ Sint-Jan Brugge

Bruges, 8000, Belgium

Location

Brussels - UNIV Saint-Luc

Brussels, 1200, Belgium

Location

Haine-St-Paul - HOSP Jolimont

Haine-Saint-Paul, 7100, Belgium

Location

Jessa Ziekenhuis - Campus Virga Jesse

Hasselt, 3500, Belgium

Location

UZ Leuven

Leuven, 3000, Belgium

Location

Centre Hospitalier Universitaire de Liège

Liège, 4000, Belgium

Location

Roeselare - HOSP AZ Delta

Roeselare, 8800, Belgium

Location

Yvoir - UNIV UCL de Mont-Godinne

Yvoir, 5530, Belgium

Location

Hospital Doutor Amaral Carvalho

Jaú, 17210-080, Brazil

Location

Hospital Mãe de Deus

Porto Alegre, 90470-340, Brazil

Location

H.C.da Fac. de Medicina de Ribeirao Preto

Ribeirão Preto, 14048-900, Brazil

Location

University of Alberta Hospital (University of Alberta)

Edmonton, Alberta, T6G 2G3, Canada

Location

Vancouver General Hospital

Vancouver, British Columbia, V5Z 1M9, Canada

Location

Maisonneuve-Rosemont Hospital

Montreal, Migration Data, H1T 2M4, Canada

Location

Princess Margaret Cancer Centre

Toronto, Ontario, M5G 2M9, Canada

Location

Montreal General Hospital - McGill University Health Centre

Montreal, Quebec, H3G 1A4, Canada

Location

Hospital Hradec Kralove

Hradec Králové, 500 05, Czechia

Location

University Hospital Plzen, Plzen-Lochotin

Plzen - Lochotin, 304 60, Czechia

Location

Univ. Hospital Kralovske Vinohrady

Prague, 100 34, Czechia

Location

Meilahden sairaala

Helsinki, 00290, Finland

Location

TYKS, Sisätautien klinikka

Turku, 20521, Finland

Location

HOP Amiens-Picardie Sud

Amiens, 80054, France

Location

HOP Côte de Nacre

Caen, 14000, France

Location

HOP Michallon

La Tronche, 38700, France

Location

HOP André Mignot

Le Chesnay, 78157, France

Location

HOP Dupuytren 1

Limoges, 87042, France

Location

INS Paoli-Calmettes

Marseille, 13273, France

Location

HOP Nantes, Hémato, Nantes

Nantes, 44000, France

Location

HOP Saint-Antoine

Paris, 75012, France

Location

HOP Haut-Lévêque

Pessac, 33604, France

Location

HOP Lyon Sud

Pierre-Bénite, 69495, France

Location

HOP Pontchaillou

Rennes, 35033, France

Location

INS Universitaire du Cancer

Toulouse, 31059, France

Location

Universitätsklinikum Augsburg

Augsburg, 86156, Germany

Location

Med. Klinik m.S. Hämatologie und Onkologie

Berlin, 13353, Germany

Location

Städtisches Klinikum Braunschweig gGmbH

Braunschweig, 38114, Germany

Location

Universitätsklinikum Erlangen

Erlangen, 91054, Germany

Location

Ruhrlandklinik, Westdeutsches Lungenzentrum am Universitätsklinikum Essen gGmbH

Essen, 45147, Germany

Location

Universitätsklinikum Frankfurt

Frankfurt am Main, 60590, Germany

Location

Universitätsmedizin Göttingen, Georg-August-Universität

Göttingen, 37075, Germany

Location

Martin-Luther-Universität Halle-Wittenberg

Halle, 06120, Germany

Location

Universitätsklinikum Hamburg-Eppendorf

Hamburg, 20246, Germany

Location

Medizinische Hochschule Hannover

Hanover, 30625, Germany

Location

Universitätsklinikum Heidelberg

Heidelberg, 69120, Germany

Location

Universitätsklinikum Schleswig-Holstein, Campus Kiel

Kiel, 24105, Germany

Location

Universitätsmedizin der Johannes Gutenberg-Universität Mainz

Mainz, 55131, Germany

Location

Universitätsklinikum Gießen und Marburg GmbH

Marburg, 35043, Germany

Location

Klinikum rechts der Isar der Technischen Universität München

München, 81675, Germany

Location

Universitätsklinikum Münster

Münster, 48149, Germany

Location

Universitätsklinikum Regensburg

Regensburg, 93053, Germany

Location

Robert-Bosch-Krankenhaus GmbH

Stuttgart, 70376, Germany

Location

Universitätsklinikum Ulm

Ulm, 89081, Germany

Location

Schwarzwald-Baar Klinikum

Villingen-Schwenningen, 78052, Germany

Location

General Hospital of Athens "G. Gennimatas"

Athens, 115 27, Greece

Location

General Hospital of Athens "Laiko"

Athens, 11526, Greece

Location

Univ. Gen. Hosp. of Ioannina

Ioannina, 45 500, Greece

Location

University of Patras Medical School

Pátrai, 26504, Greece

Location

General Hospital of Thessaloniki "G. Papanikolaou"

Thessaloniki, 57010, Greece

Location

Semmelweis University

Budapest, 1083, Hungary

Location

Petz Aldar Hospital, 2nd Dept. of Internal Med., Haematology

Győr, 9024, Hungary

Location

Univ. of Szeged, 2nd Dept. of Internal Med., Haematology

Szeged, 6725, Hungary

Location

St. John Medical College and hospital

Bangalore, 560034, India

Location

Tata Memorial Hospital

Mumbai, 400012, India

Location

A.O. Spedali Civili di Brescia

Brescia, 25123, Italy

Location

ASST Grande Ospedale Metropolitano Niguarda

Milan, 20162, Italy

Location

AO Città della Salute e della

Torino, 10126, Italy

Location

National Hospital Organization Nagoya Medical Center

Aichi, Nagoya, 460-0001, Japan

Location

Japanese Red Cross Nagoya Daini Hospital

Aichi, Nagoya, 466-8650, Japan

Location

Akita University Hospital

Akita, Akita, 010-8543, Japan

Location

University of Fukui Hospital

Fukui, Yoshida-gun, 910-1193, Japan

Location

Kyushu University Hospital

Fukuoka, Fukuoka, 812-8582, Japan

Location

Kobe University Hospital

Hyogo, Kobe, 650-0017, Japan

Location

Tokai University Hospital

Kanagawa, Isehara, 259-1193, Japan

Location

Yokohama City University Medical Center

Kanagawa, Yokohama, 232-0024, Japan

Location

Tohoku University Hospital

Miyagi, Sendai, 980-8547, Japan

Location

Nagasaki University Hospital

Nagasaki, Nagasaki, 852-8523, Japan

Location

Kurashiki Central Hospital

Okayama, Kurashiki, 710-8602, Japan

Location

Okayama University Hospital

Okayama, Okayama, 700-8558, Japan

Location

Osaka City University Hospital

Osaka, Osaka, 545-8586, Japan

Location

National Cancer Center Hospital

Tokyo, Chuo-ku, 104-0045, Japan

Location

NTT Medical Center Tokyo

Tokyo, Sinagawa-ku, 141-8625, Japan

Location

Hospital Universitario Dr Jose Eleuterio Gonzalez

Monterrey, 64460, Mexico

Location

Amsterdam UMC Locatie VUMC

Amsterdam, 1081 HV, Netherlands

Location

Haukeland Universitetssykehus

Bergen, N-5021, Norway

Location

Sykehuset Østfold Kalnes

Grålum, N-1714, Norway

Location

Reg. Specialist Hospital of M. Kopernik, Dept. Haematology

Lodz, 93-510, Poland

Location

City Hospital Torun, Department of Hematology

Torun, 87-100, Poland

Location

CHULN, EPE - Hospital de Santa Maria

Lisbon, 1649-035, Portugal

Location

Centro Hospitalar Universitário do Porto, EPE - Hospital de Santo António

Porto, 4099-001, Portugal

Location

IPO Porto Francisco Gentil, EPE

Porto, 4200-072, Portugal

Location

Centro Hospitalar Universitário São João,EPE

Porto, 4202-451, Portugal

Location

Regional Clinical Hospital 'The Badge of Honor Order'

Irkutsk, 664079, Russia

Location

FSBI "N.N Blokhin Med.Res.Cent.Onc."MoH of RF

Moscow, 115478, Russia

Location

Nizhniy Novgorod Reg. Clinical Hospital, Dept. Haematology

Nizhny Novgorod, 603126, Russia

Location

Leningrad Reg. Clin. Hosp., Oncohematology Department No. 2

Saint Petersburg, 194291, Russia

Location

Netcare Pretoria East Hospital

Moreleta Park, Pretoria, 0044, South Africa

Location

Chonnam National University Hwasun Hospital

Hwasun, 519-763, South Korea

Location

The Catholic University of Korea, Seoul St.Mary's Hospital

Seoul, 06591, South Korea

Location

Seoul National University Hospital

Seoul, 110-744, South Korea

Location

Severance Hospital

Seoul, 120-752, South Korea

Location

Samsung Medical Center

Seoul, 135-710, South Korea

Location

Asan Medical Center

Seoul, 138-736, South Korea

Location

Hospital Germans Trias i Pujol

Badalona, 08916, Spain

Location

Hospital Santa Creu i Sant Pau

Barcelona, 08025, Spain

Location

Hospital Vall d'Hebron

Barcelona, 08035, Spain

Location

Hospital Clínic de Barcelona

Barcelona, 08036, Spain

Location

Hospital Universitario 12 de Octubre

Madrid, 28041, Spain

Location

Hospital La Paz

Madrid, 28046, Spain

Location

Hospital Universitario de Salamanca

Salamanca, 37007, Spain

Location

Hospital Politècnic La Fe

Valencia, 46009, Spain

Location

Chang-Hua Christian Hospital

Changhua, 500, Taiwan

Location

National Taiwan University Hospital

Taipei, 100, Taiwan

Location

Mackay Memorial Hospital

Taipei, 112, Taiwan

Location

Related Publications (1)

  • Hagege A, Ambrosetti D, Boyer J, Bozec A, Doyen J, Chamorey E, He X, Bourget I, Rousset J, Saada E, Rastoin O, Parola J, Luciano F, Cao Y, Pages G, Dufies M. The Polo-like kinase 1 inhibitor onvansertib represents a relevant treatment for head and neck squamous cell carcinoma resistant to cisplatin and radiotherapy. Theranostics. 2021 Sep 21;11(19):9571-9586. doi: 10.7150/thno.61711. eCollection 2021.

Related Links

MeSH Terms

Conditions

Leukemia, Myeloid, Acute

Interventions

BI 6727Cytarabine

Condition Hierarchy (Ancestors)

Leukemia, MyeloidLeukemiaNeoplasms by Histologic TypeNeoplasmsHematologic DiseasesHemic and Lymphatic Diseases

Intervention Hierarchy (Ancestors)

CytidinePyrimidine NucleosidesPyrimidinesHeterocyclic Compounds, 1-RingHeterocyclic CompoundsArabinonucleosidesNucleosidesNucleic Acids, Nucleotides, and Nucleosides

Limitations and Caveats

The final analysis presented in this report was conducted after 574 Overall Survival events had occurred. The final analysis was exploratory and descriptive.

Results Point of Contact

Title
Boehringer Ingelheim, Call Center
Organization
Boehringer Ingelheim

Study Officials

  • Boehringer Ingelheim

    Boehringer Ingelheim

    STUDY CHAIR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
DOUBLE
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

November 2, 2012

First Posted

November 6, 2012

Study Start

January 29, 2013

Primary Completion

August 12, 2014

Study Completion

May 28, 2021

Last Updated

February 8, 2023

Results First Posted

November 19, 2021

Record last verified: 2023-02

Data Sharing

IPD Sharing
Will not share

Clinical studies sponsored by Boehringer Ingelheim, phases I to IV, interventional and non-interventional, are in scope for sharing of the raw clinical study data and clinical study documents. Exceptions might apply, e.g. studies in products where Boehringer Ingelheim is not the license holder; studies regarding pharmaceutical formulations and associated analytical methods, and studies pertinent to pharmacokinetics using human biomaterials; studies conducted in a single center or targeting rare diseases (in case of low number of patients and therefore limitations with anonymization). For more details refer to: https://www.mystudywindow.com/msw/datatransparency

Locations