NCT01081769

Brief Summary

The purpose of this study is to assess the efficacy (how well the drug works; primarily through the time to relapse) of long-acting injectable paliperidone palmitate compared to treatment as usual with orally administered antipsychotics in monotherapy over 24 months in the treatment of recently diagnosed (1-5 years since diagnosis) schizophrenia.

Trial Health

98
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
769

participants targeted

Target at P75+ for phase_3 schizophrenia

Timeline
Completed

Started Feb 2010

Typical duration for phase_3 schizophrenia

Geographic Reach
24 countries

92 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

February 1, 2010

Completed
1 month until next milestone

First Submitted

Initial submission to the registry

March 4, 2010

Completed
1 day until next milestone

First Posted

Study publicly available on registry

March 5, 2010

Completed
2.9 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

February 1, 2013

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

February 1, 2013

Completed
2 years until next milestone

Results Posted

Study results publicly available

February 18, 2015

Completed
Last Updated

February 18, 2015

Status Verified

February 1, 2015

Enrollment Period

3 years

First QC Date

March 4, 2010

Results QC Date

November 17, 2014

Last Update Submit

February 17, 2015

Conditions

Keywords

Schizophreniapaliperidone palmitateInvegaIntramuscular injectionOral antipsychoticsRelapse

Outcome Measures

Primary Outcomes (2)

  • Time to First Relapse Event

    Number of days from baseline (day 1 of core phase) to relapse as evaluated according the Csernansky criteria. A patient was considered to have relapsed if they met one or more of the following criteria: (1) psychiatric hospitalization; (2) an increase in the level of psychiatric care and an increase of 25 percent (%) from baseline in the Positive And Negative Syndrome Score (PANSS) total score (or an increase of 10 points if the baseline score was 40 or less); (3) deliberate self-injury; (4) suicidal or homicidal ideation that was clinically significant in the investigator's judgment; (5) violent behavior resulting in clinically significant injury to another person or property damage; (6) substantial clinical deterioration, defined as a change score of 6 ("much worse") or 7 ("very much worse") on the Clinical Global Impressions Scale (CGI-C); and/or (7) the required dose of the antipsychotic exceeds the maximum approved dose.

    from baseline (Day 1 of core phase) up to maximally 24 months.

  • Number of Participants With a Relapse Event

    Number of participants with a relapse event with relapses evaluated according the Csernansky criteria. A patient was considered to have relapsed if they met one or more of the following criteria: (1) psychiatric hospitalization; (2) an increase in the level of psychiatric care and an increase of 25% from baseline in the PANSS total score (or an increase of 10 points if the baseline score was 40 or less); (3) deliberate self-injury; (4) suicidal or homicidal ideation that was clinically significant in the investigator's judgment; (5) violent behavior resulting in clinically significant injury to another person or property damage; (6) substantial clinical deterioration, defined as a change score of 6 ("much worse") or 7 ("very much worse") on the Clinical Global Impressions Scale (CGI-C); and/or (7) the required dose of the antipsychotic exceeds the maximum approved dose.

    from baseline (Day 1 of core phase) up to maximally 24 months

Secondary Outcomes (13)

  • Percentage of Treatment Responders

    from baseline (day 1 of core phase) up to maximally 24 months

  • Change From Baseline in PANSS Total Score

    Baseline, day 8, month 1, 2, 3, 4, 6, 9, 12, 15, 18, 21, 24

  • Change From Baseline in PANSS Subscale Score

    Baseline (day 1 of core phase), day 8, month 12, 24

  • Change From Baseline in PANSS Marder Factor Scores

    Baseline (day 1 of core phase), day 8, month 12 and 24

  • Change From Baseline in Clinical Global Impression Severity (CGI-S) Score

    Baseline (day 1 of core phase), day 8, month 1, 2, 3, 4, 6, 9, 12, 15, 18, 21, 24

  • +8 more secondary outcomes

Study Arms (2)

Paliperidone Palmitate

EXPERIMENTAL

paliperidone palmitate injection with 150 mg equivalent on Day 1 100 mg equivalent on Day 8 75 mg equivalent on Day 38 and flexible dosing with 25 50 75 100 or 150 mg equivalent once monthly thereafter

Drug: paliperidone palmitate injection

Oral Antipsychotics

ACTIVE COMPARATOR

oral antipsychotics daily treatment according to local label for maximally 24 months

Drug: oral antipsychotics

Interventions

injection with 150 mg equivalent on Day 1, 100 mg equivalent on Day 8, 75 mg equivalent on Day 38 and flexible dosing with 25, 50, 75, 100 or 150 mg equivalent once monthly thereafter

Paliperidone Palmitate

daily treatment according to local label for maximally 24 months

Oral Antipsychotics

Eligibility Criteria

Age18 Years - 65 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Have been meeting the diagnostic criteria for schizophrenia for 1 to 5 years before screening, and have a history of treatment with antipsychotics
  • Have a history of two or more relapses requiring psychiatric hospitalization in the preceding 24 months, which may include the current acute episode
  • Experiencing at screening an acute schizophrenic episode with a Positive And Negative Syndrome Scale (PANSS) total score at screening between 70 and 120, inclusive
  • Be healthy on the basis of physical examination, medical history and vital signs performed at screening
  • Woman must be postmenopausal (for at least 1 year) or surgically sterile or abstinent or be practicing an effective method of birth control, must agree to continue to use the same method of contraception throughout the study and must have a negative urine pregnancy test at screening
  • be able to fill out questionnaires
  • Men must agree to use a double barrier method of birth control and to not donate sperm during the study and for 3 months after receiving the last dose of study drug

You may not qualify if:

  • Patients that have never been treated with antipsychotics before
  • Treatment resistant patient and/or currently (i.within the last 3 months) treated with clozapine
  • Substance dependence within 6 months prior to entry and current intravenous drug use or abuse
  • allergies, hypersensitivity, or intolerance to risperidone or paliperidone or excipients
  • treatment with a long-acting injectable antipsychotic within three injection cycles prior to screening
  • newly started psychotherapy program within the two months preceding the treatment phase baseline
  • evidence of clinically significant hepatic, renal, cardiac, vascular, pulmonary, gastrointestinal, endocrine, neurologic, hematologic, rheumatologic, psychiatric, or metabolic disturbances in the past 6 months (as determined by medical history, clinical laboratory or ECG results, or physical examination) that would increase the risk associated with taking study medication or would confound the interpretation of the study
  • history or current symptoms of tardive dyskinesia or neuroleptic malignant syndrome
  • involuntarily hospitalized patient
  • pregnant or breast-feeding females

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (94)

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Vienna, Austria

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Bertrix, Belgium

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Ghent, Belgium

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Liège, Belgium

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Ostend, Belgium

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Burgas, Bulgaria

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Plovdiv, Bulgaria

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Radnevo, Bulgaria

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Zagreb, Croatia

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Brno, Czechia

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Litoměřice, Czechia

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Olomouc, Czechia

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Prague, Czechia

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Přerov, Czechia

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Alexandria, Egypt

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Cairo, Egypt

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Talinn, Estonia

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Tartu, Estonia

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Colombes, France

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La Seyne-sur-Mer, France

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Limoges, France

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Metz, France

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Paris, France

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Saint-Avé, France

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Berlin, Germany

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Bochum, Germany

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Mannheim, Germany

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München, Germany

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Thessalonikis, Greece

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Budapest, Hungary

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Kalocsa, Hungary

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Nagykálló, Hungary

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Sopron, Hungary

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Bat Yam, Israel

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Beer Yaakov, Israel

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Hod HaSharon, Israel

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Ramat Gan, Israel

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Tirat Hacarmel, Israel

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Amman, Jordan

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Šiauliai, Lithuania

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Vilnius, Lithuania

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Chełmno, Poland

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Gdansk, Poland

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Torun, Poland

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Ząbki, Poland

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Arad, Romania

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Bucharest, Romania

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Jebel, Romania

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Oradea, Romania

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Sibiu, Romania

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Ekaterinburg Na, Russia

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Krasnodar, Russia

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Nizny Novgorod, Russia

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Saint Petersburg, Russia

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Samara, Russia

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Saratov, Russia

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Tomsk, Russia

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Yaroslavl, Russia

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Bratislava, Slovakia

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Michalovce, Slovakia

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Rimavská Sobota, Slovakia

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Cape Town, South Africa

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Pretoria, South Africa

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Goyang, South Korea

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Incheon, South Korea

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Kyounggi, South Korea

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Seoul, South Korea

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Barcelona, Spain

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Burgos, Spain

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Elche, Spain

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Madrid, Spain

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Sant Boi de Llobregat, Spain

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Zamora, Spain

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Taichung, Taiwan

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Taipei, Taiwan

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Taoyuan District, Taiwan

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Istanbul, Turkey (Türkiye)

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Manisa Turkey, Turkey (Türkiye)

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Zonguldak, Turkey (Türkiye)

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Dnipropetrovsk, Ukraine

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Donetsk, Ukraine

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Hlevakha, Ukraine

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Kharkiv, Ukraine

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Kherson, Ukraine

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Kiev, Ukraine

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Lviv, Ukraine

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Odesa, Ukraine

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Poltava, Ukraine

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Simferopol, Ukraine

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Uzhhorod, Ukraine

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Birmingham, United Kingdom

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Exeter, United Kingdom

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London, United Kingdom

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Warrington, United Kingdom

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Related Publications (1)

  • Lopena OJ, Alphs LD, Sajatovic M, Turkoz I, Sun L, Johnston KL, Sliwa JK, Najarian DM, Starr HL. Earlier Use of Long-Acting Injectable Paliperidone Palmitate Versus Oral Antipsychotics in Patients With Schizophrenia: An Integrated Patient-Level Post Hoc Analysis. J Clin Psychiatry. 2023 Sep 25;84(6):23m14788. doi: 10.4088/JCP.23m14788.

MeSH Terms

Conditions

SchizophreniaRecurrence

Interventions

Paliperidone PalmitateAntipsychotic Agents

Condition Hierarchy (Ancestors)

Schizophrenia Spectrum and Other Psychotic DisordersMental DisordersDisease AttributesPathologic ProcessesPathological Conditions, Signs and Symptoms

Intervention Hierarchy (Ancestors)

IsoxazolesAzolesHeterocyclic Compounds, 1-RingHeterocyclic CompoundsPyrimidinesTranquilizing AgentsCentral Nervous System DepressantsPhysiological Effects of DrugsPharmacologic ActionsChemical Actions and UsesCentral Nervous System AgentsTherapeutic UsesPsychotropic Drugs

Results Point of Contact

Title
EMEA Medical Affairs Director Psychiatry
Organization
Janssen-Cilag Germany

Study Officials

  • Janssen-Cilag International NV Clinical Trial

    Janssen-Cilag International NV

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

March 4, 2010

First Posted

March 5, 2010

Study Start

February 1, 2010

Primary Completion

February 1, 2013

Study Completion

February 1, 2013

Last Updated

February 18, 2015

Results First Posted

February 18, 2015

Record last verified: 2015-02

Locations