NCT03416179

Brief Summary

Glasdegib is being studied in combination with azacitidine for the treatment of adult patients with previously untreated acute myeloid leukemia (AML) who are not candidates for intensive induction chemotherapy (Non-intensive AML population). Glasdegib is being studied in combination with cytarabine and daunorubicin for the treatment of adult patients with previously untreated acute myeloid leukemia (Intensive AML population).

Trial Health

98
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Strong global presence with extensive site network
Enrollment
730

participants targeted

Target at P75+ for phase_3

Timeline
Completed

Started Apr 2018

Typical duration for phase_3

Geographic Reach
21 countries

146 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

December 21, 2017

Completed
1 month until next milestone

First Posted

Study publicly available on registry

January 31, 2018

Completed
3 months until next milestone

Study Start

First participant enrolled

April 20, 2018

Completed
2.1 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

June 5, 2020

Completed
1.1 years until next milestone

Results Posted

Study results publicly available

June 25, 2021

Completed
7 months until next milestone

Study Completion

Last participant's last visit for all outcomes

January 17, 2022

Completed
Last Updated

April 21, 2023

Status Verified

April 1, 2023

Enrollment Period

2.1 years

First QC Date

December 21, 2017

Results QC Date

June 2, 2021

Last Update Submit

April 20, 2023

Conditions

Keywords

glasdegib;untreated;Hedgehog Inhibitor

Outcome Measures

Primary Outcomes (2)

  • Intensive Study: Overall Survival (OS)

    OS is defined as the time from the date of randomization to the date of death due to any cause. Participants last known to be alive were to be censored at the date of last contact.

    Baseline up to 25 months

  • Non-intensive Study: Overall Survival (OS)

    OS is defined as the time from the date of randomization to the date of death due to any cause. Participants last known to be alive were to be censored at the date of last contact.

    Baseline up to 25 months

Secondary Outcomes (42)

  • Intensive Study: Percentage of Participants Who Improved in Fatigue Score Measured by the MD Anderson Symptom Inventory -Acute Myelogenous Leukemia/Myelodysplastic Syndrome (MDASI-AML/MDS) Questionnaire

    Post-baseline up to Week 8

  • Non-intensive Study: Percentage of Participants Who Improved in Fatigue Score Measured by the MDASI-AML/MDS Questionnaire at Week 12

    Post-baseline up to Week 12

  • Intensive Study: Percentage of Participants With Complete Remission Without Negative Minimal Residual Disease (CRMRD-neg)

    Day 1 up to maximum of 2 years

  • Non-intensive Study: Percentage of Participants With Complete Remission Without Negative Minimal Residual Disease (CRMRD-neg)

    Day 1 up to maximum of 3 years

  • Intensive Study: Percentage of Participants With Complete Remission Including Negative Minimal Residual Disease (CRMRD-neg)

    Day 1 up to maximum of 2 years

  • +37 more secondary outcomes

Study Arms (4)

Arm A (Intensive Study)

EXPERIMENTAL

Glasdegib + '7+3' Induction(s)

Drug: glasdegibDrug: daunorubicin + cytarabineDrug: cytarabineProcedure: HSCT

Arm B (Intensive Study)

PLACEBO COMPARATOR

Placebo + '7+3' Induction(s)

Drug: daunorubicin + cytarabineDrug: PlaceboDrug: cytarabineProcedure: HSCT

Arm A (Non-intensive study)

EXPERIMENTAL

Glasdegib + azacitidine

Drug: azacitidineDrug: glasdegib

Arm B (Non-intensive study)

PLACEBO COMPARATOR

Placebo + azacitidine

Drug: azacitidineDrug: Placebo

Interventions

Daily Glasdegib (100 mg, PO), beginning on Day 1 and is to continue up to 2 years post randomization. Following consolidation therapy, glasdegib or placebo will be administered daily for up to 2 years after randomization or until they have minimal residual disease (MRD) negative disease, whichever comes first. Daily Glasdegib (100 mg, PO) or matching placebo will continue throughout Induction(s) and Consolidation therapies regardless of dose modifications/delays in the chemotherapy.

Also known as: PF-04449913
Arm A (Intensive Study)

'7+3' (cytarabine 100 mg/m2, IV for 7 days by continuous infusion and daunorubicin 60 mg/m2 for 3 days). If a second induction is needed, Investigators may choose either a 5 day cytarabine continuous infusion plus daunorubicin for 2 days ('5+2') or a 7 day cytarabine continuous infusion plus daunorubicin for 3 days ('7+3');

Arm A (Intensive Study)Arm B (Intensive Study)

Azacitidine (75 mg/m2, SC or IV) daily for 7 days, in 28 day cycles for as long as they do not meet the criteria for disease progression, unacceptable toxicity, consent withdrawal, or death.

Arm A (Non-intensive study)Arm B (Non-intensive study)

Matching placebo (PO) given on Day 1 and is to continue up to 2 years post randomization. Following consolidation therapy, placebo will be administered daily for up to 2 years after randomization or until they have MRD negative disease, whichever comes first. Daily placebo will continue throughout Induction(s) and Consolidation therapies regardless of dose modifications/delays in the chemotherapy.

Arm B (Intensive Study)

Consolidation with single agent cytarabine 3 g/m2 IV for adults \<60 years and 1 g/m2 for adults 60 years over 3 BID on Days 1, 3, and 5, every 28 days for up to 4 cycles or alternative single agent cytarabine consolidation schedules may be used per local prescribing information.

Arm A (Intensive Study)Arm B (Intensive Study)
HSCTPROCEDURE

If required, and done per standard of care post Induction(s).

Arm A (Intensive Study)Arm B (Intensive Study)

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Subjects with untreated AML according to the World Health Organization (WHO) 2016 Classification2, including those with:
  • AML arising from MDS or another antecedent hematologic disease (AHD).
  • AML after previous cytotoxic therapy or radiation (secondary AML).
  • years of age (In Japan, 20 years of age).
  • Adequate Organ Function as defined by the following:
  • Serum aspartate aminotransferase (AST) and serum alanine aminotransferase (ALT) 3 x upper limit of normal (ULN), excluding subjects with liver function abnormalities due to underlying malignancy.
  • Total serum bilirubin 2 x ULN (except subjects with documented Gilbert's syndrome).
  • Estimated creatinine clearance 30 mL/min as calculated using the standard method for the institution.
  • QTc interval 470 msec using the Fridericia correction (QTcF).
  • All anti cancer treatments (unless specified) should be discontinued 2 weeks from study entry, for example: targeted chemotherapy, radiotherapy, investigational agents, hormones, anagrelide or cytokines.
  • For control of rapidly progressing leukemia, all trans retinoic acid (ATRA), hydroxyurea, and/or leukopheresis may be used before and for up to 1 week after the first dose of glasdegib.
  • Serum or urine pregnancy test (for female subjects of childbearing potential) with a minimum sensitivity of 25 IU/L or equivalent units of human chorionic gonadotropin (hCG) negative at screening.
  • Male and female subjects of childbearing potential and at risk for pregnancy must agree to use at least one highly effective method of contraception throughout the study and for 180 days after the last dose of azacitidine, cytarabine, or daunorubicin; and the last dose of glasdegib or placebo, whichever occurs later.
  • Female subjects of non childbearing potential must meet at least 1 of the following criteria:
  • Have undergone a documented hysterectomy and/or bilateral oophorectomy;
  • +6 more criteria

You may not qualify if:

  • Subjects with any of the following characteristics/conditions will not be included in the study:
  • Acute Promyelocytic Leukemia (APL) and APLwith PML RARA, subjects (WHO 2016 classification).
  • AML with BCR ABL1 or t(9;22)(q34;q11.2) as a sole abnormality.
  • Complex genetics may include t(9;22) cytogenetic translocation.
  • Subjects with known active CNS leukemia.
  • Participation in other clinical studies involving other investigational drug(s) (Phases 1 4) within 4 weeks prior study entry and/or during study participation.
  • Subjects known to be refractory to platelet or packed red cell transfusions per Institutional Guidelines, or a patient who refuses blood product support.
  • Subjects with another active malignancy on treatment with the exception of basal cell carcinoma, non melanoma skin cancer, cervical carcinoma in situ. Other prior or concurrent malignancies will be considered on a case by case basis.
  • Any one of the following ongoing or in the previous 6 months: myocardial infarction, congenital long QT syndrome, Torsades de pointes, symptomatic arrhythmias (including sustained ventricular tachyarrhythmia), right or left bundle branch block and bifascicular block, unstable angina, coronary/peripheral artery bypass graft, symptomatic congestive heart failure (CHF New York Heart Association class III or IV), cerebrovascular accident, transient ischemic attack or symptomatic pulmonary embolism; as well as bradycardia defined as \<50 bpms.
  • Subjects with an active, life threatening or clinically significant uncontrolled systemic infection not related to AML.
  • Subjects with left ventricular ejection fraction (LVEF) \<50% are excluded from the Intensive Chemotherapy Study only.
  • Cumulative anthracycline dose equivalent of 550 mg/m2 of daunorubicin for the Intensive Chemotherapy Study only.
  • Known malabsorption syndrome or other condition that may significantly impair absorption of study medication in the investigator's judgment (eg, gastrectomy, lap band, Crohn's disease) and inability or unwillingness to swallow tablets or capsules.
  • Current use or anticipated requirement for drugs that are known strong CYP3A4/5 inducers.
  • Concurrent administration of herbal preparations.
  • +9 more criteria

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (149)

UCLA Department of Medicine

Los Angeles, California, 90095, United States

Location

UCLA Drug Information/Investigational Drugs

Los Angeles, California, 90095, United States

Location

UCLA Hematology/Oncology Clinic

Los Angeles, California, 90095, United States

Location

UCLA Ronald Reagan Medical Center

Los Angeles, California, 90095, United States

Location

UC Irvine Health - Chao Family Comprehensive Cancer Center

Orange, California, 92868-3201, United States

Location

UCSF Helen Diller Family Comprehensive Cancer Center

San Francisco, California, 94143, United States

Location

University of California, San Francisco

San Francisco, California, 94143, United States

Location

UCLA Hematology/Oncology - Westlake Village

Westlake Village, California, 91361, United States

Location

Augusta University Medical Center

Augusta, Georgia, 30912, United States

Location

Georgia Cancer Center at Augusta University

Augusta, Georgia, 30912, United States

Location

Tufts Medical Center Investigational Drug Pharmacy

Boston, Massachusetts, 02111, United States

Location

Tufts Medical Center

Boston, Massachusetts, 02111, United States

Location

Massachusetts General Hospital

Boston, Massachusetts, 02114, United States

Location

Beth Israel Deaconess Medical Center

Boston, Massachusetts, 02215, United States

Location

MidAmerica Division, Inc., c/o Research Medical Center

Kansas City, Missouri, 64132, United States

Location

Northwell Health/Monter Cancer Center

Lake Success, New York, 11042, United States

Location

North Shore University Hospital

Manhasset, New York, 11030, United States

Location

Long Island Jewish Medical Center

New Hyde Park, New York, 11040, United States

Location

University of Rochester Medical Center

Rochester, New York, 14642, United States

Location

University Hospitals Cleveland Medical Center

Cleveland, Ohio, 44106, United States

Location

Cleveland Clinic Foundation

Cleveland, Ohio, 44195, United States

Location

OHSU Center for Health and Healing

Portland, Oregon, 97239, United States

Location

Oregon Health & Science University

Portland, Oregon, 97239, United States

Location

Centennial Medical Center

Nashville, Tennessee, 37203, United States

Location

TriStar Bone Marrow Transplant

Nashville, Tennessee, 37203, United States

Location

Baylor University Medical Center

Dallas, Texas, 75246, United States

Location

Blood Cancer and Stem Cell Transplant Clinic

San Antonio, Texas, 78229, United States

Location

Methodist Healthcare System of San Antonio

San Antonio, Texas, 78229, United States

Location

Swedish Cancer Institute

Seattle, Washington, 98104, United States

Location

Swedish Medical Center

Seattle, Washington, 98122, United States

Location

St Vincent's Hospital Sydney

Darlinghurst, New South Wales, 2010, Australia

Location

St George Hospital

Kogarah, New South Wales, 2217, Australia

Location

Royal Adelaide Hospital

Adelaide, South Australia, 5000, Australia

Location

Landeskrankenhaus Salzburg, Universitatsklinik fur Innere Medizin III der PMU

Salzburg, 5020, Austria

Location

Uniklinikum Salzburg, Landeskrankenhaus Salzburg

Salzburg, 5020, Austria

Location

Krankenhaus Hietzing mit Neurologischem Zentrum Rosenhugel

Vienna, 1130, Austria

Location

AZ Sint-Jan Brugge-Oostende av

Bruges, B-8000, Belgium

Location

Universitaire Ziekenhuizen Brussel (UZ Brussel)

Brussels, B-1090, Belgium

Location

Universitaire Ziekenhuizen Brussel

Brussels, B-1090, Belgium

Location

Universitaire Ziekenhuizen Leuven

Leuven, B-3000, Belgium

Location

Health Sciences Centre

Winnipeg, Manitoba, R3A 1R9, Canada

Location

CancerCare Manitoba

Winnipeg, Manitoba, R3E 0V9, Canada

Location

Sunnybrook Research Institute

Toronto, Ontario, M4N 3M5, Canada

Location

Princess Margaret Cancer Centre

Toronto, Ontario, M5G 2M9, Canada

Location

CIUSSS de l'Est-de-l'Ile-de- Montréal - Hôpital Maisonneuve-Rosemont

Montreal, Quebec, H1T 2M4, Canada

Location

Royal University Hospital

Saskatoon, Saskatchewan, S7N 0W8, Canada

Location

Saskatoon Cancer Centre

Saskatoon, Saskatchewan, S7N 4H4, Canada

Location

The First Affiliated Hospital of USTC, Anhui Provincial Hospital

Hefei, Anhui, 230001, China

Location

Anhui Provincial Hospital

Hefei, Anhui, 230071, China

Location

Fujian Medical University Union Hospital

Fuzhou, Fujian, 350001, China

Location

Guangdong Provincial People's Hospital

Guangzhou, Guangdong, 510080, China

Location

Guangdong Second Provincial General Hospital

Guangzhou, Guangdong, 510317, China

Location

Hebei Yanda Lu Daopei Hospital

Langfang, Hebei, 065201, China

Location

Henan Provincial People's Hospital/Hematology Department

Zhengzhou, Henan, 450003, China

Location

Henan Cancer Hospital

Zhengzhou, Henan, 450008, China

Location

Tongji Hospital, Tongji Medical College, Huazhong University of Science & Technology/Cancer Center

Wuhan, Hubei, 430030, China

Location

West China Hospital, Sichuan University

Chengdu, Sichuan, 610041, China

Location

Institute of Hematology and Blood Diseases Hospital, Chinese Academy of Medical Sciences

Tianjin, Tianjin Municipality, 300020, China

Location

The First Affiliated Hospital College of Medicine, Zhejiang University

Hangzhou, Zhejiang, 310003, China

Location

Ruijin Hospital Affiliated to Shanghai Jiaotong University School of Medicine

Shanghai, 200025, China

Location

Interni hematologicka a onkologicka klinika, Fakultni nemocnice Brno

Brno, 625 00, Czechia

Location

Nemocnicni lekarna

Brno, 625 00, Czechia

Location

Ustavni lekarna

Ostrava - Poruba, 708 52, Czechia

Location

Klinika hematoonkologie

Ostrava-Poruba, 708 52, Czechia

Location

Interní hematologická klinika, Fakultni nemocnice Královské Vinohrady

Prague, 100 34, Czechia

Location

Ústavni lékárna

Prague, 100 34, Czechia

Location

CHU Henri Mondor

Créteil, 94010, France

Location

CHU de Nantes Hotel Dieu

Nantes, 44093, France

Location

CHU de Nantes

Nantes, 44093, France

Location

Hopital Saint Louis

Paris, 75010, France

Location

Centre Hospitalier Lyon Sud - Service d'Hematologie

Pierre-Bénite, 69495, France

Location

Institut Gustave Roussy

Villejuif, 94805, France

Location

Klinikum der Universitaet Muenchen

Munich, Bavaria, 81377, Germany

Location

Philipps-Universitaet Marburg

Marburg, Hesse, 35032, Germany

Location

Universitätsklinikum Köln

Cologne, North Rhine-Westphalia, 50937, Germany

Location

Universitaetsklinikum Muenster

Münster, North Rhine-Westphalia, 48149, Germany

Location

Universitaetsklinikum Hamburg-Eppendorf

Hamburg, 20246, Germany

Location

Medizinische Hochschule Hannover

Hanover, 30625, Germany

Location

Debreceni Egyetem Klinikai Kozpont Belgyogyaszati Klinika, Hematologia Tanszek

Debrecen, 4032, Hungary

Location

Debreceni Egyetem Klinikai Kozpont Belgyogyaszati Klinika

Debrecen, 4032, Hungary

Location

Petz Aladár Megyei Oktató Kórház, II. Belgyógyászat- Hematológiai Osztály

Győr, 9024, Hungary

Location

Somogy Megyei Kaposi Mor Oktato Korhaz

Kaposvár, 7400, Hungary

Location

Szabolcs-Szatmar Bereg Megyei Korhazak es Egyetemi Oktatokorhaz, Josa Andras Korhaz, Hematologia

Nyíregyháza, 4400, Hungary

Location

Szabolcs-Szatmar Bereg Megyei Korhazak es Egyetemi Oktatokorhaz, Josa Andras Korhaz,

Nyíregyháza, 4400, Hungary

Location

Rambam Health Care Campus

Haifa, 3109601, Israel

Location

Shaare Zedek Medical Center

Jerusalem, 9103102, Israel

Location

Hadassah Medical Center (Ein Kerem)

Jerusalem, 91120, Israel

Location

Hemato-oncology ambulatory Service

Petah Tikva, 4941492, Israel

Location

Rabin Medical Center, Beilinson Hospital

Petah Tikva, 4941492, Israel

Location

AOU Ospedali Riuniti Umberto I, G.M. Lancisi, G. Salesi, Clinica Di Ematologia

Torrette Di Ancona, Ancona, 60126, Italy

Location

SOD Farmacia-Dipt dei servizi -AOU Ospedali Riuniti Umberto I, G.M. Lancisi, G. Salesi

Torette Di Ancona, AN, 60126, Italy

Location

A.O.U. di Ferrara- Arcispedale Sant'Anna,

Cona, Ferrara, FE, 44124, Italy

Location

AO Ospedali Riuniti Marche Nord - Presidio Ospedaliero San Salvatore di Pesaro -

Pesaro, PU, 61122, Italy

Location

Azienda Ospedaliera Universitaria Senese.

Siena, SI, 53100, Italy

Location

Azienda Ospedaliero Universitaria di Bologna Policlinico S.Orsola Malpighi

Bologna, 40138, Italy

Location

Azienda Ospedaliera Universitaria Senese

Siena, 53100, Italy

Location

Japanese Red Cross Nagoya Daini Hospital

Nagoya, Aichi-ken, 466-8650, Japan

Location

University of Fukui Hospital

Yoshida-gun, Fukui, 910-1193, Japan

Location

Gunma University Hospital

Maebashi, Gunma, 371-8511, Japan

Location

Kobe University Hospital

Kobe, Hyōgo, 650-0017, Japan

Location

Yokohama City University Medical Center

Yokohama, Kanagawa, 232-0024, Japan

Location

Tohoku University Hospital

Sendai, Miyagi, 980-8574, Japan

Location

Osaka City University Hospital

Osaka, Osaka, 545-8586, Japan

Location

Kindai University Hospital

Ōsaka-sayama, Osaka, 589-8511, Japan

Location

Shizuoka Cancer Center

Sunto-gun, Shizuoka, 411-8777, Japan

Location

National Hospital Organization Disaster Medical Center

Tachikawa, Tokyo, 190-0014, Japan

Location

Akita University Hospital

Akita, 010-8543, Japan

Location

Kyushu University Hospital

Fukuoka, 812-8582, Japan

Location

National Hospital Organization Kumamoto Medical Center

Kumamoto, 860-0008, Japan

Location

Nagasaki University Hospital

Nagasaki, 852-8501, Japan

Location

Tokyo Medical University Hospital

Tokyo, 160-0023, Japan

Location

Instituto Nacional de Cancerología

México, MÉX, 14080, Mexico

Location

Hospital Universitario "Dr. Jose Eleuterio Gonzalez"

Monterrey, Nuevo León, 64460, Mexico

Location

Klinika Hematologii i Transplantologii Uniwersyteckie Centrum Kliniczne

Gdansk, 80-214, Poland

Location

WWCOiT im. M. Kopernika w Lodzi

Lodz, 93-513, Poland

Location

Institutul Oncologic 'Prof. Dr. Ion Chiricuta'

Cluj-Napoca, Cluj, 400124, Romania

Location

Spitalul Clinic Municipal Filantropia Craiova, Sectia Clinica Hematologie

Craiova, Dolj, 200136, Romania

Location

Sp. Clinic de Urgenta Militar Central Dr. Carol Davila

Bucharest, 010825, Romania

Location

Spitalul Clinic Coltea, Clinica de Hematologie

Bucharest, 030171, Romania

Location

State Budgetary Healthcare Institution of Moscow

Moscow, 129301, Russia

Location

SBHI NNR NN RCH n. a. N.A. Semashko

Nizhny Novgorod, 603126, Russia

Location

State Budgetary Institution of Ryazan Region 'Regional Clinical Hospital' (SBI RR RCH)

Ryazan, 390039, Russia

Location

V.A Almazov NMRC

Saint Petersburg, 197341, Russia

Location

Chonbuk National University Hospital

Jeonju, Jeollabuk-do, 54907, South Korea

Location

Inje University Busan Paik Hospital

Busan, 47392, South Korea

Location

Keimyung University Dongsan Hospital

Daegu, 42601, South Korea

Location

Gachon University Gil Medical Center

Incheon, 21565, South Korea

Location

Seoul National University Hospital

Seoul, 03080, South Korea

Location

Clinical Trial Center, Severance Hospital, Yonsei University Health System

Seoul, 03722, South Korea

Location

Severance Hospital, Yonsei University Health System

Seoul, 03722, South Korea

Location

Samsung Medical Center

Seoul, 06351, South Korea

Location

The Catholic University of Korea Seoul St. Mary's Hospital

Seoul, 06591, South Korea

Location

Hospital del Mar

Barcelona, 08003, Spain

Location

Hospital de la Santa Creu i Sant Pau

Barcelona, 08025, Spain

Location

Hospital Universitario Arnau de Vilanova

Lleida, 25198, Spain

Location

Hospital General Universitario Gregorio Maranon

Madrid, 28007, Spain

Location

Hospital Universitario Ramon y Cajal

Madrid, 28034, Spain

Location

Hospital Universitario Virgen del Rocio

Seville, 41013, Spain

Location

Hospital Universitari i Politecnic La Fe

Valencia, 46026, Spain

Location

Universitetssjukhuset Orebro

Örebro, 701 85, Sweden

Location

Karolinska Universitetssjukhuset Huddinge

Stockholm, 141 86, Sweden

Location

National Cheng Kung University Hospital

Tainan, 704, Taiwan

Location

National Taiwan University Hospital

Taipei, 100, Taiwan

Location

Taipei Veterans General Hospital

Taipei, 11217, Taiwan

Location

Koo Foundation Sun Yat-Sen Cancer Center

Taipei, 112, Taiwan

Location

Chang Gung Memorial Hospital-Linkou Branch

Taoyuan, 333, Taiwan

Location

The Royal Marsden NHS Foundation Trust

Sutton, Surrey, SM2 5PT, United Kingdom

Location

University Hospitals Birmingham NHS Foundation Trust

Birmingham, WEST Midlands, B15 2TH, United Kingdom

Location

Imperial College Healthcare NHS Trust

London, W12 0HS, United Kingdom

Location

Related Publications (2)

  • Sekeres MA, Montesinos P, Novak J, Wang J, Jeyakumar D, Tomlinson B, Mayer J, Jou E, Robak T, Taussig DC, Dombret H, Merchant A, Shaik N, O'Brien T, Roh W, Liu X, Ma W, DiRienzo CG, Chan G, Cortes JE. Glasdegib plus intensive or non-intensive chemotherapy for untreated acute myeloid leukemia: results from the randomized, phase 3 BRIGHT AML 1019 trial. Leukemia. 2023 Oct;37(10):2017-2026. doi: 10.1038/s41375-023-02001-z. Epub 2023 Aug 21.

  • Cortes JE, Dombret H, Merchant A, Tauchi T, DiRienzo CG, Sleight B, Zhang X, Leip EP, Shaik N, Bell T, Chan G, Sekeres MA. Glasdegib plus intensive/nonintensive chemotherapy in untreated acute myeloid leukemia: BRIGHT AML 1019 Phase III trials. Future Oncol. 2019 Nov;15(31):3531-3545. doi: 10.2217/fon-2019-0373. Epub 2019 Sep 13.

Related Links

MeSH Terms

Conditions

Leukemia, Myeloid, Acute

Interventions

glasdegibDaunorubicinCytarabineAzacitidine

Condition Hierarchy (Ancestors)

Leukemia, MyeloidLeukemiaNeoplasms by Histologic TypeNeoplasmsHematologic DiseasesHemic and Lymphatic Diseases

Intervention Hierarchy (Ancestors)

AnthracyclinesNaphthacenesPolycyclic Aromatic HydrocarbonsHydrocarbons, AromaticHydrocarbons, CyclicHydrocarbonsOrganic ChemicalsPolycyclic CompoundsAminoglycosidesGlycosidesCarbohydratesCytidinePyrimidine NucleosidesPyrimidinesHeterocyclic Compounds, 1-RingHeterocyclic CompoundsArabinonucleosidesNucleosidesNucleic Acids, Nucleotides, and NucleosidesAza CompoundsRibonucleosides

Limitations and Caveats

In this study, inadvertently a participant was counted twice for an non-SAE "Pyrexia" at PCD, at SCD update this duplicity has been rectified. Due to this reason total number of participants affected by non-SAE in non-intensive placebo arm was updated to "148".

Results Point of Contact

Title
Pfizer ClinicalTrials.gov Call Center
Organization
Pfizer Inc.

Study Officials

  • Pfizer CT.gov Call Center

    Pfizer

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Masking Details
Double blind study.
Purpose
TREATMENT
Intervention Model
PARALLEL
Model Details: Randomized, double-blind, multi-center, placebo controlled study.
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

December 21, 2017

First Posted

January 31, 2018

Study Start

April 20, 2018

Primary Completion

June 5, 2020

Study Completion

January 17, 2022

Last Updated

April 21, 2023

Results First Posted

June 25, 2021

Record last verified: 2023-04

Data Sharing

IPD Sharing
Will share

Pfizer will provide access to individual de-identified participant data and related study documents (e.g. protocol, Statistical Analysis Plan (SAP), Clinical Study Report (CSR)) upon request from qualified researchers, and subject to certain criteria, conditions, and exceptions. Further details on Pfizer's data sharing criteria and process for requesting access can be found at: https://www.pfizer.com/science/clinical\_trials/trial\_data\_and\_results/data\_requests.

More information

Locations