NCT01281527

Brief Summary

This study explores the tolerability, safety and efficacy (i.e. how well the drug works) of flexibly dosed paliperidone palmitate in the treatment of schizophrenia in patients previously unsuccessfully treated with other oral or long-acting injectable (LAI) (i.e. with a long duration of action) antipsychotics.

Trial Health

98
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Strong global presence with extensive site network
Enrollment
1,044

participants targeted

Target at P75+ for phase_3 schizophrenia

Timeline
Completed

Started Nov 2010

Typical duration for phase_3 schizophrenia

Geographic Reach
19 countries

112 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

November 1, 2010

Completed
3 months until next milestone

First Submitted

Initial submission to the registry

January 20, 2011

Completed
4 days until next milestone

First Posted

Study publicly available on registry

January 24, 2011

Completed
1.8 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

November 1, 2012

Completed
1 year until next milestone

Study Completion

Last participant's last visit for all outcomes

November 1, 2013

Completed
Last Updated

March 10, 2014

Status Verified

March 1, 2014

Enrollment Period

2 years

First QC Date

January 20, 2011

Last Update Submit

March 6, 2014

Conditions

Keywords

Paliperidone palmitateSchizophreniaIntramuscular injection

Outcome Measures

Primary Outcomes (3)

  • Improved efficacy for non-acute patients transitioned due to lack of efficacy, as measured by the total PANSS score at endpoint versus baseline.

    Baseline to 6 months or early discontinuation

  • Improved efficacy for acute patients, as measured by the total PANSS score at endpoint versus baseline.

    Baseline to 6 months or early discontinuation

  • Maintained efficacy for non-acute patients transitioned for other reasons based on PANSS score at endpoint versus baseline.

    Baseline to 6 months or early discontinuation

Secondary Outcomes (5)

  • Change from baseline in Clinical Global Impression-Severity Scale [CGI-S]

    Baseline, week 1, month 1, 2, 3 and 6

  • Change from baseline in personal and social functioning (Personal and Social Performance Scale [PSP])

    Baseline, week 1, month 1, 2, 3 and 6

  • Change from baseline in Health status (Self-reported health status questionnaire [SF-36])

    Baseline, month 3 and 6

  • Change from baseline in Measure of Health Outcome (EQ-5D)

    Baseline, month 3 and 6

  • Change from baseline in Patient well-being (Subjective Well-Being under Neuroleptics Scale [SWN-S]);

    Baseline, month 3 and 6

Study Arms (1)

Paliperidone Palmitate

EXPERIMENTAL

Paliperidone Palmitate 50 - 150 mg eq. every 30 days for 6 months during the core phase and for 12 months during an optional extension phase after the last patient has completed the 6-month core treatment phase or until product will be available on market (whichever comes first)

Drug: Paliperidone Palmitate

Interventions

50 - 150 mg eq. every 30 days

Paliperidone Palmitate

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Meet the DSM-IV criteria for schizophrenia Currently non-acute, i.e., on the same antipsychotic medication used for the treatment of schizophrenia given in an adequate dose and a CGI-S change \<= 1 in the past 4 weeks before enrollment Patient has been given an adequate dose of either an appropriate oral antipsychotic, or a protocol-defined LAI antipsychotic for an adequate period of time prior to enrollment, but current treatment is considered unsuccessful OR Patients with acute symptoms of schizophrenia, previously treated with an oral antipsychotic, having a baseline total Positive and Negative Syndrome Scale (PANSS) score \>= 80 and a baseline CGI-S score \>= 4 Women must be postmenopausal for at least 1 year, surgically sterile, abstinent (at the discretion of the investigator/per local regulations), or if sexually active, be practicing a highly effective method of birth control as local regulations permit, and before entry, must agree to continue to use the same method of contraception throughout the study Is cooperative and reliable, and agrees to receive regular injections and complete all aspects of the protocol Men must agree to use a double barrier method of birth control and to not donate sperm during the study and for 3 months after receiving the last dose of study drug.

You may not qualify if:

  • The patient's psychiatric diagnosis is due to direct pharmacological effects of a substance (e.g., a drug of abuse or medication) or a general medical condition (e.g., clinically notable hypothyroidism) First antipsychotic treatment ever, i.e., patient has never been treated with antipsychotics before and antipsychotic treatment given in this study will be the first antipsychotic treatment that the patient will have ever received On clozapine during the last 3 months Patients who remain at imminent risk of suicide even after clinical intervention Serious unstable medical condition, including recent and present clinically relevant laboratory abnormalities

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (127)

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Salzburg, Austria

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Brussels, Belgium

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Dave, Belgium

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Diest, Belgium

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Kruishoutem, Belgium

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Liège, Belgium

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Melle, Belgium

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Roeselare, Belgium

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Sint-Denijs-Westrem, Belgium

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Tournai, Belgium

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Rijeka, Croatia

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Zagreb, Croatia

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Aalborg, Denmark

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København V, Denmark

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Randers, Denmark

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Tallinn, Estonia

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Bar-le-Duc, France

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Bron, France

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Clermont-Ferrand, France

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Dax, France

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Dijon, France

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Dole, France

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Lille, France

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Limoges, France

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Montpellier, France

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Nîmes, France

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Paris, France

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Saint-Nazaire, France

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Saint-Priest-en-Jarez, France

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Strasbourg, France

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Villejuif, France

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Bad Saarow, Germany

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Berlin, Germany

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Bielefeld, Germany

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Bochum, Germany

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Butzbach, Germany

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Dresden, Germany

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Gelsenkirchen, Germany

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Greifswald, Germany

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Hamburg, Germany

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Heidelberg, Germany

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Königsbrück, Germany

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Mittweida, Germany

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Oranienburg, Germany

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Regensburg, Germany

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Stralsund, Germany

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Ulm, Germany

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Westerstede, Germany

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Würzburg, Germany

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Arta, Greece

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Athens, Greece

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Katerini, Greece

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Thessaloniki, Greece

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Thessalonikis, Greece

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Budapest, Hungary

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Debrecen, Hungary

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Pécs, Hungary

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Pardesiyya, Israel

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Ramat Gan, Israel

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Tirat Hacarmel, Israel

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Daugavpils, Latvia

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Jelgava, Latvia

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Liepāja, Latvia

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Riga, Latvia

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Sigulda, Latvia

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Strenči, Latvia

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Panevezys, Lithuania

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Vilnius, Lithuania

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Groningen, Netherlands

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Almada, Portugal

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Angra do Heroísmo, Portugal

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Castelo Viegas, Portugal

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Coimbra, Portugal

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Lisbon, Portugal

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Porto, Portugal

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Alcorcón, Spain

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Alicante, Spain

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Barcelona, Spain

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Burgos, Spain

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Coslada, Spain

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Elche, Spain

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Madrid, Spain

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Málaga, Spain

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Palma de Mallorca, Spain

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Sant Boi de Llobregat, Spain

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Sant Joan d'Alacant, Spain

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Santa Coloma de Gramenet, Spain

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Vigo, Spain

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Zamora, Spain

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Zaragoza, Spain

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Gothenburg, Sweden

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Lidingö, Sweden

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Malmo, Sweden

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Mölndal, Sweden

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Spånga, Sweden

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Upplands Vasby, Sweden

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Solothurn, Switzerland

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Zurich, Switzerland

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Ankara, Turkey (Türkiye)

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Diyarbakır, Turkey (Türkiye)

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Gaziantep, Turkey (Türkiye)

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Istanbul, Turkey (Türkiye)

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Izmir, Turkey (Türkiye)

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Trabzon, Turkey (Türkiye)

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Dnipro, Ukraine

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Donetsk, Ukraine

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Hlevakha, Ukraine

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Ivano-Frankivsk, Ukraine

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Kharkiv, Ukraine

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Kiev, Ukraine

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Lviv, Ukraine

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Odesa, Ukraine

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Poltava, Ukraine

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Simferopol, Ukraine

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Smila, Ukraine

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Ternopil, Ukraine

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Uzhhorod, Ukraine

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Yevpatoria, Ukraine

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Barnet, United Kingdom

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Birmingham, United Kingdom

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Cambridge, United Kingdom

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Coventry, United Kingdom

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Darlington, United Kingdom

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Lincoln, United Kingdom

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London, United Kingdom

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Prescott, United Kingdom

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Stoke-on-Trent, United Kingdom

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Related Publications (1)

  • Schreiner A, Bergmans P, Cherubin P, Keim S, Rancans E, Bez Y, Parellada E, Carpiniello B, Vidailhet P, Hargarter L. A prospective flexible-dose study of paliperidone palmitate in nonacute but symptomatic patients with schizophrenia previously unsuccessfully treated with oral antipsychotic agents. Clin Ther. 2014 Oct 1;36(10):1372-88.e1. doi: 10.1016/j.clinthera.2014.08.014. Epub 2014 Oct 23.

Related Links

MeSH Terms

Conditions

Schizophrenia

Interventions

Paliperidone Palmitate

Condition Hierarchy (Ancestors)

Schizophrenia Spectrum and Other Psychotic DisordersMental Disorders

Intervention Hierarchy (Ancestors)

IsoxazolesAzolesHeterocyclic Compounds, 1-RingHeterocyclic CompoundsPyrimidines

Study Officials

  • Janssen-Cilag International NV Clinical Trial

    Janssen-Cilag International NV

    STUDY DIRECTOR

Study Design

Study Type
interventional
Phase
phase 3
Allocation
NA
Masking
NONE
Purpose
TREATMENT
Intervention Model
SINGLE GROUP
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

January 20, 2011

First Posted

January 24, 2011

Study Start

November 1, 2010

Primary Completion

November 1, 2012

Study Completion

November 1, 2013

Last Updated

March 10, 2014

Record last verified: 2014-03

Locations